Trial Outcomes & Findings for A Study to Evaluate Enfortumab Vedotin (ASG-22CE) in Chinese Participants With Locally Advanced or Metastatic Urothelial Cancer Who Previously Received Platinum-containing Chemotherapy and Programmed Cell Death Protein-1 ( PD 1) / (Programmed Death Ligand-1 (PD-L1) Inhibitor Therapy (NCT NCT04995419)

NCT ID: NCT04995419

Last Updated: 2025-10-07

Results Overview

ORR was defined as the percentage of participants with best overall response (BOR) as complete response (CR) or partial response (PR) based on the RECIST v1.1. CR was defined as disappearance of all target and nontarget lesions. Any pathological lymph nodes (whether target or nontarget) must have reduction in short axis to \< 10 mm from baseline measurement. PR was defined as at least a 30% decrease in the sum of diameters (longest for nonnodal lesions, short axis for nodal lesions) of target lesions taking as reference to the baseline sum of diameters.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

40 participants

Primary outcome timeframe

From first dose up to progressive disease or death (maximum duration: 9.33 months)

Results posted on

2025-10-07

Participant Flow

Adult Chinese participants with locally advanced or metastatic urothelial cancer (mUC) who had received a platinum-containing chemotherapy and programmed cell death protein-1 (PD-1) or programmed death-ligand 1 (PD-L1) inhibitors.

Participants who met inclusion criteria and none of the exclusion criteria were enrolled.

Participant milestones

Participant milestones
Measure
Enfortumab Vedotin 1.25 mg/kg
Participants received 1.25 milligrams per kilogram (mg/kg) of body weight enfortumab vedotin by intravenous (IV) infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Overall Study
STARTED
40
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
40

Reasons for withdrawal

Reasons for withdrawal
Measure
Enfortumab Vedotin 1.25 mg/kg
Participants received 1.25 milligrams per kilogram (mg/kg) of body weight enfortumab vedotin by intravenous (IV) infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Overall Study
Withdrawal by Subject
3
Overall Study
Progressive Disease
19
Overall Study
Adverse Event
2
Overall Study
Ongoing
16

Baseline Characteristics

A Study to Evaluate Enfortumab Vedotin (ASG-22CE) in Chinese Participants With Locally Advanced or Metastatic Urothelial Cancer Who Previously Received Platinum-containing Chemotherapy and Programmed Cell Death Protein-1 ( PD 1) / (Programmed Death Ligand-1 (PD-L1) Inhibitor Therapy

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Age, Continuous
60.3 years
STANDARD_DEVIATION 8.3 • n=5 Participants
Sex: Female, Male
Female
9 Participants
n=5 Participants
Sex: Female, Male
Male
31 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
40 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
40 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
0 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: From first dose up to progressive disease or death (maximum duration: 9.33 months)

Population: FAS population

ORR was defined as the percentage of participants with best overall response (BOR) as complete response (CR) or partial response (PR) based on the RECIST v1.1. CR was defined as disappearance of all target and nontarget lesions. Any pathological lymph nodes (whether target or nontarget) must have reduction in short axis to \< 10 mm from baseline measurement. PR was defined as at least a 30% decrease in the sum of diameters (longest for nonnodal lesions, short axis for nodal lesions) of target lesions taking as reference to the baseline sum of diameters.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Objective Response Rate (ORR) as Per Response Evaluation Criteria in Solid Tumors V1.1 (RECIST V1.1)
37.5 percentage of participants
Interval 22.7 to 54.2

PRIMARY outcome

Timeframe: Cycle 1 Day 1: pre-dose, end of infusion (EOI), 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: Pharmacokinetic Analysis Set (PKAS) included all participants in the PK cohort who had received at least 3 of 4 doses up through Cycle 2 Day 1, and had at least 5 blood samples collected and assayed for measurement of ADC, TAb or unconjugated MMAE serum/plasma concentrations to determine at least 1 PK parameter.

Cmax was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=13 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Pharmacokinetics (PK) of Antibody-Drug Conjugate (ADC), Total Antibody (TAb), in Serum: Maximum Concentration (Cmax) at Cycle 1 Day 1
ADC
28.1 micrograms per milliliter (ug/mL)
Standard Deviation 4.52
Pharmacokinetics (PK) of Antibody-Drug Conjugate (ADC), Total Antibody (TAb), in Serum: Maximum Concentration (Cmax) at Cycle 1 Day 1
TAb
31.7 micrograms per milliliter (ug/mL)
Standard Deviation 5.73

PRIMARY outcome

Timeframe: Cycle 1 Day 1: pre-dose, end of infusion (EOI), 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population.

