A Phase 1b/2 Study of Sonrotoclax (BGB-11417) as Monotherapy and in Various Combinations With Dexamethasone Plus Carfilzomib, Dexamethasone Plus Daratumumab, and Dexamethasone Plus Pomalidomide in Multiple Myeloma

NCT ID: NCT04973605

Last Updated: 2025-11-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

246 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-09-16

Study Completion Date

2026-11-30

Brief Summary

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The purpose of this study is to assess the safety, tolerability, and efficacy of sonrotoclax as monotherapy and in various combinations in patients with relapsed/refractory (R/R) multiple myeloma (MM) and chromosomal translocation t(11;14).

The study investigates sonrotoclax alone and in combination with dexamethasone and other agents, including carfilzomib, daratumumab, and pomalidomide.

Detailed Description

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Conditions

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Relapsed/Refractory Multiple Myeloma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Participants will be assigned sequentially in Part 1. In Part 2 participants will be assigned in parallel
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Part 1 Dose Escalation

Dose-escalation and de-escalation to determine maximum tolerated dose (MTD) of sonrotoclax plus dexamethasone, sonrotoclax plus dexamethasone plus carfilzomib, sonrotoclax plus dexamethasone plus daratumumab, and sonrotoclax plus dexamethasone plus pomalidomide.

Group Type EXPERIMENTAL

Sonrotoclax

Intervention Type DRUG

Administered orally daily

Dexamethasone

Intervention Type DRUG

Once weekly either orally or intravenously

Carfilzomib

Intervention Type DRUG

Administered intravenously weekly

Daratumumab

Intervention Type DRUG

Administered subcutaneously weekly

Pomalidomide

Intervention Type DRUG

Administered orally daily

Part 2 Cohort Expansion

There will be up to 7 expansion cohorts to further evaluate the safety and efficacy of sonrotoclax monotherapy, sonrotoclax plus dexamethasone in combination with dexamethasone plus carfilzomib, and in combination with dexamethasone plus daratumumab

Group Type EXPERIMENTAL

Sonrotoclax

Intervention Type DRUG

Administered orally daily

Dexamethasone

Intervention Type DRUG

Once weekly either orally or intravenously

Carfilzomib

Intervention Type DRUG

Administered intravenously weekly

Interventions

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Sonrotoclax

Administered orally daily

Intervention Type DRUG

Dexamethasone

Once weekly either orally or intravenously

Intervention Type DRUG

Carfilzomib

Administered intravenously weekly

Intervention Type DRUG

Daratumumab

Administered subcutaneously weekly

Intervention Type DRUG

Pomalidomide

Administered orally daily

Intervention Type DRUG

Other Intervention Names

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BGB-11417

Eligibility Criteria

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Inclusion Criteria

1. Eastern Cooperative Oncology Group (ECOG) performance status of 0 to 2
2. A confirmed diagnosis of multiple myeloma (must have an M-component in serum and/or urine)
3. Measurable disease defined as:

i. M-spike ≥ 500mg/dL, or ii. Urine protein M-spike of ≥ 200 mg/day, or iii. Serum free light chains ≥ 10 mg/dL, and an abnormal κ:λ ratio
4. Participant has documented relapsed or progressive MM on or after any regimen or who are refractory to the most recent line of therapy.

i. Relapsed MM is defined as previously treated MM that progresses and requires initiation of salvage therapy but does not meet the criteria for refractory MM.

ii. Refractory MM is defined as disease that is nonresponsive (failure to achieve minimal response or development of progressive disease) while on primary or salvage therapy or progresses within 60 days of last therapy.
1. In Part 1 and Part 2 Cohorts 1 and 2 participants should have relapsed or progressive disease and have had ≥ 3 prior lines of therapy including a proteasome inhibitor, an IMiD, and an anti-CD38 monoclonal antibody, and no more available approved therapies.
2. Participants in Part 2 Cohorts 3, 4, and 5 should have relapsed or progressive disease and have had ≥ 1 prior line of therapy. Prior treatment with carfilzomib is allowed but the patient must not be considered carfilzomib refractory by the investigator.
3. Participants in Part 2 Cohorts 6 and 7 should have relapsed or progressive disease and have had 1 to 3 prior lines of therapy and previously treated with a proteasome inhibitor and an IMiD
5. Positivity for t(11;14) translocation must be confirmed by validated fluorescence in situ hybridization (FISH) testing assay in a pre-defined laboratory

a. fresh bone marrow aspirate sample must be collected at screening and sent to central laboratory for t(11;14) FISH testing.
6. Adequate organ function defined as:

1. Hemoglobin ≥ 8.0 g/dL within 7 days before first dose of study treatment, (transfusions, in accordance with institutional guidelines, are permitted)
2. Platelet count ≥ 75,000/μL, within 7 days before first dose of study treatment, independent of growth factor support and transfusions
3. Absolute neutrophil count (ANC) ≥ 1000/mm\^3 within 7 days before first dose of study treatment
4. Alanine aminotransferase (ALT) and aspartate aminotransferase (AST) ≤ 3 x upper limit of normal (ULN) and total bilirubin ≤ 2.0 x ULN N (total bilirubin must be \< 3 x ULN for patients with Gilbert's syndrome)

Exclusion Criteria

1. Participant has any of the following conditions:

1. Non secretory MM (Serum free light chains \< 10 mg/dL)
2. Solitary plasmacytoma
3. Active plasma cell leukemia (ie, either 20% of peripheral white blood cells or \> 2.0 x 109/L circulating plasma cells by standard differential)
4. Waldenström macroglobulinemia (WM)
5. Amyloidosis.
6. Polyneuropathy, organomegaly, endocrinopathy, monoclonal protein, skin changes (POEMS) syndrome
7. Chronic respiratory disease that requires continuous oxygen
2. Significant cardiovascular disease, including but not limited to:

1. Myocardial infarction ≤ 6 months before screening
2. Ejection fraction ≤ 50%
3. Unstable angina≤ 3 months before screening
4. New York Heart Association Class III or IV congestive heart failure
5. History of clinically significant arrhythmias (eg, sustained ventricular tachycardia, ventricular fibrillation, or torsades de pointes)
6. Heart rate-corrected QT interval \> 480 milliseconds based on Fridericia's formula
7. History of Mobitz II second-degree or third-degree heart block without a permanent pacemaker in place
8. Uncontrolled hypertension at screening, defined as systolic blood pressure \> 170 mmHg and diastolic blood pressure \> 105 mmHg by ≥ 2 consecutive measurements. Prior therapy with sonrotoclax or other agents inhibiting BCL2 activity (eg, venetoclax)
3. Known infection with human immunodeficiency virus (HIV)
4. Serologic status reflecting active viral hepatitis B (HBV) or viral hepatitis C (HCV) infection as follows:

1. Presence of hepatitis B surface antigen (HBsAg) or hepatitis B core antibody (HBcAb). Participants with presence of HBcAb, but absence of HBsAg, are eligible if HBV DNA is undetectable (limitation of sensitivity \< 20 IU/mL) ,), and if they are willing to undergo monthly monitoring for HBV reactivation.
2. Presence of HCV antibody. Participants with presence of HCV antibody are eligible if HCV RNA is undetectable (limitation of sensitivity \< 15 IU/mL).
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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BeOne Medicines

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama At Birmingham Hospital

Birmingham, Alabama, United States

Site Status RECRUITING

City of Hope National Medical Center

Duarte, California, United States

Site Status RECRUITING

City of Hope At Irvine Lennar

Irvine, California, United States

Site Status RECRUITING

University of California At San Francisco

San Francisco, California, United States

Site Status RECRUITING

University of Miami

Miami, Florida, United States

Site Status RECRUITING

Emory University Winship Cancer Center

Atlanta, Georgia, United States

Site Status RECRUITING

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status RECRUITING

Southern Illinois University School of Medicine

Springfield, Illinois, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Washington University School of Medicine

