Expanded Access Program (EAP) for Ciltacabtagene Autoleucel (Cilta-Cel) Out-of-Specification (OOS) in Participants With Multiple Myeloma

NCT ID: NCT05346835

Last Updated: 2026-02-13

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

AVAILABLE

Study Classification

EXPANDED_ACCESS

Brief Summary

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The purpose of this expanded access program (EAP) is to provide ciltacabtagene autoleucel (cilta-cel) that does not meet the commercial release specifications of CARVYKTI and is not available via the local health care system in the country where the treatment is requested.

Detailed Description

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Conditions

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Multiple Myeloma

Interventions

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Cilta-cel OOS Therapy

Ciltacabtagene Autoleucel (Cilta-cel) Out-of-Specification (OOS) will be provided as a one-time administration as an intravenous infusion.

Intervention Type DRUG

Other Intervention Names

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JNJ-68284528

Eligibility Criteria

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Inclusion Criteria

* Eligible for treatment with cilta-cel per United States Prescribing Information (USPI)
* Has serious or life-threatening multiple myeloma per USPI, and where re-apheresis, re-manufacturing, or other anti-myeloma directed therapy is not considered feasible or adequate per treating physician discretion
* Favorable participant benefit/risk assessment determined by Janssen medical review
* Treating physician confirms the favorable risk benefit profile, and that proceeding with this treatment is in the best interest of the participant
* Able to provide informed consent indicating they understand the purpose of this expanded access program (EAP)
* A woman of childbearing potential must have a negative highly sensitive serum (beta-human chorionic gonadotropin \[beta-hCG\]) pregnancy test during screening and prior to the first dose of cyclophosphamide and fludarabine
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Janssen Scientific Affairs, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status AVAILABLE

Banner MD Anderson Cancer Center

Gilbert, Arizona, United States

Site Status AVAILABLE

Cancer Treatment Center of America Phoenix

Goodyear, Arizona, United States

Site Status AVAILABLE

HonorHealth Cancer Transplant Institute

Scottsdale, Arizona, United States

Site Status AVAILABLE

Mayo Clinic

Scottsdale, Arizona, United States

Site Status AVAILABLE

University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status AVAILABLE

The University of Arkansas for Medical Sciences Myeloma Institute for Research and Therapy

Little Rock, Arkansas, United States

Site Status AVAILABLE

Alta Bates Medical Center Cancer Center

Berkeley, California, United States

Site Status AVAILABLE

City of Hope

Duarte, California, United States

Site Status AVAILABLE

University of California at San Diego

La Jolla, California, United States

Site Status AVAILABLE

USC Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status AVAILABLE

Samuel Oschin Comprehensive Cancer Center Cedars-Sinai Medical Center

Los Angeles, California, United States

Site Status AVAILABLE

University of California, Los Angeles UCLA

Los Angeles, California, United States

Site Status AVAILABLE

Hoag Memorial Hospital

Newport Beach, California, United States

Site Status AVAILABLE

Sutter Medical Foundation

Sacramento, California, United States

Site Status AVAILABLE

University of Calif Davis Medical Center

Sacramento, California, United States

Site Status AVAILABLE

UCSF

San Francisco, California, United States

Site Status AVAILABLE

Stanford University Medical Center

Stanford, California, United States

Site Status AVAILABLE

UCHealth Cancer Care Anschutz Medical Campus University of Colorado Cancer Center

Aurora, Colorado, United States

Site Status AVAILABLE

Colorado Blood Cancer Institute

Denver, Colorado, United States

Site Status AVAILABLE

Yale New Haven Hospital

New Haven, Connecticut, United States

Site Status AVAILABLE

Christiana Care

Newark, Delaware, United States

Site Status AVAILABLE

MedStar Georgetown Hospital

Washington D.C., District of Columbia, United States

Site Status AVAILABLE

University of Florida at Shands

Gainesville, Florida, United States

Site Status AVAILABLE

Mayo Clinic

Jacksonville, Florida, United States

Site Status AVAILABLE

University of Miami Sylvester Comprehensive Cancer Center

Miami, Florida, United States

Site Status AVAILABLE

Miami Cancer Institute at Baptist Health / Baptist Health Medical Group

Miami, Florida, United States

Site Status AVAILABLE

Advent Health Orlando

Orlando, Florida, United States

Site Status AVAILABLE

Orlando Health

Orlando, Florida, United States

Site Status AVAILABLE

Memorial Healthcare System

Pembroke Pines, Florida, United States

Site Status AVAILABLE

Tampa General Hospital

Tampa, Florida, United States

Site Status AVAILABLE

H Lee Moffitt Cancer Center

Tampa, Florida, United States

Site Status AVAILABLE

Emory University

Atlanta, Georgia, United States

Site Status AVAILABLE

Northside Hospital Cancer Institute

Atlanta, Georgia, United States

Site Status AVAILABLE

City of Hope Cancer Center

Newnan, Georgia, United States

Site Status AVAILABLE

Kapi Olani Medical Center for Women and Children Hawaii Pacific

Honolulu, Hawaii, United States

Site Status AVAILABLE

St. Luke's Mountain State Tumor Institute

Boise, Idaho, United States

Site Status AVAILABLE

Northwestern Medicine - Northwestern Memorial Hospital Galter Pavilion

Chicago, Illinois, United States

Site Status AVAILABLE

Rush University Medical Center

Chicago, Illinois, United States

Site Status AVAILABLE

University Of Illinois

Chicago, Illinois, United States

Site Status AVAILABLE

The University of Chicago Medical Center (UCMC)

