Trial Outcomes & Findings for Pevonedistat and Pembrolizumab for the Treatment of dMMR/MSI-H Metastatic or Locally Advanced Unresectable Solid Tumor (NCT NCT04800627)

NCT ID: NCT04800627

Last Updated: 2022-12-27

Results Overview

Recruitment status

TERMINATED

Study phase

PHASE1/PHASE2

Target enrollment

2 participants

Primary outcome timeframe

21 days

Results posted on

2022-12-27

Participant Flow

Company stopped development of the drug and shut down the entire program with pevonedistat. Takeda had a negative phase III of the agent in liquid tumors and thus shut the program. It was not due to any toxicity, but lack of path for FDA indication.

Participant milestones

Participant milestones
Measure
Treatment (Pevonedistat, Pembrolizumab)
Patients receive pevonedistat IV over 60 minutes on days 1, 3, and 5, and pembrolizumab IV over 30 minutes on day 1. Cycles repeat every 21 days in the absence of disease progression or unacceptable toxicity.
Overall Study
STARTED
2
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
2

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Pevonedistat and Pembrolizumab for the Treatment of dMMR/MSI-H Metastatic or Locally Advanced Unresectable Solid Tumor

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Treatment (Pevonedistat, Pembrolizumab)
n=2 Participants
Patients receive pevonedistat IV over 60 minutes on days 1, 3, and 5, and pembrolizumab IV over 30 minutes on day 1. Cycles repeat every 21 days in the absence of disease progression or unacceptable toxicity.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
1 Participants
n=5 Participants
Age, Categorical
>=65 years
1 Participants
n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
Sex: Female, Male
Male
2 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
2 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Region of Enrollment
United States
2 participants
n=5 Participants

PRIMARY outcome

Timeframe: 21 days

Population: No data collected due to early termination of the protocol.

Outcome measures

Outcome data not reported

PRIMARY outcome

Timeframe: Through study completion, an average of 1 year

Population: No data collected due to early termination of the protocol.

Will be assessed by immune modified Response Evaluation Criteria in Solid Tumors (iRECIST) version (v) 1.1.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 24 weeks

Population: No data collected due to early termination of the protocol.

Will analyze the pharmacodynamics impact of pevonedistat by evaluating changes in protein misfolding between pre-treatment and on-treatment tumor biopsies.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Through study completion, an average of 1 year

Population: No data collected due to early termination of the protocol.

Will be assessed by iRECIST v1.1. Will be estimated using the method of Kaplan and Meier.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Through study completion, an average of 1 year

Population: No data collected due to early termination of the protocol.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Through study completion, an average of 1 year

Population: No data collected due to early termination of the protocol.

Will be estimated using the method of Kaplan and Meier.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Through study completion, an average of 1 year

Population: No data collected due to early termination of the protocol.

Outcome measures

Outcome data not reported

Adverse Events

Treatment (Pevonedistat, Pembrolizumab)

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Dr. Michael Overman,MD- Assoc VP, CN Research, SVP, Cancer NW Clin & Acad Dev

UT MD Anderson Cancer Center

Phone: (713) 792-2828

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place