Cmax was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=13 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of Monomethyl Auristatin E (MMAE) in Serum: Maximum Concentration (Cmax) at Cycle 1 Day 1
3.33 nanograms per milliliter (ng/mL)
Standard Deviation 1.74

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

Cmax was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=10 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb in Serum: Maximum Concentration (Cmax) at Cycle 1 Day 15
ADC
27.6 ug/mL
Standard Deviation 4.01
PK of ADC, TAb in Serum: Maximum Concentration (Cmax) at Cycle 1 Day 15
TAb
34.4 ug/mL
Standard Deviation 4.64

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

Cmax was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=10 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of MMAE in Serum: Maximum Concentration (Cmax) at Cycle 1 Day 15
4.49 ng/mL
Standard Deviation 3.58

PRIMARY outcome

Timeframe: Cycle 1 Day 1: pre-dose

Population: PKAS population.

As per planned analysis, if more than 50% of PK concentrations were below the limit of quantification (i.e 0) at a given time point, standard deviation was not reported.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=13 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC , TAb in Serum: Trough Concentration (Ctrough) at Cycle 1 Day 1
ADC
0 ug/mL
Standard Deviation NA
Standard Deviation was not reported in summary statistics because more than 50% of ADC concentrations at pre-dose were 0.
PK of ADC , TAb in Serum: Trough Concentration (Ctrough) at Cycle 1 Day 1
TAb
0 ug/mL
Standard Deviation NA
Standard Deviation was not reported in summary statistics because more than 50% of TAb concentrations at pre-dose were 0.

PRIMARY outcome

Timeframe: Cycle 1 Day 1: pre-dose

Population: PKAS population.

As per planned analysis, if more than 50% of PK concentrations were below the limit of quantification (i.e 0) at a given time point, standard deviation was not reported.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=13 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of MMAE in Serum: Trough Concentration (Ctrough) at Cycle 1 Day 1
0 ng/mL
Standard Deviation NA
Standard Deviation was not reported in summary statistics because more than 50% of MMAE concentrations at pre-dose were 0.

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose

Population: PKAS population with available data were analyzed.

Ctrough was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=12 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb in Serum: Trough Concentration (Ctrough) at Cycle 1 Day 15
ADC
1020 ug/mL
Standard Deviation 410
PK of ADC, TAb in Serum: Trough Concentration (Ctrough) at Cycle 1 Day 15
TAb
4620 ug/mL
Standard Deviation 1590

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose

Population: PKAS population with available data were analyzed.

Ctrough was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=12 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of MMAE in Serum: Trough Concentration (Ctrough) at Cycle 1 Day 15
1880 picograms per milliliter (pg/mL)
Standard Deviation 1680

PRIMARY outcome

Timeframe: Cycle 1 Day 1: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population.

Tmax was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=13 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb, MMAE in Serum: Time to Maximum Concentration (Tmax) at Cycle 1 Day 1
ADC
0.0340 days
Interval 0.0278 to 0.0917
PK of ADC, TAb, MMAE in Serum: Time to Maximum Concentration (Tmax) at Cycle 1 Day 1
TAb
0.0340 days
Interval 0.0243 to 1.89
PK of ADC, TAb, MMAE in Serum: Time to Maximum Concentration (Tmax) at Cycle 1 Day 1
MMAE
2.00 days
Interval 1.87 to 2.93

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

Tmax was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=10 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb, MMAE in Serum: Time to Maximum Concentration (Tmax) at Cycle 1 Day 15
ADC
0.0337 days
Interval 0.0257 to 0.0805
PK of ADC, TAb, MMAE in Serum: Time to Maximum Concentration (Tmax) at Cycle 1 Day 15
TAb
0.0337 days
Interval 0.0278 to 0.0854
PK of ADC, TAb, MMAE in Serum: Time to Maximum Concentration (Tmax) at Cycle 1 Day 15
MMAE
1.93 days
Interval 0.858 to 2.92

PRIMARY outcome

Timeframe: Cycle 1 Day 1: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: Per protocol, data for AUC0-28d was planned to be calculated using non-compartment analysis (NCA) only if data permits, therefore AUC 0-28d was removed from the planned analysis in SAP.

