Study of Efficacy and Safety of NIS793 in Combination With Standard of Care (SOC) Chemotherapy in First-line Metastatic Pancreatic Ductal Adenocarcinoma (mPDAC) - daNIS-2

NCT ID: NCT04935359

Last Updated: 2025-01-07

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

511 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-09-30

Study Completion Date

2024-08-13

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of NIS793 in combination with gemcitabine/nab-paclitaxel versus gemcitabine/nab-paclitaxel and placebo in first-line metastatic pancreatic ductal adenocarcinoma (mPDAC).

This study aims to explore whether blockade of Transforming Growth Factor β (TGFβ) in combination with gemcitabine/nab-paclitaxel can reduce fibrosis in PDAC, restore chemo-sensitivity and ultimately lead to improvements in overall survival (OS) and other clinically relevant outcomes.

Detailed Description

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This is a randomized, double-blind, multicenter two-arm, phase III study that has two parts:

* Safety run-in part: An open-label safety run-in part will be conducted to confirm recommended phase 3 dose (RP3D) of NIS793 in combination with gemcitabine and nab-paclitaxel. Up to approximately 10 participants will be enrolled at each dose level to achieve at least 6 evaluable participants; however, if the starting dose is not recommended and a lower dose level is tested, 10 additional participants will be enrolled. The decision to open the randomized part will be based on dose confirmation and available safety, relevant PK, and other relevant data from run-in part
* Randomized part: Enrolled participants will be randomized to the two treatment arms.

The study treatment will be administered as a 28-day treatment cycle. Participants will be treated until unacceptable toxicity, disease progression per RECIST 1.1, withdrawal of consent or any other condition of treatment discontinuation specified in the protocol.

Note: As of 07-Jul-2023, treatment with NIS793/placebo was stopped. The trial was unblinded and study participants were allowed to continue with standard of care (SoC) chemotherapy (gemcitabine+ nab-paclitaxel) per investigator assessment.

Conditions

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Metastatic Pancreatic Ductal Adenocarcinoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Safety run-in part: NIS793+gemcitabine+nab-paclitaxel

In the safety run-in part, participants will receive a combination of NIS793, gemcitabine and nab-paclitaxel.

Group Type EXPERIMENTAL

NIS793

Intervention Type DRUG

Concentrate for solution infusion (Liquid in Vial)

Nab-paclitaxel

Intervention Type DRUG

Per locally approved formulation

Gemcitabine

Intervention Type DRUG

Per locally approved formulation

Randomized part: NIS793+gemcitabine+nab-paclitaxel

Participants will receive a combination of NIS793, gemcitabine and nab-paclitaxel

Note: As of 07-Jul-2023, treatment with NIS793/placebo was stopped.

Group Type EXPERIMENTAL

NIS793

Intervention Type DRUG

Concentrate for solution infusion (Liquid in Vial)

Nab-paclitaxel

Intervention Type DRUG

Per locally approved formulation

Gemcitabine

Intervention Type DRUG

Per locally approved formulation

Placebo

Intervention Type DRUG

Dextrose 5% in water (D5W) solution for infusion

Randomized part: placebo+gemcitabine+nab-paclitaxel

Participants will receive a combination of placebo, gemcitabine and nab-paclitaxel

Note: As of 07-Jul-2023, treatment with NIS793/placebo was stopped.

Group Type PLACEBO_COMPARATOR

Nab-paclitaxel

Intervention Type DRUG

Per locally approved formulation

Gemcitabine

Intervention Type DRUG

Per locally approved formulation

Placebo

Intervention Type DRUG

Dextrose 5% in water (D5W) solution for infusion

Interventions

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NIS793

Concentrate for solution infusion (Liquid in Vial)

Intervention Type DRUG

Nab-paclitaxel

Per locally approved formulation

Intervention Type DRUG

Gemcitabine

Per locally approved formulation

Intervention Type DRUG

Placebo

Dextrose 5% in water (D5W) solution for infusion

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Applicable for both Safety run-in and Randomized part

* Participants aged ≥18 years with histologically or cytologically confirmed (based on local assessment and per local guidelines) mPDAC eligible for treatment in the first line setting and not amenable for potentially curative surgery
* Presence of at least one measurable lesion assessed by Computerized Tomography (CT) and/or Magnetic Resonance Imaging (MRI) according to RECIST 1.1
* Eastern Cooperative Oncology Group (ECOG) Performance Status 0-1
* Adequate organ function (assessed by central laboratory for eligibility)
* Participants must have recovered from treatment-related toxicities of prior anticancer therapies to grade ≤ 1 (CTCAE v 5.0) at time of screening, except alopecia.

