Mocravimod as Adjunctive and Maintenance Treatment in AML Patients Undergoing Allo-HCT

NCT ID: NCT05429632

Last Updated: 2025-12-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

366 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-06-16

Study Completion Date

2029-11-30

Brief Summary

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This is a multi-center, randomized, double-blinded, placebo controlled trial.

Detailed Description

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The purpose of this study is to evaluate the efficacy and safety of mocravimod as an adjunctive and maintenance treatment in adult acute myeloid leukemia (AML) patients undergoing allogeneic hematopoietic cell transplantation (HCT).

Conditions

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Adult Acute Myeloid Leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

prospective, multicenter, randomized, double-blind, placebo-controlled, and 3-arm parallel group study
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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3mg mocravimod arm

3 mg of mocravimod orally once per day for 12 months

Group Type EXPERIMENTAL

mocravimod

Intervention Type DRUG

S1PR modulator

1mg mocravimod arm

1 mg of mocravimod orally once per day for 12 months

Group Type EXPERIMENTAL

mocravimod

Intervention Type DRUG

S1PR modulator

Placebo arm

placebo orally once per day for 12 months

Group Type PLACEBO_COMPARATOR

mocravimod

Intervention Type DRUG

S1PR modulator

Interventions

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mocravimod

S1PR modulator

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of AML (excluding acute promyelocytic leukemia) according to the WHO 2022 classification of AML and related precursor neoplasm, including AML with myelodysplasia-related gene mutations
* European Leukemia Net (ELN) high-risk or intermediate-risk AML in CR1, or AML of any risk in CR2, \[CRi\] is also allowable
* Planned allogeneic HCT from fully matched related or unrelated donor with no more than 1 antigen mismatch or planned use of haploidentical donor using PBSC graft
* Any conditioning regimen with a Transplant Conditioning Score (TCI) ≥ 1.5
* Planned use of TAC-based GvHD prophylaxis
* age ≥ 18 years and ≤ 75 years
* Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1

Exclusion Criteria

* Use of CsA, anti-thymocyte globulin (ATG), alemtuzumab, abatacept for GvHD prophylaxis
* Diagnosis of macular edema during screening
* Cardiac/pulmonary/hepatic/renal dysfunction
* Hepatic dysfunction as defined by aspartate aminotransferase (AST) and/or alanine aminotransferase (ALT) \> 2.5 x upper limit of normal (ULN); or total bilirubin \> 1.5 mg/dL
* Renal dysfunction with estimated creatinine clearance \< 45 mL/min by the Cockcroft-Gault formula

* Diabetes mellitus
* History or presence of uveitis at screening
* History or diagnosis of macular edema
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Priothera SAS

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Marcos DeLima, MD

Role: PRINCIPAL_INVESTIGATOR

The Ohio State University Comprehensive Cancer Center

Locations

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University of Alabama Hospital (UAB Hospital)

Birmingham, Alabama, United States

Site Status RECRUITING

Banner MD Anderson Cancer Center

Gilbert, Arizona, United States

Site Status ACTIVE_NOT_RECRUITING

City of Hope Comprehensive Cancer Center - Duarte

Duarte, California, United States

Site Status ACTIVE_NOT_RECRUITING

University of California Los Angeles (UCLA) - David Geffen School of Medicine

Los Angeles, California, United States

Site Status ACTIVE_NOT_RECRUITING

Emory University - Winship Cancer Institute (WCI)

Atlanta, Georgia, United States

Site Status RECRUITING

University of Kansas Cancer Center

Westwood, Kansas, United States

Site Status ACTIVE_NOT_RECRUITING

Ochsner Medical Center (OMC) - New Orleans

New Orleans, Louisiana, United States

Site Status ACTIVE_NOT_RECRUITING

University of Maryland Medical Center (UMMC)

Baltimore, Maryland, United States

Site Status ACTIVE_NOT_RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status ACTIVE_NOT_RECRUITING

Henry Ford Cancer Institute

Detroit, Michigan, United States

Site Status ACTIVE_NOT_RECRUITING

Spectrum Health Medical Group (SHMG) - Blood & Marrow Transplant - Adult (BMT)

Grand Rapids, Michigan, United States

Site Status RECRUITING

University of Rochester Medical Center (URMC)

Rochester, New York, United States

Site Status RECRUITING

Stony Brook University (SBU) - Cancer Center

Stony Brook, New York, United States

Site Status RECRUITING

University of Cincinnati Medical Center (University Hospital)

