A Prospective Registry Study to Assess Real-world Patient Characteristics, Treatment Patterns, and Longitudinal Outcomes in Patients Receiving Mavacamten and Other Treatments for Symptomatic Obstructive Hypertrophic Cardiomyopathy (Obstructive-HCM)

NCT ID: NCT05489705

Last Updated: 2025-11-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Total Enrollment

1600 participants

Study Classification

OBSERVATIONAL

Study Start Date

2022-08-16

Study Completion Date

2029-08-17

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This registry evaluates patient characteristics, real-world treatment patterns, and short- and long-term outcomes in a population of patients in the United States and Europe with symptomatic obstructive hypertrophic cardiomyopathy (HCM) who are receiving mavacamten, receiving other treatment for obstructive HCM, or not receiving treatment for obstructive HCM due to intolerance or failure of prior treatment.

United States Sub-Study: The purpose of this study is to evaluate the safety of mavacamten in patients with symptomatic obstructive HCM in the real-world setting.

Europe Sub-Study: The purpose of this study is to evaluate the effectiveness and safety of mavacamten in patients with symptomatic obstructive HCM in the real-world setting.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Obstructive Hypertrophic Cardiomyopathy

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

Obstructive hypertrophic cardiomyopathy Obstructive HCM (oHCM) Mavacamten Heart failure oHCM

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Mavacamten

Participants will receive mavacamten as prescribed by a physician according to standard of care for symptomatic oHCM

Mavacamten

Intervention Type DRUG

As per product label

Beta-blocker (BB) / non-dihydropyridine (non-DHP) calcium channel blocker (CCB) / disopyramide

Participants will receive BB/non-DHP CCB/disopyramide as prescribed by a physician according to standard of care for symptomatic oHCM

Non-mavacamten symptomatic oHCM therapy

Intervention Type DRUG

Including Beta-blocker (BB), non-dihydropyridine (non-DHP) calcium channel blocker (CCB) and/or disopyramide as per product label

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Mavacamten

As per product label

Intervention Type DRUG

Non-mavacamten symptomatic oHCM therapy

Including Beta-blocker (BB), non-dihydropyridine (non-DHP) calcium channel blocker (CCB) and/or disopyramide as per product label

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* ≥ 18 years of age at the time of informed consent.
* Willing and able to provide written informed consent form (ICF) and any required privacy authorization prior to the initiation of study procedures (or in those situations where consent cannot be given by participants, consent provided by their legally acceptable representatives)

United States Sub-Study

* Diagnosis of obstructive HCM consistent with 2020 American Heart Association/American College of Cardiology (AHA/ACC) guidelines.

* Obstructive HCM is defined clinically by the presence of increased LV wall thickness ≥ 15 mm (or ≥ 13 mm with positive family history of HCM) in a nondilated ventricular chamber that is not solely explained by abnormal loading conditions (eg, another cardiac or systemic disease) and peak LVOT gradient of ≥ 30 mmHg at rest or with provocation.
* Has documented LVEF of ≥ 55% recorded by echocardiography within the last 6 months.
* Symptoms consistent with NYHA functional class II-IV.
* Receiving beta blocker (BB)s, non-dihydropyridine calcium. channel blockers (nonDHP CCBs), disopyramide, and/or mavacamten (once available) as part of routine clinical care; or currently receiving no treatment due to intolerance or failure of prior treatment (eg, BBs, non-DHP CCBs, or disopyramide) for obstructive HCM.

European Sub-study

* Diagnosis of obstructive HCM consistent with the most recent European Society of Cardiology (ESC) and American Heart Association/American College of Cardiology (AHA/ACC) guidelines
* Documented LVEF of ≥55% recorded by TTE
* Documented symptoms consistent with NYHA functional class II-III at enrollment or within 6 months prior to enrollment (if not available at enrollment).
* As part of routine clinical care for obstructive HCM: receiving BBs, non-DHP CCBs, disopyramide; initiating mavacamten at enrollment; or currently receiving no treatment due to intolerance or failure of prior treatment (e.g., BBs, non-DHP CCBs, or disopyramide).