AUC0-28d was derived from the PK blood samples collected.

Outcome measures

Outcome data not reported

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: Per protocol, data for AUC0-28d was planned to be calculated using non-compartment analysis (NCA) only if data permits, therefore AUC 0-28d was removed from the planned analysis in SAP.

AUC0-28d was derived from the PK blood samples collected.

Outcome measures

Outcome data not reported

PRIMARY outcome

Timeframe: Cycle 1 Day 1 : pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

AUC0-7d was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=12 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb in Serum: Area Under Concentration-time Curve From 0 to Day 7 (AUC0-7d) at Cycle 1 Day 1
ADC
32.4 day*ug/mL
Standard Deviation 6.24
PK of ADC, TAb in Serum: Area Under Concentration-time Curve From 0 to Day 7 (AUC0-7d) at Cycle 1 Day 1
TAb
77.4 day*ug/mL
Standard Deviation 17.3

PRIMARY outcome

Timeframe: Cycle 1 Day 1 : pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

AUC0-7d was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=12 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of MMAE in Serum: Area Under Concentration-time Curve From 0 to Day 7 (AUC0-7d) at Cycle 1 Day 1
16.9 day*ng/mL
Standard Deviation 9.21

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

AUC0-7d was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=10 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb in Serum: Area Under Concentration-time Curve From 0 to Day 7 (AUC0-7d) at Cycle 1 Day 15
ADC
36.5 day*ug/mL
Standard Deviation 7.93
PK of ADC, TAb in Serum: Area Under Concentration-time Curve From 0 to Day 7 (AUC0-7d) at Cycle 1 Day 15
TAb
94.7 day*ug/mL
Standard Deviation 15.7

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

AUC0-7d was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=10 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of MMAE in Serum: Area Under Concentration-time Curve From 0 to Day 7 (AUC0-7d) at Cycle 1 Day 15
23.3 day*ng/mL
Standard Deviation 16.4

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

Accumulation ratio is the ratio of Cmax after the dosing interval (Cycle 1 Day 15) divided by Cmax after the first dosing interval (Cycle 1 Day 1).

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=10 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb, MMAE in Plasma: Accumulation Ratio of Cmax (RacCmax)
ADC
1.03 ratio
Standard Deviation 0.150
PK of ADC, TAb, MMAE in Plasma: Accumulation Ratio of Cmax (RacCmax)
TAb
1.13 ratio
Standard Deviation 0.137
PK of ADC, TAb, MMAE in Plasma: Accumulation Ratio of Cmax (RacCmax)
MMAE
1.28 ratio
Standard Deviation 0.499

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

RacAUC0-7d was calculated using AUC0-7d and derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=10 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb, MMAE in Serum: Accumulation Ratio of AUC0-7d ( RacAUC0-7d)
ADC
1.20 ratio
Standard Deviation 0.228
PK of ADC, TAb, MMAE in Serum: Accumulation Ratio of AUC0-7d ( RacAUC0-7d)
TAb
1.29 ratio
Standard Deviation 0.208
PK of ADC, TAb, MMAE in Serum: Accumulation Ratio of AUC0-7d ( RacAUC0-7d)
MMAE
1.32 ratio
Standard Deviation 0.486

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

t1/2 was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=10 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb, MMAE in Serum: Terminal Elimination Half-life (t1/2)
ADC
2.81 days
Interval 2.28 to 3.7
PK of ADC, TAb, MMAE in Serum: Terminal Elimination Half-life (t1/2)
TAb
3.82 days
Interval 3.11 to 5.49
PK of ADC, TAb, MMAE in Serum: Terminal Elimination Half-life (t1/2)
MMAE
3.12 days
Interval 2.83 to 3.82

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

CL was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=10 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb, MMAE in Serum: Systemic Clearance (CL)
ADC
0.104 Liters/hour (L/hr)
Standard Deviation 0.0239
PK of ADC, TAb, MMAE in Serum: Systemic Clearance (CL)
TAb
0.0396 Liters/hour (L/hr)
Standard Deviation 0.00847
PK of ADC, TAb, MMAE in Serum: Systemic Clearance (CL)
MMAE
196 Liters/hour (L/hr)
Standard Deviation 76.2

PRIMARY outcome

Timeframe: Cycle 1 Day 15: pre-dose, EOI, 2 hour, 4 hour post-dose (each cycle = 28 days)

Population: PKAS population with available data were analyzed.

