A Dose-Escalation and Expansion Study of BGB-16673 in Participants With B-Cell Malignancies

NCT ID: NCT05006716

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

614 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-09-13

Study Completion Date

2029-11-30

Brief Summary

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Study consists of two main parts to explore BGB-16673 recommended dosing, a Phase 1 monotherapy dose finding comprised of monotherapy dose escalation and monotherapy safety expansion of selected doses, and a Phase 2 (expansion cohorts)

Detailed Description

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Conditions

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B-cell Malignancy Marginal Zone Lymphoma Follicular Lymphoma Non-Hodgkin Lymphoma Waldenström Macroglobulinemia Chronic Lymphocytic Leukemia Small Lymphocytic Lymphoma Mantle Cell Lymphoma Diffuse Large B Cell Lymphoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Part 1a (Monotherapy Dose Escalation)

Dose escalation in specific subtypes of non-Hodgkin lymphoma (NHL), including relapsed or refractory (R/R) marginal zone lymphoma (MZL), R/R follicular lymphoma (FL) Grades 1, 2, and 3a, R/R mantle cell lymphoma (MCL), R/R chronic lymphocytic leukemia/small lymphocytic lymphoma (CLL/SLL), R/R diffuse large B-cell lymphoma (DLBCL), R/R Richter's transformation (RT), and R/R Waldenström macroglobulinemia (WM), to evaluate the safety and tolerability of BGB-16673.

Group Type EXPERIMENTAL

BGB-16673

Intervention Type DRUG

Orally administered

Part 1b (Monotherapy Safety Expansion)

Participants with R/R MZL, MCL, CLL/SLL, and WM will be enrolled at selected doses to help determine the recommended dose(s) for expansion (RDFE(s)) for BGB-16673.

Group Type EXPERIMENTAL

BGB-16673

Intervention Type DRUG

Orally administered

Part 1c (Additional Monotherapy Safety Expansion)

Additional safety data will be collected from participants with R/R MZL, WM, RT, DLBCL, or FL to confirm the RDFE(s) of BGB-16673 for those with non-CLL/SLL/MCL histologies.

Group Type EXPERIMENTAL

BGB-16673

Intervention Type DRUG

Orally administered

Part 1d (Additional Monotherapy Safety Expansion in R/R CLL/SLL)

Participants with R/R CLL/SLL will be enrolled at selected RDFE(s) to generate additional safety and efficacy data for BGB-16673.

Group Type EXPERIMENTAL

BGB-16673

Intervention Type DRUG

Orally administered

Part 1e (Japan-only Cohort)

Japanese participants with R/R MZL, FL, MCL, CLL/SLL, and WM will be enrolled at selected RDFE(s) to assess the safety and tolerability of BGB-16673.

Group Type EXPERIMENTAL

BGB-16673

Intervention Type DRUG

Orally administered

Part 1f (Additional Monotherapy Safety Expansion in BTKi Naive B-Cell Malignancies)

Participants with CLL/SLL, MCL, WM, MZL, or Richter's transformation to DLBCL who have not received a prior BTKi (either covalent or noncovalent) will be enrolled at selected dose levels.

Group Type EXPERIMENTAL

BGB-16673

Intervention Type DRUG

Orally administered

Phase 2 (Monotherapy Expansion)

Cohorts of participants with R/R CLL/SLL, R/R MCL, R/R WM, R/R MZL, R/R FL, R/R RT, and R/R DLBCL will be enrolled to receive the RDFE(s) identified in Phase 1 to further evaluate the safety and efficacy of BGB-16673.