Exclusion Criteria

* Known phenocopy disease (e.g., Fabry disease, amyloidosis) or LV hypertrophy associated with hypertension.
* Documentation of any fixed obstruction of the outflow tract such as aortic valve stenosis or replacement.
* Prior treatment of obstructive HCM with invasive septal reduction (surgical myectomy or percutaneous alcohol septal ablation \[ASA\]) within 6 months prior to enrollment; participants with an unsuccessful myectomy or percutaneous ASA performed \> 6 months prior to enrollment may be enrolled.
* Naïve to treatment for obstructive HCM (ie, never treated with BBs, nonDHP CCBs, or disopyramide).

United States Sub-Study

* Receiving an investigational therapeutic agent for obstructive HCM (eg, myosin-inhibitors other than mavacamten) in an interventional clinical trial at participant enrollment.
* Previously or currently enrolled in a long-term safety extension study of mavacamten (eg, EXPLORER-HCM \[ClinicalTrials.gov, NCT03470545\], MAVA-LTE \[NCT03723655\], PIONEER-OLE \[NCT03496168\], VALORHCM \[NCT04349072\], or MAVERICK \[NCT03442764\])

European Sub-study

* Receiving an investigational therapeutic agent or any cardiac myosin inhibitor and/or modulators for obstructive HCM at patient enrolment
* Previously or currently enrolled in other HCM registry studies (e.g., TORCH, REMY, EU-PASS)
* Previously or currently enrolled in a study of mavacamten (e.g., EXPLORER-HCM \[ClinicalTrials.gov, NCT03470545\], MAVA-LTE \[NCT03723655\], PIONEER-OLE \[NCT03496168\], VALOR-HCM \[NCT04349072\], MAVERICK \[NCT03442764\], or MEMENTO \[NCT2264899\])
* Previously treated with mavacamten
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Alaska Heart Institute

Anchorage, Alaska, United States

Site Status RECRUITING

Pima Heart and Vascular

Tucson, Arizona, United States

Site Status RECRUITING

UAMS

Little Rock, Arkansas, United States

Site Status RECRUITING

UC San Diego School of Medicine

La Jolla, California, United States

Site Status RECRUITING

Keck School of Medicine of USC-Usc

Los Angeles, California, United States

Site Status RECRUITING

Stanford Health Care Hospital & Clinics

Palo Alto, California, United States

Site Status RECRUITING

University Of California San Francisco Medical Center

San Francisco, California, United States

Site Status RECRUITING

UC Denver, AMC

Aurora, Colorado, United States

Site Status RECRUITING

Hartford HealthCare

Hartford, Connecticut, United States

Site Status RECRUITING

MedStar Washington Hospital Center

Washington D.C., District of Columbia, United States

Site Status RECRUITING

Uf Health Jacksonville

Jacksonville, Florida, United States

Site Status RECRUITING

University of Hawaii Cancer Center

Honolulu, Hawaii, United States

Site Status RECRUITING

University of Chicago Dept of Medicine

Chicago, Illinois, United States

Site Status RECRUITING

Indiana. University

Indianapolis, Indiana, United States

Site Status RECRUITING

Franciscan Physician Network-Indiana Heart Physicians

Indianapolis, Indiana, United States

Site Status RECRUITING

University of Iowa Hospitals & Clinics

Iowa City, Iowa, United States

Site Status RECRUITING

University Of Kansas Medical Center & Medical Pavilion

Kansas City, Kansas, United States

Site Status RECRUITING

University Of Maryland, Ihv

Baltimore, Maryland, United States

Site Status RECRUITING

MedStar Health Research Institute

Baltimore, Maryland, United States

Site Status RECRUITING

Harvard (Massachusetts General Hospital)

Boston, Massachusetts, United States

Site Status RECRUITING

Harvard Medical School - Brigham and Women's Hospital (BWH)

