Study of BOTOX Injections in Prevention of Migraine in Adult Participants With Episodic Migraine

NCT ID: NCT05028569

Last Updated: 2025-12-09

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

775 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-11-05

Study Completion Date

2024-11-06

Brief Summary

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Migraine is a neurological disease characterized by moderate or severe headache, associated with nausea, vomiting, and/or sensitivity to light and sound (International Classification of Headache Disorders, 2018). Migraine can be further categorized according to the frequency of attacks as episodic migraine (EM) or chronic migraine (CM). This study will assess the effects of BOTOX in preventing migraine in adult participants with EM.

BOTOX is being developed for the prevention of migraine in adults with episodic migraine (EM). Participants will be enrolled in 3 different treatment groups. There is 1 in 3 chance that participants will be assigned to receive placebo. Approximately 777 adult participants with EM will be enrolled in approximately 125 sites across the world.

Participants will receive intramuscular injections (injected into the muscle) of BOTOX or Placebo on Day 1 and Week 12. Eligible participants will receive BOTOX on Week 24 and Week 36.

There may be higher treatment burden for participants in this trial compared to their standard of care. Participants will attend regular visits during the study at a hospital or clinic. The effect of the treatment will be checked by medical assessments, blood tests, checking for side effects and completing questionnaires.

Detailed Description

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Conditions

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Episodic Migraine

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

PREVENTION

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Double-Blind Phase: Placebo

Participants received placebo for BOTOX intramuscular injections in the head/neck muscles on Day 1 and Week 12.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Intramuscular Injection

Double-Blind Phase: BOTOX 155 U

Participants received intramuscular injections of BOTOX 155 U in the head/neck muscles on Day 1 and Week 12.

Group Type EXPERIMENTAL

BOTOX

Intervention Type DRUG

Intramuscular Injection

Double-Blind Phase: BOTOX 195 U

Participants received intramuscular injections of BOTOX 195 U in the head/neck muscles on Day 1 and Week 12.

Group Type EXPERIMENTAL

BOTOX

Intervention Type DRUG

Intramuscular Injection

Open-Label Phase: BOTOX 195 U

Eligible participants received intramuscular injections of BOTOX 195 U in the head/neck muscles on Weeks 24 and 36.

Group Type EXPERIMENTAL

BOTOX

Intervention Type DRUG

Intramuscular Injection

Interventions

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BOTOX

Intramuscular Injection

Intervention Type DRUG

Placebo

Intramuscular Injection

Intervention Type DRUG

Other Intervention Names

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Botulinum Toxin Type A

Eligibility Criteria

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Inclusion Criteria

* History of migraine headache disorder meeting International Classification of Headache Disorders (ICHD)-3 diagnostic criteria for migraine with aura or migraine without aura for \>= 12 months.
* Onset of migraine before 50 years of age.
* History of 6 to 14 migraine days/month in each of the 3 months prior to Visit 1.
* Six to 14 migraine/probable migraine days during the 4-week screening/baseline phase.
* Less than 15 headache days/month in each of the 3 months prior to Visit 1 and during the 4-week screening/baseline phase.

Exclusion Criteria

* Current diagnosis of chronic migraine according to ICHD-3.
* History or current diagnosis of migraine with brainstem aura, retinal migraine, complications of migraine, chronic tension-type headache, trigeminal autonomic cephalalgias, hypnic headache, hemicrania continua, or new daily persistent headache.
* History of headache attributed to another disorder (e.g., cervical dystonia, craniotomy, head/neck trauma) with exception that medication overuse headache per ICHD-3 criteria is allowed.
* History of inadequate response to \> 4 prophylactic treatment for migraine, 2 of which have different mechanisms of action.
* Female who is pregnant, breastfeeding, or considering becoming pregnant during the study or within 90 days after the last dose of study drug.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AbbVie

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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ABBVIE INC.

Role: STUDY_DIRECTOR

AbbVie

Locations

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Neurology and Neurodiagnostics of Alabama /ID# 231918

