Belzutifan/MK-6482 for the Treatment of Advanced Pheochromocytoma/Paraganglioma (PPGL), Pancreatic Neuroendocrine Tumor (pNET), Von Hippel-Lindau (VHL) Disease-Associated Tumors, Advanced Gastrointestinal Stromal Tumor (wt GIST), or Solid Tumors With HIF-2α Related Genetic Alterations (MK-6482-015)

NCT ID: NCT04924075

Last Updated: 2025-11-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

322 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-08-12

Study Completion Date

2029-06-04

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a study to evaluate the efficacy and safety of belzutifan monotherapy in participants with advanced pheochromocytoma/paraganglioma (PPGL), pancreatic neuroendocrine tumor (pNET), von Hippel-Lindau (VHL) disease-associated tumors, advanced wt (wild-type) gastrointestinal stromal tumor (wt GIST), or advanced solid tumors with hypoxia inducible factor-2 alpha (HIF-2α) related genetic alterations. The primary objective of the study is to evaluate the objective response rate (ORR) of belzutifan per response evaluation criteria in solid tumors version 1.1 (RECIST 1.1) by blinded independent central review (BICR).

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Pheochromocytoma/Paraganglioma Pancreatic Neuroendocrine Tumor Von Hippel-Lindau Disease Advanced Gastrointestinal Stromal Tumor HIF-2α Mutated Cancers

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

HIF-2α Pheochromocytoma/paraganglioma Pancreatic NET

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Belzutifan

Belzutifan, 120 mg, oral, once daily (QD) until progressive disease or discontinuation.

Group Type EXPERIMENTAL

Belzutifan

Intervention Type DRUG

Belzutifan, 120 mg, oral, once daily (QD) until progressive disease or discontinuation.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Belzutifan

Belzutifan, 120 mg, oral, once daily (QD) until progressive disease or discontinuation.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

MK-6482 WELIREG™

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Male and female participants at least 12 years of age (at least 18 years of age for Cohort B1)
* Diagnosis of one of the following: Advanced/metastatic pheochromocytoma/paraganglioma (PPGL), pancreatic neuroendocrine tumors (pNET), von Hippel-Lindau (VHL) disease associated localized tumors, or advanced wild-type gastrointestinal stromal tumor (wt GIST) or advanced solid tumors with Hypoxia Inducible Factor- 2 alpha subunit (HIF-2α) related genetic alterations
* Cohort BI: VHL Disease-associated tumors:

* Have a diagnosis of VHL disease as determined by a germline test locally and/or clinical diagnosis
* Must be ≥18 years of age
* Has a life expectancy of at least 3 months

Exclusion Criteria

* Unable to swallow orally administered medication or has a disorder that might affect the absorption of belzutifan
* History of a second malignancy, unless potentially curative treatment has been completed with no evidence of malignancy for 2 years
* Any of the following: A pulse oximeter reading \<92% at rest, or requires intermittent supplemental oxygen, or requires chronic supplemental oxygen
* Clinically significant cardiac disease, including unstable angina, acute myocardial infarction, or arterial bypass (CABG) or Percutaneous transluminal coronary angioplasty (PTCA) ≤6 months from study entry, or New York Heart Association Class III or IV congestive heart failure
* Received prior treatment (except somatostatin analogs) with chemotherapy, targeted therapy, biologics, or other investigational therapy within the past 4 weeks of first dose of study intervention
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Cedars-Sinai Medical Center ( Site 0110)

Los Angeles, California, United States

Site Status RECRUITING

Northwestern University - Robert H. Lurie Comprehensive Cancer Center ( Site 0130)

Chicago, Illinois, United States

Site Status RECRUITING

University of Iowa ( Site 0104)

Iowa City, Iowa, United States

Site Status RECRUITING

Johns Hopkins Hospital-Sidney Kimmel Comprehensive Cancer Center - Developmental Therapeutics ( Site 0108)

Baltimore, Maryland, United States

Site Status RECRUITING

National Institutes of Health ( Site 0125)

Bethesda, Maryland, United States

Site Status RECRUITING

Massachusetts General Hospital ( Site 0111)

Boston, Massachusetts, United States

Site Status RECRUITING

University of Michigan ( Site 0126)