Cincinnati, Ohio, United States

Site Status ACTIVE_NOT_RECRUITING

The Ohio State University Comprehensive Cancer Center (OSUCCC)

Cleveland, Ohio, United States

Site Status RECRUITING

Oregon Health & Science University (OHSU) - Knight Cancer Institute

Portland, Oregon, United States

Site Status RECRUITING

University of Pennsylvania - Abramson Cancer Center

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

Baylor Charles A. Sammons Cancer Center

Dallas, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

Hospital El Cruce - Dr. Nestor Kirchner

Buenos Aires, , Argentina

Site Status ACTIVE_NOT_RECRUITING

Centro de Educacion Medica E Investigacines Clinicas Norberto Quirno CEMIC

Buenos Aires, , Argentina

Site Status ACTIVE_NOT_RECRUITING

Sanatorio Allende (SA) - Nueva Cordoba

Córdoba, , Argentina

Site Status ACTIVE_NOT_RECRUITING

Hospital Italiano La Plata

La Plata, , Argentina

Site Status ACTIVE_NOT_RECRUITING

CEPON - Centro de Pesquisas Oncologicas

Florianópolis, Santa Catarina, Brazil

Site Status ACTIVE_NOT_RECRUITING

Hospital Erasto Gaertner

Curicica, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Hospital Alemao Oswaldo Cruz (HAOC)

São Paulo, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Universidade de Sao Paulo (USP) - Hospital das Clinicas da Faculdade de Medicina (HCFMUSP)

São Paulo, , Brazil

Site Status RECRUITING

Hospital Israelita Albert Einstein

São Paulo, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Unicamp

São Paulo, , Brazil

Site Status RECRUITING

Hospital Amaral Carvalho

São Paulo, , Brazil

Site Status ACTIVE_NOT_RECRUITING

Centre Hospitalier Universitaire (CHU) Angers

Angers, , France

Site Status RECRUITING

Centre Hospitalier Regional Universitaire (CHRU) de Lille - Hopital Claude Huriez -

Lille, , France

Site Status ACTIVE_NOT_RECRUITING

Centre Hospitalier Lyon-Sud

Lyon, , France

Site Status ACTIVE_NOT_RECRUITING

CHU de Nantes - Hôtel Dieu

Nantes, , France

Site Status RECRUITING

Hospital Saint Antoine

Paris, , France

Site Status RECRUITING

Hôpital Saint Louis

Paris, , France

Site Status RECRUITING

Institut Universitaire du Cancer de Toulouse Oncopole

Toulouse, , France

Site Status ACTIVE_NOT_RECRUITING

Centre de Lutte Contre le Cancer (CLCC) - Institut Gustave-Roussy

Villejuif, , France

Site Status ACTIVE_NOT_RECRUITING

Universitätsklinikum Halle

Halle, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitaetsklinikum Jena - Klinik fuer Innere Medizin II

Jena, , Germany

Site Status ACTIVE_NOT_RECRUITING

University of Leipzig Medical Center

Leipzig, , Germany

Site Status RECRUITING

LMU Klinikum Grosshadern Klinikum der Universitaet Muenchen

Munich, , Germany

Site Status ACTIVE_NOT_RECRUITING

Rambam Health Care Campus

Haifa, , Israel

Site Status RECRUITING

Hadassah Medical Center

Jerusalem, , Israel

Site Status ACTIVE_NOT_RECRUITING

The Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status RECRUITING

The Chaim Sheba Medical Center

Tel Litwinsky, , Israel

Site Status RECRUITING

Grande Ospedale Metropolitano Bianchi Melacrino Morelli

Reggio Calabria, Calabria, Italy

Site Status ACTIVE_NOT_RECRUITING

Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS) - Ospedale Casa Sollievo della Sofferenza (CSS)

San Giovanni Rotondo, Foggia, Italy

Site Status RECRUITING

Azienda Ospedaliera Nazionale SS. Antonio e Biagio e Cesare Arrigo Alessandria

Alessandria, , Italy

Site Status ACTIVE_NOT_RECRUITING

Azienda Sanitaria Locale 13 - Ospedale "C. e G. Mazzoni"- Ascoli Piceno

Ascoli Piceno, , Italy

Site Status RECRUITING

Azienda Sanitaria Localedella provincia di Brindisi -

Brindisi, , Italy

Site Status ACTIVE_NOT_RECRUITING

Universita degli Studi di Firenze - Azienda Ospedaliero-Universitaria Careggi (AOUC) LAB TMO

