Trial Outcomes & Findings for Immunotherapy With or Without Radiation Therapy for Metastatic Urothelial Cancer (NCT NCT04936230)

NCT ID: NCT04936230

Last Updated: 2025-08-17

Results Overview

Will be defined as a complete response (CR) or partial response (PR) as assessed by the treating physician using Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1 criteria.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

1 participants

Primary outcome timeframe

Up to 6 months from randomization

Results posted on

2025-08-17

Participant Flow

Participant milestones

Participant milestones
Measure
Arm A (Pembrolizumab)
Patients receive pembrolizumab IV over 25-40 minutes on day 1 of each cycle. Cycles repeat every 3 weeks in the absence of disease progression or unacceptable toxicity. Patients undergo CT scan, MRI, bone scan and/or PET scan, as well as optional urine and blood sample collection throughout the study. Biospecimen Collection: Undergo urine and blood sample collection Bone Scan: Undergo bone scan Computed Tomography: Undergo CT scan Magnetic Resonance Imaging: Undergo MRI Pembrolizumab: Given IV Positron Emission Tomography: Undergo PET scan Questionnaire Administration: Ancillary studies
Arm B (Pembrolizumab, SBRT)
Patients receive pembrolizumab as in Arm A. Patients also undergo SBRT QD every other day for 3 fractions over 2 weeks that must be completed before 12 weeks after the first dose of pembrolizumab in the absence of disease progression or unacceptable toxicity. Patients undergo CT scan, MRI, bone scan, and/or PET scan, as well as optional urine and blood sample collection throughout the study. Biospecimen Collection: Undergo urine and blood sample collection Bone Scan: Undergo bone scan Computed Tomography: Undergo CT scan Magnetic Resonance Imaging: Undergo MRI Pembrolizumab: Given IV Positron Emission Tomography: Undergo PET scan Questionnaire Administration: Ancillary studies Stereotactic Body Radiation Therapy: Undergo SBRT
Overall Study
STARTED
1
0
Overall Study
COMPLETED
1
0
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Immunotherapy With or Without Radiation Therapy for Metastatic Urothelial Cancer

Baseline characteristics by cohort

Baseline data not reported

PRIMARY outcome

Timeframe: Up to 6 months from randomization

Population: In order to maintain the deidentification of the 1 patient accrued, this outcome measure will not be shared.

Will be defined as a complete response (CR) or partial response (PR) as assessed by the treating physician using Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1 criteria.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 3 years from randomization

Population: In order to maintain the deidentification of the 1 patient accrued, this outcome measure will not be shared.

Will be determined to have a tumor response if they have a CR or PR as assessed by immune modified RECIST.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Time from randomization until disease progression as assessed by the treating physician using RECIST 1.1 or death due to any cause, assessed up to 3 years

Population: In order to maintain the deidentification of the 1 patient accrued, this outcome measure will not be shared.

Stratified Cox models will be used to compare the outcomes between the two treatment groups. The results will be summarized with a forest plot displaying the estimate of the hazard ratio and corresponding 95% confidence interval.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Time from randomization until death due to any cause. Patients who are not known to be dead at time of analysis will be censored at the time of their last follow-up, assessed up to 3 years

Population: In order to maintain the deidentification of the 1 patient accrued, this outcome measure will not be shared.

Stratified Cox models will be used to compare the outcomes between the two treatment groups. The results will be summarized with a forest plot displaying the estimate of the hazard ratio and corresponding 95% confidence interval.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: At 1 year

Population: In order to maintain the deidentification of the 1 patient accrued, this outcome measure will not be shared.

The proportion of patients who discontinue their protocol directed treatment prior to one year from date of study registration will be determined. Patients who stop their protocol directed treatment for any reason prior to one year from study registration will be considered to have discontinued their treatment. The rates of treatment discontinuation at one year will be summarized with a binomial point estimate and corresponding 95% confidence interval by arm. A comparison between the rates will be performed with a chi-square test or a Fisher's exact test if the assumptions of the chi-square test are violated.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 3 years from randomization

Population: In order to maintain the deidentification of the 1 patient accrued, this outcome measure will not be shared.

Will be assessed by Common Terminology Criteria for Adverse Events version 5.0. Adverse events will be summarized with frequencies and relative frequencies.

Outcome measures

Outcome data not reported

Adverse Events

Arm A (Pembrolizumab)

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Arm B (Pembrolizumab, SBRT)

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Himanshu Nagar, MD

Weill Cornell Medicine

Phone: 212-746-3704

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60