Trial Outcomes & Findings for Pilot Decentralized Clinical Trial in Men and Pre and Post-menopausal Women With Breast Cancer and a Specific Mutation (PIK3CA) Treated With Alpelisib in Combination With Fulvestrant (NCT NCT04862143)

NCT ID: NCT04862143

Last Updated: 2024-06-20

Results Overview

The TFQ was designed to capture the patient's experience during a clinical trial. The questionnaire consisted of 23 questions that assessed various aspects of the trial experience. Each question in the TFQ scored on a scale ranging from 1 (representing the worst response) to 5 (representing the best response). To calculate the total score, the scores obtained from each of the 23 questions were summed up. The resulting sum represented the participant's total score, which could ranged from 23 (indicating the lowest possible score) to 115 (indicating the highest possible score).

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

2 participants

Primary outcome timeframe

Baseline, and on Day 1 of Cycle 4 and 7. Cycle= 28 days

Results posted on

2024-06-20

Participant Flow

The study was conducted in 1 center from Sweden

Participant milestones

Participant milestones
Measure
Alpelisib + Fulvestrant
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Overall Study
STARTED
2
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Alpelisib + Fulvestrant
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Overall Study
Adverse Event
1
Overall Study
Study terminated by sponsor
1

Baseline Characteristics

Race and Ethnicity were not collected from any participant.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Age, Continuous
54 Years
STANDARD_DEVIATION 0 • n=2 Participants
Sex/Gender, Customized
Unknown
2 Participants
n=2 Participants

PRIMARY outcome

Timeframe: Baseline, and on Day 1 of Cycle 4 and 7. Cycle= 28 days

Population: All enrolled participants who received at least one dose of any component of study treatment

The TFQ was designed to capture the patient's experience during a clinical trial. The questionnaire consisted of 23 questions that assessed various aspects of the trial experience. Each question in the TFQ scored on a scale ranging from 1 (representing the worst response) to 5 (representing the best response). To calculate the total score, the scores obtained from each of the 23 questions were summed up. The resulting sum represented the participant's total score, which could ranged from 23 (indicating the lowest possible score) to 115 (indicating the highest possible score).

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Participant Satisfaction Assessed Through the Trial Feedback Questionnaire (TFQ)
Baseline
99.5 Score on a Scale
Interval 92.0 to 107.0
Participant Satisfaction Assessed Through the Trial Feedback Questionnaire (TFQ)
Cycle 4 Day 1
89 Score on a Scale
Participant Satisfaction Assessed Through the Trial Feedback Questionnaire (TFQ)
Cycle 7 Day 1
98 Score on a Scale

SECONDARY outcome

Timeframe: At 3 and 6 months

Population: Participants receiving treatment at the specified time points

Patient retention on the DCT approach was calculated as the percentage of participants on remote monitoring for participants still on treatment

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=1 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Patient Retention on the Decentralized Clinical Trial (DCT) Approach
3 months
1 Participants
Patient Retention on the Decentralized Clinical Trial (DCT) Approach
6 months
1 Participants

SECONDARY outcome

Timeframe: From the date of the first study treatment up to the end of study, assessed up to 6 months

Population: All enrolled participants who received at least one dose of any component of study treatment

Unscheduled in-clinic visits were defined as visits that were originally intended to be conducted remotely but were ultimately carried out on-site, or visits that were not originally scheduled but took place on-site or at the local oncologist's (regional hospital). The total number of unscheduled in-clinic visits was evaluated

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Number of Unscheduled In-clinic Visits
0 Visits

SECONDARY outcome

Timeframe: From the date of the first study treatment up to the end of study, assessed up to 6 months

Population: All enrolled participants who received at least one dose of any component of study treatment

Unscheduled in-clinic visits were defined as visits that were originally intended to be conducted remotely but were ultimately carried out on-site, or visits that were not originally scheduled but took place on-site or at the local oncologist's (regional hospital). The total number of unscheduled in-clinic visits that were prompted by safety reasons was evaluated

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Number of Unscheduled In-clinic Visits Because of Safety Reasons
0 Visits
Interval 0.0 to 0.0

SECONDARY outcome

Timeframe: From the date of the first study treatment up to the end of study, assessed up to 6 months

Population: All enrolled participants who received at least one dose of any component of study treatment