Vss was derived from the PK blood samples collected.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=10 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
PK of ADC, TAb, MMAE in Serum: Volume of Distribution at Steady State (Vss)
ADC
7.13 Liters
Standard Deviation 1.39
PK of ADC, TAb, MMAE in Serum: Volume of Distribution at Steady State (Vss)
TAb
4.97 Liters
Standard Deviation 1.27
PK of ADC, TAb, MMAE in Serum: Volume of Distribution at Steady State (Vss)
MMAE
28900 Liters
Standard Deviation 10800

SECONDARY outcome

Timeframe: From date of the first CR/PR up to progressive disease or death (maximum duration: 9.33 months)

Population: FAS population with available data were analyzed.

DOR: time from the date of the first CR/PR (whichever is first recorded) that was subsequently confirmed as assessed by IRC to the date of documented progressive disease. or death due to any cause whichever occurred first. CR was defined as disappearance of all target and nontarget lesions. Any pathological lymph nodes (whether target or nontarget) must have reduction in short axis to \< 10 mm from baseline measurement. PR was defined as at least a 30% decrease in the sum of diameters (longest for nonnodal lesions, short axis for nodal lesions) of target lesions taking as reference to the baseline sum of diameters. Progressive Disease:\>= 20% increase in sum of diameters of target lesions taking as reference the smallest sum, and sum must also demonstrate an absolute increase of \>= 5 mm. Appearance of 1 or more new lesions is also considered progression.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=15 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Duration of Response (DOR) as Per RECIST V1.1 Per IRC
NA months
Interval 2.04 to
Due to low number of events, median and upper limit of CI was not estimable.

SECONDARY outcome

Timeframe: From date of the first CR/PR up to progressive disease or death (maximum duration: 9.33 months)

Population: FAS population with available data were analyzed.

DOR: time from the date of the first CR/PR (whichever is first recorded) that was subsequently confirmed as assessed by Investigator's Assesment to the date of documented progressive disease or death due to any cause whichever occurred first. CR was defined as disappearance of all target and nontarget lesions. Any pathological lymph nodes (whether target or nontarget) must have reduction in short axis to \< 10 mm from baseline measurement. PR was defined as at least a 30% decrease in the sum of diameters (longest for nonnodal lesions, short axis for nodal lesions) of target lesions taking as reference to the baseline sum of diameters. Progressive disease:\>= 20% increase in sum of diameters of target lesions taking as reference the smallest sum, and sum must also demonstrate an absolute increase of \>= 5 mm. Appearance of 1 or more new lesions is also considered progression.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=17 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Duration of Response (DOR) as Per RECIST V1.1 Per Investigator's Assessment
NA months
Interval 2.04 to
Due to low number of events, median and upper limit of CI was not estimable.

SECONDARY outcome

Timeframe: From first dose up to progressive disease or death (maximum duration: 9.33 months)

Population: FAS population

ORR was defined as the percentage of participants with BOR as CR or PR based on the RECIST v1.1 as per investigator's assesment. CR was defined as disappearance of all target and nontarget lesions. Any pathological lymph nodes (whether target or nontarget) must have reduction in short axis to \< 10 mm from baseline measurement. PR was defined as at least a 30% decrease in the sum of diameters (longest for nonnodal lesions, short axis for nodal lesions) of target lesions taking as reference to the baseline sum of diameters.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Objective Response Rate (ORR) as Per Investigator Assessment
42.5 percentage of participants
Interval 27.0 to 59.1

SECONDARY outcome

Timeframe: From first dose up to progressive disease or death (maximum duration: 9.33 months)

Population: FAS population.

DCR: percentage of participants with a CR, PR or SD based on RECIST v1.1 as assessed by IRC. CR was defined as disappearance of all target and nontarget lesions. Any pathological lymph nodes (whether target or nontarget) must have reduction in short axis to \< 10 mm from baseline measurement. PR was defined as at least a 30% decrease in the sum of diameters (longest for nonnodal lesions, short axis for nodal lesions) of target lesions taking as reference to the baseline sum of diameters. SD was defined as neither sufficient decrease to qualify for PR nor sufficient increase to qualify for progressive disease taking as reference the smallest sum of diameters while on study drug. Progressive disease:\>= 20% increase in sum of diameters of target lesions taking as reference the smallest sum, and sum must also demonstrate an absolute increase of \>= 5 mm. Appearance of 1 or more new lesions is also considered progression.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Disease Control Rate (DCR) as Per RECIST V1.1 Per IRC
72.5 percentage of participants
Interval 56.1 to 85.4

SECONDARY outcome

Timeframe: From first dose up to progressive disease or death (maximum duration: 9.33 months)

Population: FAS population.

