A Prospective, Open Label, Dose-escalation, SAD/MAD, Multicenter, 24weeks, Phase I/IIa Clinical Trial to Evaluate the Safety, Tolerability and Pharmacodynamics of Investigational Product (VM-001) in Patients With Graft-versus-host Disease(GvHD)

NCT ID: NCT05276076

Last Updated: 2022-03-11

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

NOT_YET_RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

12 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-11-20

Study Completion Date

2025-11-20

Brief Summary

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The present study is multi center, phase I/IIa clinical trial to evaluate the safety and pharmacodynamics of investigational Product (VM-001) in patients with graft-versus-host disease(GvHD). A total of 12 subjects (Part 1 SAD\[3 cohort(2 subjects/cohort)\], Part 2 MAD\[2 cohort(3subjects/cohort)\]) are recruited.

Detailed Description

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Conditions

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Graft Versus Host Disease

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Part 1 Single Ascending Dose, Cohort 1

Cohort 1 : 1X10\^6 cells/kg The safety of 2 subjects is evaluated for 1 week after single dose of IP. If CTCAE grade 3 or higher adverse drug events (ADR) do not occur in the two subjects: Begin enrollment for Cohort 2.

Group Type EXPERIMENTAL

VM-001 1X10^6 cells/kg

Intervention Type BIOLOGICAL

Administration: Inject intravenously single dose

Part 1 Single Ascending Dose, Cohort 2

Cohort 2 : 3X10\^6 cells/kg The safety of 2 subjects is evaluated for 1 week after single dose of IP. If CTCAE grade 3 or higher adverse drug events (ADR) do not occur in the two subjects: Begin enrollment for Cohort 3.

Group Type EXPERIMENTAL

VM-001 3X10^6 cells/kg

Intervention Type BIOLOGICAL

Administration: Inject intravenously single dose

Part 1 Single Ascending Dose, Cohort 3

Cohort 3 : 5X10\^6 cells/kg The safety of 2 subjects is evaluated for 1 week after single dose of IP.

Group Type EXPERIMENTAL

VM-001 5X10^6 cells/kg

Intervention Type BIOLOGICAL

Administration: Inject intravenously single dose

Part 2 Multiple Ascending Dose, Cohort 1

Cohort 1 : two doses in total, 1X10\^6 cells/kg per dose, weekly The safety of 3 subjects is evaluated for 4 week after two dose of IP. If CTCAE grade 3 or higher adverse drug events (ADR) do not occur in the three subjects: Begin enrollment for Cohort 2.

Group Type EXPERIMENTAL

VM-001 1X10^6 cells/kg two dose

Intervention Type BIOLOGICAL

Administration: Inject intravenously

1X10\^6 cells/kg per dose, two dose in total, weekly

Part 2 Multiple Ascending Dose, Cohort 2

Cohort 2 : four doses in total, 1X10\^6 cells/kg per dose, weekly The safety of 3 subjects is evaluated for 8 week after two dose of IP.

Group Type EXPERIMENTAL

VM-001 1X10^6 cells/kg four dose

Intervention Type BIOLOGICAL

Administration: Inject intravenously

1X10\^6 cells/kg per dose, four dose in total, weekly

Interventions

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VM-001 1X10^6 cells/kg

Administration: Inject intravenously single dose

Intervention Type BIOLOGICAL

VM-001 3X10^6 cells/kg

Administration: Inject intravenously single dose

Intervention Type BIOLOGICAL

VM-001 5X10^6 cells/kg

Administration: Inject intravenously single dose

Intervention Type BIOLOGICAL

VM-001 1X10^6 cells/kg two dose

Administration: Inject intravenously

1X10\^6 cells/kg per dose, two dose in total, weekly

Intervention Type BIOLOGICAL

VM-001 1X10^6 cells/kg four dose

Administration: Inject intravenously

1X10\^6 cells/kg per dose, four dose in total, weekly

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Men and women ≥19 years of age
* Acute GvHD or chronic GvHD after hematopoietic stem cell transplant
* Subjects who no longer have available standard treatment.
* ANC≥1,000cells./mm\^3
* AST, ALT, total bilirubin less than 3 times the upper limit of normal
* serum creatinine less than 1.5 times the upper limit of normal

Exclusion Criteria

* Received an anti-thymocyte globulin(ATG) within 14 days before enrollment
* FCV or FEV less than 70%
* Any uncontrolled infection or active infection requiring ongoing systemic treatment
* Received an investigational agent within 6 months before enrollment.
* Evidence of bleeding diathesis or coagulopathy.
* Active hepatitis C virus (HCV) or hepatitis B virus (HBV)
* Breastfeeding or pregnant.
Minimum Eligible Age

19 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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ViGenCell Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Chang-Ki Min, MD, Ph.D.

Role: PRINCIPAL_INVESTIGATOR

The Catholic University of Korea

Central Contacts

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Hyo Jung Park, Ph.D.

Role: CONTACT

82-70-4348-7457

Hyun-Jung Sohn, Ph.D.

Role: CONTACT

82-70-4348-7527

Other Identifiers

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VM-201

Identifier Type: -

Identifier Source: org_study_id

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