Hoover, Alabama, United States

Site Status

Rehabilitation & Neurological Services /ID# 252441

Huntsville, Alabama, United States

Site Status

Alea Research /ID# 233329

Phoenix, Arizona, United States

Site Status

Duplicate_Barrow Neurological Institute /ID# 231799

Phoenix, Arizona, United States

Site Status

Clinical Endpoints /ID# 232625

Scottsdale, Arizona, United States

Site Status

Tucson Neuroscience Research /ID# 232288

Tucson, Arizona, United States

Site Status

Arkansas Clinical Research /ID# 231640

Little Rock, Arkansas, United States

Site Status

Woodland International Research Group /ID# 231492

Little Rock, Arkansas, United States

Site Status

Hope Clinical Research /ID# 232189

Canoga Park, California, United States

Site Status

Pharmacology Research Institute (PRI) - Encino (Wake) /ID# 231351

Encino, California, United States

Site Status

Duplicate_Neuro Pain Medical Center /ID# 231478

Fresno, California, United States

Site Status

Sun Valley Research Center /ID# 231350

Imperial, California, United States

Site Status

Wake Research - Pharmacology Research Institute (WR-PRI), LLC (Alamitos) /ID# 231908

Los Alamitos, California, United States

Site Status

Pharmacology Research Institute (PRI) - Newport Beach (Wake) /ID# 231337

Newport Beach, California, United States

Site Status

Colorado Springs Neurological Associates (CSNA) /ID# 230662

Colorado Springs, Colorado, United States

Site Status

Summit Headache and Neurologic Institute /ID# 231809

Englewood, Colorado, United States

Site Status

Advanced Neurosciences Research, LLC /ID# 230658

Fort Collins, Colorado, United States

Site Status

Georgetown University Hospital /ID# 232129

Washington D.C., District of Columbia, United States

Site Status

Neurology Offices of South Florida, PLLC /ID# 232281

Boca Raton, Florida, United States

Site Status

Nova Clinical Research, LLC /ID# 245256

Bradenton, Florida, United States

Site Status

Velocity Clinical Research - Hallandale Beach /ID# 232442

Hallandale, Florida, United States

Site Status

CNS Healthcare - Jacksonville /ID# 231345

Jacksonville, Florida, United States

Site Status

Brainstorm Research /ID# 243825

Miami, Florida, United States

Site Status

Sensible Healthcare /ID# 231340

Ocoee, Florida, United States

Site Status

Clinical Neuroscience Solutions, Inc /ID# 231362

Orlando, Florida, United States

Site Status

Pain Relief Centers /ID# 232415

Sun City Center, Florida, United States

Site Status

University of South Florida- Neuroscience Institute /ID# 231808

Tampa, Florida, United States

Site Status

Olympian Clinical Research - Tampa /ID# 239519

Tampa, Florida, United States

Site Status

Accel Research Sites - Tampa Clinical Research Unit /ID# 231670

Tampa, Florida, United States

Site Status

Premiere Research Institute - Palm Beach /ID# 230646

West Palm Beach, Florida, United States

Site Status

Conquest Research /ID# 232604

Winter Park, Florida, United States

Site Status

Accel Research Sites Neurostudies /ID# 230665

Decatur, Georgia, United States

Site Status

CenExcel iResearch LLC /ID# 231335

Decatur, Georgia, United States

Site Status

Clinical Research Institute /ID# 239517

Stockbridge, Georgia, United States

Site Status

Northwest Clinical Trials /ID# 230657

Boise, Idaho, United States

Site Status

Velocity Clinical Research - Boise /ID# 230660

Meridian, Idaho, United States

Site Status

Robbins Headache Clinic /ID# 230970

Riverwoods, Illinois, United States

Site Status

Josephson-Wallack-Munshower Neurology - Northeast /ID# 230654

Indianapolis, Indiana, United States

Site Status

Deaconess Clinic - Gateway Health Center /ID# 231329

Newburgh, Indiana, United States

Site Status

Duplicate_Accellacare - McFarland Clinic /ID# 231496

Ames, Iowa, United States

Site Status

Kansas Institute of Research /ID# 231862

Overland Park, Kansas, United States

Site Status

Ochsner Clinic Foundation /ID# 230645

Covington, Louisiana, United States

Site Status

Brigham and Women's Faulkner Hospital /ID# 231865

Boston, Massachusetts, United States

Site Status

Boston Clinical Trials /ID# 231367

Boston, Massachusetts, United States

Site Status