Exclusion Criteria

* Applicable for both Safety run-in and Randomized part

* Previous systemic anti-cancer treatment for metastatic PDAC
* Pancreatic neuroendocrine (islet) or acinar tumors
* Participants with known status of microsatellite instability-high (MSI-H) or mismatch repair-deficient pancreatic cancer (if status is not already available, testing is not required at screening).
* Participant has not recovered from a major surgery performed prior to start of study treatment or has had a major surgery within 4 weeks prior to start of study treatment.
* Radiation therapy or brain radiotherapy ≤ 4 weeks prior to start of study treatment (palliative radiotherapy to bone lesions allowed \> 2 weeks prior to start of study treatment).
* Impaired cardiac function or clinically significant cardio-vascular disease
* Use of hematopoietic growth factors or transfusion support ≤ 2 weeks prior to start of study treatment.
* Participant has conditions that are considered to have a high risk of clinically significant gastrointestinal tract bleeding or any other condition associated with or history of significant bleeding.
* Serious non-healing wounds.
* Pregnant or breast-feeding women
* Women of childbearing potential, unless willing to use highly effective contraception methods during treatment and after stopping study treatments as indicated
* Pre-existing peripheral neuropathy \> grade 1 (CTCAE v5.0)
Minimum Eligible Age

18 Years

Maximum Eligible Age

100 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Highlands Oncology Group

Fayetteville, Arkansas, United States

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University of California LA

Los Angeles, California, United States

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Advent Health Cancer Institute

Orlando, Florida, United States

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Fort Wayne Medical Oncology Hematology Inc

Fort Wayne, Indiana, United States

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NYU Clinical Cancer Center

New York, New York, United States

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US Oncology Research Dallas

Dallas, Texas, United States

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Houston Methodist Hospital

Houston, Texas, United States

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Huntsman Cancer Institute

Salt Lake City, Utah, United States

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Seattle Cancer Care Alliance

Seattle, Washington, United States

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Novartis Investigative Site

Adelaide, South Australia, Australia

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Perth, Western Australia, Australia

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Bonheiden, , Belgium

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Brussels, , Belgium

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Edegem, , Belgium

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Leuven, , Belgium

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Brasília, Federal District, Brazil

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Ijuí, Rio Grande do Sul, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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São Paulo, São Paulo, Brazil

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Brampton, Ontario, Canada

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Cambridge, Ontario, Canada

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Toronto, Ontario, Canada

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Guangzhou, Guangdong, China

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Harbin, Heilongjiang, China

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Nanjing, Jiangsu, China

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Dalian, Liaoning, China

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Jining, Shandong, China

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Xian, Shanxi, China

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Chengdu, Sichuan, China

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Hangzhou, Zhejiang, China

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Beijing, , China

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Beijing, , China

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Beijing, , China

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Shanghai, , China

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Shanghai, , China

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Shanghai, , China

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Shanghai, , China

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Tianjin, , China

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Brno, Czech Republic, Czechia

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Nový Jičín, Czech Republic, Czechia

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Hradec Králové, CZE, Czechia

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Prague, , Czechia

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Helsinki, , Finland

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Tampere, , Finland

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Nice, Alpes Maritimes, France

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Avignon, , France

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Besançon, , France

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Créteil, , France

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Lyon 08, , France

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Marseille, , France

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Montpellier, , France

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Nantes, , France

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Paris, , France

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Berlin, , Germany

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Bochum, , Germany

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Essen, , Germany

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Frankfurt, , Germany

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Halle S, , Germany

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Hamburg, , Germany

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Ulm, , Germany

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Thessaloniki, , Greece

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Thessaloniki, , Greece

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Budapest, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Jerusalem, , Israel

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Ramat Gan, , Israel

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Tel Aviv, , Israel

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Florence, FI, Italy

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Milan, MI, Italy

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Milan, MI, Italy

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Verona, VR, Italy

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Nagoya, Aichi-ken, Japan

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Kashiwa, Chiba, Japan

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Yokohama, Kanagawa, Japan

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Osaka, Osaka, Japan

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Chuo Ku, Tokyo, Japan

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Koto Ku, Tokyo, Japan

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Utrecht, , Netherlands

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Nordbyhagen, Oslo County, Norway

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Oslo, , Norway

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Omsk, , Russia

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Pushkin Saint Petersburg, , Russia

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Singapore, , Singapore

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Bratislava, Slovak Republic, Slovakia

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Banská Bystrica, , Slovakia

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Košice, , Slovakia

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Seoul, Seocho Gu, South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Barcelona, Catalonia, Spain

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L'Hospitalet de Llobregat, Catalonia, Spain

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Santiago de Compostela, Galicia, Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Malmo, , Sweden

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Umeå, , Sweden

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Bellinzona, , Switzerland

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Geneva, , Switzerland

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Sankt Gallen, , Switzerland

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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Adana, , Turkey (Türkiye)

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Ankara, , Turkey (Türkiye)

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Istanbul, , Turkey (Türkiye)

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Izmir, , Turkey (Türkiye)

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Sutton, Surrey, United Kingdom

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Cambridge, , United Kingdom

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Liverpool, , United Kingdom

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London, , United Kingdom

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Oxford, , United Kingdom

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Countries

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United States Australia Belgium Brazil Canada China Czechia Finland France Germany Greece Hungary Israel Italy Japan Netherlands Norway Russia Singapore Slovakia South Korea Spain Sweden Switzerland Taiwan Turkey (Türkiye) United Kingdom

Other Identifiers

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2021-000591-10

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CNIS793B12301

Identifier Type: -

Identifier Source: org_study_id

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