Neoadjuvant HAIC of TACE Plus Donafenib in BCLC B Stage HCC: a Multi-center Randomized Controlled Trial.

NCT ID: NCT05171166

Last Updated: 2025-12-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2/PHASE3

Total Enrollment

18 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-12-24

Study Completion Date

2025-10-31

Brief Summary

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The purpose of this study is to evaluate the safety and efficacy of the combination therapy with HAIC-TACE and donafenib compared to TACE plus donafenib in patients with BCLC B stage unresectable hepatocellular carcinoma (HCC) out of up-to-seven criteria.

Detailed Description

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Trans-arterial chemoembolization (TACE) is the most widely used palliative treatment for BCLC B stage hepatocellular carcinoma (HCC) patients. While a number of studies demonstrated poor effect of TACE for patients with large hepatocellular carcinoma especially for those with tumor that out of up-to-7 criteria. Some recent studies suggested that, compared with TACE, hepatic arterial infusion chemotherapy (HAIC) may improve the survivals for HCC with large tumor. Thus, the investigators carried out this prospective randomized controlled trial to demonstrate the superiority of neoadjuvant HAIC of TACE.

Total 156 subjects will be recruited in this study, each group of 78 subjects in treatment group (HAIC-TACE-Dona group) and control group (TACE-Dona group). Primary efficacy analysis will be done in the full analysis set. PFS will be used as primary outcome measures. OS, TTP, ORR, DCR and safety will be the secondary endpoints. In addition, the safety evaluation will be carried out according to the standard of adverse reaction classification (Common Terminology Criteria for Adverse Events, CTCAE v5.0).

Conditions

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Hepatocellular Carcinoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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HAIC-TACE-Dona Group

200 mg of donafenib (consisting of two 100-mg tablets) twice daily combine with hepatic arterial infusion chemotherapy that consists of oxaliplatin (35 mg/m2 for 2 hours), followed by 5-fluorouracil (600 mg/m2 for 22 hours) on day1-3 every 4 weeks. After 2-4 cycles of HAIC treatment, the sequential TACE therapy would be performed.

Group Type EXPERIMENTAL

HAIC

Intervention Type PROCEDURE

Hepatic arterial infusion chemotherapy is consist of oxaliplatin (35 mg/m2 for 2 hours), followed by 5-fluorouracil (600 mg/m2 for 22 hours) on day1-3 every 4 weeks. For each cycle, leucovorin calcium 200 mg/m2 would be intravenously administered for 2 hours from beginning of 5-fluorouracil infusion.

TACE

Intervention Type PROCEDURE

A standard hepatic artery catheter would be introduced via the femoral artery percutaneously. Selective catheterization of the proper hepatic artery would be performed using standard diagnostic catheters and fluoroscopic guidance. In the event of multiple arterial supply, the proportion of the liver supplied by each artery would be estimated by the arteriography. After optimal positioning of the catheter, cTACE or DEB-TACE protocol would be performed to embolize the tumor supplying artery blood flow until the stasis of the supplying artery.

FOLFOX

Intervention Type DRUG

oxaliplatin,leucovorin, and 5-FU

cTACE or DEB-TACE

Intervention Type DRUG

lipiodol or microspheres that mixed with EPI

Donafenib

Intervention Type DRUG

200 mg of donafenib (consisting of two 100-mg tablets) twice daily.

TACE-Dona Group

200 mg of donafenib (consisting of two 100-mg tablets) twice daily combine with cTACE or DEB-TACE that mixed with EPI.

Group Type ACTIVE_COMPARATOR

TACE

Intervention Type PROCEDURE

A standard hepatic artery catheter would be introduced via the femoral artery percutaneously. Selective catheterization of the proper hepatic artery would be performed using standard diagnostic catheters and fluoroscopic guidance. In the event of multiple arterial supply, the proportion of the liver supplied by each artery would be estimated by the arteriography. After optimal positioning of the catheter, cTACE or DEB-TACE protocol would be performed to embolize the tumor supplying artery blood flow until the stasis of the supplying artery.

cTACE or DEB-TACE

Intervention Type DRUG

lipiodol or microspheres that mixed with EPI

Donafenib

Intervention Type DRUG

200 mg of donafenib (consisting of two 100-mg tablets) twice daily.

Interventions

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HAIC

Hepatic arterial infusion chemotherapy is consist of oxaliplatin (35 mg/m2 for 2 hours), followed by 5-fluorouracil (600 mg/m2 for 22 hours) on day1-3 every 4 weeks. For each cycle, leucovorin calcium 200 mg/m2 would be intravenously administered for 2 hours from beginning of 5-fluorouracil infusion.

Intervention Type PROCEDURE

TACE

A standard hepatic artery catheter would be introduced via the femoral artery percutaneously. Selective catheterization of the proper hepatic artery would be performed using standard diagnostic catheters and fluoroscopic guidance. In the event of multiple arterial supply, the proportion of the liver supplied by each artery would be estimated by the arteriography. After optimal positioning of the catheter, cTACE or DEB-TACE protocol would be performed to embolize the tumor supplying artery blood flow until the stasis of the supplying artery.