Michigan Headache & Neurological Institute (MHNI) /ID# 230659

Ann Arbor, Michigan, United States

Site Status

Minneapolis Clinic of Neurology - Burnsville /ID# 231780

Burnsville, Minnesota, United States

Site Status

StudyMetrix Research /ID# 230642

City of Saint Peters, Missouri, United States

Site Status

Clinvest Research LLC /ID# 252440

Springfield, Missouri, United States

Site Status

Excel Clinical Research /ID# 232188

Las Vegas, Nevada, United States

Site Status

Las Vegas Clinical Trials /ID# 232628

North Las Vegas, Nevada, United States

Site Status

Albuquerque Clinical Trials, Inc. /ID# 231101

Albuquerque, New Mexico, United States

Site Status

Duplicate_Dent Neurosciences Research Center, Inc. /ID# 252442

Amherst, New York, United States

Site Status

Fieve Clinical Research, Inc. /ID# 231365

New York, New York, United States

Site Status

Montefiore Headache Center /ID# 232130

The Bronx, New York, United States

Site Status

Upstate Clinical Research Associates /ID# 231343

Williamsville, New York, United States

Site Status

Headache Wellness Center /ID# 230819

Greensboro, North Carolina, United States

Site Status

M3 Wake Research Inc. /ID# 232285

Raleigh, North Carolina, United States

Site Status

Neurology - Triad /ID# 231733

Winston-Salem, North Carolina, United States

Site Status

Duplicate_Duplicate_University Of Cincinnati Medical Center /ID# 231739

Cincinnati, Ohio, United States

Site Status

IPS Research Company /ID# 231085

Oklahoma City, Oklahoma, United States

Site Status

Lynn Institute of Oklahoma City /ID# 231349

Oklahoma City, Oklahoma, United States

Site Status

Cutting Edge Research Group /ID# 231095

Oklahoma City, Oklahoma, United States

Site Status

Sooner Clinical Research /ID# 231096

Oklahoma City, Oklahoma, United States

Site Status

Abington Neurological Associates - Abington /ID# 231798

Abington, Pennsylvania, United States

Site Status

Lehigh Center for Clinical Research /ID# 231355

Allentown, Pennsylvania, United States

Site Status

Suburban Research Associates - Media /ID# 231354

Media, Pennsylvania, United States

Site Status

Jefferson Hospital for Neuroscience /ID# 230664

Philadelphia, Pennsylvania, United States

Site Status

Duplicate_Frontier Clinical Research /ID# 232623

Smithfield, Pennsylvania, United States

Site Status

Clinical Trials of SC /ID# 231369

Charleston, South Carolina, United States

Site Status

Coastal Carolina Research Center - North Charleston /ID# 231353

North Charleston, South Carolina, United States

Site Status

Clinical Neuroscience Solutions - Memphis /ID# 231328

Memphis, Tennessee, United States

Site Status

Nashville Neuroscience Group /ID# 231642

Nashville, Tennessee, United States

Site Status

Austin Clinical Trial Partners /ID# 231092

Austin, Texas, United States

Site Status

Texas Neurology /ID# 230661

Dallas, Texas, United States

Site Status

NeuroCare Plus /ID# 252499

Houston, Texas, United States

Site Status

Charlottesville Medical Research /ID# 231368

Charlottesville, Virginia, United States

Site Status

Integrated Neurology Services - Falls Church /ID# 244776

Falls Church, Virginia, United States

Site Status

Tidewater Integr Med Research /ID# 231359

Virginia Beach, Virginia, United States

Site Status

Sentara Neurology Specialists - Virginia Beach /ID# 231341

Virginia Beach, Virginia, United States

Site Status

Northwest Clinical Research Center /ID# 231336

Bellevue, Washington, United States

Site Status

Puget Sound Neurology /ID# 230640

Tacoma, Washington, United States

Site Status

Frontier Clinical Research - Kingwood /ID# 234127

Kingwood, West Virginia, United States

Site Status

CHAMP Clinic /ID# 231635

Calgary, Alberta, Canada

Site Status

Vancouver Island Health Authority /ID# 231992

Victoria, British Columbia, Canada

Site Status

Maritime Neurology /ID# 232048

Halifax, Nova Scotia, Canada

Site Status

Toronto Memory Program /ID# 240006

Toronto, Ontario, Canada

Site Status

Clinique Neuro Levis /ID# 232049

Lévis, Quebec, Canada

Site Status

Fakultní Nemocnice U Sv. Anny V Brně /ID# 232213

Brno, Brno-mesto, Czechia

Site Status

Fakultni Nemocnice Ostrava /ID# 232211

Ostrava, Ostrava-mesto, Czechia

Site Status