Group Type EXPERIMENTAL

BGB-16673

Intervention Type DRUG

Orally administered

Interventions

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BGB-16673

Orally administered

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Confirmed diagnosis (per World Health Organization (WHO) guidelines, unless otherwise noted) of one of the following: Marginal Zone Lymphoma (MZL), R/R follicular lymphoma (FL), mantle cell lymphoma (MCL), chronic lymphocytic leukemia and small lymphocytic lymphoma (CLL/SLL), Waldenström macroglobulinemia (WM), R/R diffuse large B-cell lymphoma (DLBCL), or Richter's transformation to DLBCL.
2. Participants who have previously received a covalently-binding Bruton´s tyrosine kinase (BTK) inhibitor (BTKi) in any line of therapy must have received treatment with the BTK inhibitor for ≥ 8 weeks (unless reason for discontinuation is intolerance).
3. For dose-finding and dose-expansion, participants who had previously received a covalently-binding BTK inhibitor as monotherapy or in combination with other anticancer agents are eligible for the study if they meet any of the following criteria: discontinued the previous BTK inhibitor due to disease progression, experienced disease progression after completing treatment with a BTK inhibitor or discontinued the BTK inhibitor due to toxicity or intolerance.
4. Measurable disease by radiographic assessment or serum IgM level (WM only)
5. Eastern Cooperative Oncology Group (ECOG) Performance Status of 0 to 2
6. Participants enrolling in the dose finding phase of the study may be previously treated with a BTKi or may be naïve to BTKi therapy depending on the diagnosis and country of enrollment; participants with MCL enrolling in the expansion cohorts (Phase 2) must have been treated with a BTKi in a prior line of therapy; CLL/SLL participants, in addition to being treated with a BTKi in a prior line of therapy, must also have received a Bcl-2 inhibitor in a prior line of therapy as well (Phase 2).

Exclusion Criteria

1. Prior malignancy (other than the disease under study) within the past 2 years, except in situ malignancies that have been curatively resected, localized breast cancer treated with curative intent with no evidence of breast active disease for more than 3 years and receiving adjuvant hormonal therapy, localized Gleason score ≤ 6 prostate cancer undergoing observation or treatment with androgen depravation, or any other cancer treated with curative intent, not on adjuvant treatment, and in the opinion of the investigator is unlikely to recur.
2. Requires ongoing systemic treatment for any other malignancy
3. Requires ongoing systemic (defined as ≥ 10 mg/day of prednisone or equivalent) corticosteroid treatment.
4. Current or history of central nervous system involvement including the brain, spinal cord, leptomeninges, and cerebrospinal fluid (as documented by imaging, cytology, or biopsy) by B-cell malignancy, regardless of whether participants had received treatment for central nervous system disease
5. Known active plasma cell neoplasm, prolymphocytic leukemia, T-cell lymphoma, Burkitt lymphoma, acquired immunodeficiency syndrome (AIDS)-related B-cell lymphoma, Castleman disease, post-transplant lymphoproliferative disorders, hairy cell leukemia, germinal center B-cell (GCB), DLBCL, EBV+ DLBCL NOS, primary DLBCL of the central nervous system (CNS), primary cutaneous DLBCL - leg type, DLBCL associated with chronic inflammation, primary mediastinal (thymic) large B-cell lymphoma, intravascular large B-cell lymphoma, ALK+ large B-cell lymphoma, primary effusion lymphoma, high-grade B-cell lymphoma with MYC and BCL2 and/or BCL6 rearrangements, high-grade B-cell lymphoma - NOS, B-cell lymphoma unclassifiable with features intermediate between DLBCL and classical Hodgkin lymphoma, or history of or currently suspected transformation of an indolent lymphoma to an aggressive histology (except for participants with Richter Transformation to DLBCL are eligible for Part 1a, 1c, or Phase 2 and participants with history of follicular lymphoma transforming to non-GCB DLBCL who are eligible for Part 1a, 1c, or Phase 2).
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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BeOne Medicines

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

BeOne Medicines

Locations

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University of Alabama At Birmingham Hospital

Birmingham, Alabama, United States

Site Status RECRUITING

Mayo Clinic Phoenix

Phoenix, Arizona, United States

Site Status COMPLETED

Honor Health Research Institute

Scottsdale, Arizona, United States

Site Status RECRUITING

University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status RECRUITING

University of California San Diego (Ucsd) Moores Cancer Center

La Jolla, California, United States

Site Status RECRUITING

Stanford Medicine

Palo Alto, California, United States

Site Status RECRUITING

UCLA Santa Monica Cancer Care

Santa Monica, California, United States

Site Status RECRUITING

Uchealth North

Fort Collins, Colorado, United States

Site Status RECRUITING

Mayo Clinic Jacksonville

Jacksonville, Florida, United States

Site Status RECRUITING

Mount Sinai Comprehensive Cancer Center

Miami Beach, Florida, United States

Site Status RECRUITING

Tampa General Hospital Cancer Institute

Tampa, Florida, United States

Site Status RECRUITING

Augusta University

Augusta, Georgia, United States

Site Status RECRUITING

Southeastern Regional Medical Center

Newnan, Georgia, United States

Site Status RECRUITING

Midwestern Regional Medical Center

Zion, Illinois, United States

Site Status RECRUITING

University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Site Status RECRUITING