Unscheduled in-clinic visits were defined as visits that were originally intended to be conducted remotely but were ultimately carried out on-site, or visits that were not originally scheduled but took place on-site or at the local oncologist's (regional hospital). The total number of unscheduled in-clinic visits per participants was evaluated

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Number of Unscheduled In-clinic Visits Per Participant in the Study
0 Visits per participant
Interval 0.0 to 0.0

SECONDARY outcome

Timeframe: From the date of the first study treatment up to the end of treatment, assessed up to 6 months

Population: All enrolled participants who received at least one dose of any component of study treatment

An AE refers to any untoward medical occurrence, such as an unfavorable and unintended sign (including abnormal laboratory findings), symptom, or disease. The number of participants who discontinued the treatment due to adverse events was evaluated

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Number of Participants Who Discontinue Treatment Due to Adverse Events (AEs)
1 Participants

SECONDARY outcome

Timeframe: From the date of the first study treatment up to the end of treatment, assessed up to 6 months

Population: All enrolled participants who received at least one dose of any study treatment

Number of participants with dose reductions and interruptions for alpelisib

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Number of Participants With Dose Reductions/Interruptions for Alpelisib
Dose interruptions
1 Participants
Number of Participants With Dose Reductions/Interruptions for Alpelisib
Dose reductions
1 Participants

SECONDARY outcome

Timeframe: From the date of the first study treatment up to the end of study, assessed up to 6 months

Population: All enrolled participants who received at least one dose of any study treatment

AESIs (Adverse Events of Special Interest) are defined as events, whether serious or non-serious, that are of scientific and medical concern specific to the sponsor's product or program. These events may require ongoing monitoring and communication by the investigator to the sponsor. For this study, the following AESIs were defined: hyperglycemia, rash, and diarrhea. The number of participants experiencing these events per the Common Terminology Criteria for Adverse Events (CTCAE) v4.03 was evaluated.

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Number of Participants With Adverse Events of Special Interest (AESIs)- Hyperglycemia, Rash and Diarrhea
Diarrhea
1 Participants
Number of Participants With Adverse Events of Special Interest (AESIs)- Hyperglycemia, Rash and Diarrhea
Hyperglycaemia
2 Participants
Number of Participants With Adverse Events of Special Interest (AESIs)- Hyperglycemia, Rash and Diarrhea
Rash
0 Participants

SECONDARY outcome

Timeframe: From the date of the first study treatment up to the end of study, assessed up to 6 months

Population: All enrolled participants who received at least one dose of any study treatment

An AE refers to any untoward medical occurrence, such as an unfavorable and unintended sign (including abnormal laboratory findings), symptom, or disease. The number of participants with AEs per the Common Terminology Criteria for Adverse Events (CTCAE) v4.03 leading to in-clinic visits was assessed.

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Number of Participants With Adverse Events (AEs) Leading to In-clinic Visits
0 Participants

SECONDARY outcome

Timeframe: Baseline, and on Day 1 of Cycle 4, and 7 and end of treatment, assessed up to 6 months. Cycle= 28 days

Population: All enrolled participants who received at least one dose of any study treatment. Number analyzed indicates the number of participants with data available at the designated time point.

The EORTC QLQ-C30 questionnaire contained 30 items and was composed of both multi-item scales and single item measures. These included five functional scales (physical, role, emotional, cognitive, and social functioning), three symptom scales (fatigue, nausea/vomiting, and pain), six single items (dyspnea, insomnia, appetite loss, constipation, diarrhea, and financial impact), and a global health status/quality of life (QoL) scale. All of the scales and single items ranged from 0 to 100. A high scale score represented a higher response level. Thus, a high score for a functional scale indicated a high/healthy level of functioning, a high score for the QoL indicated high QoL, but a high score for a symptom scale/single item indicated a high level of symptomatology/problems. The EORTC QLQ-C30 scores for all functional and symptom scales were evaluated

