ML-004 in Adolescents and Adults With Autism Spectrum Disorders (ASD)

NCT ID: NCT05081245

Last Updated: 2025-12-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

150 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-09-13

Study Completion Date

2026-11-30

Brief Summary

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ML-004-002 is a multi-center, randomized, double-blind, parallel-group, placebo-controlled study that will enroll approximately 150 adolescent and adult subjects with ASD. The primary objective is to evaluate the efficacy of ML-004 compared with placebo in the improvement of social communication deficits in subjects with ASD.

Detailed Description

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Conditions

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Autism Spectrum Disorder

Keywords

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ASD Autism Autism Spectrum Disorder Social Communication

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Multi-center, randomized, double-blind, placebo-controlled study
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Double-blind

Study Groups

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ML-004 (IR)/(ER) tablet

ML-004 is a bilayer immediate-release (IR)/extended-release (ER, gastroretentive) oral tablet formulation. ML-004 is taken orally once daily and provided as a tablet in two dose strengths of 12 mg (3 mg IR/9 mg ER) and 24 mg tablet (6 mg IR/18 mg ER). Dose levels for this study are 12 mg (provided as one 12 mg tablet), 24 mg (one 24 mg tablet), 48 mg (two 24 mg tablets), and 72 mg (three 24 mg tablets).

Group Type EXPERIMENTAL

ML-004 (IR)/(ER) tablet

Intervention Type DRUG

Participants will receive ML-004 once daily.

ML-004 Placebo

Matched placebo oral tablets will consist of same excipients as the investigational drug but without any ML-004. Placebo taken orally once daily to match tablet number of ML-004 dose levels for 12 mg (1 tablet), 24 mg (1 tablet), 48 mg (2 tablets), and 72 mg (3 tablets).

Group Type PLACEBO_COMPARATOR

ML-004 Placebo

Intervention Type DRUG

Participants will receive matching placebo once daily.

Interventions

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ML-004 (IR)/(ER) tablet

Participants will receive ML-004 once daily.

Intervention Type DRUG

ML-004 Placebo

Participants will receive matching placebo once daily.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Age 12 to 45 at screening
* Has a designated care/study partner who can reliably report on symptoms
* Has a diagnosis of Autism Spectrum Disorder (ASD)
* Has a body mass index (BMI) 18 through 34 kg/m², inclusive
* Full scale IQ (or equivalent) ≥55 score, with adequate verbal fluency, as determined by the Principal Investigator.
* Psychoactive medications and adjunctive therapies are stable for 4 weeks prior to screening
* Must be able to swallow study medication

Exclusion Criteria

* Has Rett syndrome or Child Disintegrative Disorder
* Has participated in any other study and received any other investigational medication (other than COVID-19 vaccination) or device within 60 days prior to screening
* History of epilepsy without current adequate control, or any seizure in the 6 months preceding screening
* History of suicidal ideation or behavior in the past 12 months, or a positive response to C-SSRS questions 4 and/or 5
* Systolic blood pressure ≥140 mmHg (if adult) or \>135 mmHg (if adolescent), or diastolic blood pressure ≥90 (if adult) or \>85 mmHg (if adolescent), or a clinical history of uncontrolled or severe hypertension
* If female, is pregnant or lactating
Minimum Eligible Age

12 Years

Maximum Eligible Age

45 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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MapLight Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Harmonex Neuroscience Research

Dothan, Alabama, United States

Site Status

Southwest Autism Research & Resource Center, Clinical Research

Phoenix, Arizona, United States

Site Status

Cortica Healthcare

Glendale, California, United States

Site Status

NRC Research Institute

Orange, California, United States

Site Status

Cortica

San Rafael, California, United States

Site Status

Yale Child Study Center

New Haven, Connecticut, United States

Site Status

Children's National Health System - The Children's Research Institute (CRI)

Washington D.C., District of Columbia, United States

Site Status

Abba Medical Group

Miami, Florida, United States

Site Status

APG Research, LLC

Orlando, Florida, United States

Site Status

University of South Florida Psychiatry and Behavioral Neurosciences

Tampa, Florida, United States

Site Status

Neurobehavioral Medicine Group

Bloomfield Hills, Michigan, United States

Site Status

University of Missouri, Thompson Center for Autism & Neurodevelopmental Disorders

Columbia, Missouri, United States

Site Status

Jersey Shore University Medical Center

Neptune City, New Jersey, United States

Site Status

Nathan Kline Institute for Psychiatric Research

Orangeburg, New York, United States

Site Status

Richmond Behavioral Associates

Staten Island, New York, United States

Site Status

Center for Autism and the Developing Brain, New York State Psychiatric Institute

White Plains, New York, United States

Site Status

Ohio State University Nisonger Center

Columbus, Ohio, United States

Site Status

Suburban Research Associates

Media, Pennsylvania, United States

Site Status

BioBehavioral Research of Austin

Austin, Texas, United States

Site Status

Red Oak Psychiatry Associates, PA

Houston, Texas, United States

Site Status

Road Runner Research, Ltd.

San Antonio, Texas, United States

Site Status

Family Psychiatry of The Woodlands

The Woodlands, Texas, United States

Site Status

Cedar Clinical Research

Draper, Utah, United States

Site Status

Virginia Commonwealth University

Richmond, Virginia, United States

Site Status

Brain and Mind Centre

Camperdown, New South Wales, Australia

Site Status

The Royal Children's Hospital, Murdoch Children's Research Institute

Parkville, Victoria, Australia

Site Status

OCT Research ULC (dba Okanagan Clinical Trials)

Kelowna, British Columbia, Canada

Site Status

Lawson Health Research Institute/ London Health Sciences Centre

London, Ontario, Canada

Site Status

Holland Bloorview Kids Rehabilitation Hospital

Toronto, Ontario, Canada

Site Status

Countries

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United States Australia Canada

Other Identifiers

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ML-004-002

Identifier Type: -

Identifier Source: org_study_id