Florence, , Italy

Site Status ACTIVE_NOT_RECRUITING

Ospedale Vito Fazzi Lecce

Lecce, , Italy

Site Status ACTIVE_NOT_RECRUITING

Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico

Milan, , Italy

Site Status RECRUITING

Azienda Ospedaliera San Gerardo - Monza

Monza, , Italy

Site Status RECRUITING

Fondazione IRCCS Policlinico San Matteo

Pavia, , Italy

Site Status RECRUITING

Azienda Ospedaliera Ospedali Riuniti Marche Nord

Pesaro, , Italy

Site Status RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Roma, , Italy

Site Status ACTIVE_NOT_RECRUITING

Anjo-kosei Hospital

Anjo-shi, Aichi-ken, Japan

Site Status ACTIVE_NOT_RECRUITING

Japanese Red Cross Nagoya Daiichi Hospital (First Hospital)

Nagoya, Aichi-ken, Japan

Site Status ACTIVE_NOT_RECRUITING

Kanazawa University Hospital

Kanazawa, Ishikawa-ken, Japan

Site Status ACTIVE_NOT_RECRUITING

Osaka Metropolitan University Hospital

Osaka, Osaka, Japan

Site Status ACTIVE_NOT_RECRUITING

Jichi Medical University (JMU) Hospital

Shimotsuke-shi, Tochigi, Japan

Site Status ACTIVE_NOT_RECRUITING

Kyushu University Hospital,

Fukuoka, , Japan

Site Status ACTIVE_NOT_RECRUITING

Hiroshima Red Cross Hospital & Atomic-Bomb Survivors Hospital

Hiroshima, , Japan

Site Status ACTIVE_NOT_RECRUITING

Kobe City Medical Center General Hospital

Kobe, , Japan

Site Status RECRUITING

Kyoto University Hospital

Kōtoku, , Japan

Site Status RECRUITING

Ehime Prefectural Centeral Hospital, Ehime

Matsuyama, , Japan

Site Status ACTIVE_NOT_RECRUITING

Okayama University Hospital

Okayama, , Japan

Site Status ACTIVE_NOT_RECRUITING

Jichi Medical University Saitama Medical Center

Saitama, , Japan

Site Status ACTIVE_NOT_RECRUITING

Hokkaido University Hospital

Sapporo, , Japan

Site Status ACTIVE_NOT_RECRUITING

Tokyo Metropolitan Cancer and infection Disese Center Komagome Hospital

Tokyo, , Japan

Site Status ACTIVE_NOT_RECRUITING

Oita University (OU) Hospital

Yufu, , Japan

Site Status ACTIVE_NOT_RECRUITING

Sp Zoz Szpital Uniwersytecki W Krakowie

Krakow, Aichi-Ken, Poland

Site Status ACTIVE_NOT_RECRUITING

Slaski Uniwersytet Medyczny (SUM) w Katowicach - Samodzielny Publiczny Szpital Kliniczny im. Andrzeja Mieleckiego (SPSKM) - Slaskie Centrum Hematologii I Transplantacji Szpiku

Katowice, Silesian Voivodeship, Poland

Site Status RECRUITING

Uniwersyteckie Centrum Kliniczne (UCK)

Gdansk, , Poland

Site Status RECRUITING

Apteka NSSU

Krakow, , Poland

Site Status ACTIVE_NOT_RECRUITING

Centralny Szpital Kliniczny Apteka Szpitalna

Warsaw, , Poland

Site Status RECRUITING

Institutul Clinic Fundeni

Bucharest, , Romania

Site Status ACTIVE_NOT_RECRUITING

Spitalul Clinic Coltea

Bucharest, , Romania

Site Status ACTIVE_NOT_RECRUITING

Institutul Regional de Oncologie Iasi, - Haematology Department

Iași, , Romania

Site Status RECRUITING

Hospital Universitari Vall d'Hebron - Institut de Recerca (VHIR)

Barcelona, , Spain

Site Status RECRUITING

Institut Catala d'Oncologia (ICO)

Barcelona, , Spain

Site Status RECRUITING

Institut Catala d'Oncologia (ICO) - Hospital Universitari Germans Trias i Pujol (HUGTP) Location

Barcelona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Virgen de las Nieves

Granada, , Spain

Site Status RECRUITING

Hospital Universitario de Gran Canaria ""

