Study of Efficacy, Safety, and Tolerability of LNA043 in Patients With Knee Osteoarthritis

NCT ID: NCT04864392

Last Updated: 2025-07-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

582 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-05-31

Study Completion Date

2025-05-29

Brief Summary

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The study will determine the optimal dosing regimen of LNA043 in patients with knee osteoarthritis (OA).

Detailed Description

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This study is a 2-period, multicenter, randomized, parallel-group, double-blind, placebo-controlled study consisting of a 2-year Core period, followed by a 3 year extension period. The primary objective of this study is to assess the efficacy of LNA043 compared to placebo at Week 104 as measured by the mean change from baseline in cartilage thickness using qMRI of the target knee

Conditions

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Osteoarthritis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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LNA043 Dosing Regimen A

LNA043 injection to the knee with dosing regimen A

Group Type EXPERIMENTAL

LNA043 Dosing Regimen A

Intervention Type DRUG

Injection to the knee

LNA043 Dosing Regimen B

LNA04 injection to the knee with dosing regimen B

Group Type EXPERIMENTAL

LNA043 Dosing Regimen B

Intervention Type DRUG

Injection to the knee

LNA043 Dosing Regimen C

LNA043 injection to the knee with dosing regimen C

Group Type EXPERIMENTAL

LNA043 Dosing Regimen C

Intervention Type DRUG

Injection to the knee

LNA043 Dosing Regimen D

LNA043 injection to the knee with dosing regimen D

Group Type EXPERIMENTAL

LNA043 Dosing Regimen D

Intervention Type DRUG

Injection to the knee

Placebo

Injection to the knee

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Injection to the knee

Interventions

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LNA043 Dosing Regimen A

Injection to the knee

Intervention Type DRUG

LNA043 Dosing Regimen B

Injection to the knee

Intervention Type DRUG

LNA043 Dosing Regimen C

Injection to the knee

Intervention Type DRUG

LNA043 Dosing Regimen D

Injection to the knee

Intervention Type DRUG

Placebo

Injection to the knee

Intervention Type DRUG

Other Intervention Names

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LNA043 LNA043 LNA043 LNA043

Eligibility Criteria

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Inclusion Criteria

* Males and females between 40 and 75 years of age
* Body mass index (BMI) \< 40 kg/m2
* Diagnosis of primary tibiofemoral knee OA by standard American College of Rheumatology clinical and radiographic criteria
* and other criteria as specified by the protocol

Exclusion Criteria

* Participants with radiographic knee OA K-L grade = 4 on the non-target knee
* Arthroscopy of the target knee within the 6 months prior to Screening
* Hemoglobin \< 8.5 g/dL (85 g/L) or platelet count \< 100,000/μL
* and other criteria as specified by the protocol
Minimum Eligible Age