DCR: percentage of participants with a CR, PR or SD based on RECIST v1.1 as assessed by investigator's assessment. CR was defined as disappearance of all target and nontarget lesions. Any pathological lymph nodes (whether target or nontarget) must have reduction in short axis to \< 10 mm from baseline measurement. PR was defined as at least a 30% decrease in the sum of diameters (longest for nonnodal lesions, short axis for nodal lesions) of target lesions taking as reference to the baseline sum of diameters. SD was defined as neither sufficient decrease to qualify for PR nor sufficient increase to qualify for progressive disease taking as reference the smallest sum of diameters while on study drug. Progressive disease:\>= 20% increase in sum of diameters of target lesions taking as reference the smallest sum, and sum must also demonstrate an absolute increase of \>= 5 mm. Appearance of 1 or more new lesions is also considered progression.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Disease Control Rate (DCR) as Per RECIST V1.1 Per Investigator's Assesment
82.5 percentage of participants
Interval 67.2 to 92.7

SECONDARY outcome

Timeframe: From first dose up to progressive disease or death (maximum duration: 9.33 months)

Population: FAS population

PFS: time from first dose of the study drug until date of documented radiological disease progression per IRC based on RECIST V1.1, or until death due to any cause, whichever occurred first. Progressive disease: \>= 20% increase in sum of diameters of target lesions taking as reference the smallest sum, and sum must also demonstrate an absolute increase of \>= 5 mm. Appearance of 1 or more new lesions is also considered progression. A participant who neither progressed nor died was censored at date of last radiological assessment (RA)/ date of randomization if no post-baseline RA was available. Participants who received any further anticancer therapy (ACT) for disease before radiological progression was censored at date of last RA before ACT started and participants who had PD/death after \>=2 missed RAs were censored at last RA prior to 2 or more missed RAs. Kaplan-Meier estimates was used.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Progression Free-Survival Per RECIST V1.1 Per IRC
4.67 months
Interval 3.65 to 5.62

SECONDARY outcome

Timeframe: From first dose up to progressive disease or death (maximum duration: 9.33 months)

Population: FAS population

PFS: time from first dose of the study drug until date of documented radiological disease progression per investigator based on RECIST V1.1, or until death due to any cause, whichever occurred first. Progressive disease: \>= 20% increase in sum of diameters of target lesions taking as reference the smallest sum, and sum must also demonstrate an absolute increase of \>= 5 mm. Appearance of 1 or more new lesions is also considered progression. A participant who neither progressed nor died was censored at date of last RA/ date of randomization if no post-baseline RA was available. Participants who received any further ACT for disease before radiological progression was censored at date of last RA before ACT started and participants who had progressive disease/death after \>=2 missed RAs were censored at last RA prior to 2 or more missed RAs. Kaplan-Meier estimates was used.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Progression Free-Survival Per RECIST V1.1 Per Investigator's Assessment
4.24 months
Interval 3.75 to 7.2

SECONDARY outcome

Timeframe: From first dose up to death (maximum duration: 9.33 months)

Population: FAS population

OS was defined as the time from first dose of the study drug until the documented date of death from any cause. OS was analyzed using Kaplan-Meier estimates. Participants who were still alive at the time of data cutoff date were to be censored at the last known alive date or at the data cutoff date, whichever was earlier.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Overall Survival (OS)
NA months
Interval 6.74 to
Due to low number of events, median and upper limit of CI was not estimable.

SECONDARY outcome

Timeframe: From first dose until 9.33 months

Population: FAS population with available data were analyzed.

Number of participants with ATA were reported.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=38 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Number of Participants With Antitherapeutic Antibodies (ATA)
Baseline Positive, Positive post-baseline
0 Participants
Number of Participants With Antitherapeutic Antibodies (ATA)
Baseline Negative, Negative post-baseline
37 Participants
Number of Participants With Antitherapeutic Antibodies (ATA)
Baseline Negative, Positive post-baseline
0 Participants
Number of Participants With Antitherapeutic Antibodies (ATA)
Baseline Positive, Negative post-baseline
1 Participants

SECONDARY outcome

Timeframe: Baseline up to 9.33 months

Population: Safety analysis set (SAF) included all participants who were enrolled and received any amount of study drug in the study.