Ann Arbor, Michigan, United States

Site Status RECRUITING

Washington University-Internal Medicine/Oncology ( Site 0124)

St Louis, Missouri, United States

Site Status ACTIVE_NOT_RECRUITING

Icahn School of Medicine at Mount Sinai ( Site 0123)

New York, New York, United States

Site Status ACTIVE_NOT_RECRUITING

Penn Medicine: University of Pennsylvania Health System-Heme/Onc ( Site 0127)

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

SCRI Oncology Partners ( Site 7000)

Nashville, Tennessee, United States

Site Status RECRUITING

Vanderbilt University Medical Center ( Site 0107)

Nashville, Tennessee, United States

Site Status RECRUITING

University of Texas MD Anderson Cancer Center ( Site 0112)

Houston, Texas, United States

Site Status RECRUITING

Prince of Wales Hospital-Medical Oncology ( Site 1601)

Randwick, New South Wales, Australia

Site Status RECRUITING

The Royal Melbourne Hospital ( Site 1602)

Parkville, Victoria, Australia

Site Status RECRUITING

Arthur J.E. Child Comprehensive Cancer Centre ( Site 0203)

Calgary, Alberta, Canada

Site Status RECRUITING

Princess Margaret Cancer Centre ( Site 0202)

Toronto, Ontario, Canada

Site Status RECRUITING

FALP ( Site 2200)

Santiago, Region M. de Santiago, Chile

Site Status RECRUITING

Centro de Oncología de Precisión ( Site 2203)

Santiago, Region M. de Santiago, Chile

Site Status RECRUITING

Peking University First Hospital-Urology ( Site 1900)

Beijing, Beijing Municipality, China

Site Status ACTIVE_NOT_RECRUITING

Sun Yat-sen University Cancer Center ( Site 1905)

Guangzhou, Guangdong, China

Site Status RECRUITING

Renji Hospital Shanghai Jiao Tong University School of Medicine ( Site 1904)

Shanghai, Shanghai Municipality, China

Site Status ACTIVE_NOT_RECRUITING

West China Hospital of Sichuan University ( Site 1906)

Chengdu, Sichuan, China

Site Status COMPLETED

Rigshospitalet ( Site 0304)

Copenhagen, Capital Region, Denmark

Site Status RECRUITING

Rigshospitalet-Department of Endocrinology ( Site 0303)

Copenhagen, Capital Region, Denmark

Site Status RECRUITING

Odense Universitetshospital ( Site 0302)

Odense C, Region Syddanmark, Denmark

Site Status RECRUITING

CHU Strasbourg-Hautepierre-Medecine Interne, Endocrinologie et Nutrition ( Site 0402)

Strasbourg, Alsace, France

Site Status RECRUITING

Hôpital Edouard Herriot-oncologie ( Site 0405)

Lyon, Auvergne-Rhône-Alpes, France

Site Status RECRUITING

Institut Paoli-Calmettes-Oncology ( Site 0406)

Marseille, Bouches-du-Rhone, France

Site Status COMPLETED

Hôpitaux Universitaires Paris Sud - Hôpital Bicêtre ( Site 0407)

Le Kremlin-Bicêtre, Paris, France

Site Status RECRUITING

Hopitaux Universitaires Paris Centre-Hopital Cochin ( Site 0404)

Paris, , France

Site Status RECRUITING

Gustave Roussy ( Site 0403)

Villejuif, Île-de-France Region, France

Site Status RECRUITING

Klinikum der Ludwig-Maximilians-Universitaet Muenchen-Department of Internal Medicine IV, Division ( Site 0501)

München, Bavaria, Germany

Site Status COMPLETED

Comprehensive Cancer Center Mainfranken-Div. of Endocrinology and Diabetes ( Site 0500)

Würzburg, Bavaria, Germany

Site Status RECRUITING

Universitaetsklinikum Freiburg ( Site 0504)

Freiburg, Brandenburg, Germany

Site Status RECRUITING

Universitaetsklinikum Duesseldorf-Gastroenterology, Hepatology and Infectiology ( Site 0505)

Düsseldorf, North Rhine-Westphalia, Germany

Site Status RECRUITING

Charité Universitaetsmedizin Berlin - Campus Mitte-Department of Endocrinology and Metabolism ( Site 0503)