Chicago, Illinois, United States

Site Status AVAILABLE

NorthShore University Health System, Evanston Hospital

Evanston, Illinois, United States

Site Status AVAILABLE

Loyola University Medical Center

Maywood, Illinois, United States

Site Status AVAILABLE

Advocate Lutheran General Hospital

Park Ridge, Illinois, United States

Site Status AVAILABLE

City of Hope Chicago

Zion, Illinois, United States

Site Status AVAILABLE

IU Health University Hospital

Indianapolis, Indiana, United States

Site Status AVAILABLE

St Francis Hospital & Health Centers Indiana Blood and Marrow Transplantation

Indianapolis, Indiana, United States

Site Status AVAILABLE

Community Health Network MD Anderson Cancer Center

Kokomo, Indiana, United States

Site Status AVAILABLE

University of Iowa Hospital and Clinics

Iowa City, Iowa, United States

Site Status AVAILABLE

University of Kansas Cancer Center

Fairway, Kansas, United States

Site Status AVAILABLE

Ascension via Christi Research

Wichita, Kansas, United States

Site Status AVAILABLE

University of Kentucky Chandler Medical Center

Lexington, Kentucky, United States

Site Status AVAILABLE

University of Louisville - James Graham Brown Cancer Center

Louisville, Kentucky, United States

Site Status AVAILABLE

Norton Cancer Institute

Louisville, Kentucky, United States

Site Status AVAILABLE

Ochsner Clinic Foundation

New Orleans, Louisiana, United States

Site Status AVAILABLE

University of Maryland School of Medicine

Baltimore, Maryland, United States

Site Status AVAILABLE

Johns Hopkins University School of Medicine JHUSOM

Baltimore, Maryland, United States

Site Status AVAILABLE

Tufts New England Medical Center

Boston, Massachusetts, United States

Site Status AVAILABLE

Massachusetts General

Boston, Massachusetts, United States

Site Status AVAILABLE

Boston University Medical Center

Boston, Massachusetts, United States

Site Status AVAILABLE

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status AVAILABLE

Dana-Farber Brigham and Women's Cancer Center

Weymouth, Massachusetts, United States

Site Status AVAILABLE

University of Massachusetts Medical School

Worcester, Massachusetts, United States

Site Status AVAILABLE

University of Michigan Rogel Cancer Center

Ann Arbor, Michigan, United States

Site Status AVAILABLE

Barbara Ann Karmanos Cancer Institute - Lawrence and Idell Weisberg Cancer Treatment Center

Farmington Hills, Michigan, United States

Site Status AVAILABLE

Corewell Health Grand Rapids Hospitals Butterworth

Grand Rapids, Michigan, United States

Site Status AVAILABLE

William Beaumont Health System

Royal Oak, Michigan, United States

Site Status AVAILABLE

M Health Fairview University of Minnesota Medical Center East Bank

Minneapolis, Minnesota, United States

Site Status AVAILABLE

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status AVAILABLE

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status AVAILABLE

Ellis Fischel Cancer Center

Columbia, Missouri, United States

Site Status AVAILABLE

Saint Louis University

St Louis, Missouri, United States

Site Status AVAILABLE

Washington University School Of Medicine

St Louis, Missouri, United States

Site Status AVAILABLE

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status AVAILABLE

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status AVAILABLE

John Theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status AVAILABLE

Rutgers, The State Univ of NJ-Robert Wood Johnson Medical School-The Cancer Institute of NJ (CINJ)

New Brunswick, New Jersey, United States

Site Status AVAILABLE

University of New Mexico School of Medicine

Albuquerque, New Mexico, United States

Site Status AVAILABLE

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States

Site Status AVAILABLE

The Feinstein Institute for Medical Research (Northwell Health Inc.)