St Louis, Missouri, United States

Site Status RECRUITING

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status RECRUITING

Weill Cornell Medical College Newyork Presbyterian Hospital

New York, New York, United States

Site Status RECRUITING

Memorial Sloan Kettering Cancer Center Mskcc

New York, New York, United States

Site Status RECRUITING

The James Cancer Hospital and Solove Research Institute At Ohio State University

Columbus, Ohio, United States

Site Status RECRUITING

Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status RECRUITING

University of Washington

Seattle, Washington, United States

Site Status RECRUITING

University of Wisconsin Carbone Cancer Center

Madison, Wisconsin, United States

Site Status RECRUITING

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status RECRUITING

Canberra Hospital

Garran, Australian Capital Territory, Australia

Site Status RECRUITING

Nepean Hospital

Kingswood, New South Wales, Australia

Site Status RECRUITING

Monash Health

Clayton, Victoria, Australia

Site Status RECRUITING

St Vincents Hospital Melbourne

Fitzroy, Victoria, Australia

Site Status RECRUITING

The Alfred Hospital

Melbourne, Victoria, Australia

Site Status RECRUITING

Royal Perth Hospital

Perth, Western Australia, Australia

Site Status RECRUITING

Hospital Sirio Libanes Brasilia

Brasília, , Brazil

Site Status RECRUITING

Instituto Dor de Pesquisa E Ensino Distrito Federal

Brasília, , Brazil

Site Status RECRUITING

Centro Gaucho Integrado de Oncologia Hospital Mae de Deus

Porto Alegre, , Brazil

Site Status RECRUITING

Hospital Sao Rafael (Rede Dor)

Salvador, , Brazil

Site Status RECRUITING

Hospital Sirio Libanes

São Paulo, , Brazil

Site Status RECRUITING

Hospital Nove de Julho Dasa

São Paulo, , Brazil

Site Status COMPLETED

Accamargo Cancer Center

São Paulo, , Brazil

Site Status COMPLETED

Instituto Dor de Pesquisa E Ensino Sao Paulo

São Paulo, , Brazil

Site Status RECRUITING

Clinica Sao Germano

São Paulo, , Brazil

Site Status COMPLETED

Sociedade Beneficente Israelita Brasileira Hospital Albert Einstein

São Paulo, , Brazil

Site Status RECRUITING

Cross Cancer Institute

Edmonton, Alberta, Canada

Site Status RECRUITING

British Columbia Cancer Agency the Vancouver Centre

Vancouver, British Columbia, Canada

Site Status RECRUITING

Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Site Status RECRUITING

Peking University Third Hospital

Beijing, Beijing Municipality, China

Site Status RECRUITING

Beijing Chao Yang Hospital

Beijing, Beijing Municipality, China

Site Status RECRUITING

Peking University Peoples Hospital

Beijing, Beijing Municipality, China

Site Status RECRUITING

Chongqing Cancer Hospital

Chongqing, Chongqing Municipality, China

Site Status RECRUITING

Fujian Medical University Union Hospital

Fuzhou, Fujian, China

Site Status RECRUITING

The First Affiliated Hospital of Xiamen University

Xiamen, Fujian, China

Site Status COMPLETED

Sun Yat Sen University Cancer Center

Guangzhou, Guangdong, China

Site Status RECRUITING

The Second Hospital of Hebei Medical University

Shijiazhuang, Hebei, China

Site Status COMPLETED

Henan Cancer Hospital

Zhengzhou, Henan, China

Site Status RECRUITING

The First Affiliated Hospital of Zhengzhou University

Zhengzhou, Henan, China

Site Status RECRUITING

Union Hospital of Tongji Medical College, Huazhong University of Science and Technology

Wuhan, Hubei, China

Site Status RECRUITING

Tongji Hospital of Tongji Medical College Huazhong University of Science and Technology

Wuhan, Hubei, China

Site Status RECRUITING

Hunan Cancer Hospital

Changsha, Hunan, China

Site Status COMPLETED

Nanjing Drum Tower Hospital,the Affiliated Hospital of Nanjing University Medical School