Berlin, , Germany

Site Status RECRUITING

Semmelweis University-Belgyógyászati és Onkológiai Klinika Hematológia Osztály ( Site 0600)

Budapest, , Hungary

Site Status RECRUITING

Sheba Medical Center-Institute of Endocrinology, Diabetes and Metabolism ( Site 1400)

Ramat Gan, , Israel

Site Status RECRUITING

Sourasky Medical Center ( Site 1401)

Tel Aviv, , Israel

Site Status RECRUITING

University of Naples Federico II-Dipartimento di Medicina Clinica e Chirurgia ( Site 0704)

Naples, Campania, Italy

Site Status COMPLETED

Fondazione IRCCS Istituto Nazionale dei Tumori-S.C. Oncologia Medica 2- Sarcomi ( Site 0709)

Milan, Lombardy, Italy

Site Status RECRUITING

Azienda Ospedaliero Universitaria Senese-U.O.C. Immunoterapia Oncologica ( Site 0706)

Siena, Tuscany, Italy

Site Status RECRUITING

IRCCS Azienda Ospedaliero-Universitaria di Bologna, Policlinico di Sant'Orsola ( Site 0708)

Bologna, , Italy

Site Status RECRUITING

Azienda Ospedaliera Spedali Civili di Brescia-Oncology ( Site 0701)

Brescia, , Italy

Site Status RECRUITING

Ospedale San Raffaele-Oncologia Medica ( Site 0705)

Milan, , Italy

Site Status COMPLETED

Istituto Europeo di Oncologia IRCCS-Divisione di Oncologia Medica Gastrointestinale e Tumori Neuroe ( Site 0700)

Milan, , Italy

Site Status RECRUITING

Azienda Ospedaliera Universitaria Integrata Verona - Ospedale Borgo Roma ( Site 0703)

Verona, , Italy

Site Status RECRUITING

Hokkaido University Hospital ( Site 1800)

Sapporo, Hokkaido, Japan

Site Status ACTIVE_NOT_RECRUITING

Yokohama City University Hospital ( Site 1804)

Yokohama, Kanagawa, Japan

Site Status ACTIVE_NOT_RECRUITING

Kochi Medical School Hospital ( Site 1807)

Nankoku, Kochi, Japan

Site Status ACTIVE_NOT_RECRUITING

National Cancer Center Hospital ( Site 1802)

Chuo-ku, Tokyo, Japan

Site Status ACTIVE_NOT_RECRUITING

Kyoto University Hospital ( Site 1806)

Kyoto, , Japan

Site Status ACTIVE_NOT_RECRUITING

Tokyo Women's Medical University Adachi Medical Center ( Site 1803)

Tokyo, , Japan

Site Status ACTIVE_NOT_RECRUITING

Universitair Medisch Centrum Utrecht ( Site 1530)

Utrecht, , Netherlands

Site Status RECRUITING

Oslo Universitetssykehus Radiumhospitalet ( Site 2400)

Oslo, , Norway

Site Status RECRUITING

START Lisbon - Hospital de Santa Maria ( Site 2601)

Lisbon, Lisbon District, Portugal

Site Status RECRUITING

Instituto Portugues de Oncologia Do Porto Francisco Gentil E.P.E. ( Site 2600)

Porto, , Portugal

Site Status RECRUITING

GBUZ Republican Clinical Oncological Dispensary ( Site 0804)

Ufa, Baskortostan, Respublika, Russia

Site Status RECRUITING

Saint Petersburg State University-Clinic of advanced medical technologies n. a. Nicolay I. Pirogov ( Site 0805)

Saint Petersburg, Leningradskaya Oblast', Russia

Site Status COMPLETED

Saint-Petersburg City Clinical Oncology Dispensary-Department of chemotherapy ( Site 0803)

Saint Petersburg, Leningradskaya Oblast', Russia

Site Status RECRUITING

Fed State Budgetary Inst N.N. Blokhin Med Center of Oncology MHRF ( Site 0801)

Moscow, Moscow, Russia

Site Status RECRUITING

Endocrinology Research Center of Rosmedtechnologies-Surgery ( Site 0809)

Moscow, Moscow, Russia

Site Status COMPLETED

National Cancer Centre Singapore ( Site 1700)