Norton Cancer Institute Pavilion

Louisville, Kentucky, United States

Site Status COMPLETED

Mary Bird Perkins Cancer Center

Baton Rouge, Louisiana, United States

Site Status RECRUITING

American Oncology Partners of Maryland Pa

Bethesda, Maryland, United States

Site Status RECRUITING

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status RECRUITING

Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status RECRUITING

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status RECRUITING

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, United States

Site Status RECRUITING

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States

Site Status RECRUITING

Columbia University Medical Center

New York, New York, United States

Site Status RECRUITING

Weill Cornell Medical College Newyork Presbyterian Hospital

New York, New York, United States

Site Status RECRUITING

Memorial Sloan Kettering Cancer Center Mskcc

New York, New York, United States

Site Status RECRUITING

Tennesse Oncology Chattanooga Downtown

Chattanooga, Tennessee, United States

Site Status RECRUITING

Tennessee Oncology, Pllc Nashville

Nashville, Tennessee, United States

Site Status RECRUITING

Md Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Virginia Commonwealth University Massey Cancer Center

Richmond, Virginia, United States

Site Status RECRUITING

Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status RECRUITING

Concord Repatriation General Hospital

Concord, New South Wales, Australia

Site Status RECRUITING

Calvary Mater Newcastle

Waratah, New South Wales, Australia

Site Status RECRUITING

Princess Alexandra Hospital

Woolloongabba, Queensland, Australia

Site Status RECRUITING

St Vincents Hospital Melbourne

Fitzroy, Victoria, Australia

Site Status RECRUITING

Austin Health

Heidelberg, Victoria, Australia

Site Status RECRUITING

Peter Maccallum Cancer Centre

Melbourne, Victoria, Australia

Site Status RECRUITING

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status RECRUITING

Linear Clinical Research

Nedlands, Western Australia, Australia

Site Status RECRUITING

Perth Blood Institute

West Perth, Western Australia, Australia

Site Status RECRUITING

Hospital Sirio Libanes Brasilia

Brasília, , Brazil

Site Status RECRUITING

Hospital Erasto Gaertner

Curitiba, , Brazil

Site Status RECRUITING

Centro Gaucho Integrado de Oncologia Hospital Mae de Deus

Porto Alegre, , Brazil

Site Status RECRUITING

Real E Benemerita Associacao Portuguesa de Sao Paulo

São Paulo, , Brazil

Site Status RECRUITING

Hospital Alemao Oswaldo Cruz

São Paulo, , Brazil

Site Status RECRUITING

Hospital Nove de Julho Dasa

São Paulo, , Brazil

Site Status RECRUITING

Instituto Dor de Pesquisa E Ensino Sao Paulo

São Paulo, , Brazil

Site Status RECRUITING

Sociedade Beneficente Israelita Brasileira Hospital Albert Einstein

São Paulo, , Brazil

Site Status RECRUITING

Hospital Santa Rita de Cassia Afecc

Vitória, , Brazil

Site Status RECRUITING

Arthur Je Child Comprehensive Cancer Centre

Calgary, Alberta, Canada

Site Status RECRUITING

Cross Cancer Institute

Edmonton, Alberta, Canada

Site Status RECRUITING

British Columbia Cancer Agency the Vancouver Centre

Vancouver, British Columbia, Canada

Site Status RECRUITING

Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Site Status RECRUITING

Chu de Quebec Universite Laval, Hopital de Lenfant Jesus, Centre Integre de Cancerologie (Cic)

Québec, , Canada

Site Status RECRUITING

Centre de Lutte Contre Le Cancer Institut Bergonie

Bordeaux, , France

Site Status RECRUITING

Hopital Estaing

Clermontferrand, , France

Site Status RECRUITING

Chu Henri Mondor

Créteil, , France

Site Status RECRUITING

Hopital Claude Huriez Chu Lille

Lille, , France

Site Status RECRUITING

Centre Leon Berard

Lyon, , France

Site Status RECRUITING

Institut Paoli Calmettes

Marseille, , France

Site Status RECRUITING

Chu Montpellier Hopital Saint Eloi

Montpellier, , France

Site Status RECRUITING

Hopital de La Pitie Salpetriere

Paris, , France

Site Status RECRUITING

Centre Henri Becquerel

Rouen, , France

Site Status RECRUITING

Arensia Exploratory Medicine Llc

Tbilisi, , Georgia

Site Status RECRUITING

Uniklinik Koeln (Aoer)

