Safety and Efficacy of CDCA in CTX Chenodeoxycholic Acid (CDCA) in Patients Affected by Cerebrotendinous Xanthomatosis (CTX)

NCT ID: NCT05499026

Last Updated: 2022-08-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

28 participants

Study Classification

OBSERVATIONAL

Study Start Date

2014-12-09

Study Completion Date

2015-06-03

Brief Summary

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Retrospective study of CTX patients to investigate the safety and clinical efficacy of Chenodeoxycholic Acid

Detailed Description

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Conditions

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Cerebrotendinous Xanthomatoses

Study Design

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Observational Model Type

COHORT

Study Time Perspective

RETROSPECTIVE

Interventions

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Chenodeoxycholic Acid

Bile acid

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Diagnosis of CTX Received treatment with CDCA Age between 2 and 75 years Having at least one cholestanol level and/or urinary bile alcohol level no more than 3 months prior to treatment with CDCA and one cholestanol level and/or urinary bile alcohol level post-treatment within 2 years from the beginning of therapy with CDCA

Exclusion Criteria

\-
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Leadiant Biosciences Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Other Identifiers

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CDCA-STUK-15-001

Identifier Type: -

Identifier Source: org_study_id

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