A Study of the Efficacy and Safety of Enclitide Chloride (MK-0616 Oral PCSK9 Inhibitor) in Adults With Hypercholesterolemia (MK-0616-008)

NCT ID: NCT05261126

Last Updated: 2024-12-09

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

381 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-03-10

Study Completion Date

2022-11-28

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of enclitide chloride, an oral PCSK9 inhibitor, in lowering low-density lipoprotein cholesterol (LDL-C) in participants with hypercholesterolemia. The primary hypothesis is that at least one of the four doses of enclitide chloride tested in this study is superior to placebo on percent change from baseline in LDL-C at Week 8.

Detailed Description

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Conditions

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Hypercholesterolemia Familial Hypercholesterolemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Enclitide Chloride 6 mg

Participants will receive 6 mg of enlicitide chloride orally QD for 8 weeks

Group Type EXPERIMENTAL

Enclitide Chloride

Intervention Type DRUG

Enclitide Chloride administered orally

Enclitide Chloride 12 mg

Participants will receive 12 mg of enlicitide chloride orally QD for 8 weeks

Group Type EXPERIMENTAL

Enclitide Chloride

Intervention Type DRUG

Enclitide Chloride administered orally

Enclitide Chloride 18 mg

Participants will receive 18 mg of enlicitide chloride orally QD for 8 weeks

Group Type EXPERIMENTAL

Enclitide Chloride

Intervention Type DRUG

Enclitide Chloride administered orally

Enclitide Chloride 30 mg

Participants will receive 30 mg of enlicitide chloride orally QD for 8 weeks

Group Type EXPERIMENTAL

Enclitide Chloride

Intervention Type DRUG

Enclitide Chloride administered orally

Placebo

Participants will receive enlicitide chloride-matching placebo orally QD for 8 weeks

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo matching enclitide chloride administered orally

Interventions

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Enclitide Chloride

Enclitide Chloride administered orally

Intervention Type DRUG

Placebo

Placebo matching enclitide chloride administered orally

Intervention Type DRUG

Other Intervention Names

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MK-0616

Eligibility Criteria

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Inclusion Criteria

* History of clinical atherosclerotic cardiovascular disease (ASCVD), or has an ASCVD risk equivalent and/or a 10-year risk of having an ASCVD event ≥5.0%, AND has a corresponding LDL-C that falls within the protocol-specified range at screening.
* Treatment with a stable dose of one or more lipid-lowering therapies for ≥30 days before screening, or has not received treatment with any lipid-lowering therapy for ≥30 days before screening.
* A female participant is not pregnant or breastfeeding, not a woman of child-bearing potential (WOCBP) or is a WOCBP and agrees to follow contraceptive guidance during the intervention period and for at least 8 weeks after the last dose of study intervention.

Exclusion Criteria

* History of homozygous familial hypercholesterolemia (FH) based on genetic or clinical criteria.
* History of nephrotic syndrome.
* History of unstable angina, a myocardial infarction, percutaneous transluminal coronary angioplasty, transient ischemic attack, or stroke within 3 months before Screening.
* Has poorly controlled diabetes mellitus, defined as hemoglobin A1C (A1C) ≥9.0% at Screening.
* History of malignancy ≤3 years before screening, except for adequately treated basal cell or squamous cell skin cancer or in situ cervical cancer, which have no timeframe limitations relative to screening.
* Currently participating in or has previously participated in an interventional clinical study within 3 months before Screening.
* Has moderate or greater renal insufficiency.
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

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Westside Medical Associates of Los Angeles ( Site 0026)

Beverly Hills, California, United States

Site Status

Clinical Trials Research ( Site 0007)

Sacramento, California, United States

Site Status

National Research Institute (NRI) - Santa Ana ( Site 0024)

Santa Ana, California, United States

Site Status

Excel Medical Clinical Trials ( Site 0042)

Boca Raton, Florida, United States

Site Status

Alliance for Multispecialty Research, LLC ( Site 0050)