Nanjing, Jiangsu, China

Site Status RECRUITING

Jiangsu Province Hospital

Nanjing, Jiangsu, China

Site Status RECRUITING

The First Affiliated Hospital of Nanchang University Branch Xianghu

Nanchang, Jiangxi, China

Site Status RECRUITING

The First Hospital of China Medical University

Shenyang, Liaoning, China

Site Status RECRUITING

Qingdao Municipal Hospital

Qingdao, Shandong, China

Site Status RECRUITING

Affiliated Zhongshan Hospital of Fudan University

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

Shanghai Fourth Peoples Hospital Affiliated to Tongji University

Shanghai, Shanghai Municipality, China

Site Status RECRUITING

Tianjin Medical University General Hospital

Tianjin, Tianjin Municipality, China

Site Status COMPLETED

Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciencestuanbo Branch

Tianjin, Tianjin Municipality, China

Site Status RECRUITING

The First Affiliated Hospital, Zhejiang University School of Medicine

Hangzhou, Zhejiang, China

Site Status RECRUITING

Universitaetsklinikum Aachen

Aachen, , Germany

Site Status RECRUITING

Universitatsklinikum Carl Gustav Carus An Der Technischen Universitat Dresden

Dresden, , Germany

Site Status RECRUITING

Universitatsklinikum Hamburg Eppendorf

Hamburg, , Germany

Site Status RECRUITING

Universitatsklinikum Wurzburg

Würzburg, , Germany

Site Status RECRUITING

University Hospital of Alexandroupolis

Alexandroupoli, , Greece

Site Status RECRUITING

General Hospital of Athens Alexandra

Athens, , Greece

Site Status RECRUITING

Rabin Medical Center

Petah Tikva, , Israel

Site Status COMPLETED

Sourasky Medical Center

Tel Aviv, , Israel

Site Status RECRUITING

Azienda Ospedaliera Policlinico Di Bari

Bari, , Italy

Site Status RECRUITING

Policlinico Sorsola Malpighi, Aou Di Bologna

Bologna, , Italy

Site Status RECRUITING

Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori Irst

Meldola, , Italy

Site Status RECRUITING

Istituto Europeo Di Oncologia

Milan, , Italy

Site Status RECRUITING

Istituto Di Candiolo Irccs

Torino, , Italy

Site Status RECRUITING

Azienda Ospedaliera Universitaria Delle Marche

Torrette, , Italy

Site Status RECRUITING

National University Hospital Singapore

Singapore, , Singapore

Site Status RECRUITING

Samsung Medical Center

GangnamGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

The Catholic University of Korea, Seoul St Marys Hospital

SeochoGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Severance Hospital Yonsei University Health System

SeodaemunGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Seoul National University Hospital

Seoul, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Asan Medical Center

SongpaGu, Seoul Teugbyeolsi, South Korea

Site Status RECRUITING

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status RECRUITING

Hospital San Pedro de Alcantara

Cáceres, , Spain

Site Status RECRUITING

Hospital Universitario Virgen de La Victoria

Málaga, , Spain

Site Status RECRUITING

Hospital Universitario Virgen Del Rocio

Seville, , Spain

Site Status RECRUITING

Churchill Hospital Oxford University Hospital Nhs Trust

Headington, , United Kingdom

Site Status RECRUITING

University College Hospital

London, , United Kingdom

Site Status RECRUITING

Royal Marsden Nhs Foundation Royal Marsden Hospital

Sutton, , United Kingdom

Site Status RECRUITING

Royal Cornwall Hospitalsnhs Trust

Truro, , United Kingdom

Site Status RECRUITING

Countries

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France New Zealand Switzerland United States Australia Brazil Canada China Germany Greece Israel Italy Singapore South Korea Spain United Kingdom

Central Contacts

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BeOne Medicines

Role: CONTACT

Phone: 1.877.828.5568

Email: [email protected]

Other Identifiers

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2023-507751-30-00

Identifier Type: CTIS

Identifier Source: secondary_id

2021-003614-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

U1111-1277-5444

Identifier Type: OTHER

Identifier Source: secondary_id

CTR20231932

Identifier Type: OTHER

Identifier Source: secondary_id

BGB-11417-105

Identifier Type: -

Identifier Source: org_study_id