Apomorphine in Severe Brain-injured Patients

NCT ID: NCT05213169

Last Updated: 2025-04-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2/PHASE3

Total Enrollment

48 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-06-18

Study Completion Date

2026-12-31

Brief Summary

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Background:

Patients who survive severe brain injury may develop chronic disorders of consciousness (DoC). Treating these patients to improve recovery is extremely challenging because of scarce and inefficient therapeutical options. Among pharmacological treatments, apomorphine, a potent direct dopamine agonist, has exhibited promising behavioral effects, but its true efficacy and its mechanism remains unknown. This randomized controlled study aims to verify the effects of apomorphine subcutaneous infusion in patients with disorders of consciousness and investigate the neural networks targeted by this treatment.

Methods/design:

The double-blind randomized controlled trial will include 48 patients: 24 patients will be randomly assigned to the apomorphine and 24 to the placebo group. Investigators and the patients will be unaware of the nature of the treatment rendered.

Primary outcome will be determined as behavioral response to treatment as measured by changes of diagnosis using the Coma Recovery Scale - Revised (CRS-R), while secondary outcome measures will include the Nociception Coma Scale - Revised (NCS-R), Disability Rating Scale (DRS), Wessex Head Injury Matrix (WHIM), circadian rhythm using actimetry, electroencephalography (EEG), positron emission tomography (PET) and functional magnetic resonance imaging (fMRI). The Glasgow Outcome Scale - Extended (GOS-E) and a phone-adapted version of the CRS-R will be used for long-term follow-up.

Statistical analyses will focus on the detection of changes induced by apomorphine treatment at the individual level (comparing data before and after treatment) and at the group level (comparing responders with non-responders). Response to treatment will be measured at four different levels: 1. behavioral response (CRS-R, NCS-R, DRS, WHIM, GOS-E, phone CRS-R), 2. brain metabolism (PET), 3. network connectivity (resting-state fMRI, clinical EEG and high-density EEG) and 4. Circadian rhythm changes (actimetry, body temperature, 24h-EEG).

Discussion:

Apomorphine is a promising and safe strategy for the treatment of DoC but efficacy, profile of the responding population and underlying mechanism remain to be determined. This trial will provide unprecedented data that will allow to investigate the response to apomorphine using multimodal methods and shed new light on the brain networks targeted by this drug in terms of behavioral response, functional connectivity and metabolism.

Detailed Description

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Conditions

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Disorder of Consciousness

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Apomorphine treatment or placebo
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors
Double-blind trial

Study Groups

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Apomorphine

Apomorphine hydrochloride subcutaneous infusion 12 hours per day during 30 days: titration phase from 0 to 4 mg/h (5 days), maintenance phase at 4 mg/h, titration-maintenance phase with possible increase up to 6 mg/h depending on tolerance (18 days).

Domperidone 20mg t.i.d per os (or via gastric tube) will be initiated to reduce common side effects 2 days before the initiation of apomorphine and maintained at least 7 days before an optional tapering off in the absence side effects.

Group Type EXPERIMENTAL

Apomorphine Hydrochloride 5mg/ml

Intervention Type DRUG

Product administered using an external continuous subcutaneous infusion pump.

Isotonic saline

Sodium chloride infusion following the administration procedure described for apomorphine

Group Type PLACEBO_COMPARATOR

Sodium chloride 9mg/ml

Intervention Type OTHER

Product administered using an external continuous subcutaneous infusion pump.

Interventions

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Apomorphine Hydrochloride 5mg/ml

Product administered using an external continuous subcutaneous infusion pump.

Intervention Type DRUG

Sodium chloride 9mg/ml

Product administered using an external continuous subcutaneous infusion pump.

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* 18-80 years old.
* Clinically stable, not dependent on medical ventilators for respiration.
* Diagnosed as in an unresponsive wakefulness syndrome or minimally conscious state according to the international criteria and based on at least 2 consistent CRS-R in the last 14 days (one CRS-R in the last 7 days).
* More than 4 weeks post-insult.
* No serious neurological impairments others than related to their acquired brain injury.
* No neurological medications other than anti-epileptic or anti-spasticity drugs within the last two weeks.
* No use of dopaminergic medications other than apomorphine within the last two weeks.
* Informed consent from legal representative of the patient (if patients recover, their consent will also be obtained).