Coral Gables, Florida, United States

Site Status

ForCare Clinical Research ( Site 0017)

Tampa, Florida, United States

Site Status

Healthcare Research Network - Chicago ( Site 0037)

Flossmoor, Illinois, United States

Site Status

Midwest Institute For Clinical Research ( Site 0036)

Indianapolis, Indiana, United States

Site Status

Cotton O'Neil Mulvane ( Site 0022)

Topeka, Kansas, United States

Site Status

L-MARC Research Center ( Site 0003)

Louisville, Kentucky, United States

Site Status

The University of Mississippi Medical Center-Clinical Research and Trials Unit ( Site 0028)

Jackson, Mississippi, United States

Site Status

Jubilee Clinical Research ( Site 0047)

Las Vegas, Nevada, United States

Site Status

New Mexico Clinical Research & Osteoporosis Center ( Site 0032)

Albuquerque, New Mexico, United States

Site Status

Mid Hudson Medical Research ( Site 0004)

New Windsor, New York, United States

Site Status

altoona center for clinical research ( Site 0045)

Duncansville, Pennsylvania, United States

Site Status

Piedmont Research Partners ( Site 0005)

Fort Mill, South Carolina, United States

Site Status

Dallas Diabetes Research Center ( Site 0012)

Dallas, Texas, United States

Site Status

Center for Cardiometabolic Disease Prevention/Baylor College of Medicine ( Site 0051)

Houston, Texas, United States

Site Status

Northeast Clinical Research of San Antonio ( Site 0014)

San Antonio, Texas, United States

Site Status

National Clinical Research, Inc-research office ( Site 0019)

Richmond, Virginia, United States

Site Status

Klinikum der Ludwig-Maximilians-Universitaet Muenchen ( Site 0504)

München, Bavaria, Germany

Site Status

Kardiologische Gemeinschaftspraxis ( Site 0502)

Nuremberg, Bavaria, Germany

Site Status

Ambulantes Herzzentrum Kassel ( Site 0501)

Kassel, Hesse, Germany

Site Status

Universitätsklinikum Leipzig ( Site 0500)

Leipzig, Saxony, Germany

Site Status

Charité Campus Virchow-Klinikum ( Site 0505)

Berlin, , Germany

Site Status

Chubu Rosal Hospital ( Site 1612)

Nagoya, Aichi-ken, Japan

Site Status

Kyoto Okamoto Memorial Hospital ( Site 1611)

Kuse-gun Kumiyama-cho, Kyoto, Japan

Site Status

Kitada Clinic ( Site 1604)

Osaka, Osaka, Japan

Site Status

Medical Corporation Heishinkai OCROM Clinic ( Site 1600)

Suita-shi, Osaka, Japan

Site Status

Seiwa Clinic ( Site 1605)

Adachi-ku, Tokyo, Japan

Site Status

meiwa hospital ( Site 1602)

Chiyoda-ku, Tokyo, Japan

Site Status

Heishinkai Medical Group ToCROM Clinic ( Site 1601)

Shinjuku-ku, Tokyo, Japan

Site Status

Sekino Hospital ( Site 1603)

Toshimaku, Tokyo, Japan

Site Status

Instituto Jalisciense de Investigacion en Diabetes y Obesidad-Endocrinology ( Site 0205)

Guadalajara, Jalisco, Mexico

Site Status

Unidad de Investigaci�n Cl�nica Cardiometabolica de Occident-Unidad de Investigación Clínica Cardio

Guadalajara, Jalisco, Mexico

Site Status

Bio Investigación AMARC, S.C. ( Site 0204)

Mexico City, Mexico City, Mexico

Site Status

Hospital Angeles Mocel ( Site 0209)

Mexico City, Mexico City, Mexico

Site Status

Instituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran ( Site 0212)

Mexico City, Mexico City, Mexico

Site Status

Unidad biomedica avanzada monterrey-Clinical Trials ( Site 0200)