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
QoL- Baseline
75 Score on a Scale
Interval 67.0 to 83.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
QoL- Cycle 4 Day 1
83 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
QoL- Cycle 7 Day 1
92 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
QoL- End of Treatment
75 Score on a Scale
Interval 67.0 to 83.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Physical Functioning- Baseline
90 Score on a Scale
Interval 80.0 to 100.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Physical Functioning- Cycle 4 Day 1
93 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Physical Functioning- Cycle 7 Day 1
100 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Physical Functioning-End of Treatment
86.5 Score on a Scale
Interval 80.0 to 93.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Role Functioning- Baseline
91.5 Score on a Scale
Interval 83.0 to 100.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Role Functioning- Cycle 4 Day 1
100 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Role Functioning- Cycle 7 Day 1
100 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Role Functioning-End of Treatment
83.5 Score on a Scale
Interval 67.0 to 100.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Emotional Functioning- Baseline
71 Score on a Scale
Interval 67.0 to 75.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Emotional Functioning- Cycle 4 Day 1
83 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Emotional Functioning- Cycle 7 Day 1
92 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Emotional Functioning- End of treatment
83 Score on a Scale
Interval 83.0 to 83.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Cognitive Functioning- Baseline
91.5 Score on a Scale
Interval 83.0 to 100.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Cognitive Functioning- Cycle 4 Day 1
100 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Cognitive Functioning- Cycle 7 Day 1
100 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Cognitive Functioning- End of treatment
75 Score on a Scale
Interval 67.0 to 83.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Social Functioning- Baseline
91.5 Score on a Scale
Interval 83.0 to 100.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Social Functioning- Cycle 4 Day 1
100 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Social Functioning- Cycle 7 Day 1
100 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Social Functioning- End of treatment
91.5 Score on a Scale
Interval 83.0 to 100.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Fatigue- Baseline
22 Score on a Scale
Interval 0.0 to 44.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Fatigue- Cycle 4 Day 1
22 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Fatigue- Cycle 7 Day 1
0 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Fatigue- End of treatment
33 Score on a Scale
Interval 22.0 to 44.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Nausea/vomiting- Baseline
0 Score on a Scale
Interval 0.0 to 0.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Nausea/vomiting- Cycle 4 Day 1
17 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Nausea/vomiting- Cycle 7 Day 1
0 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Nausea/vomiting- End of treatment
0 Score on a Scale
Interval 0.0 to 0.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Pain- Baseline
8.5 Score on a Scale
Interval 0.0 to 17.0
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Pain- Cycle 4 Day 1
0 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Pain- Cycle 7 Day 1
0 Score on a Scale
European Organisation for Research and Treatment of Cancer Quality of Life Questionnaire Core 30 (EORTC QLQ-C30)
Pain- End of treatment
16.5 Score on a Scale
Interval 0.0 to 33.0

SECONDARY outcome

Timeframe: Baseline, and on Day 1 of Cycle 4, and 7 and end of treatment, assessed up to 6 months. Cycle= 28 days

Population: All enrolled participants who received at least one dose of any study treatment. Number analyzed indicates the number of participants with data available at the designated time point.

The 5-level EQ-5D (EQ-5D-5L) questionnaire is a standardized measure of health status. The EQ-5D descriptive system comprises of the 5 following dimensions: mobility, self-care, usual activities, pain/discomfort and anxiety/depression. Along with the five dimensions of health, the EQ-5D-5L includes a VAS where respondents rate their overall health status on a scale from 0 to 100, where 0 represents the worst possible health state and 100 represents the best possible health state. The EQ-5D-5L VAS scores were evaluated

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
EuroQol 5-Dimension 5-Level (EQ-5D-5L)- Visual Analog Scale (VAS) Score
Baseline
80 Score on a scale
Interval 75.0 to 85.0
EuroQol 5-Dimension 5-Level (EQ-5D-5L)- Visual Analog Scale (VAS) Score
Cycle 4 Day 1
93 Score on a scale
EuroQol 5-Dimension 5-Level (EQ-5D-5L)- Visual Analog Scale (VAS) Score
Cycle 7 Day 1
95 Score on a scale
EuroQol 5-Dimension 5-Level (EQ-5D-5L)- Visual Analog Scale (VAS) Score
End of treatment
82.5 Score on a scale
Interval 70.0 to 95.0

SECONDARY outcome

Timeframe: Baseline, and on Day 1 of Cycle 4, and 7 and end of treatment, assessed up to 6 months. Cycle= 28 days

Population: All enrolled participants who received at least one dose of any study treatment. Number analyzed indicates the number of participants with data available at the designated time point.

