Trial Outcomes & Findings for Amiloride in Nephrotic Syndrome (NCT NCT05079789)

NCT ID: NCT05079789

Last Updated: 2025-01-14

Results Overview

Decrease of overhydration (OH) measured by bioimpedance spectroscopy, expressed as percent of extracellular water (%ECW)

Recruitment status

TERMINATED

Study phase

PHASE3

Target enrollment

20 participants

Primary outcome timeframe

8 days

Results posted on

2025-01-14

Participant Flow

Participant milestones

Participant milestones
Measure
Amiloride
Treatment wirh Amiloride, start dose 5 mg Amiloride: Treatment with amiloride, start dose 5 mg
Furosemide
Treatment with Furosemide, start dose 40 mg Furosemide: Treatment with furosemide, start dose 40 mg
Overall Study
STARTED
10
10
Overall Study
COMPLETED
10
10
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Amiloride in Nephrotic Syndrome

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Amiloride
n=10 Participants
Treatment wirh Amiloride, start dose 5 mg Amiloride: Treatment with amiloride, start dose 5 mg
Furosemide
n=10 Participants
Treatment with Furosemide, start dose 40 mg Furosemide: Treatment with furosemide, start dose 40 mg
Total
n=20 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
8 Participants
n=5 Participants
8 Participants
n=7 Participants
16 Participants
n=5 Participants
Age, Categorical
>=65 years
2 Participants
n=5 Participants
2 Participants
n=7 Participants
4 Participants
n=5 Participants
Age, Continuous
51 years
n=5 Participants
50 years
n=7 Participants
51 years
n=5 Participants
Sex: Female, Male
Female
5 Participants
n=5 Participants
2 Participants
n=7 Participants
7 Participants
n=5 Participants
Sex: Female, Male
Male
5 Participants
n=5 Participants
8 Participants
n=7 Participants
13 Participants
n=5 Participants
Race/Ethnicity, Customized
Ethnicity · European
9 Participants
n=5 Participants
10 Participants
n=7 Participants
19 Participants
n=5 Participants
Race/Ethnicity, Customized
Ethnicity · Indian
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Region of Enrollment
Germany
10 participants
n=5 Participants
10 participants
n=7 Participants
20 participants
n=5 Participants

PRIMARY outcome

Timeframe: 8 days

Decrease of overhydration (OH) measured by bioimpedance spectroscopy, expressed as percent of extracellular water (%ECW)

Outcome measures

Outcome measures
Measure
Amiloride
n=10 Participants
Treatment wirh Amiloride, start dose 5 mg Amiloride: Treatment with amiloride, start dose 5 mg
Furosemide
n=10 Participants
Treatment with Furosemide, start dose 40 mg Furosemide: Treatment with furosemide, start dose 40 mg
Decrease of Overhydration, %ECW After 8 Days
1.95 %ECW
Interval 0.8 to 6.4
5.15 %ECW
Interval 0.9 to 8.3

SECONDARY outcome

Timeframe: 16 days

Decrease of overhydration (OH) measured by bioimpedance spectroscopy, expressed as percent of extracellular water (%ECW)

Outcome measures

Outcome measures
Measure
Amiloride
n=9 Participants
Treatment wirh Amiloride, start dose 5 mg Amiloride: Treatment with amiloride, start dose 5 mg
Furosemide
n=10 Participants
Treatment with Furosemide, start dose 40 mg Furosemide: Treatment with furosemide, start dose 40 mg
Decrease of Overhydration, %ECW After 16 Days
10.10 %ECW
Interval 1.3 to 14.4
7.40 %ECW
Interval 2.8 to 10.1

SECONDARY outcome

Timeframe: 8 days

Decrease of body weight after 8 days

Outcome measures

Outcome measures
Measure
Amiloride
n=10 Participants
Treatment wirh Amiloride, start dose 5 mg Amiloride: Treatment with amiloride, start dose 5 mg
Furosemide
n=10 Participants
Treatment with Furosemide, start dose 40 mg Furosemide: Treatment with furosemide, start dose 40 mg
Decrease of Body Weight, kg
3.8 kg
Interval 1.7 to 7.2
2.0 kg
Interval 1.5 to 4.6

Adverse Events

Amiloride

Serious events: 1 serious events
Other events: 9 other events
Deaths: 0 deaths

Furosemide

Serious events: 4 serious events
Other events: 10 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Amiloride
n=10 participants at risk
Treatment wirh Amiloride, start dose 5 mg Amiloride: Treatment with amiloride, start dose 5 mg
Furosemide
n=10 participants at risk
Treatment with Furosemide, start dose 40 mg Furosemide: Treatment with furosemide, start dose 40 mg
Surgical and medical procedures
delayed discharge from hospital due to macrohematuria after kidneybiopsy
10.0%
1/10 • Number of events 1 • 23 days for everey subject
0.00%
0/10 • 23 days for everey subject
Cardiac disorders
myocardial infarction
0.00%
0/10 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject
Cardiac disorders
pericardial effusion with in-hospital monitoring
0.00%
0/10 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject
Gastrointestinal disorders
abdominal pain with diarrhea with inhospital treatment
0.00%
0/10 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject
Renal and urinary disorders
AKI stage 2 with in-hospital treatment
0.00%
0/10 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject

Other adverse events

Other adverse events
Measure
Amiloride
n=10 participants at risk
Treatment wirh Amiloride, start dose 5 mg Amiloride: Treatment with amiloride, start dose 5 mg
Furosemide
n=10 participants at risk
Treatment with Furosemide, start dose 40 mg Furosemide: Treatment with furosemide, start dose 40 mg
Surgical and medical procedures
planned hospitalization for kidney biopsy
20.0%
2/10 • Number of events 2 • 23 days for everey subject
30.0%
3/10 • Number of events 3 • 23 days for everey subject
Nervous system disorders
dizziness
0.00%
0/10 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject
Nervous system disorders
headache
0.00%
0/10 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject
Gastrointestinal disorders
nausea
20.0%
2/10 • Number of events 2 • 23 days for everey subject
0.00%
0/10 • 23 days for everey subject
Respiratory, thoracic and mediastinal disorders
epistaxis
10.0%
1/10 • Number of events 1 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject
Hepatobiliary disorders
elevated liver enzymes
0.00%
0/10 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject
Skin and subcutaneous tissue disorders
rash
0.00%
0/10 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject
Renal and urinary disorders
urinary infection
10.0%
1/10 • Number of events 1 • 23 days for everey subject
0.00%
0/10 • 23 days for everey subject
Renal and urinary disorders
hypervolemia (worsening)
10.0%
1/10 • Number of events 1 • 23 days for everey subject
0.00%
0/10 • 23 days for everey subject
Infections and infestations
SARS CoV 2 infection
20.0%
2/10 • Number of events 2 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject
Musculoskeletal and connective tissue disorders
cramps of legs and hands
0.00%
0/10 • 23 days for everey subject
10.0%
1/10 • Number of events 1 • 23 days for everey subject

Additional Information

Dr. Anja Schork

University Hospital Tuebingen

Phone: +49 707129 83172

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place