A Study to Evaluate the Safety and Efficacy of CT1812 in Early Alzheimer's Disease

NCT ID: NCT05531656

Last Updated: 2025-09-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

540 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-06-28

Study Completion Date

2027-04-30

Brief Summary

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This is a multicenter randomized, double-blind, placebo-controlled Phase 2 study designed to evaluate the efficacy, safety, and tolerability of two doses of CT1812 compared to placebo in participants diagnosed with early Alzheimer's disease.

Detailed Description

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This is a multicenter randomized, double-blind, placebo-controlled Phase 2 study designed to evaluate the efficacy, safety, and tolerability of two doses of CT1812 compared to placebo for approximately 18 months (72 weeks) in approximately 540 participants diagnosed with early Alzheimer's disease

Participants will be randomized 1:1:1 to receive either 100mg or 200mg of CT1812 or placebo. CT1812 or placebo will be administered as 2 capsules to be taken orally once daily.

Conditions

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Early Alzheimer's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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CT1812 100 mg

CT1812 at a dose of 100 n=180 group

Group Type ACTIVE_COMPARATOR

CT1812

Intervention Type DRUG

Study Drug

CT1812 200 mg

CT1812 at a dose of 300mg, n=180 group

Group Type ACTIVE_COMPARATOR

CT1812

Intervention Type DRUG

Study Drug

Placebo

Placebo, n=180 group

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Non-active study drug

Interventions

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CT1812

Study Drug

Intervention Type DRUG

Placebo

Non-active study drug

Intervention Type DRUG

Other Intervention Names

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Study Drug Active Matching Placebo

Eligibility Criteria

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Inclusion Criteria

1. Ages 50-85 years.
2. Diagnosis of either MCI due to AD or mild AD dementia.
3. MMSE 20-30 (inclusive).
4. Amyloid PET scan of the brain or CSF biomarkers consistent with AD.
5. Neuroimaging (MRI) obtained during screening consistent with the clinical diagnosis of Alzheimer's disease, as based on central read.

Exclusion Criteria

1. Screening MRI of the brain indicative of significant abnormality.
2. Clinically significant abnormalities in screening laboratory tests.
3. Clinical or laboratory findings consistent with:

1. Other primary degenerative dementia, (dementia with Lewy bodies, fronto-temporal dementia, Huntington's disease, Creutzfeldt-Jakob Disease, Down syndrome, etc.).
2. Other neurodegenerative condition (Parkinson's disease, amyotrophic lateral sclerosis, etc.).
3. Other infectious, metabolic or systemic diseases affecting the central nervous system (syphilis, present hypothyroidism, present vitamin B12, other laboratory values etc.)
4. A participant known to be actively infected with hepatitis B or hepatitis C at screening. History of acute/chronic hepatitis B or C and/or carriers of hepatitis B (seropositive for hepatitis B surface antigen \[HbsAg\] or anti-hepatitis C \[HCV\] antibody). Participants who have evidence of resolved hepatitis infection (e.g., HCV RNA negative) may be considered following discussion with the Medical Monitor.
5. A current DSM-V diagnosis of active major depression or GDS \> 6, schizophrenia, or bipolar disorder.
Minimum Eligible Age

50 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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National Institute on Aging (NIA)

NIH

Sponsor Role collaborator

Alzheimer's Clinical Trials Consortium

OTHER

Sponsor Role collaborator

Cognition Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Anthony Caggiano, MD

Role: STUDY_DIRECTOR

Cognition Therapeutics

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Banner Alzheimer's Institute

Phoenix, Arizona, United States

Site Status

Banner Sun Health Research Institute

Sun City, Arizona, United States

Site Status

University of California

Irvine, California, United States

Site Status

Stanford University

Palo Alto, California, United States

Site Status

Sutter Institute for Medical Research

Sacramento, California, United States

Site Status

Yale University

New Haven, Connecticut, United States

Site Status

Georgetown University

Washington D.C., District of Columbia, United States

Site Status

Howard University

Washington D.C., District of Columbia, United States

Site Status

Brain Matters Research

Delray Beach, Florida, United States

Site Status

Neuropsychiatric Research Center of Southwest Florida

Fort Myers, Florida, United States

Site Status

Mayo Clinic,Jacksonville

Jacksonville, Florida, United States

Site Status

JEM Research Institute

Lake Worth, Florida, United States

Site Status

K2 Medical Research, LLC

Maitland, Florida, United States

Site Status

Advanced Clinical Research Network, Corp

Miami, Florida, United States

Site Status

Charter Research

Orlando, Florida, United States

Site Status

Headlands Research Orlando

Orlando, Florida, United States

Site Status

Brain Matters Research Stuart

Stuart, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Conquest Research, LLC

Winter Park, Florida, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Indiana University

Indianapolis, Indiana, United States

Site Status

Sanders-Brown Center on Aging

Lexington, Kentucky, United States

Site Status

John Hopkins University

Baltimore, Maryland, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

Highlands Research Eastern MA

Plymouth, Massachusetts, United States

Site Status

University of Michigan, Ann Arbor

Ann Arbor, Michigan, United States

Site Status

Mayo Clinic, Rochester

Rochester, Minnesota, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Cleveland Clinic Lou Ruvo Center for Brain Health

Las Vegas, Nevada, United States

Site Status

Mount Sinai School of Medicine

New York, New York, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

University of Rochester Medical Center

Rochester, New York, United States

Site Status

Wake Forest University Health Sciences

Winston-Salem, North Carolina, United States

Site Status

Case Western Reserve University / University Hospitals

Beachwood, Ohio, United States

Site Status

Ohio State University

Columbus, Ohio, United States

Site Status

Central States Research, LLC

Tulsa, Oklahoma, United States

Site Status

Summit Headlands LLC

Portland, Oregon, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

Abington Neurological Associates

Abington, Pennsylvania, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Butler Hospital

Providence, Rhode Island, United States

Site Status

Ralph H. Johnson VA MC

Charleston, South Carolina, United States

Site Status

Vanderbilt University Medical Center Center for Cognitive Medicine

Nashville, Tennessee, United States

Site Status

Vanderbilt University Medical Center Center for Cognitive Medicine

Nashville, Tennessee, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

Houston Methodist Neurological Institute

Houston, Texas, United States

Site Status

University of Texas Health Science Center

San Antonio, Texas, United States

Site Status

University of Wisconsin

Madison, Wisconsin, United States

Site Status

Countries

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United States

Other Identifiers

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R01AG065248

Identifier Type: NIH

Identifier Source: secondary_id

View Link

COG0203

Identifier Type: -

Identifier Source: org_study_id

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