Nemocnice Jihlava, prispevkova organizace /ID# 232164

Jihlava, , Czechia

Site Status

Clintrial s.r.o. /ID# 232208

Prague, , Czechia

Site Status

DADO MEDICAL s.r.o. /ID# 232157

Prague, , Czechia

Site Status

Axon Clinical, s.r.o. /ID# 232212

Prague, , Czechia

Site Status

Fakultni Thomayerova nemocnice /ID# 232214

Prague, , Czechia

Site Status

Duplicate_Neurologie Klinikum Großhadern /ID# 232479

Munich, Bavaria, Germany

Site Status

Duplicate_Kopfschmerzzentrum Frankfurt /ID# 234066

Frankfurt am Main, Hesse, Germany

Site Status

Universitaetsmedizin Rostock /ID# 232471

Rostock, Mecklenburg-Vorpommern, Germany

Site Status

Universitaetsklinikum Carl Gustav Carus Dresden /ID# 239283

Dresden, Saxony, Germany

Site Status

Schmerzklinik Kiel /ID# 232480

Kiel, Schleswig-Holstein, Germany

Site Status

Zentrum für Neurologie, Neurochirurgie und Psychiatrie /ID# 232472

Berlin, , Germany

Site Status

Praxis Dr. Gendolla /ID# 232474

Essen, , Germany

Site Status

Universitaetsklinikum Essen /ID# 232478

Essen, , Germany

Site Status

Universitaetsklinikum Halle (Saale) /ID# 241506

Halle, , Germany

Site Status

Vitos Orthopaedische Klinik Kassel gemeinnuetzige GmbH /ID# 232475

Kassel, , Germany

Site Status

Maccabi Healthcare Services /ID# 238605

Kfar Saba, Central District, Israel

Site Status

Hillel Yaffe Medical Center /ID# 232122

Hadera, Haifa District, Israel

Site Status

Shaare Zedek Medical Center /ID# 239485

Jerusalem, Jerusalem, Israel

Site Status

The Chaim Sheba Medical Center /ID# 232119

Ramat Gan, Tel Aviv, Israel

Site Status

Tel Aviv Sourasky Medical Center /ID# 232598

Tel Aviv, Tel Aviv, Israel

Site Status

Rambam Health Care Campus /ID# 238732

Haifa, , Israel

Site Status

Solumed Centrum Medyczne /ID# 238446

Poznan, Greater Poland Voivodeship, Poland

Site Status

Specjalistyczne Gabinety Sp. z o.o. /ID# 233526

Krakow, Lesser Poland Voivodeship, Poland

Site Status

Linden Sp. z o.o. sp.k. /ID# 245685

Krakow, Lesser Poland Voivodeship, Poland

Site Status

Instytut Zdrowia Dr Boczarska Jedynak /ID# 251857

Oświęcim, Lesser Poland Voivodeship, Poland

Site Status

Indywidualna Praktyka Lekarska dr hab. med. Anna Szczepanska-Szerej /ID# 232355

Lublin, Lublin Voivodeship, Poland

Site Status

Warszawska Klinika Sp. z o.o. /ID# 240612

Warsaw, Masovian Voivodeship, Poland

Site Status

Silmedic Sp. z o.o. /ID# 232358

Katowice, Silesian Voivodeship, Poland

Site Status

MIGRE Polskie Centrum Leczenia Migreny Anna Gryglas-Dworak /ID# 241887

Wroclaw, , Poland

Site Status

Clinica Universidad de Navarra - Pamplona /ID# 232270

Pamplona, Navarre, Spain

Site Status

Hospital Universitario Central de Asturias /ID# 232428

Oviedo, Principality of Asturias, Spain

Site Status

Hospital Universitario Vall d'Hebron /ID# 232268

Barcelona, , Spain

Site Status

CLINICA UNIVERSIDAD DE NAVARRA-Madrid /ID# 233320

Madrid, , Spain

Site Status

Hospital Universitario La Paz /ID# 232495

Madrid, , Spain

Site Status

Hospital Clinico Universitario de Valladolid /ID# 232272

Valladolid, , Spain

Site Status

Skaneuro Privatmottagning /ID# 232175

Lund, Skåne County, Sweden

Site Status

Neurology Clinic /ID# 234067

Stockholm, Stockholm County, Sweden

Site Status

Optimuskliniken /ID# 232174

Upplands Vasby, , Sweden

Site Status

Linkoping University Hospital /ID# 234040

Linköping, Östergötland County, Sweden

Site Status

Hull University Teaching Hospitals NHS Trust /ID# 242763

Hull, East Riding Of Yorkshire, United Kingdom

Site Status

Duplicate_Queen Elizabeth University Hospital /ID# 244870

Glasgow, Glasgow City, United Kingdom

Site Status

NHS Highland /ID# 242855

Inverness, , United Kingdom

Site Status

Walton Centre /ID# 242857

Liverpool, , United Kingdom

Site Status

St Pancras Clinical Research /ID# 242764

London, , United Kingdom

Site Status

Countries

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United States Canada Czechia Germany Israel Poland Spain Sweden United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2021-001979-16

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

M21-307

Identifier Type: -

Identifier Source: org_study_id

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