Singapore, Central Singapore, Singapore

Site Status RECRUITING

Seoul National University Hospital ( Site 2001)

Jongno-gu, Seoul, South Korea

Site Status RECRUITING

Asan Medical Center ( Site 2000)

Songpa-gu, Seoul, South Korea

Site Status RECRUITING

MD Anderson Cancer Center-Oncology ( Site 1102)

Madrid, Madrid, Comunidad de, Spain

Site Status COMPLETED

Hospital Universitario 12 de Octubre-Medical Oncology ( Site 1103)

Madrid, Madrid, Comunidad de, Spain

Site Status RECRUITING

Hospital Universitario Central de Asturias-Medical Oncology ( Site 1101)

Oviedo, Principality of Asturias, Spain

Site Status RECRUITING

Hospital Universitari Vall d'Hebron ( Site 1100)

Barcelona, , Spain

Site Status RECRUITING

Skanes University Hospital Lund ( Site 1200)

Lund, Skåne County, Sweden

Site Status RECRUITING

Karolinska Universitetssjukhuset Solna ( Site 1202)

Stockholm, Stockholm County, Sweden

Site Status COMPLETED

Akademiska sjukhuset-Blod- och tumörsjukdomar ( Site 1201)

Uppsala, Uppsala County, Sweden

Site Status RECRUITING

Sahlgrenska Universitetssjukhuset-Department of Oncology CTU Clinical Trial Unit ( Site 1204)

Gothenburg, Västra Götaland County, Sweden

Site Status RECRUITING

Baskent University Adana Training Hospital ( Site 0906)

Yüreğir, Adana, Turkey (Türkiye)

Site Status RECRUITING

Ege University Medicine of Faculty ( Site 0900)

Bornova, İzmir, Turkey (Türkiye)

Site Status RECRUITING

Hacettepe Universitesi-oncology hospital ( Site 0901)

Ankara, , Turkey (Türkiye)

Site Status RECRUITING

Ankara Bilkent Şehir Hastanesi. ( Site 0904)

Ankara, , Turkey (Türkiye)

Site Status RECRUITING

Istanbul Universitesi Cerrahpasa-Medical Oncology ( Site 0902)

Istanbul, , Turkey (Türkiye)

Site Status COMPLETED

Addenbrooke's Hospital ( Site 1309)

Cambridge, Cambridgeshire, United Kingdom

Site Status RECRUITING

Royal Free Hospital ( Site 1302)

London, England, United Kingdom

Site Status COMPLETED

The Beatson West of Scotland Cancer Centre ( Site 1308)

Glasgow, Glasgow City, United Kingdom

Site Status RECRUITING

Hammersmith Hospital-Medical Oncology ( Site 1304)

London, London, City of, United Kingdom

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Canada Chile China Denmark France Germany Hungary Israel Italy Japan Netherlands Norway Portugal Russia Singapore South Korea Spain Sweden Turkey (Türkiye) United Kingdom

Central Contacts

Reach out to these primary contacts for questions about participation or study logistics.

Toll Free Number

Role: CONTACT

Phone: 1-888-577-8839

Email: [email protected]

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

References

Explore related publications, articles, or registry entries linked to this study.

Jimenez C, Andreassen M, Durand A, Moog S, Hendifar A, Welin S, Spada F, Sharma R, Wolin E, Ruether J, Garcia-Carbonero R, Fassnacht M, Capdevila J, Del Rivero J, Iliopoulos O, Huillard O, Jang R, Mai K, Artamonova E, Hallqvist A, Else T, Odeleye-Ajakaye A, Gozman A, Naik GS, Berruti A; LITESPARK-015 Investigators. Belzutifan for Advanced Pheochromocytoma or Paraganglioma. N Engl J Med. 2025 Oct 18. doi: 10.1056/NEJMoa2504964. Online ahead of print.

Reference Type RESULT
PMID: 41124218 (View on PubMed)

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

MK-6482-015

Identifier Type: OTHER

Identifier Source: secondary_id

PT2977

Identifier Type: OTHER

Identifier Source: secondary_id

jRCT2011220024

Identifier Type: REGISTRY

Identifier Source: secondary_id

2023-504853-11-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

2020-005028-13

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

6482-015

Identifier Type: -

Identifier Source: org_study_id