Efficacy and Safety of Evinacumab in Adult Patients With Severe Hypertriglyceridemia for the Prevention of Recurrent Acute Pancreatitis

NCT ID: NCT04863014

Last Updated: 2024-05-22

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

21 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-07-12

Study Completion Date

2023-02-15

Brief Summary

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The primary objective of the study is to determine the proportion of patients with elevated triglycerides (TG), without familial chylomicronemia syndrome (FCS) due to loss of function (LoF) mutations in lipoprotein lipase (LPL), and a history of hypertriglyceridemia (HTG)-associated acute pancreatitis (AP) who experience a recurrent episode of AP after treatment with evinacumab versus placebo.

The secondary objectives of the study are:

* To determine the change in the standard lipid profile after therapy with evinacumab versus placebo
* To determine the changes in specialty lipoprotein parameters (ApoC3, ApoB48, ApoB100, and nuclear magnetic resonance \[NMR\] lipid profile) after therapy with evinacumab versus placebo
* To measure the number of AP episodes per patient
* To assess the safety and tolerability of evinacumab
* To assess the potential immunogenicity of evinacumab
* To assess the concentrations of total evinacumab and total angiopoietin-like 3 (ANGPTL3)

Detailed Description

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Conditions

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Hypertriglyceridemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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evinacumab

Randomized 1:1

Group Type EXPERIMENTAL

evinacumab

Intervention Type DRUG

Intravenous infusion every 4 weeks (Q4W)

Placebo

Randomized 1:1

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Intravenous infusion Q4W

Interventions

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evinacumab

Intravenous infusion every 4 weeks (Q4W)

Intervention Type DRUG

Placebo

Intravenous infusion Q4W

Intervention Type OTHER

Other Intervention Names

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REGN1500 Evkeeza™

Eligibility Criteria

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Inclusion Criteria

1. Adults without FCS due to LPL loss of function mutations
2. Documented history of 1 HTG-associated AP episode within 24 months of screening
3. Fasting serum TG value \>880 mg/dL (10 mmol/L) or \>500 mg/dL (5.6mmol/L) determined during the screening period as described in the protocol
4. Stable dose of lipid-lowering therapy (≥8 weeks) and willingness to maintain a stable regimen throughout the study
5. Body mass index ≥18.0 and ≤45.0 kg/m2
6. Compliance with a stable diet and exercise regimen at screening and willingness to continue the diet through the end of the study

Exclusion Criteria

1. Hospitalization for AP within 4 weeks of screening
2. Known genetic FCS defined as homozygous or compound heterozygous LoF mutations in LPL as defined in the protocol
3. Symptomatic gallstone disease within 6 months prior to screening as defined in the protocol
4. Use of any medication or nutraceutical known to alter serum lipids which has not been part of a stable therapeutic regimen for at least 8 weeks, and there are no plans to change the regimen during the study
5. Presence of any clinically significant, uncontrolled endocrine disease known to influence serum lipids as defined in the protocol
6. Has received a COVID-19 vaccination within 1-week of planned start medication or for which the planned COVID-19 vaccination would not be completed 1-week prior to start of the study
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Regeneron Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trial Management

Role: STUDY_DIRECTOR

Regeneron Pharmaceuticals

Locations

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Radin Cardivascular Medical Group, Inc

Newport Beach, California, United States

Site Status

Yale Cancer Center - Yale University

New Haven, Connecticut, United States

Site Status

Excel Medical Clinical Trials, LLC

Boca Raton, Florida, United States

Site Status

Harmony Medical Research Institute, Inc.

Hialeah, Florida, United States

Site Status

Northeast Georgia Medical Center

Gainesville, Georgia, United States

Site Status

NorthShore Medical Group

Evanston, Illinois, United States

Site Status

Advocate Medical Group Midwest Heart Specialists

Park Ridge, Illinois, United States

Site Status

Methodist Medical Center of Illiniois - UnityPoint Clinic

Peoria, Illinois, United States

Site Status

Quincy Medical Group

Quincy, Illinois, United States

Site Status

St. Vincent Medical Group, Inc.

Carmel, Indiana, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Johns Hopkins University School of Medicine

Baltimore, Maryland, United States

Site Status

Minneapolis Heart Institute

Minneapolis, Minnesota, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Saint Louis University

St Louis, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Northwell Health

Manhasset, New York, United States

Site Status

NYU Langone Hospital - Long Island

Mineola, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Mt Sinai - Ichan Medical Institute

New York, New York, United States

Site Status

Wake Forest University Health Sciences

Winston-Salem, North Carolina, United States

Site Status

University of Cincinnati Hospital

Cincinnati, Ohio, United States

Site Status

Penn Medicine: University of Pennsylvania Health System

Philadelphia, Pennsylvania, United States

Site Status

University Of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

University Diabetes & Endocrine Consultants

Chattanooga, Tennessee, United States

Site Status

Methodist Dallas Medical Center

Dallas, Texas, United States

Site Status

Sante Clinical Research

Kerrville, Texas, United States

Site Status

University of Washington

Seattle, Washington, United States

Site Status

MultiCare Institute for Research

Spokane, Washington, United States

Site Status

West Virginia University Heart & Vascular Institute

Morgantown, West Virginia, United States

Site Status

Wisconsin Center for Advanced Research - a division of GI Associates, LLC

Milwaukee, Wisconsin, United States

Site Status

Robarts Research Institute

London, Ontario, Canada

Site Status

Centre Etudes Cliniques Ecogene-21

Chicoutimi, Quebec, Canada

Site Status

Clinique des maladies lipidiques de Quebec

Québec, , Canada

Site Status

University Hospital Carl Gustav Carus

Dresden, , Germany

Site Status

University Hospital of Leipzig

Leipzig, , Germany

Site Status

Amsterdam University Medical Center (Amsterdam UMC), Academic Medical Center (AMC)

Amsterdam, , Netherlands

Site Status

Ziekenhuis Rijnstate

Arnhem, , Netherlands

Site Status

Countries

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United States Canada Germany Netherlands

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2021-000437-13

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

R1500-HTG-20118

Identifier Type: -

Identifier Source: org_study_id

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