Pembrolizumab (MK-3475) Plus Gemcitabine/Cisplatin Versus Placebo Plus Gemcitabine/Cisplatin for First-Line Advanced and/or Unresectable Biliary Tract Carcinoma (BTC) (MK-3475-966/KEYNOTE-966)-China Extension Study

NCT ID: NCT04924062

Last Updated: 2025-04-17

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

158 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-07-10

Study Completion Date

2025-03-25

Brief Summary

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In this China Extension study, pembrolizumab plus gemcitabine/cisplatin will be compared with placebo plus gemcitabine/cisplatin as first-line therapy in Chinese adults with advanced and/or unresectable biliary tract carcinoma. The primary hypothesis is pembrolizumab plus gemcitabine/cisplatin is superior to placebo plus gemcitabine/cisplatin with respect to overall survival (OS).

Detailed Description

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The China extension study will include participants previously enrolled in China in the global study for MK-3475-966 (NCT04003636) plus those enrolled during the China extension enrollment period. A total of approximately 158 Chinese participants will be enrolled.

Conditions

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Biliary Tract Carcinoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Arm A (Pembrolizumab+Gemcitabine+Cisplatin)

Pembrolizumab, 200 mg, every 3 weeks (Q3W), Day 1 of each 3-week cycle for up to 35 cycles PLUS Gemcitabine, 1000 mg/m\^2, Q3W, Day 1 and Day 8 of each cycle until progressive disease or unacceptable toxicity PLUS Cisplatin, 25 mg/m\^2, Q3W, Day 1 and Day 8 of each cycle for up to 8 cycles.

Group Type EXPERIMENTAL

Pembrolizumab

Intervention Type BIOLOGICAL

Pembrolizumab by intravenous (IV) infusion

Gemcitabine

Intervention Type DRUG

Gemcitabine by IV infusion

Cisplatin

Intervention Type DRUG

Cisplatin by IV infusion

Arm B (Placebo+Gemcitabine+Cisplatin)

Placebo to Pembrolizumab, 200 mg, every 3 weeks (Q3W), Day 1 of each 3-week cycle for up to 35 cycles PLUS Gemcitabine, 1000 mg/m\^2, Q3W, Day 1 and Day 8 of each cycle until progressive disease or unacceptable toxicity PLUS Cisplatin, 25 mg/m\^2, Q3W, Day 1 and Day 8 of each cycle for up to 8 cycles.

Group Type PLACEBO_COMPARATOR

Gemcitabine

Intervention Type DRUG

Gemcitabine by IV infusion

Cisplatin

Intervention Type DRUG

Cisplatin by IV infusion

Placebo

Intervention Type DRUG

Placebo to pembrolizumab

Interventions

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Pembrolizumab

Pembrolizumab by intravenous (IV) infusion

Intervention Type BIOLOGICAL

Gemcitabine

Gemcitabine by IV infusion

Intervention Type DRUG

Cisplatin

Cisplatin by IV infusion

Intervention Type DRUG

Placebo

Placebo to pembrolizumab

Intervention Type DRUG

Other Intervention Names

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MK-3475 Gemzar Platinol® Platinol®-AQ

Eligibility Criteria

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Inclusion Criteria

* Has histologically confirmed diagnosis of advanced (metastatic) and/or unresectable (locally advanced) biliary tract cancer (intra-or extrahepatic cholangiocarcinoma or gallbladder cancer)
* Has measurable disease based on Response Evaluation Criteria in Solid Tumors (RECIST 1.1), as determined by the site investigator
* Participants with a history of hepatitis B or hepatitis C can be enrolled if they meet study criteria
* Is able to provide archival tumor tissue sample or newly obtained core or excisional biopsy of a tumor lesion
* Has a life expectancy of greater than 3 months
* Has adequate organ function