Boston, Massachusetts, United States

Site Status RECRUITING

Spectrum Health Medical Group

Grand Rapids, Michigan, United States

Site Status RECRUITING

Henry Ford Health System

West Bloomfield, Michigan, United States

Site Status RECRUITING

Minneapolis Heart Institute Foundation

Minneapolis, Minnesota, United States

Site Status RECRUITING

Cardiology Associates Research, Llc

Tupelo, Mississippi, United States

Site Status RECRUITING

St. Luke's Mid-America Heart Institute

Kansas City, Missouri, United States

Site Status RECRUITING

Washington University

St Louis, Missouri, United States

Site Status RECRUITING

CHI Health Reseach Center

Omaha, Nebraska, United States

Site Status RECRUITING

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status RECRUITING

Morristown Medical Center

Morristown, New Jersey, United States

Site Status RECRUITING

Bassett Medical Center

Cooperstown, New York, United States

Site Status RECRUITING

Northwell Health

Manhasset, New York, United States

Site Status RECRUITING

Mount Sinai West

New York, New York, United States

Site Status RECRUITING

Mount Sinai Hospital

New York, New York, United States

Site Status RECRUITING

Saint Francis Hospital

Roslyn, New York, United States

Site Status RECRUITING

WMCHealth Advanced Physician Services

Valhalla, New York, United States

Site Status RECRUITING

Focus Clinical Research

Charlotte, North Carolina, United States

Site Status RECRUITING

Duke University Health System

Durham, North Carolina, United States

Site Status RECRUITING

Christ Hospital Health Network

Cincinnati, Ohio, United States

Site Status RECRUITING

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status RECRUITING

Cleveland Clinic

Cleveland, Ohio, United States

Site Status RECRUITING

St. Luke's University Health Network

Bethlehem, Pennsylvania, United States

Site Status RECRUITING

Lancaster General Hospital

Lancaster, Pennsylvania, United States

Site Status RECRUITING

AHN Allegheny General Hospital

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

University Of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Geisinger Health System

Wilkes-Barre, Pennsylvania, United States

Site Status RECRUITING

Prisma Health - Upstate

Greenville, South Carolina, United States

Site Status RECRUITING

Tristar Centennial Medical Ctr

Nashville, Tennessee, United States

Site Status RECRUITING

Saint Thomas Health

Nashville, Tennessee, United States

Site Status RECRUITING

North Texas Cardiology Center

Dallas, Texas, United States

Site Status RECRUITING

Baylor Scott & White Research Institute

Dallas, Texas, United States

Site Status RECRUITING

The Methodist Hospital, Methodist Cancer Cencer

Houston, Texas, United States

Site Status RECRUITING

BI Research Center

Houston, Texas, United States

Site Status RECRUITING

Baylor Scott & White The Heart Hospital Plano

Plano, Texas, United States

Site Status RECRUITING

Baylor Scott & White Medical Centre - Temple

Temple, Texas, United States

Site Status RECRUITING

The Rector and Visitors of the Univ of Virginia

Charlottesville, Virginia, United States

Site Status RECRUITING

VCU Medical Center

Richmond, Virginia, United States

Site Status RECRUITING

Carilion Clinic; Virginia Tech-Carilion School of Medicine

Roanoke, Virginia, United States

Site Status RECRUITING

Virginia Mason Medical Center

Seattle, Washington, United States

Site Status RECRUITING

WVU Hospitals

Morgantown, West Virginia, United States

Site Status RECRUITING

University Of Wisconsin - Madison

Madison, Wisconsin, United States

Site Status RECRUITING

Medical College of Wisconsin, Inc (PI Address)

