A Clinical Trial of BP1002 in Patients With Refractory/Relapsed Acute Myeloid Leukemia (AML)

NCT ID: NCT05190471

Last Updated: 2025-03-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1

Total Enrollment

48 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-08-16

Study Completion Date

2027-09-30

Brief Summary

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This study evaluates the safety and tolerability of escalating doses of BP1002 (Liposomal Bcl-2 Antisense Oligodeoxynucleotide) in patients with refractory/relapsed AML. The study is designed to assess the safety profile, identify DLTs, biologically effective doses, PK, PD and potential anti-leukemic effects of BP1002 as single agent (dose escalation phase) followed by assessing BP1002 in combination with decitabine (dose expansion phase).

Detailed Description

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Conditions

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Acute Myeloid Leukemia, in Relapse Acute Myeloid Leukemia Refractory

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Relapsed/Refractory AML - BP1002 monotherapy

BP1002 monotherapy dose escalation

Group Type EXPERIMENTAL

BP1002; Liposomal Bcl-2 Antisense Oligodeoxynucleotide

Intervention Type DRUG

Dose escalation of BP1002 monotherapy

Relapsed/Refractory AML - BP1002 in combination with decitabine

BP1002 single dose in combination with decitabine

Group Type EXPERIMENTAL

BP1002; Liposomal Bcl-2 Antisense Oligodeoxynucleotide

Intervention Type DRUG

Dose escalation of BP1002 monotherapy

Decitabine (in combination with BP1002)

Intervention Type DRUG

Dose expansion of BP1002 in combination with decitabine

Interventions

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BP1002; Liposomal Bcl-2 Antisense Oligodeoxynucleotide

Dose escalation of BP1002 monotherapy

Intervention Type DRUG

Decitabine (in combination with BP1002)

Dose expansion of BP1002 in combination with decitabine

Intervention Type DRUG

Other Intervention Names

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Liposomal Bcl-2; L-Bcl-2 Decitabine

Eligibility Criteria

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Inclusion Criteria

1. Adults ≥18 years of age, with histologic evidence of refractory/relapsed AML who have failed treatment with available therapies known to be active for refractory/relapsed AML
2. Eastern Cooperative Oncology Group (ECOG) Performance Status Score of 0, 1 or 2
3. For the dose expansion phase, participants with documented diagnosis of AML who are eligible for decitabine therapy
4. Participants must have adequate hepatic and renal functions as defined by:

1. Aspartate transaminase (AST) and alanine transaminase (ALT) ≤2.5 times the upper limit of normal (ULN); and
2. Usually total bilirubin ≤ 1.5 ULN. In specific cases the PI may request a waiver of this requirement with medical justification and agreement with the medical monitor and Bio-Path Holdings. And;
3. Estimated creatinine clearance of at least 60 mL/min. These estimations are calculated using the Cockcroft-Gault equation.
5. Female participants of childbearing potential must agree to use an acceptable method of birth control (i.e. a hormonal contraceptive, intrauterine device, diaphragm with spermicide, condom with spermicide or abstinence) for the duration of the study and for at least 6 months after the last dose of study drug or decitabine
6. Male participants must agree to use an acceptable method of contraception for the duration of the study
7. Recovered from the effects of any prior surgery, radiotherapy, or antineoplastic treatment (with the exception of alopecia), based on Investigator assessment
8. Participants must be willing and able to provide written informed consent

Exclusion Criteria

1. Active non-hematologic or lymphoid malignancy other than AML treated with immunotherapy, targeted therapy or chemotherapy within the previous 12 months
2. Known, active leptomeningeal leukemia requiring intrathecal therapy. NOTE: Participants with a history of CNS disease may be allowed to participate based on at least 1 documented, negative spinal fluid assessment within 28 days prior to Screening
3. Isolated potentially treatable extramedullary leukemia without also meeting bone marrow criteria for acute leukemia (for AML usually ≥ 5% blasts in BMA or biopsy). Participants may have leukemia with lower blast counts (Döhner 2017). Bio-Path Holdings and Investigator concurrence required.
4. Acute promyelocytic leukemia (APL) with t(15;17)(q22;q12) PML-RARA
5. Chronic myeloid leukemia in any phase
6. Receipt of any anti-cancer therapy within 14 days prior to C1D1, with the exception of hydroxyurea or leukapheresis
7. Participants may not be receiving any other investigational agents
8. Female participants who are pregnant or breast-feeding
9. Substance abuse, medical, psychological or social conditions that may interfere with the patient's participation in the study or evaluation of the study results
10. Participants with human immunodeficiency virus (HIV) infection who have CD4+ T-cell counts \< 350 cells/mcL or with clinically active hepatitis B or C infection
11. History of any hypersensitivity to hypomethylating agents, unless reaction is deemed irrelevant to the study by the Investigator and Medical Monitor
12. Unresolved toxicity higher than CTCAE Grade 1 attributed to any prior therapy or procedure, excluding alopecia
13. Presence of concurrent conditions that, in the opinion of the Investigator and/or Medical Monitor, may compromise the participant's ability to tolerate study treatment or interfere with any aspect of study conduct or interpretation of results. This includes, but is not limited to, unstable or uncontrolled angina, New York Heart Association (NYHA) class III or IV congestive heart failure, uncontrolled and sustained hypertension, clinically significant cardiac dysrhythmia or clinically significant baseline ECG abnormality (e.g., QTcF \>470 msec)
14. Within the past 6 months, has had any of the following: myocardial infarction, unstable angina pectoris, coronary/peripheral artery bypass graft, cerebrovascular accident or transient ischemic attack
15. Uncontrolled seizure disorder (i.e., seizures within the past 2 months)
16. Unable or unwilling to communicate or cooperate with the Investigator or follow the protocol for any reason
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bio-Path Holdings, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gail J Roboz, MD

Role: PRINCIPAL_INVESTIGATOR

Weill Cornell Medical College - New York-Presbyterian Hospital

Locations

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Scripps Green Hospital

La Jolla, California, United States

Site Status RECRUITING

UCLA Medical Center

Los Angeles, California, United States

Site Status RECRUITING

Weill Cornell Medical College - NewYork-Presbyterian Hospital

New York, New York, United States

Site Status RECRUITING

MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Michael Hickey

Role: CONTACT

832-742-1361

Facility Contacts

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Kiley Borchard

Role: primary

858-554-9253

Gary Schiller, MD

Role: primary

Dunay Bach

Role: primary

212-746-4447

Gail Roboz, MD

Role: backup

646-962-2700

Miranda Lim, BSN, RN

Role: primary

713-794-1722

Maro Ohanian, D.O.

Role: backup

713-792-2631

Other Identifiers

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BP1002-102-AML

Identifier Type: -

Identifier Source: org_study_id

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