Cologne, , Germany

Site Status RECRUITING

Universitatsklinikum Carl Gustav Carus An Der Technischen Universitat Dresden

Dresden, , Germany

Site Status RECRUITING

Universitares Krebszentrum Leipzig

Leipzig, , Germany

Site Status RECRUITING

Universitaetsklinikum Schleswig Holstein Campus Luebeck

Lübeck, , Germany

Site Status RECRUITING

Klinikum Johannes Gutenberg Universitaet Mainz

Mainz, , Germany

Site Status RECRUITING

Klinikum Grosshadern Ludwig Maximilians Universitat Munchen

München, , Germany

Site Status RECRUITING

Universitaetsklinikum Ulm

Ulm, , Germany

Site Status RECRUITING

Policlinico Sorsola Malpighi, Aou Di Bologna

Bologna, , Italy

Site Status RECRUITING

Ospedale San Raffaele

Milan, , Italy

Site Status RECRUITING

Istituto Europeo Di Oncologia

Milan, , Italy

Site Status RECRUITING

Niguarda Cancer Center Division of Hematology

Milan, , Italy

Site Status RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli

Roma, , Italy

Site Status RECRUITING

Centroricerche Cliniche Di Verona Srl

Verona, , Italy

Site Status RECRUITING

Aichi Cancer Center Hospital Clinical Oncology

Nagoya, Aichi-ken, Japan

Site Status RECRUITING

Chiba Cancer Center

Chiba, Chiba, Japan

Site Status RECRUITING

Cancer Institute Hospital of Jfcr

Kotoku, Tokyo, Japan

Site Status RECRUITING

Yokohama Municipal Citizens Hospital

Yokohama, , Japan

Site Status RECRUITING

The Institute of Oncology, Arensia Exploratory Medicine

Chisinau, , Moldova

Site Status RECRUITING

Inje University Busan Paik Hospital

BusanjinGu, Busan Gwang'yeogsi, South Korea

Site Status RECRUITING

Pusan National University Hospital

Seogu, Busan Gwang'yeogsi, South Korea

Site Status RECRUITING

Samsung Medical Center

GangnamGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

The Catholic University of Korea, Seoul St Marys Hospital

SeochoGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Severance Hospital Yonsei University Health System

SeodaemunGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Asan Medical Center

SongpaGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Hospital Universitario Vall Dhebron

Barcelona, , Spain

Site Status RECRUITING

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status RECRUITING

Md Anderson Cancer Center Madrid Spain

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario Puerta de Hierro Majadahonda

Majadahonda, , Spain

Site Status RECRUITING

Hospital Clinico Universitario de Valencia

Valencia, , Spain

Site Status RECRUITING

Sahlgrenska University Hospital Hematology

Gothenburg, , Sweden

Site Status RECRUITING

Karolinska Universitetssjukhuset Solna

Stockholm, , Sweden

Site Status RECRUITING

Dokuz Eylul University

Balçova, , Turkey (Türkiye)

Site Status RECRUITING

Erciyes University

Kayseri, , Turkey (Türkiye)

Site Status RECRUITING

Sakarya Training and Research Hospital

Sakarya, , Turkey (Türkiye)

Site Status RECRUITING

Ondokuz Mayis University

Samsun, , Turkey (Türkiye)

Site Status RECRUITING

Edinburgh Cancer Centre

Edinburgh, , United Kingdom

Site Status RECRUITING

Churchill Hospital Oxford University Hospital Nhs Trust

Headington, , United Kingdom

Site Status RECRUITING

St Jamess University Hospital

Leeds, , United Kingdom

Site Status RECRUITING

Freeman Hospital

Newcastle upon Tyne, , United Kingdom

Site Status RECRUITING

Nottingham University Hospitals Nhs Trust

Nottingham, , United Kingdom

Site Status RECRUITING

Derriford Hospital

Plymouth, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Brazil Canada France Georgia Germany Italy Japan Moldova South Korea Spain Sweden Turkey (Türkiye) United Kingdom

Central Contacts

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BeOne Medicines

Role: CONTACT

Phone: 1.877.828.5568

Email: [email protected]

Study Director, MD

Role: CONTACT

Other Identifiers

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2022-502157-33-00

Identifier Type: OTHER

Identifier Source: secondary_id

BGB-16673-101

Identifier Type: -

Identifier Source: org_study_id