The BPI-SF was a questionnaire used to assess pain intensity and interference with daily activities. The Pain Severity Subscale included four questions asking individuals to rate their pain intensity on a scale from 0 to 10, with higher scores indicating more severe pain. The Pain Interference Subscale consisted of seven items that assessed how pain had interfered with activities, rated on the same scale. Both subscales had a total score range of 0 to 10, with higher scores indicating more significant pain or interference.

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Brief Pain Inventory Short Form (BPI-SF) Scores
Pain severity- Baseline
1.63 Score on a scale
Interval 1.25 to 2.0
Brief Pain Inventory Short Form (BPI-SF) Scores
Pain severity- Cycle 4 Day 1
0 Score on a scale
Brief Pain Inventory Short Form (BPI-SF) Scores
Pain severity- Cycle 7 Day 1
0.75 Score on a scale
Brief Pain Inventory Short Form (BPI-SF) Scores
Pain severity- End of treatment
1.13 Score on a scale
Interval 0.0 to 2.25
Brief Pain Inventory Short Form (BPI-SF) Scores
Pain interference- Baseline
0.79 Score on a scale
Interval 0.0 to 1.57
Brief Pain Inventory Short Form (BPI-SF) Scores
Pain interference- Cycle 4 Day 1
0 Score on a scale
Brief Pain Inventory Short Form (BPI-SF) Scores
Pain interference- Cycle 7 Day 1
0 Score on a scale
Brief Pain Inventory Short Form (BPI-SF) Scores
Pain interference- End of treatment
1.07 Score on a scale
Interval 0.0 to 2.14

SECONDARY outcome

Timeframe: Up to 6 months

Population: All enrolled participants who received at least one dose of any component of study treatment

The number of participants with PFS was defined as the count of participants who did not experience disease progression or death due to any cause during the study. Progression was assessed by the Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 based on local radiology review.

Outcome measures

Outcome measures
Measure
Alpelisib + Fulvestrant
n=2 Participants
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Number of Participants With Progression-free Survival (PFS) According to RECIST 1.1
2 Participants

Adverse Events

Alpelisib + Fulvestrant

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Alpelisib + Fulvestrant
n=2 participants at risk
Participants were administered alpelisib at a daily dose of 300 mg for 12 cycles of 28 days and fulvestrant at a dose of 500 mg via intramuscular injection on Cycle 1 Day 1 and Cycle 1 Day 15, and Day 1 of each subsequent cycle up to Cycle 12. Pre-menopausal women also received goserelin at a dose of 3.6 mg on Day 1 of each cycle.
Metabolism and nutrition disorders
Hyperglycaemia
100.0%
2/2 • From start up to end of study, assessed up to 6 months
General disorders
Fatigue
100.0%
2/2 • From start up to end of study, assessed up to 6 months
Gastrointestinal disorders
Nausea
100.0%
2/2 • From start up to end of study, assessed up to 6 months
Gastrointestinal disorders
Abdominal pain
50.0%
1/2 • From start up to end of study, assessed up to 6 months
Skin and subcutaneous tissue disorders
Alopecia
50.0%
1/2 • From start up to end of study, assessed up to 6 months
Metabolism and nutrition disorders
Decreased appetite
50.0%
1/2 • From start up to end of study, assessed up to 6 months
Gastrointestinal disorders
Diarrhea
50.0%
1/2 • From start up to end of study, assessed up to 6 months
Gastrointestinal disorders
Dry mouth
50.0%
1/2 • From start up to end of study, assessed up to 6 months
Gastrointestinal disorders
Gastritis
50.0%
1/2 • From start up to end of study, assessed up to 6 months
Gastrointestinal disorders
Stomatitis
50.0%
1/2 • From start up to end of study, assessed up to 6 months
Investigations
Weight decreased
50.0%
1/2 • From start up to end of study, assessed up to 6 months

Additional Information

Study director

Novartis Pharmaceuticals

Phone: 862-778-8300

Results disclosure agreements

  • Principal investigator is a sponsor employee The terms and conditions of Novartis' agreements with its investigators may vary. However, Novartis does not prohibit any investigator from publishing. Any publications from a single-site are postponed until the publication of the pooled data (ie, data from all sites) in the clinical trial.
  • Publication restrictions are in place

Restriction type: OTHER