Trial Outcomes & Findings for A Study to Assess the Safety, Tolerability, and Efficacy of Namilumab in Participants With Active Cardiac Sarcoidosis (NCT NCT05351554)

NCT ID: NCT05351554

Last Updated: 2025-04-17

Results Overview

An AE was defined as any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship. SAEs were defined as death, a life-threatening AE, inpatient hospitalization or prolongation of existing hospitalization, persistent or significant disability or incapacity, a congenital anomaly or birth defect, or an important medical event that jeopardized participant and required medical intervention to prevent 1 of the outcomes listed in this definition. A summary of other non-serious AEs and all serious AEs, regardless of causality is located in Reported AE section.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

1 participants

Primary outcome timeframe

Baseline up to approximately 2 months

Results posted on

2025-04-17

Participant Flow

The sponsor terminated the study for business reasons, not related to safety, after a single subject had received 2 doses. A separate cohort (Cohort A) was planned but did not enroll any participants.

Participant milestones

Participant milestones
Measure
Namilumab
A single participant received two doses of 150 mg (milligrams) of namilumab subcutaneously (SC) at baseline (Day 1) and on Day 15.
Overall Study
STARTED
1
Overall Study
Received at Least 1 Dose of Study Drug
1
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Namilumab
A single participant received two doses of 150 mg (milligrams) of namilumab subcutaneously (SC) at baseline (Day 1) and on Day 15.
Overall Study
Study terminated by sponsor
1

Baseline Characteristics

A Study to Assess the Safety, Tolerability, and Efficacy of Namilumab in Participants With Active Cardiac Sarcoidosis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Namilumab
n=1 Participants
A single participant received two doses of 150 mg of namilumab SC at baseline (Day 1) and on Day 15.
Age, Customized
50 - 70 years
1 Participants
n=5 Participants
Sex/Gender, Customized
Male or Female
1 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
0 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The Safety Population included all randomized participants who received at least one dose of study drug.

An AE was defined as any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship. SAEs were defined as death, a life-threatening AE, inpatient hospitalization or prolongation of existing hospitalization, persistent or significant disability or incapacity, a congenital anomaly or birth defect, or an important medical event that jeopardized participant and required medical intervention to prevent 1 of the outcomes listed in this definition. A summary of other non-serious AEs and all serious AEs, regardless of causality is located in Reported AE section.

Outcome measures

Outcome measures
Measure
Namilumab
n=1 Participants
A single participant received two doses of 150 mg of namilumab SC at baseline (Day 1) and on Day 15.
Number of Participants With Adverse Events (AEs), Serious Adverse Events (SAEs), and AEs Leading to Discontinuation
AEs
1 Participants
Number of Participants With Adverse Events (AEs), Serious Adverse Events (SAEs), and AEs Leading to Discontinuation
SAEs
0 Participants
Number of Participants With Adverse Events (AEs), Serious Adverse Events (SAEs), and AEs Leading to Discontinuation
AEs leading to discontinuation
0 Participants

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The Safety Population included all randomized participants who received at least one dose of study drug.

Outcome measures

Outcome measures
Measure
Namilumab
n=1 Participants
A single participant received two doses of 150 mg of namilumab SC at baseline (Day 1) and on Day 15.
Number of Participants With Treatment-emergent Laboratory Abnormalities
0 Participants

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The Safety Population included all randomized participants who received at least one dose of study drug.

Outcome measures

Outcome measures
Measure
Namilumab
n=1 Participants
A single participant received two doses of 150 mg of namilumab SC at baseline (Day 1) and on Day 15.
Number of Participants With Treatment-emergent Vital Sign Abnormalities
0 Participants

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The Safety Population included all randomized participants who received at least one dose of study drug.

Outcome measures

Outcome measures
Measure
Namilumab
n=1 Participants
A single participant received two doses of 150 mg of namilumab SC at baseline (Day 1) and on Day 15.
Number of Participants With Treatment-emergent Electrocardiogram (ECG) Abnormalities
0 Participants

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

The mGTI is a composite measure of the changes in OCS toxicity measured at 3-month intervals across 11 domains and 23 items. For the purposes of this study, radiographic assessment of bone mineral density is not being performed; therefore, this item is not being assessed in the tool and the tool is termed "modified" for this study. The change in the total score is from -35 to +410 with the exclusion of bone mineral density, with minimum score representing least toxicity (better outcomes) and maximum score representing most toxicity (worse outcomes).

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: 0 participants were enrolled in Cohort A.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

The KSQ is a modular, multi-organ health status measure for participants with sarcoidosis for use in the clinic and the evaluation of therapies. The KSQ consists of 5 modules: General health status (10 items), Lung (6 items), Medication (3 items), Skin (3 items), and Eye (7 items). Results are given as a number between 1-100 with higher numbers indicating better health.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

The FAS is a 10-item self-reported fatigue questionnaire. Participants indicate their responses on a 5-point scale (from 1 never to 5 always). Total scores on the FAS can therefore range from 10 to 50, with high scores indicating more fatigue and worse outcomes.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline up to approximately 2 months

Population: The study was terminated by the Sponsor due to a business decision (no safety concerns). The study participant did not consent to publishing his/her individual data. As there was only 1 participant in this study, no data are reported in order to protect and maintain participant privacy/confidentiality.

The SGA is a participant reported outcome instrument used to assess their overall perception of the frequency and severity of sarcoid symptoms. The SGA is a 5-point Likert scale; the participant rates how he/she feels regarding their sarcoidosis in the previous 2 weeks prior to the study visit based on the frequency and severity of their symptoms. Scores range from 1 to 5 with lower scores representing better outcomes.

Outcome measures

Outcome data not reported

Adverse Events

Namilumab

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Namilumab
n=1 participants at risk
Participant received two doses of 150 mg of namilumab SC at baseline (Day 1) and on Day 15.
Skin and subcutaneous tissue disorders
Rash
100.0%
1/1 • Baseline (Day 1) up to approximately 2 months
Nervous system disorders
Headache
100.0%
1/1 • Baseline (Day 1) up to approximately 2 months
General disorders
Injection site papule
100.0%
1/1 • Baseline (Day 1) up to approximately 2 months

Additional Information

Study Director

Kinevant

Phone: Please email

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place