Intervention Type PROCEDURE

FOLFOX

oxaliplatin,leucovorin, and 5-FU

Intervention Type DRUG

cTACE or DEB-TACE

lipiodol or microspheres that mixed with EPI

Intervention Type DRUG

Donafenib

200 mg of donafenib (consisting of two 100-mg tablets) twice daily.

Intervention Type DRUG

Other Intervention Names

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oxaliplatin leucovorin 5-fluorouracil EPI Dona

Eligibility Criteria

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Inclusion Criteria

1. Subjects must volunteer to participate in the study, signed informed consent, and were able to comply with the program requirements of visits and related procedures.
2. Age and gender: \>18 years old and≤75 years old, both men and women.
3. All subjects must have Hepatocellular Carcinoma confirmed by pathological or clinical diagnosis.
4. Subjects are not suitable for radical resection or radical ablative therapy.
5. BCLC B based on Barcelona Clinic Liver Cancer staging system, and the lesions in the liver exceed up to 7 criteria, the number of tumors + the maximum diameter of tumors \> 7.
6. Patients with viable and measurable target lesion per mRECIST.
7. Patients who are expected to live more than 3 months.
8. ECOG PS 0-1.
9. Child-Pugh class A.
10. Patients with laboratory values that meet the following criteria:

1. Hemoglobin≥90 g/L;
2. Neutrophile granulocytes≥1.5×109/L;
3. Platelet count≥75×109/L;
4. Albumin≥30 g/L;
5. Total serum bilirubin ≤ 2 times upper limits of normal;
6. AST and ALT ≤ 5 times upper limits of normal;
7. Serum creatinine ≤ 1.5 times upper limits of normal;
8. Alkaline phosphatase ≤ 5 times upper limits of normal;
9. Prothrombin time or international normalized ratio ≤ 1.5 times upper limits of normal, activated partial thromboplastin time (APTT) ≤ 1.5×ULN;

Exclusion Criteria

1. Fibrolamellar hepatocellular carcinoma, sarcomatoid hepatocellular carcinoma, cholangiocarcinoma confirmed by histology or cytology.
2. History of malignant tumor, excluding the following cases:

1. Malignant tumor that was curatively treated more than 5 years prior to study entry and has not recurred since then;
2. Successful radical resection of basal cell carcinoma of the skin, squamous cell carcinoma of the skin, superficial bladder carcinoma, preinvasive cervix carcinoma, and other preinvasive cancers.
3. Diffuse tumor lesion.
4. The lesions load in the liver exceeds 20, the number of tumors + the maximum diameter of tumors \> 20.
5. Vascular invasion or extrahepatic metastasis.
6. Preexisting or history of hepatic encephalopathy, hepatorenal syndrome or liver transplantation.
7. Clinically uncontrolled ascites or pleural effusion.
8. History of surgical excision or ablation within 4 weeks of the start of treatment.
9. History of hepatic arterial infusion, more than twice TACE therapy, or history of TACE within 6 months of the start of treatment.
10. History of systemic therapy, including but not limited to chemotherapy, targeted therapy, immunotherapy.
11. History of thrombosis and/or embolism within 6 months of the start of treatment.
12. Clinically severe gastrointestinal bleeding within 6 months of the start of treatment or any life-threatening bleeding events within 3 months of the start of treatment.
13. Clinically significant cardiovascular disease, including, but not limited to, acute myocardial infarction, severe/unstable angina or prior coronary artery bypass surgery, congestive heart failure (NYHA \>2), poorly controlled arrhythmias or arrhythmias requiring pacemaker therapy, hypertension not controlled by medication (systolic blood pressure ≥140 mmHg and/or diastolic blood pressure ≥90 mmHg) within the past 6 months.
14. Other significant clinical and laboratory abnormalities, such as uncontrolled diabetes, chronic kidney disease, grade II or above peripheral neuropathy (CTCAE V5.0), and thyroid dysfunction, that may affect the safety evaluation.
15. Severe infections that are active or clinically poorly controlled.
16. If accompanied by acute or chronic active hepatitis B, unless taking antiviral drugs.
17. Female patients who are pregnant, lactating, possibly pregnant, or planning to become pregnant, and fertile female or male patient who is unwilling or unable to use effective contraception.
18. Multiple branches of hepatic artery with severe variation.
19. Any other subjects that the investigator considers ineligible.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Peking University

OTHER

Sponsor Role lead

Responsible Party

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Xiaodong Wang, MD

Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Xiaodong Wang, MD

Role: PRINCIPAL_INVESTIGATOR

Department of Interventional Therapy, Peking University Cancer Hospital

Locations

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Peking University Cancer Hospital

Beijing, Beijing Municipality, China

Site Status

Countries

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China

References

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Other Identifiers

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Neo-TACE

Identifier Type: -

Identifier Source: org_study_id