Milwaukee, Wisconsin, United States

Site Status RECRUITING

KH St.Josef Braunau am Inn

Braunau am Inn, , Austria

Site Status RECRUITING

LKH-Univ. Klinikum Graz

Graz, , Austria

Site Status RECRUITING

Local Institution - 0088

Innsbruck, , Austria

Site Status NOT_YET_RECRUITING

Local Institution - 0084

Klagenfurt, , Austria

Site Status WITHDRAWN

Kepler Universitätsklinikum Linz

Linz, , Austria

Site Status RECRUITING

Local Institution - 0085

Sankt Pölten, , Austria

Site Status NOT_YET_RECRUITING

Local Institution - 0083

Vienna, , Austria

Site Status NOT_YET_RECRUITING

Centre Hospitalier Haguenau

Haguenau, Bas Rhin, France

Site Status RECRUITING

CHU Nantes Hopital Nord Laennec

Saint-Herblain, Loire Atlantique, France

Site Status RECRUITING

Hôpital Saint Vincent-de-Paul

Lille, Nord, France

Site Status RECRUITING

CHU Amiens-Picardie

Amiens, Somme, France

Site Status RECRUITING

Hôpital Sainte Musse

Toulon, Var, France

Site Status RECRUITING

CHU De Poitiers - Hopital De La Miletrie

Poitiers, Vienne, France

Site Status RECRUITING

Local Institution - 0117

Montpellier, , France

Site Status WITHDRAWN

Ostalb-Klinikum Aalen

Aalen, Baden-Wurttemberg, Germany

Site Status RECRUITING

Local Institution - 0101

Erlangen, Bavaria, Germany

Site Status WITHDRAWN

Universitatsklinikum Muenster

Münster, North Rhine-Westphalia, Germany

Site Status RECRUITING

Praxisklinik Herz Und Gefasse-Klinikum Weisser Hirsch

Dresden, Saxony, Germany

Site Status RECRUITING

Universitaetsklinikum Leipzig Aoer

Leipzig, Saxony, Germany

Site Status RECRUITING

Immanuel Klinikum Bernau

Bernau, State of Berlin, Germany

Site Status RECRUITING

Kardiologische und angiologische Praxen im Spreebogen

Berlin, , Germany

Site Status RECRUITING

Research & Cardiovascular Corp

Ponce, , Puerto Rico

Site Status RECRUITING

Hospital Fundacion Son Llatzer

Palma de Mallorca, Balearic Islands, Spain

Site Status RECRUITING

Hospital Universitario Puerta de Hierro Majadahonda

Majadahonda, Madrid, Spain

Site Status RECRUITING

Hospital Universitario Virgen de La Arrixaca

El Palmar, Murcia, Spain

Site Status RECRUITING

Hospital Universitario Central de Asturias

Oviedo, Principality of Asturias, Spain

Site Status RECRUITING

Hospital Universitario de Burgos

Burgos, , Spain

Site Status RECRUITING

Local Institution - 0102

Madrid, , Spain

Site Status WITHDRAWN

Hospital Clinico San Carlos

Madrid, , Spain

Site Status RECRUITING

Hospital Clinico Universitario Virgen de La Victoria

Málaga, , Spain

Site Status RECRUITING

Local Institution - 0113

London, Greater London, United Kingdom

Site Status NOT_YET_RECRUITING

Imperial College Healthcare NHS Trust

London, Greater London, United Kingdom

Site Status RECRUITING

University Of Manchester

Manchester, Greater Manchester, United Kingdom

Site Status RECRUITING

Liverpool Heart and Chest Hospital

Liverpool, Merseyside, United Kingdom

Site Status RECRUITING

University Hospitals Birmingham NHS Foundation Trust

Birmingham, West Midlands, United Kingdom

Site Status RECRUITING

Leeds General Infirmary

Leeds, West Yorkshire, United Kingdom

Site Status RECRUITING

University Hospital of Wales

Cardiff, , United Kingdom

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Austria France Germany Puerto Rico Spain United Kingdom

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

BMS Study Connect Contact Center www.BMSStudyConnect.com

Role: CONTACT

Phone: 855-907-3286

Email: [email protected]

First line of the email MUST contain the NCT# and Site #.