Manhasset, New York, United States

Site Status AVAILABLE

New York University Langone Medical Center

New York, New York, United States

Site Status AVAILABLE

Icahn School of Medicine at Mount Sinai - The Derald H. Ruttenberg

New York, New York, United States

Site Status AVAILABLE

Columbia University Medical Center

New York, New York, United States

Site Status AVAILABLE

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status AVAILABLE

Weill Cornell Medical Center

New York, New York, United States

Site Status AVAILABLE

University of Rochester Medical Center

Rochester, New York, United States

Site Status AVAILABLE

Montefiore Medical Center

The Bronx, New York, United States

Site Status AVAILABLE

University of North Carolina Hospital

Chapel Hill, North Carolina, United States

Site Status AVAILABLE

Atrium Health

Charlotte, North Carolina, United States

Site Status AVAILABLE

Novant Health

Charlotte, North Carolina, United States

Site Status AVAILABLE

Duke University

Durham, North Carolina, United States

Site Status AVAILABLE

Novant Health Forsyth Medical Center

Winston-Salem, North Carolina, United States

Site Status AVAILABLE

Atrium Health Wake Forest Baptist Comprehensive Cancer Center

Winston-Salem, North Carolina, United States

Site Status AVAILABLE

Sanford Health

Fargo, North Dakota, United States

Site Status AVAILABLE

Good Samaritan Hospital

Cincinnati, Ohio, United States

Site Status AVAILABLE

The Jewish Hospital - Mercy

Cincinnati, Ohio, United States

Site Status AVAILABLE

University Hospital of Cleveland

Cleveland, Ohio, United States

Site Status AVAILABLE

Cleveland Clinic

Cleveland, Ohio, United States

Site Status AVAILABLE

The Ohio State University Wexner Medical Center - James Cancer Hospital

Columbus, Ohio, United States

Site Status AVAILABLE

OhioHealth Mansfield Hospital

Columbus, Ohio, United States

Site Status AVAILABLE

University of Oklahoma Stephenson Cancer Center

Oklahoma City, Oklahoma, United States

Site Status AVAILABLE

Providence Portland Medical Center

Portland, Oregon, United States

Site Status AVAILABLE

Oregon Health And Science University

Portland, Oregon, United States

Site Status AVAILABLE

Geisinger Medical Center

Danville, Pennsylvania, United States

Site Status AVAILABLE

Penn State Milton S Hershey Medical Ctr

Hershey, Pennsylvania, United States

Site Status AVAILABLE

University of Pennsylvania Division of Hematology Oncology Perelman Center for Advanced Medicine

Philadelphia, Pennsylvania, United States

Site Status AVAILABLE

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status AVAILABLE

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status AVAILABLE

University Of Pittsburgh Medical Center UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, United States

Site Status AVAILABLE

Roger Williams Medical Center

Providence, Rhode Island, United States

Site Status AVAILABLE

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status AVAILABLE

Prisma Health

Greenville, South Carolina, United States

Site Status AVAILABLE

Avera McKennan Hospital

Sioux Falls, South Dakota, United States

Site Status AVAILABLE

University of Tennessee Medical Center

Knoxville, Tennessee, United States

Site Status AVAILABLE

Baptist Clinical Research Institute

Memphis, Tennessee, United States

Site Status AVAILABLE

Sarah Cannon Cancer Institute

Nashville, Tennessee, United States

Site Status AVAILABLE

Tennessee Valley Healthcare System

Nashville, Tennessee, United States

Site Status AVAILABLE

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status AVAILABLE

St. David's South Austin Medical Center

Austin, Texas, United States

Site Status AVAILABLE

Texas Oncology-Medical City Dallas

Dallas, Texas, United States

Site Status AVAILABLE

Baylor University Medical Center

Dallas, Texas, United States

Site Status AVAILABLE

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status AVAILABLE

Houston Methodist Hospital

Houston, Texas, United States

Site Status AVAILABLE

MD Anderson Cancer Center

Houston, Texas, United States

Site Status AVAILABLE

San Antonio Methodist TX Transplant Physicians Group

San Antonio, Texas, United States

Site Status AVAILABLE

Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status AVAILABLE

Intermountain Healthcare

Salt Lake City, Utah, United States

Site Status AVAILABLE

University of Virginia

Charlottesville, Virginia, United States

Site Status AVAILABLE

Inova Schar Cancer Institute Dept of Fairfax Hospital

Fairfax, Virginia, United States

Site Status AVAILABLE

Virginia Oncology Associates

Norfolk, Virginia, United States

Site Status AVAILABLE

VCU Medical Center

Richmond, Virginia, United States

Site Status AVAILABLE

Swedish Cancer Institute First Hill

Seattle, Washington, United States

Site Status AVAILABLE

University of Washington School of Medicine

Seattle, Washington, United States

Site Status AVAILABLE

West Virginia University Medical Center

Morgantown, West Virginia, United States

Site Status AVAILABLE

University Of Wisconsin Hospital

Madison, Wisconsin, United States

Site Status AVAILABLE

Aurora Saint Lukes Medical Center

Milwaukee, Wisconsin, United States

Site Status AVAILABLE

Medical College Of Wisconsin

Milwaukee, Wisconsin, United States

Site Status AVAILABLE

DUMMY

Dummy, , Germany

Site Status AVAILABLE

Countries

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United States Germany

Central Contacts

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Study Contact

Role: CONTACT

1-800-526-7736

Other Identifiers

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68284528MMY4006

Identifier Type: OTHER

Identifier Source: secondary_id

CR108968

Identifier Type: -

Identifier Source: org_study_id

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