An AE is any untoward medical occurrence in a participant temporally associated with the use of a medicinal product, whether or not considered related to the medicinal product. An AE can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding), symptom, or disease (new or exacerbated) temporally associated with the use of a medicinal product. TEAE is defined as an adverse event observed after starting administration of the study drug and within 30 days after taking the last dose of study drug.

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Number of Participants With Treatment Emergent Adverse Events
40 Participants

SECONDARY outcome

Timeframe: End of Treatment (Baseline up to 9.33 months)

Population: SAF population

ECOG performance status was measured on an 6 point scale. 0-Fully active, able to carry on all pre-disease performance without restriction. 1. Restricted in physically strenuous activity but ambulatory and able to carry out work of a light or sedentary nature, e.g., light house work, office work. 2. Ambulatory and capable of all self-care but unable to carry out any work activities. Up and about more than 50% of waking hours. 3. Capable of only limited self-care, confined to bed or chair more than 50% of waking hours. 4. Completely disabled. Cannot carry on any self-care. Totally confined to bed or chair. 5. Dead. Number of participants with ECOG PS was reported."

Outcome measures

Outcome measures
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 Participants
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Number of Participants With Eastern Cooperative Oncology Group (ECOG) Performance Status (PS)
ECOG PS= 0
2 Participants
Number of Participants With Eastern Cooperative Oncology Group (ECOG) Performance Status (PS)
ECOG PS= 1
8 Participants
Number of Participants With Eastern Cooperative Oncology Group (ECOG) Performance Status (PS)
ECOG PS= 2
1 Participants
Number of Participants With Eastern Cooperative Oncology Group (ECOG) Performance Status (PS)
ECOG PS= 3
1 Participants
Number of Participants With Eastern Cooperative Oncology Group (ECOG) Performance Status (PS)
ECOG PS= 4
0 Participants
Number of Participants With Eastern Cooperative Oncology Group (ECOG) Performance Status (PS)
ECOG PS= 5
0 Participants

Adverse Events

Enfortumab Vedotin 1.25 mg/kg

Serious events: 18 serious events
Other events: 40 other events
Deaths: 10 deaths

Serious adverse events

Serious adverse events
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 participants at risk
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Blood and lymphatic system disorders
Leukopenia
5.0%
2/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Blood and lymphatic system disorders
Pancytopenia
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Cardiac disorders
Acute coronary syndrome
2.5%
1/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Eye disorders
Cataract
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Intestinal obstruction
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
General disorders
Chest pain
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
General disorders
Pyrexia
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Infections and infestations
Febrile infection
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Infections and infestations
Pneumonia
12.5%
5/40 • Number of events 6 • Baseline up to 9.33 months
SAF
Infections and infestations
Respiratory tract infection
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Infections and infestations
Urinary tract infection
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Investigations
Alanine aminotransferase increased
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Investigations
Aspartate aminotransferase increased
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Investigations
Neutrophil count decreased
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Investigations
Platelet count decreased
2.5%
1/40 • Number of events 4 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Diabetes mellitus
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypercalcaemia
2.5%
1/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hyperglycaemia
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypokalaemia
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hyponatraemia
2.5%
1/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Malignant neoplasm progression
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Psychiatric disorders
Confusional state
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Respiratory, thoracic and mediastinal disorders
Interstitial lung disease
2.5%
1/40 • Number of events 1 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Dermatitis exfoliative
2.5%
1/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Drug eruption
5.0%
2/40 • Number of events 3 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Rash
7.5%
3/40 • Number of events 4 • Baseline up to 9.33 months
SAF
Vascular disorders
Deep vein thrombosis
2.5%
1/40 • Number of events 2 • Baseline up to 9.33 months
SAF