Monterrey, Nuevo León, Mexico

Site Status

Centro de Estudios de Investigacion Metabolicos y Cardiovasculares-Subinvestigation ( Site 0201)

Ciudad Madero, Tamaulipas, Mexico

Site Status

Hospital Angeles Xalapa-Internal Medicine-Cardiology ( Site 0202)

Xalapa, Veracruz, Mexico

Site Status

Medical Care and Research SA de CV ( Site 0211)

Mérida, Yucatán, Mexico

Site Status

Centro de Atención e Investigación Clínica ( Site 0214)

Aguascalientes, , Mexico

Site Status

Akershus Universitetssykehus-Hjertemedisinsk Avdeling ( Site 0705)

Lørenskog, Akershus, Norway

Site Status

Nordlandssykehuset ( Site 0709)

Bodø, Nordland, Norway

Site Status

Stavanger Universitetssykehus ( Site 0706)

Stavanger, Rogaland, Norway

Site Status

Sykehuset i Vestfold-Hjerteseksjonen ( Site 0703)

Tønsberg, Vestfold, Norway

Site Status

Oslo Universitetssykehus Aker-Preventiv kardiologi Aker ( Site 0704)

Oslo, , Norway

Site Status

Oslo Universitetssykehus Rikshospitalet-Kardiologisk avdeling ( Site 0702)

Oslo, , Norway

Site Status

Oslo Universitetssykehus Ullevål-Hjertemedisinsk avdeling, Ullevål ( Site 0701)

Oslo, , Norway

Site Status

Oslo Universitetssykehus Aker-Lipidklinikken ( Site 0700)

Oslo, , Norway

Site Status

Keimyung University Dongsan Hospital ( Site 1703)

Daegu, Taegu-Kwangyokshi, South Korea

Site Status

Seoul National University Hospital ( Site 1702)

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System ( Site 1701)

Seoul, , South Korea

Site Status

Samsung Medical Center ( Site 1700)

Seoul, , South Korea

Site Status

Ege University Medicine of Faculty-Cardilogy Department ( Site 1003)

Bornova, İzmir, Turkey (Türkiye)

Site Status

Hacettepe Universitesi ( Site 1002)

Ankara, , Turkey (Türkiye)

Site Status

Eskisehir Osmangazi University-Cardiology ( Site 1000)

Eskişehir, , Turkey (Türkiye)

Site Status

Royal Free Hospital ( Site 1311)

London, England, United Kingdom

Site Status

Queen Elizabeth University Hospital-Glasgow Clinical Research Facility ( Site 1310)

Glasgow, Glasgow City, United Kingdom

Site Status

Layton Medical Centre ( Site 1303)

Blackpool, Lancashire, United Kingdom

Site Status

William Harvey Heart Centre ( Site 1308)

London, London, City of, United Kingdom

Site Status

Walsall Manor Hospital ( Site 1309)

West Midlands, Walsall, United Kingdom

Site Status

Countries

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United States Germany Japan Mexico Norway South Korea Turkey (Türkiye) United Kingdom

References

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Ballantyne CM, Banka P, Mendez G, Garcia R, Rosenstock J, Rodgers A, Mendizabal G, Mitchel Y, Catapano AL. Phase 2b Randomized Trial of the Oral PCSK9 Inhibitor MK-0616. J Am Coll Cardiol. 2023 Apr 25;81(16):1553-1564. doi: 10.1016/j.jacc.2023.02.018. Epub 2023 Mar 6.

Reference Type RESULT
PMID: 36889610 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

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http://www.merckclinicaltrials.com

Merck Clinical Trials Information

Other Identifiers

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MK-0616-008

Identifier Type: OTHER

Identifier Source: secondary_id

jRCT2031210701

Identifier Type: REGISTRY

Identifier Source: secondary_id

2021-005221-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

0616-008

Identifier Type: -

Identifier Source: org_study_id