Trial Outcomes & Findings for A Roll-over Study to Provide Continued Treatment With Lyophilized Pegaspargase (S95014) in Pediatric Patients With Acute Lymphoblastic Leukemia (ALL) (NCT NCT04956666)

NCT ID: NCT04956666

Last Updated: 2023-12-29

Results Overview

All Adverse events (AEs) including Treatment Emergent Adverse Events (TEAEs) causality and severity based on NCI CTCAE 5.0.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

75 participants

Primary outcome timeframe

Through study completion, approximately 19 months

Results posted on

2023-12-29

Participant Flow

Participant milestones

Participant milestones
Measure
Lyophilized S95014
Lyophilized S95014 reconstituted provided 5 mL of extractable volume with the concentration of 750 U/mL.
Overall Study
STARTED
75
Overall Study
COMPLETED
52
Overall Study
NOT COMPLETED
23

Reasons for withdrawal

Reasons for withdrawal
Measure
Lyophilized S95014
Lyophilized S95014 reconstituted provided 5 mL of extractable volume with the concentration of 750 U/mL.
Overall Study
Adverse Event
18
Overall Study
Physician Decision
5

Baseline Characteristics

A Roll-over Study to Provide Continued Treatment With Lyophilized Pegaspargase (S95014) in Pediatric Patients With Acute Lymphoblastic Leukemia (ALL)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Lyophilized S95014
n=74 Participants
Lyophilized S95014 reconstituted was provided 5 mL of extractable volume with the concentration of 750 U/mL.
Age, Continuous
6.1 years
STANDARD_DEVIATION 3.83 • n=5 Participants
Age, Customized
Age Category · < 10 years
60 Participants
n=5 Participants
Age, Customized
Age Category · [10, 15] years
12 Participants
n=5 Participants
Age, Customized
Age Category · ≥ 16 years
2 Participants
n=5 Participants
Sex: Female, Male
Female
36 Participants
n=5 Participants
Sex: Female, Male
Male
38 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
74 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race/Ethnicity, Customized
Race · White
71 Participants
n=5 Participants
Race/Ethnicity, Customized
Race · Asian
2 Participants
n=5 Participants
Race/Ethnicity, Customized
Race · Multiple
1 Participants
n=5 Participants
ECOG Performance Status
ECOG Performance Status: 0
14 Participants
n=5 Participants
ECOG Performance Status
ECOG Performance Status: 1
46 Participants
n=5 Participants
ECOG Performance Status
ECOG Performance Status: 2
14 Participants
n=5 Participants
Body Mass Index (kg/m^2)
16.45 kg/m^2
STANDARD_DEVIATION 3.51 • n=5 Participants
Body Surface Area (m^2)
0.902 m^2
STANDARD_DEVIATION 0.356 • n=5 Participants

PRIMARY outcome

Timeframe: Through study completion, approximately 19 months

All Adverse events (AEs) including Treatment Emergent Adverse Events (TEAEs) causality and severity based on NCI CTCAE 5.0.

Outcome measures

Outcome measures
Measure
Lyophilized S95014
n=74 Participants
Lyophilized S95014 reconstituted provided 5 mL of extractable volume with the concentration of 750 U/mL.
Incidence of Adverse Events (AEs) (Safety and Tolerability)
Number of Participants with an Adverse Event
74 Participants
Incidence of Adverse Events (AEs) (Safety and Tolerability)
Number of Participants with an Treatment Emergent Adverse Event
74 Participants
Incidence of Adverse Events (AEs) (Safety and Tolerability)
Number of Participants with a Grade 3 or 4 Treatment Emergent Adverse Event
72 Participants
Incidence of Adverse Events (AEs) (Safety and Tolerability)
Number of Participants with a Serious Treatment Emergent Adverse Event
27 Participants

