Frequency of SOD1 and C9orf72 Gene Mutations in French ALS

NCT ID: NCT04819555

Last Updated: 2023-11-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

1000 participants

Study Classification

OBSERVATIONAL

Study Start Date

2021-04-30

Study Completion Date

2023-05-15

Brief Summary

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The purpose of the study is to determine the frequency of mutations in the C9orf72 and SOD1 genes in the incident population of ALS patients followed in the FILSLAN centres

Detailed Description

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After obtaining free and informed consent for genetic characteristic tests, a blood sample will be taken during hospitalisation for diagnostic confirmation or during the quarterly multidisciplinary consultations planned for these patients in the classic follow-up set up within the ALS centres of the FILSLAN network if the genetic status is not already known. This sample will be integrated into the standard management of ALS patients, which includes a neurological examination and paraclinical explorations, including a biological assessment.

The patient will then be reviewed during the standard multidisciplinary follow-up consultations. Information to the patient on his or her C9orf72 or SOD1 genetic status will be included in the quarterly multidisciplinary consultations for the classic follow-up of ALS patients.

It should also be noted that the data (ALSFRS-r score, weight, FEV) collected during the 6 and 12 month consultations will be processed for the purposes of this research.

For patients included in the quarterly multidisciplinary consultations planned in the classic follow-up, if the genetic blood sample was taken during the initial hospitalisation for diagnosis, then it will not be repeated in the framework of the research. In this case, the genetic status of C9orf72 or SOD1 will be available at the inclusion visit and the patient will receive specific information about his or her genetic status.

Consent for the research will nevertheless be obtained in order to have the patient's agreement to the processing of their health data for the purposes of the research at inclusion, 6 months and 12 months.

Conditions

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Amyotrophic Lateral Sclerosis

Keywords

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Blood sample Genetic features

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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adult patients with ALS

incident population of ALS patients followed in the FILSLAN centres.

Blood

Intervention Type GENETIC

a blood sample will be taken during hospitalisation for diagnostic confirmation or during the quarterly multidisciplinary consultations scheduled as part of the standard follow-up set up for these patients in the ALS centres of the FILSLAN network. If the genetic status is not yet known, this sample will be taken (1 tube of 7mL EDTA) and then sent within 24-48 hours at room temperature to one of the 3 participating molecular biology laboratories according to the criteria defined in the manual of samples being taken in the 3 laboratories.

Interventions

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Blood

a blood sample will be taken during hospitalisation for diagnostic confirmation or during the quarterly multidisciplinary consultations scheduled as part of the standard follow-up set up for these patients in the ALS centres of the FILSLAN network. If the genetic status is not yet known, this sample will be taken (1 tube of 7mL EDTA) and then sent within 24-48 hours at room temperature to one of the 3 participating molecular biology laboratories according to the criteria defined in the manual of samples being taken in the 3 laboratories.

Intervention Type GENETIC

Eligibility Criteria

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Inclusion Criteria

* Adult aged ≥ 18 years old
* ALS defined, probable or likely based on neurophysiological data according to Airlie House criteria (Brooks, 2000)
* Sporadic ALS or familial ALS defined by the existence of a case of ALS or FTD among first or second degree relatives of the patient included (Byrne et al, 2011).
* Participant affiliated to a social security scheme
* Free, informed and signed consent for the examination of the genetic characteristics of the participant

Exclusion Criteria

* All conditions mimicking ALS including motor neuropathies with multiple conduction blocks and all cases of ALS that do not meet the criteria of the Airlie House classification.
* Patients who are cognitively incapable of signing the consent to participate in this study.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biogen

INDUSTRY

Sponsor Role collaborator

University Hospital, Tours

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Philippe CORCIA

Role: PRINCIPAL_INVESTIGATOR

University Hospital, Tours

Locations

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CHU Angers

Angers, , France

Site Status

CHU Bordeaux

Bordeaux, , France

Site Status

CHU de Brest

Brest, , France

Site Status

CHU Lyon

Bron, , France

Site Status

CHU Caen

Caen, , France

Site Status

CHU Clermont Ferrand

Clermont-Ferrand, , France

Site Status

CHU Dijon

Dijon, , France

Site Status

CHU Lille

Lille, , France

Site Status

CHU Limoges

Limoges, , France

Site Status

CHU Marseille

Marseille, , France

Site Status

CHU Montpellier

Montpellier, , France

Site Status

CHU Nancy

Nancy, , France

Site Status

CHU Nice

Nice, , France

Site Status

Paris - Groupe hospitalier de la Pitié Salpetrière

Paris, , France

Site Status

CHU de Rennes

Rennes, , France

Site Status

CHU La Réunion

Saint-Pierre, , France

Site Status

CHU St Etienne

Saint-Priest-en-Jarez, , France

Site Status

CHU Strasbourg

Strasbourg, , France

Site Status

CHU Toulouse

Toulouse, , France

Site Status

University hospital

Tours, , France

Site Status

Countries

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France

Other Identifiers

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RIPH3-RNI20-GENIALS

Identifier Type: -

Identifier Source: org_study_id