A Study of Single Ascending Doses of IW-3300 in Healthy Volunteers

NCT ID: NCT05188261

Last Updated: 2023-12-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

32 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-01-18

Study Completion Date

2022-03-21

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a first-in-human study to evaluate the safety and tolerability of single ascending doses of IW-3300. The study drug will be administered rectally as a low-volume (20 mL) enema. Study participants will be randomized in a 3:1 ratio to receive a single dose of IW-3300 or placebo. Up to 5 different doses of IW-3300 will be studied. Safety reviews will be conducted before proceeding to each higher dose.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This is a Phase 1, single-center, randomized, double-blind, placebo-controlled, single-ascending-dose study assessing the safety, tolerability, and pharmacokinetics (PK) of IW 3300 administered rectally as a low-volume enema in healthy adult volunteers. This first-in-human study will assess participants for safety, tolerability, and PK.

The study includes up to 6 treatments: placebo and up to 5 dose levels of IW-3300 which will be determined after safety reviews of previous cohorts.

This study will enroll a maximum of 40 participants (up to 5 cohorts of 8 participants each). The 8 participants within each cohort will be randomized in a double-blind manner to receive a single dose of IW-3300 (6 participants) or placebo (2 participants), administered rectally as a low-volume \[20 mL\] enema. Each cohort will progress through a Screening Period, Clinic Period, and Follow-up Period. Treatment duration will be 1 day. Participants will remain in the Phase 1 unit for approximately 24 hours after dosing and will be contacted by phone for follow-up approximately 2 weeks after dosing. Total participation will be 22 to 45 days, including the Screening, Clinic, and Follow-up Periods.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Healthy Volunteers

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

healthy volunteers

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators
The investigator and all other clinical research unit staff, sponsor study personnel, and the participant will remain blinded to individual participant treatment assignments throughout the study. Treatment assignments of individual participants will only be unblinded to a sponsor representative for regulatory reporting purposes or if warranted by emerging safety or tolerability issues.

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Cohort 1: 100 μg IW-3300

Dose 1: within the cohort, 6 participants receive active drug (IW-3300)

Group Type EXPERIMENTAL

IW-3300

Intervention Type DRUG

A single dose of IW-3300 administered rectally (as a low-volume \[20 mL\] enema) following a fast of at least 6 hours.

Cohort 1: Placebo

Within the cohort, 2 participants will receive the matching placebo dose

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

A single dose of placebo administered rectally (as a low-volume \[20 mL\] enema) following a fast of at least 6 hours.

Cohort 2: 300 μg IW-3300

Dose 2: within the cohort, 6 participants receive active drug (IW-3300)

Group Type EXPERIMENTAL

IW-3300

Intervention Type DRUG

A single dose of IW-3300 administered rectally (as a low-volume \[20 mL\] enema) following a fast of at least 6 hours.

Cohort 2: Placebo

Within the cohort, 2 participants will receive the matching placebo dose

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

A single dose of placebo administered rectally (as a low-volume \[20 mL\] enema) following a fast of at least 6 hours.

Cohort 3: 900 μg IW-3300

Dose 3: within the cohort, 6 participants receive active drug (IW-3300)

Group Type EXPERIMENTAL

IW-3300

Intervention Type DRUG

A single dose of IW-3300 administered rectally (as a low-volume \[20 mL\] enema) following a fast of at least 6 hours.

Cohort 3: Placebo

Within the cohort, 2 participants will receive the matching placebo dose

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

A single dose of placebo administered rectally (as a low-volume \[20 mL\] enema) following a fast of at least 6 hours.

Cohort 4: 2500 μg IW-3300

Dose 4: within the cohort, 6 participants receive active drug (IW-3300)

Group Type EXPERIMENTAL

IW-3300

Intervention Type DRUG

A single dose of IW-3300 administered rectally (as a low-volume \[20 mL\] enema) following a fast of at least 6 hours.

Cohort 4: Placebo

Within the cohort, 2 participants will receive the matching placebo dose

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

A single dose of placebo administered rectally (as a low-volume \[20 mL\] enema) following a fast of at least 6 hours.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

IW-3300

A single dose of IW-3300 administered rectally (as a low-volume \[20 mL\] enema) following a fast of at least 6 hours.

Intervention Type DRUG

Placebo

A single dose of placebo administered rectally (as a low-volume \[20 mL\] enema) following a fast of at least 6 hours.

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Males and female subjects of non-childbearing potential
2. Ages 18 to 60 years
3. Medically healthy with no clinically significant findings during medical evaluation including physical examination, 12-lead electrocardiogram (ECG), and clinical laboratory tests.
4. Normal bowel movement frequency of formed stool at baseline (≥3 per week and ≤3 per day; average Bristol stool form scale (BSFS) score of \>2 and \<6).
5. Body mass index (BMI) within the range 18.5 to 35.0 kg/m2 (inclusive) at the Screening Visit.
6. Male subjects and female partners are willing to use double-barrier method of contraception during the study.
7. If subject is ≥45 years of age, subject is compliant with colorectal cancer screening guidelines according to the American College of Gastroenterology (ACG) Clinical Guidelines: Colorectal Cancer Screening 2021.

Exclusion Criteria

1. Evidence or history of clinically significant acute or chronic disease, or clinically significant illness within 30 days of the Screening Visit.
2. History of clinically significant hypersensitivity or allergies to any of the inactive ingredients contained in the active or placebo drug products.
3. History of any condition that would interfere with their ability to receive an enema, or has had difficulty receiving an enema in the past.
4. Recent history of anal fissure, anal abscess, complicated hemorrhoids, or presence or history of inflammatory bowel disease.
5. Used a prescription medication during the 14 days before Check-in
6. Used any over-the-counter medications, including laxatives, and herbal supplements during the 7 days before Check-in.
7. Received a licensed or investigational vaccine during the 30 days before Check-in or is planning to receive any vaccine during the study.
8. Recently received or donated blood products.
9. Undergone a surgical procedure during the 30 days before Check-in, other than minor dermatologic procedures, or has a history of surgery involving the GI tract or anal canal (with the exception of endoscopic procedures, appendectomy, and cholecystectomy).
10. Received any investigational drug during the 30 days or 5 half-lives of that investigational drug (whichever is longer) before the Screening Visit, or is planning to receive another investigational drug at any time during the study.
11. Abnormal laboratory tests or clinically significant findings on safety tests conducted at the Screening Visit or at Check-in.
12. Confirmed or suspected infection with COVID-19 at the Screening Visit or Check-in.
13. Positive serology for human immunodeficiency virus (HIV) 1, HIV 2, or hepatitis B surface antigen (HBsAg), or positive for anti-HIV 1, anti-HIV 2, or anti hepatitis C virus (HCV) antibodies at the Screening Visit.
14. History of alcohol or drug addiction during the year before the Screening Visit, or has a positive drug or alcohol screen at the Screening Visit or Check-in.
Minimum Eligible Age

18 Years

Maximum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Ironwood Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Ironwood Study Chair

Role: STUDY_DIRECTOR

Ironwood Pharmaceuticals

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

PPD

Austin, Texas, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

C3300-101

Identifier Type: -

Identifier Source: org_study_id