Las Palmas de Gran Canaria, , Spain

Site Status RECRUITING

Hospital De La Princesa

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status RECRUITING

Hospital Clinico Universitario - Universidad de Salamanca

Salamanca, , Spain

Site Status RECRUITING

Hospital Universitari i Politecnic La Fe

Valencia, , Spain

Site Status RECRUITING

Universitaetsspital Basel

Basel, , Switzerland

Site Status ACTIVE_NOT_RECRUITING

Changhua Christian Hospital

Changhua, , Taiwan

Site Status ACTIVE_NOT_RECRUITING

National Cheng-Kung University Hospital

Tainan, , Taiwan

Site Status ACTIVE_NOT_RECRUITING

National Taiwan University Hospital (NTUH)

Taipei, , Taiwan

Site Status RECRUITING

National Taiwan University Cancer Center

Taipei, , Taiwan

Site Status RECRUITING

Queen Elizabeth Hospital

Birmingham, , United Kingdom

Site Status RECRUITING

University Hospital of Wales, Cardiff

Cardiff, , United Kingdom

Site Status RECRUITING

Queen Elizabeth University Hospital

Glasgow, , United Kingdom

Site Status RECRUITING

University College Hospital,

London, , United Kingdom

Site Status RECRUITING

Imperial College, London

London, , United Kingdom

Site Status RECRUITING

Manchester Royal Infirmary;Manchester University

Manchester, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Newcastle Upon Tyne Hospitals Norhtern Center for Cancer Care

Newcastle upon Tyne, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Nottingham University Hospitals NHS Trust

Nottingham, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Oxford University Hospitals

Oxford, , United Kingdom

Site Status RECRUITING

Royal Hallamshire Hospital

Sheffield, , United Kingdom

Site Status RECRUITING

Countries

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United States Argentina Brazil France Germany Israel Italy Japan Poland Romania Spain Switzerland Taiwan United Kingdom

Central Contacts

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Malika Souquieres, MSc

Role: CONTACT

+33 (0) 6 40 91 26 76

Jens Hasskarl, MD

Role: CONTACT

+41 79 5432099

Facility Contacts

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Antonio Di Stasi, MD

Role: primary

Edmund Waller, MD

Role: primary

Sami Brake, MD

Role: primary

Eric Huselton, MD

Role: primary

Fengshuo Lan, MD

Role: primary

Gabriella Pettito, MD

Role: primary

Arpita Gandhi, MD

Role: primary

David Porter, MD

Role: primary

Gian Carlo Fatobene, MD

Role: primary

Marcos P Colella, MD

Role: primary

Sylvain Thepot, MD

Role: primary

Patrice Chevallier, MD

Role: primary

Florent Mallard, MD

Role: primary

Marie Robin, MD

Role: primary

Georg-Nikolaus Franke, MP

Role: primary

.+49 341 97-13132

Tsila Zuckermann, MD

Role: primary

Ron Ram, MD

Role: primary

Avichai Shimoni, MD

Role: primary

Angelo M Carella, MD

Role: primary

Piero Galieni, MD

Role: primary

Giorgia Saporiti, MD

Role: primary

Elisabetta Terruzzi, MD

Role: primary

Nicola Polverelli, MD

Role: primary

Guiseppe Visiani, MD

Role: primary

Takayuki Ishikawa, MD

Role: primary

Junya Kanda, MD

Role: primary

Agata Wieczorkiewicz-Kabut

Role: primary

Agnieszka Piekarska, MD

Role: primary

Gregorz Basak, MD

Role: primary

Angela Dascalescu, MD

Role: primary

David Valcarcel Ferreiras, MD

Role: primary

Annalisa Paviglianiti -surpased, MD

Role: primary

Marta Pena new PI, MD

Role: backup

Pedro Gonalez-Sierra, MD

Role: primary

Melisa Karina Torres Ochando, MD

Role: primary

Maria Calbacho Robles, MD

Role: primary

Anabelle Rodriguez_Chinea, MD

Role: primary

Estefanía Pérez López, MD

Role: primary

Jaime Sanz Caballer, MD

Role: primary

Bor Sheng Ko, MD

Role: primary

2-2312-3456 Ext 63576;

Ko Bor-Sheng, MD

Role: primary

886 2 2312 3456 x63576

Maria Maroto, MD

Role: primary

Wendy Ingram, MD

Role: primary

David Irvine, MD

Role: primary

Kate Stringaris, MD

Role: primary

Eduardo Olavarria, MD

Role: primary

Kirsty Sharplin, MD

Role: primary

Harpreet Knaur, MD

Role: primary

Other Identifiers

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Priothera SAS

Identifier Type: -

Identifier Source: org_study_id

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