Phase 1/2 Study of ZN-d5 for the Treatment of Relapsed or Refractory Light Chain (AL) Amyloidosis

NCT ID: NCT05199337

Last Updated: 2024-09-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

18 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-11-30

Study Completion Date

2024-02-14

Brief Summary

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This is a single arm, Open-Label, Phase 1/2 Study of ZN-d5 for the Treatment of Relapsed or Refractory Light Chain (AL) Amyloidosis.

Detailed Description

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A Single Arm, Open-Label, Phase 1/2 Study of ZN-d5 for the Treatment of Relapsed or Refractory Light Chain (AL) Amyloidosis. The first part of the study is phase 1 dose-escalation and the second part will be phase 2.

Conditions

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Amyloidosis AL Amyloidosis

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Treatment Arm

Subjects will receive ZN-d5 orally (PO), once (QD) on days 1-28. Cycles repeat every 28 days in the absence of disease progression or unacceptable toxicity.

Group Type EXPERIMENTAL

ZN-d5

Intervention Type DRUG

ZN-d5 will be administered orally

Interventions

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ZN-d5

ZN-d5 will be administered orally

Intervention Type DRUG

Other Intervention Names

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Study Drug

Eligibility Criteria

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Inclusion Criteria

1. Diagnosis of AL amyloidosis based on histopathology, the presence of characteristic appearance on electron microscopy, or mass spectrometry typing of amyloid.
2. Prior AL amyloidosis treatment and has received at least one, but no more than three lines of prior therapy;
3. At least 3 months from hematopoietic stem cell transplantation or the shorter of 60 days or 5 half-lives for biologics, small molecules, or investigational drugs prior to starting treatment;
4. Measurable disease defined by serum differential free light chain;
5. Assessment of t(11,14) status by FISH;
6. Eastern Cooperative Oncology Group performance status ≤2 ;
7. History of organ involvement
8. Adequate bone marrow function prior to first administration of study drug;
9. Adequate organ function;

Exclusion Criteria

1. Presence of non-AL amyloidosis, including wild-type or mutated ATTR amyloidosis;
2. Diagnosis of multiple myeloma according to the 2014 International Myeloma Working Group diagnostic criteria;
3. Mayo 2012 Stage IV disease;
4. Cardiac involvement exclusions apply to some subjects, including heart failure and cardiac arrhythmias.
5. Prior treatment with other BCL-2 inhibitors;
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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K-Group Alpha, Inc., a wholly owned subsidiary of Zentalis Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Affairs

Role: STUDY_DIRECTOR

K-Group Alpha subsidiary of Zentalis Pharmaceuticals

Locations

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University of Southern California

Los Angeles, California, United States

Site Status

Colorado Blood Cancer Institute

Denver, Colorado, United States

Site Status

Tulane University

New Orleans, Louisiana, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Tennessee Oncology

Nashville, Tennessee, United States

Site Status

Blackwater (Westmead) Hospital

Westmead, New South Wales, Australia

Site Status

Princess Alexandra Hospital

Brisbane, Queensland, Australia

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Sir Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

Bank of Cyprus Hospital

Nicosia, , Cyprus

Site Status

National and Kapodistrian University of Athens

Athens, , Greece

Site Status

Rambam Hospital

Haifa, , Israel

Site Status

Hadassah Medical Center

Jerusalem, , Israel

Site Status

Sheba Medical Center

Tel Aviv, , Israel

Site Status

Tel Aviv Sourasky Medical Center PPDS

Tel Aviv, , Israel

Site Status

IRCCS Azienda Ospedaliero Universitaria di Bologna Policlinico Sant'Orsola Malpighi

Bologna, , Italy

Site Status

Fondazione I.R.C.C.S. Policlinico San Matteo

Pavia, , Italy

Site Status

ICO Badalona-H.U. Germans Trias i Pujol

Barcelona, Badalona, Spain

Site Status

Hospital Clínico Universitario Virgen de la Arrixaca

El Palmar, Murcia, Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Clinico de Salamanca

Salamanca, , Spain

Site Status

Countries

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United States Australia Cyprus Greece Israel Italy Spain

References

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Locke M, Nieto M. AL Amyloidosis: Current Treatment and Outcomes. Adv Hematol. 2025 Mar 3;2025:7280805. doi: 10.1155/ah/7280805. eCollection 2025.

Reference Type DERIVED
PMID: 40226119 (View on PubMed)

Other Identifiers

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ZN-d5-003

Identifier Type: -

Identifier Source: org_study_id

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