Role: CONTACT

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Ahmed Abuzaid, Site 0023

Role: primary

Greg Koshkarian, Site 0025

Role: primary

Srikanth Vallurupalli, Site 0007

Role: primary

Jorge Silva Enciso, Site 0037

Role: primary

Eugene DePasquale, Site 0057

Role: primary

Matthew Wheeler, Site 0012

Role: primary

Theodore Abraham, Site 0021

Role: primary

David Raymer, Site 0050

Role: primary

Adaya Weissler-Snir, Site 0067

Role: primary

Patrick Bering, Site 0081

Role: primary

Andres Pineda, Site 0065

Role: primary

Dipanjan Banerjee, Site 0046

Role: primary

Gene Kim, Site 0063

Role: primary

Roopa Rao, Site 0013

Role: primary

George Lolay, Site 0016

Role: primary

Ernesto Ruiz Duque, Site 0045

Role: primary

Loren Berenbom, Site 0033

Role: primary

Manjula Ananthram, Site 0059

Role: primary

Sandeep Jani, Site 0030

Role: primary

Albree Tower-Rader, Site 0024

Role: primary

Carolyn Ho, Site 0068

Role: primary

David Fermin, Site 0073

Role: primary

Karthikeyan Ananthasubramaniam, Site 0034

Role: primary

Robert Fraser, Site 0010

Role: primary

Barry Bertolet, Site 0062

Role: primary

Michael Nassif, Site 0069

Role: primary

Richard Bach, Site 0036

Role: primary

Amjad Kabach, Site 0070

Role: primary

Dmitry Nemirovsky, Site 0029

Role: primary

Matthew Martinez, Site 0026

Role: primary

Mun Hong, Site 0006

Role: primary

Ronald Wharton, Site 0001

Role: primary

Kim Kim, Site 0009

Role: primary

Johanna Contreras, Site 0035

Role: primary

Allen Jeremias, Site 0075

Role: primary

Srihari Naidu, Site 0053

Role: primary

Aamer Qurehshi, Site 0040

Role: primary

Andrew Wang, Site 0022

Role: primary

Wojciech Mazur, Site 0015

Role: primary

Anene Clair Ukaigwe, Site 0041

Role: primary

Milind Desai, Site 0003

Role: primary

Jamshid Shirani, Site 0043

Role: primary

Robert Donovan, Site 0076

Role: primary

Craig Alpert, Site 0002

Role: primary

Timothy Wong, Site 0027

Role: primary

Vernon Mascarenhas, Site 0056

Role: primary

Josh Doll, Site 0042

Role: primary

Bryan Doherty, Site 0048

Role: primary

Mark Zenker, Site 0019

Role: primary

Manavjot Sidhu, Site 0018

Role: primary

Robert Gottlieb, Site 0008

Role: primary

Sherif Nagueh, Site 0058

Role: primary

Asif Akhtar, Site 0039

Role: primary

David Rawitscher, Site 0028

Role: primary

Vinh Nguyen, Site 0051

Role: primary

Christopher Kramer, Site 0011

Role: primary

Mohammed Makkiya, Site 0080

Role: primary

Ali Hama Amin, Site 0044

Role: primary

Mariko Harper, Site 0052

Role: primary

Christopher Bianco, Site 0055

Role: primary

Ravi Dhingra, Site 0004

Role: primary

Abhinav Sharma, Site 0054

Role: primary

Johann Auer, Site 0082

Role: primary

Nicolas Verheyen, Site 0087

Role: primary

Site 0088

Role: primary

Christian Reiter, Site 0086

Role: primary

Site 0085

Role: primary

Site 0083

Role: primary

Charlotte Dagrenat, Site 0092

Role: primary

Nicolas Piriou, Site 0093

Role: primary

Ludovic Appert, Site 0090

Role: primary

Yohann Bohbot, Site 0091

Role: primary

Jean-Michel Tartière, Site 0094

Role: primary

Benjamin Alos, Site 0089

Role: primary

Stephanie Loebig, Site 0098

Role: primary

Jürgen Sindermann, Site 0100

Role: primary

Gregor Simonis, Site 0099

Role: primary

Karsten Lenk, Site 0097

Role: primary

Christian Butter, Site 0095

Role: primary

Wilhelm Haverkamp, Site 0096

Role: primary

Jose Vazquez-Tanus, Site 0077

Role: primary

Tomas Ripoll, Site 0109

Role: primary

Pablo García Pavia, Site 0104

Role: primary

Juan Ramon Gimeno Blanes, Site 0105

Role: primary

Rebeca Lorca Gutierrez, Site 0106

Role: primary

Ana Merino Merino, Site 0107

Role: primary

Maria Alejandra Restrepo Cordoba, Site 0108

Role: primary

José Manuel García Pinilla, Site 0103

Role: primary

Site 0113

Role: primary

Amanda Varnava, Site 0115

Role: primary

Andrew Crean, Site 0112

Role: primary

Robert Cooper, Site 0111

Role: primary

William Bradlow, Site 0110

Role: primary

Alex Simms, Site 0114

Role: primary

Zaheer Yousef, Site 0116

Role: primary

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

CV027-012

Identifier Type: -

Identifier Source: org_study_id