Other adverse events

Other adverse events
Measure
Enfortumab Vedotin 1.25 mg/kg
n=40 participants at risk
Participants received 1.25 mg/kg of body weight enfortumab vedotin by IV infusion over approximately 30 minutes on days 1, 8 and 15 of every 28-day cycle. Participants received study treatment until radiological disease progression as determined per investigator assessment or other discontinuation criteria were met or upon study termination, or study completion, whichever occurred first.
Blood and lymphatic system disorders
Anaemia
70.0%
28/40 • Number of events 81 • Baseline up to 9.33 months
SAF
Blood and lymphatic system disorders
Leukopenia
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Cardiac disorders
Sinus tachycardia
10.0%
4/40 • Number of events 6 • Baseline up to 9.33 months
SAF
Eye disorders
Dry eye
7.5%
3/40 • Number of events 3 • Baseline up to 9.33 months
SAF
Eye disorders
Eye discharge
12.5%
5/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Eye disorders
Vision blurred
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Abdominal discomfort
10.0%
4/40 • Number of events 4 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Abdominal pain
10.0%
4/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Abdominal pain upper
12.5%
5/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Constipation
47.5%
19/40 • Number of events 25 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Diarrhoea
47.5%
19/40 • Number of events 31 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Dyspepsia
17.5%
7/40 • Number of events 10 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Dysphagia
15.0%
6/40 • Number of events 10 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Flatulence
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Gastrooesophageal reflux disease
10.0%
4/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Intestinal obstruction
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Mouth ulceration
17.5%
7/40 • Number of events 7 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Nausea
50.0%
20/40 • Number of events 39 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Stomatitis
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Gastrointestinal disorders
Vomiting
30.0%
12/40 • Number of events 17 • Baseline up to 9.33 months
SAF
General disorders
Asthenia
10.0%
4/40 • Number of events 4 • Baseline up to 9.33 months
SAF
General disorders
Fatigue
25.0%
10/40 • Number of events 31 • Baseline up to 9.33 months
SAF
General disorders
Malaise
15.0%
6/40 • Number of events 7 • Baseline up to 9.33 months
SAF
General disorders
Oedema peripheral
17.5%
7/40 • Number of events 15 • Baseline up to 9.33 months
SAF
General disorders
Pyrexia
35.0%
14/40 • Number of events 17 • Baseline up to 9.33 months
SAF
Infections and infestations
Herpes dermatitis
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Infections and infestations
Herpes virus infection
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Infections and infestations
Pneumonia
7.5%
3/40 • Number of events 4 • Baseline up to 9.33 months
SAF
Infections and infestations
Skin infection
15.0%
6/40 • Number of events 8 • Baseline up to 9.33 months
SAF
Infections and infestations
Urinary tract infection
7.5%
3/40 • Number of events 3 • Baseline up to 9.33 months
SAF
Investigations
Alanine aminotransferase increased
45.0%
18/40 • Number of events 30 • Baseline up to 9.33 months
SAF
Investigations
Aspartate aminotransferase increased
65.0%
26/40 • Number of events 43 • Baseline up to 9.33 months
SAF
Investigations
Bilirubin conjugated increased
5.0%
2/40 • Number of events 8 • Baseline up to 9.33 months
SAF
Investigations
Blood bilirubin increased
10.0%
4/40 • Number of events 18 • Baseline up to 9.33 months
SAF
Investigations
Blood bilirubin unconjugated increased
5.0%
2/40 • Number of events 3 • Baseline up to 9.33 months
SAF
Investigations
Blood creatinine increased
12.5%
5/40 • Number of events 7 • Baseline up to 9.33 months
SAF
Investigations
Blood glucose increased
10.0%
4/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Investigations
Blood lactate dehydrogenase increased
5.0%
2/40 • Number of events 3 • Baseline up to 9.33 months
SAF
Investigations
Blood triglycerides increased
5.0%
2/40 • Number of events 3 • Baseline up to 9.33 months
SAF
Investigations
Gamma-glutamyltransferase increased
7.5%
3/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Investigations
Glycosylated haemoglobin increased
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Investigations
Lymphocyte count decreased
7.5%
3/40 • Number of events 6 • Baseline up to 9.33 months
SAF
Investigations
Neutrophil count decreased
47.5%
19/40 • Number of events 36 • Baseline up to 9.33 months
SAF
Investigations
Occult blood positive
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Investigations
Platelet count decreased
22.5%
9/40 • Number of events 22 • Baseline up to 9.33 months
SAF
Investigations
Weight decreased
25.0%
10/40 • Number of events 17 • Baseline up to 9.33 months
SAF
Investigations
White blood cell count decreased
40.0%
16/40 • Number of events 43 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Decreased appetite
65.0%
26/40 • Number of events 46 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypercalcaemia
12.5%