Adverse Events

Lyophilized S95014

Serious events: 27 serious events
Other events: 68 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Lyophilized S95014
n=74 participants at risk
Lyophilized S95014 reconstituted provided 5 mL of extractable volume with the concentration of 750 U/mL.
Immune system disorders
Hypersensitivity
14.9%
11/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Immune system disorders
Anaphylactic reaction
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Immune system disorders
Drug hypersensitivity
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Immune system disorders
Haemophagocytic lymphohistiocytosis
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
COVID-19
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
COVID-19 pneumonia
2.7%
2/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Bronchitis
2.7%
2/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Sepsis
2.7%
2/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Neutropenic sepsis
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Appendicitis
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Cellulitis gangrenous
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Device related bacteraemia
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Device related infection
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Laryngitis
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Pneumonia fungal
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Neutropenia
6.8%
5/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Febrile neutropenia
5.4%
4/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Agranulocytosis
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Anaemia
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Leukopenia
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Gastrointestinal disorders
Enterocolitis haemorrhagic
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Gastrointestinal disorders
Oedematous pancreatitis
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Gastrointestinal disorders
Pancreatitis
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Ejection fraction decreased
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Neutrophil count decreased
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
General disorders
General physical health deterioration
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Hepatobiliary disorders
Hepatomegaly
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Hepatobiliary disorders
Hepatotoxicity
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Musculoskeletal and connective tissue disorders
Back pain
1.4%
1/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.

Other adverse events

Other adverse events
Measure
Lyophilized S95014
n=74 participants at risk
Lyophilized S95014 reconstituted provided 5 mL of extractable volume with the concentration of 750 U/mL.
Investigations
Antithrombin III decreased
71.6%
53/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Neutropenia
62.2%
46/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Blood fibrinogen decreased
64.9%
48/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Alanine aminotransferase increased
47.3%
35/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Anaemia
43.2%
32/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Gamma-glutamyltransferase increased
41.9%
31/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Aspartate aminotransferase increased
32.4%
24/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Immune system disorders
Hypersensitivity
17.6%
13/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Leukopenia
27.0%
20/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Metabolism and nutrition disorders
Hypoalbuminaemia
18.9%
14/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Protein S decreased
16.2%
12/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Blood bilirubin increased
14.9%
11/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Neutrophil count decreased
13.5%
10/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Thrombocytopenia
14.9%
11/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
COVID-19
9.5%
7/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
White blood cell count decreased
10.8%
8/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Activated partial thromboplastin time prolonged
9.5%
7/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
General disorders
Pyrexia
9.5%
7/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Immune system disorders
Drug hypersensitivity
6.8%
5/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Lipase increased
8.1%
6/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Metabolism and nutrition disorders
Hypoglycaemia
6.8%
5/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Nervous system disorders
Toxic neuropathy
6.8%
5/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Blood albumin decreased
5.4%
4/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Haemoglobin decreased
5.4%
4/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Hypofibrinogenaemia
5.4%
4/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Upper respiratory tract infection
5.4%
4/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Ammonia increased
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Amylase increased
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Metabolism and nutrition disorders
Hyperammonaemia
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Metabolism and nutrition disorders
Hypertriglyceridaemia
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Lymphocyte count decreased
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Blood and lymphatic system disorders
Lymphopenia
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Gastrointestinal disorders
Nausea
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Investigations
Platelet count decreased
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Rhinitis
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.
Infections and infestations
Viral upper respiratory tract infection
4.1%
3/74 • Through study completion, approximately 19 months
Throughout the study multiple safety visits were conducted and patients underwent physical examinations, electrocardiograms, hematology, blood biochemistry, coagulation parameters, urinalysis, hepatitis serology, cardiac imaging, and vital sign measurements. During these assessments any abnormal values, test or exam results constituted an adverse event if they meet criteria or were deemed clinically significant by the investigator.

Additional Information

Clinical Studies Department

Institut de Recherches Internationales Servier (I.R.I.S.)

Phone: +33 1 55 72 60 00

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60