Exclusion Criteria

* Use of dopamine agonists or antagonists (e.g. amantadine, bromocriptine, l-dopa, pramipexole, ropinirole, amphetamine, bupropion, methylphenidate / risperidone, haloperidol, chlorpromazine, flupentixol, clozapine, olanzapine, quetiapine) in the last 4 weeks or 4 half-lives of the drug.
* Use of drugs with known significant prolongation of the QT interval (e.g. class 1 antiarrythmics, sotalol, macrolides, quinolones, antipsychotic drugs, tricyclic antidepressants. Methadone, chloroquine, quinine)
* A corrected QT interval over 480ms (calculated using Bazett's formula on a standard 12-lead ECG recorded in the last 14 days) or other risk factors for arrhythmia (congestive cardiac failure, severe hepatic impairment or significant electrolyte disturbance).
* A history of previous neurological functional impairment.
* Contraindication to MRI, EEG, or PET (e.g., electronic implanted devices, active epilepsy, external ventricular drain).
* Use of nitrates or other vasodilators, central nervous system acting agents such as barbiturates, morphine and related drugs (relative exclusion criterion)
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Centre Hospitalier Neurologique William Lennox (Belgium)

UNKNOWN

Sponsor Role collaborator

Hôpital Valdor - ISoSL (Belgium)

UNKNOWN

Sponsor Role collaborator

VITHAS hospitales (Spain)

UNKNOWN

Sponsor Role collaborator

University of Liege

OTHER

Sponsor Role lead

Responsible Party

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Olivia Gosseries

Research Associate

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Olivia Gosseries, Ph.D.

Role: PRINCIPAL_INVESTIGATOR

University of Liege

Steven Laureys, M.D., Ph.D.

Role: STUDY_DIRECTOR

University hospital of Liège

Locations

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University of Liege

Liège, Liege, Belgium

Site Status ACTIVE_NOT_RECRUITING

Hôpital Valdor - ISoSL

Liège, Liège, Belgium

Site Status RECRUITING

Centre Hospitalier Neurologique William Lennox

Ottignies-Louvain-la-Neuve, , Belgium

Site Status RECRUITING

VITHAS

Valencia, , Spain

Site Status NOT_YET_RECRUITING

Countries

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Belgium Spain

Central Contacts

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Emilie Szymkowicz, MSc.

Role: CONTACT

+32492319947

Leandro RD Sanz, M.D.

Role: CONTACT

+3243663915

Facility Contacts

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Gwennaig Joris, MSc

Role: primary

Nicolas Lejeune, M.D., Ph.D.

Role: primary

+3210430298

Loles Navarro Pérez, Ph.D.

Role: primary

Roberto Llorens, Ph.D.

Role: backup

References

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Fridman EA, Calvar J, Bonetto M, Gamzu E, Krimchansky BZ, Meli F, Leiguarda RC, Zafonte R. Fast awakening from minimally conscious state with apomorphine. Brain Inj. 2009 Feb;23(2):172-7. doi: 10.1080/02699050802649662.

Reference Type BACKGROUND
PMID: 19191097 (View on PubMed)

Fridman EA, Krimchansky BZ, Bonetto M, Galperin T, Gamzu ER, Leiguarda RC, Zafonte R. Continuous subcutaneous apomorphine for severe disorders of consciousness after traumatic brain injury. Brain Inj. 2010;24(4):636-41. doi: 10.3109/02699051003610433.

Reference Type BACKGROUND
PMID: 20235766 (View on PubMed)

Gosseries O, Charland-Verville V, Thonnard M, Bodart O, Laureys S, Demertzi A. Amantadine, apomorphine and zolpidem in the treatment of disorders of consciousness. Curr Pharm Des. 2014;20(26):4167-84.

Reference Type BACKGROUND
PMID: 24025057 (View on PubMed)

Sanz LRD, Lejeune N, Blandiaux S, Bonin E, Thibaut A, Stender J, Farber NM, Zafonte RD, Schiff ND, Laureys S, Gosseries O. Treating Disorders of Consciousness With Apomorphine: Protocol for a Double-Blind Randomized Controlled Trial Using Multimodal Assessments. Front Neurol. 2019 Mar 19;10:248. doi: 10.3389/fneur.2019.00248. eCollection 2019.

Reference Type BACKGROUND
PMID: 30941094 (View on PubMed)

Other Identifiers

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2017/81b

Identifier Type: -

Identifier Source: org_study_id

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