Exclusion Criteria

* Has had previous systemic therapy for advanced (metastatic) or unresectable (locally advanced) biliary tract cancer (intra-or extra hepatic cholangiocarcinoma or gallbladder cancer)
* Has ampullary cancer
* Has small cell cancer, neuroendocrine tumors, lymphoma, sarcoma, mixed tumor histology and/or mucinous cystic neoplasms
* Has received prior therapy with an anti-programmed cell death 1 (anti-PD-1), anti- programmed cell death ligand 1 or 2 (anti-PD-L1, anti-PD-L2) agent or with an agent directed to another stimulatory or coinhibitory T-cell receptor (e.g., cytotoxic T-lymphocyte-associated protein 4 \[CTLA-4\], OX-40, CD137)
* Has a known history of, or any evidence of, central nervous system (CNS) metastases and/or carcinomatous meningitis, as assessed by local site investigator
* Has had an allogenic tissue/solid organ transplant
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

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Anhui Provincial Hospital ( Site 0140)

Hefei, Anhui, China

Site Status

Beijing Cancer Hospital ( Site 0138)

Beijing, Beijing Municipality, China

Site Status

Peking Union Medical College Hospital ( Site 0150)

Beijing, Beijing Municipality, China

Site Status

First Affiliated Hospital of The Third Military Medical University ( Site 0130)

Chongqing, Chongqing Municipality, China

Site Status

Fujian Provincial Cancer Hospital ( Site 0154)

Fuzhou, Fujian, China

Site Status

900 Hospital of the Joint ( Site 0137)

Fuzhou, Fujian, China

Site Status

Guangdong Provincial People s Hospital ( Site 0161)

Guangzhou, Guangdong, China

Site Status

Harbin Medical University Cancer Hospital ( Site 0133)

Harbin, Heilongjiang, China

Site Status

Hunan Provincial People Hospital ( Site 0142)

Changsha, Hunan, China

Site Status

Hunan Cancer Hospital ( Site 0132)

Changsha, Hunan, China

Site Status

The Third Xiangya Hospital of Central South University ( Site 0157)

Changsha, Hunan, China

Site Status

The 81st Hospital of PLA ( Site 0128)

Nanjing, Jiangsu, China

Site Status

The First Hospital of Jilin University ( Site 0131)

Changchun, Jilin, China

Site Status

Zhongshan Hospital Fudan University ( Site 0129)

Shanghai, Shanghai Municipality, China

Site Status

Renji Hospital Shanghai Jiaotong University School of Medicine ( Site 0158)

Shanghai, Shanghai Municipality, China

Site Status

Fudan University Shanghai Cancer Center ( Site 0160)

Shanghai, Shanghai Municipality, China

Site Status

Tangdu Hospital ( Site 0146)

Xi’an, Shanxi, China

Site Status

The First Affiliated Hospital of Xi an Jiaotong University ( Site 0145)

Xi’an, Shanxi, China

Site Status

West China Hospital of Sichuan University ( Site 0147)

Chengdu, Sichuan, China

Site Status

Tianjin Medical University Cancer Institute & Hospital ( Site 0155)

Tianjin, Tianjin Municipality, China

Site Status

The First Affiliated Hospital Zhejiang University ( Site 0136)

Hangzhou, Zhejiang, China

Site Status

Zhejiang Cancer Hospital ( Site 0134)

Hangzhou, Zhejiang, China

Site Status

Countries

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China

References

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Yoo C, Ueno M, Klumpen HJ, Kelley RK, Vogel A, Furuse J, Ren Z, Yau T, Chan SL, Ozaka M, Oh SC, Gu S, Park JO, Valle JW, Edeline J, Kim JG, Kamble S, Norquist JM, Yu L, Malhotra U, Finn RS. Health-related quality of life in participants with advanced biliary tract cancer from the randomized phase III KEYNOTE-966 study. J Hepatol. 2025 Sep;83(3):692-700. doi: 10.1016/j.jhep.2025.03.019. Epub 2025 Mar 27.

Reference Type DERIVED
PMID: 40154623 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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MK-3475-966

Identifier Type: OTHER

Identifier Source: secondary_id

KEYNOTE-966

Identifier Type: OTHER

Identifier Source: secondary_id

195007

Identifier Type: REGISTRY

Identifier Source: secondary_id

3475-966 China Extension

Identifier Type: -

Identifier Source: org_study_id

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