40 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Elite Clinical Studies

Phoenix, Arizona, United States

Site Status

Tucson Orthopedic Institute PC

Tucson, Arizona, United States

Site Status

Sharps Hospital Grossmont

La Mesa, California, United States

Site Status

Clinical Trials Research

Lincoln, California, United States

Site Status

Long Beach Clinical Trials

Long Beach, California, United States

Site Status

Artemis Institute Clinical Research

Riverside, California, United States

Site Status

Northern California Research

Sacramento, California, United States

Site Status

Arthemis Clinical Research

San Diego, California, United States

Site Status

Stamford Therapeutics Consortium LLC

Stamford, Connecticut, United States

Site Status

Sensible Healthcare

Ocoee, Florida, United States

Site Status

Clinical Research of West Florida Inc

Tampa, Florida, United States

Site Status

Conquest Research

Winter Park, Florida, United States

Site Status

Chicago Clinical Research Inst

Chicago, Illinois, United States

Site Status

Tandem clinical research

Marrero, Louisiana, United States

Site Status

The Center for Rheumatology and Bone Research

Wheaton, Maryland, United States

Site Status

Center For Pharmaceutical Research

Kansas City, Missouri, United States

Site Status

Drug Trials America

Hartsdale, New York, United States

Site Status

AMR Knoxville

Knoxville, Tennessee, United States

Site Status

Metroplex Clinical Research

Dallas, Texas, United States

Site Status

Pioneer Research Solutions

Sugar Land, Texas, United States

Site Status

Charlottesville Medical Research

Charlottesville, Virginia, United States

Site Status

Annapolis Rheumatology LLC

Fairfax, Virginia, United States

Site Status

Virginia Ispine Physicians PC

Richmond, Virginia, United States

Site Status

Novartis Investigative Site

Ciudad Autonoma de Bs As, , Argentina

Site Status

Novartis Investigative Site

Córdoba, , Argentina

Site Status

Novartis Investigative Site

San Miguel de Tucumán, , Argentina

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Novartis Investigative Site

Broadmeadow, New South Wales, Australia

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Novartis Investigative Site

Maroochydore, Queensland, Australia

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Novartis Investigative Site

Woodville South, South Australia, Australia

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Novartis Investigative Site

Hobart, Tasmania, Australia

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Novartis Investigative Site

Malvern East, Victoria, Australia

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Novartis Investigative Site

Christchurch, , Australia

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Novartis Investigative Site

St Leonards, , Australia

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Novartis Investigative Site

Waikanae Beach, , Australia

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Novartis Investigative Site

Québec, Quebec, Canada

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Novartis Investigative Site

Trois-Rivières, Quebec, Canada

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Novartis Investigative Site

Beijing, Beijing Municipality, China

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Novartis Investigative Site

Bengbu, , China

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Novartis Investigative Site

Brno, Czech Republic, Czechia

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Novartis Investigative Site

Pardubice, Czech Republic, Czechia

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Novartis Investigative Site

Brno-Zidonice, CZE, Czechia

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Novartis Investigative Site

Brno, , Czechia

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Novartis Investigative Site

Prague, , Czechia

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Novartis Investigative Site

Uherské Hradiště, , Czechia

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Novartis Investigative Site

Aarhus N, , Denmark

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Gandrup, , Denmark

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Novartis Investigative Site

Vejle, , Denmark

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Novartis Investigative Site

Tallinn, , Estonia

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Novartis Investigative Site

Tartu, , Estonia

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Novartis Investigative Site

Vadodara, Gujarat, India

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Novartis Investigative Site

Belagavi, Karnataka, India

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Novartis Investigative Site

Lucknow, Uttar Pradesh, India

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Novartis Investigative Site

Pune, , India

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Novartis Investigative Site

Shinagawa, Tokyo, Japan

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Novartis Investigative Site

Shinjuku Ku, Tokyo, Japan

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Novartis Investigative Site

Suginami, Tokyo, Japan

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Novartis Investigative Site

Chuoh-ku, , Japan

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Novartis Investigative Site

Osaka, , Japan

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Novartis Investigative Site

Guadalajara, Jalisco, Mexico

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Novartis Investigative Site

Culiacán, Sinaloa, Mexico

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Novartis Investigative Site

Ciudad de, , Mexico

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Novartis Investigative Site

Kielce, , Poland

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Novartis Investigative Site

Krakow, , Poland

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Novartis Investigative Site

Poznan, , Poland

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Novartis Investigative Site

Warsaw, , Poland

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Novartis Investigative Site

Santiago de Compostela, A Coruna, Spain

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Novartis Investigative Site

Sabadell, Barcelona, Spain

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Novartis Investigative Site

Barcelona, Catalonia, Spain

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Novartis Investigative Site

A Coruña, , Spain

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Novartis Investigative Site

Madrid, , Spain

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Novartis Investigative Site

Seville, , Spain

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Novartis Investigative Site

Changhua, , Taiwan

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Novartis Investigative Site

Tainan City, , Taiwan

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Novartis Investigative Site

Barnet, , United Kingdom

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Novartis Investigative Site

Glasgow, , United Kingdom

Site Status

Novartis Investigative Site

Norwich, , United Kingdom

Site Status

Countries

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United States Argentina Australia Canada China Czechia Denmark Estonia India Japan Mexico Poland Spain Taiwan United Kingdom

References

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Gerwin N, Scotti C, Halleux C, Fornaro M, Elliott J, Zhang Y, Johnson K, Shi J, Walter S, Li Y, Jacobi C, Laplanche N, Belaud M, Paul J, Glowacki G, Peters T, Wharton KA Jr, Vostiar I, Polus F, Kramer I, Guth S, Seroutou A, Choudhury S, Laurent D, Gimbel J, Goldhahn J, Schieker M, Brachat S, Roubenoff R, Kneissel M. Angiopoietin-like 3-derivative LNA043 for cartilage regeneration in osteoarthritis: a randomized phase 1 trial. Nat Med. 2022 Dec;28(12):2633-2645. doi: 10.1038/s41591-022-02059-9. Epub 2022 Dec 1.

Reference Type DERIVED
PMID: 36456835 (View on PubMed)

Other Identifiers

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2020-004897-22

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-509937-37-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

CLNA043A12202

Identifier Type: -

Identifier Source: org_study_id

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