Tovorafenib (DAY101) Monotherapy for Patients With Melanoma and Other Solid Tumors

NCT ID: NCT04985604

Last Updated: 2025-10-02

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

23 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-07-15

Study Completion Date

2024-07-08

Brief Summary

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This is a Phase 2, multi-center, open-label to evaluate the efficacy and safety of tovorafenib (DAY101) in participants ≥12 years of age with recurrent or progressive melanoma or solid tumors with BRAF fusion or CRAF/RAF1 fusions or amplification.

Detailed Description

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Conditions

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Melanoma Solid Tumor CRAF Gene Amplification RAF1 Gene Amplification BRAF Gene Fusion BRAF Fusion CRAF Gene Fusion CRAF Fusion RAF1 Gene Fusion RAF1 Fusion Thyroid Cancer, Papillary Spitzoid Melanoma Pilocytic Astrocytoma Pilocytic Astrocytoma, Adult Non Small Cell Lung Cancer Non-Small Cell Adenocarcinoma Colorectal Cancer Pancreatic Acinar Carcinoma Spitzoid Malignant Melanoma Bladder Cancer Bladder Urothelial Carcinoma MAP Kinase Family Gene Mutation RAF Mutation

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Melanoma Cohort

Tovorafenib monotherapy

Group Type EXPERIMENTAL

Tovorafenib

Intervention Type DRUG

Tovorafenib tablet for oral use.

Tissue Agnostic Cohort

Tovorafenib monotherapy

Group Type EXPERIMENTAL

Tovorafenib

Intervention Type DRUG

Tovorafenib tablet for oral use.

Interventions

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Tovorafenib

Tovorafenib tablet for oral use.

Intervention Type DRUG

Other Intervention Names

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DAY101

Eligibility Criteria

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Inclusion Criteria

* Signed informed consent by participants ≥ 12 years of age either a Consent or an Assent Form will be provided to the patient based on their capacity, local regulations, and guidelines.
* Participants must have a histologically confirmed diagnosis of melanoma or other solid tumor and a BRAF fusion, CRAF/RAF1 fusion, or CRAF/RAF1 amplifications obtained through a tumor or liquid biopsy as assessed by genomic sequencing, polymerase chain reaction (PCR), fluorescence in situ hybridization (FISH), or another clinically accepted molecular diagnostic method recognized by local laboratory or regulatory agency.
* Participants must have radiographically-recurrent or radiographically-progressive disease that is measurable using the appropriate tumor response criteria (e.g. RECIST version 1.1 or RANO).
* Archival tumor tissue (preferably less than 3 years old) or fresh tumor tissue for correlative studies is required
* If brain metastases are present, they must have been previously treated and be stable as assessed by radiographic imaging

Exclusion Criteria

* Prior therapy of any RAS-, RAF-, MEK-, or ERK-directed inhibitor therapy
* Known presence of concurrent activating mutation
* Participants with current evidence or a history of central serous retinopathy (CSR), retinal vein occlusion (RVO)
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Day One Biopharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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The Angeles Clinic

Los Angeles, California, United States

Site Status

Hoag Health

Newport Beach, California, United States

Site Status

University of Colorado Hospital

Aurora, Colorado, United States

Site Status

Cancer Specialists of North Florida

Jacksonville, Florida, United States

Site Status

Community North Cancer Center

Indianapolis, Indiana, United States

Site Status

OHSU Knight Cancer Institute

Portland, Oregon, United States

Site Status

UPMC Hillman Cancer Center

Pittsburgh, Pennsylvania, United States

Site Status

Vanderbilt-Ingram Cancer Center

Nashville, Tennessee, United States

Site Status

Monash Medical Centre

Clayton, Victoria, Australia

Site Status

Antwerp University Hospital

Edegem, , Belgium

Site Status

Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Site Status

The Hospital for Sick Children

Toronto, Ontario, Canada

Site Status

Hopital de La Timone - APHM

Marseille, Bouches-du-Rhône, France

Site Status

Dong-A University Hospital

Busan, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Hospital Clinic Barcelona

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario Ramón y Cajal

Madrid, , Spain

Site Status

Countries

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United States Australia Belgium Canada France South Korea Spain

Provided Documents

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Document Type: Study Protocol: Sub-protocol DAY102-102a

View Document

Document Type: Study Protocol: Umbrella (Master) Protocol- DAY102-102

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2021-003768-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

DAY101-102a

Identifier Type: -

Identifier Source: org_study_id

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