5/40 • Number of events 20 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypercholesterolaemia
10.0%
4/40 • Number of events 6 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hyperglycaemia
50.0%
20/40 • Number of events 57 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hyperlipidaemia
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypertriglyceridaemia
15.0%
6/40 • Number of events 17 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hyperuricaemia
27.5%
11/40 • Number of events 24 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypoalbuminaemia
25.0%
10/40 • Number of events 22 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypocalcaemia
20.0%
8/40 • Number of events 22 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypochloraemia
12.5%
5/40 • Number of events 9 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypoglycaemia
5.0%
2/40 • Number of events 4 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypokalaemia
37.5%
15/40 • Number of events 28 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hyponatraemia
32.5%
13/40 • Number of events 35 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypophosphataemia
17.5%
7/40 • Number of events 14 • Baseline up to 9.33 months
SAF
Metabolism and nutrition disorders
Hypoproteinaemia
5.0%
2/40 • Number of events 3 • Baseline up to 9.33 months
SAF
Musculoskeletal and connective tissue disorders
Back pain
10.0%
4/40 • Number of events 4 • Baseline up to 9.33 months
SAF
Musculoskeletal and connective tissue disorders
Muscular weakness
10.0%
4/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Musculoskeletal and connective tissue disorders
Myalgia
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Musculoskeletal and connective tissue disorders
Pain in extremity
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Nervous system disorders
Dizziness
7.5%
3/40 • Number of events 3 • Baseline up to 9.33 months
SAF
Nervous system disorders
Dysgeusia
25.0%
10/40 • Number of events 21 • Baseline up to 9.33 months
SAF
Nervous system disorders
Hypoaesthesia
15.0%
6/40 • Number of events 7 • Baseline up to 9.33 months
SAF
Nervous system disorders
Neuropathy peripheral
20.0%
8/40 • Number of events 9 • Baseline up to 9.33 months
SAF
Nervous system disorders
Peripheral sensory neuropathy
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Psychiatric disorders
Insomnia
20.0%
8/40 • Number of events 15 • Baseline up to 9.33 months
SAF
Renal and urinary disorders
Dysuria
7.5%
3/40 • Number of events 3 • Baseline up to 9.33 months
SAF
Renal and urinary disorders
Haematuria
7.5%
3/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Respiratory, thoracic and mediastinal disorders
Cough
20.0%
8/40 • Number of events 12 • Baseline up to 9.33 months
SAF
Respiratory, thoracic and mediastinal disorders
Dry throat
10.0%
4/40 • Number of events 4 • Baseline up to 9.33 months
SAF
Respiratory, thoracic and mediastinal disorders
Dysphonia
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Respiratory, thoracic and mediastinal disorders
Haemoptysis
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Respiratory, thoracic and mediastinal disorders
Hiccups
5.0%
2/40 • Number of events 3 • Baseline up to 9.33 months
SAF
Respiratory, thoracic and mediastinal disorders
Interstitial lung disease
7.5%
3/40 • Number of events 4 • Baseline up to 9.33 months
SAF
Respiratory, thoracic and mediastinal disorders
Oropharyngeal pain
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Respiratory, thoracic and mediastinal disorders
Productive cough
10.0%
4/40 • Number of events 6 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Alopecia
30.0%
12/40 • Number of events 17 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Dermatitis
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Drug eruption
10.0%
4/40 • Number of events 8 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Eczema
7.5%
3/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Erythema
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Papule
12.5%
5/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Pigmentation disorder
20.0%
8/40 • Number of events 8 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Pruritus
35.0%
14/40 • Number of events 27 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Rash
42.5%
17/40 • Number of events 56 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Rash maculo-papular
15.0%
6/40 • Number of events 13 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Skin exfoliation
12.5%
5/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Skin and subcutaneous tissue disorders
Skin ulcer
7.5%
3/40 • Number of events 5 • Baseline up to 9.33 months
SAF
Vascular disorders
Hypotension
5.0%
2/40 • Number of events 2 • Baseline up to 9.33 months
SAF

Additional Information

Clinical Transparency

Astellas Pharma China, Inc.

Phone: +86-(0)10-85216666

Results disclosure agreements

  • Principal investigator is a sponsor employee Institute and/or Principal Investigator may publish trial data generated at their specific study site after Sponsor publication of the multi-center data. Sponsor must receive a site's manuscript prior to publication for review and comment as specified in the Investigator Agreement.
  • Publication restrictions are in place

Restriction type: OTHER