A Safety, Tolerability, and Efficacy Study of VX-880 in Participants With Type 1 Diabetes

NCT ID: NCT04786262

Last Updated: 2025-08-01

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

52 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-03-29

Study Completion Date

2030-06-30

Brief Summary

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This study will evaluate the safety, tolerability and efficacy of VX-880 infusion in participants with Type 1 diabetes (T1D) and impaired awareness of hypoglycemia (IAH) and severe hypoglycemia.

Detailed Description

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Conditions

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Diabetes Mellitus, Type 1 Impaired Hypoglycemic Awareness Severe Hypoglycemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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VX-880

Group Type EXPERIMENTAL

VX-880

Intervention Type BIOLOGICAL

Infused into the hepatic portal vein.

Interventions

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VX-880

Infused into the hepatic portal vein.

Intervention Type BIOLOGICAL

Other Intervention Names

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Zimislecel Formerly known as STx-02

Eligibility Criteria

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Inclusion Criteria

* Clinical history of T1D with \> 5 years of duration of insulin dependence
* At least two episodes of documented severe hypoglycemia in the 12 months prior to enrollment
* Stable diabetic treatment
* Consistent use of continuous glucose monitor (CGM) for at least 3 months before Screening and willingness to use CGM for the duration of the study

Exclusion Criteria

-Prior islet cell transplant, organ transplant, or cell therapy
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Vertex Pharmaceuticals Incorporated

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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City of Hope

Duarte, California, United States

Site Status RECRUITING

University of California San Francisco

San Francisco, California, United States

Site Status RECRUITING

UHealth Diabetes Research Institute

Miami, Florida, United States

Site Status RECRUITING

Northwestern Organ Transplant Center

Chicago, Illinois, United States

Site Status COMPLETED

University of Chicago

Chicago, Illinois, United States

Site Status RECRUITING

Johns Hopkins University

Baltimore, Maryland, United States

Site Status RECRUITING

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status RECRUITING

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status RECRUITING

University of Pittsburgh Medical Center Montefiore

Pittsburgh, Pennsylvania, United States

Site Status RECRUITING

Baylor Scott and White Research Institute

Dallas, Texas, United States

Site Status RECRUITING

VCU Medical Center, Richmond

Richmond, Virginia, United States

Site Status RECRUITING

University of Wisconsin

Madison, Wisconsin, United States

Site Status RECRUITING

University of Alberta, Edmonton

Edmonton, , Canada

Site Status RECRUITING

McGill University Health Centre

Montreal, , Canada

Site Status RECRUITING

Toronto General Hospital (TGH)

Toronto, , Canada

Site Status RECRUITING

Vancouver General Hospital

Vancouver, , Canada

Site Status RECRUITING

CHU Lille

Lille, , France

Site Status RECRUITING

Centre de recherche en Biomédecine de Strasbourg

Strasbourg, , France

Site Status RECRUITING

Dresden Center for Islet Transplantation

Dresden, , Germany

Site Status RECRUITING

IRCCS Ospedale San Raffaele

Milan, , Italy

Site Status RECRUITING

Leiden University

Leiden, , Netherlands

Site Status RECRUITING

Oslo University Hospital

Oslo, , Norway

Site Status RECRUITING

King Abdullah International Medical Research Center (KAIMRC) - Riyadh - Endocrinology

Riyadh, , Saudi Arabia

Site Status RECRUITING

King Faisal Specialist Hospital & Research Centre - Riyadh - Endocrinology

Riyadh, , Saudi Arabia

Site Status RECRUITING

Hopiteaux Universitaires de Geneve

Geneva, , Switzerland

Site Status RECRUITING

Churchill Hospital

Headington, Oxford, United Kingdom

Site Status RECRUITING

Royal Infirmary of Edinburgh

Edinburgh, , United Kingdom

Site Status RECRUITING

Cardiovascular, Metabolic Medicine and Sciences, King's College London

London, , United Kingdom

Site Status RECRUITING

The Newcastle upon Tyne Hospitals NHS Foundation Trust

Newcastle upon Tyne, , United Kingdom

Site Status RECRUITING

Countries

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United States Canada France Germany Italy Netherlands Norway Saudi Arabia Switzerland United Kingdom

Central Contacts

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Medical Information

Role: CONTACT

617-341-6777

References

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Reichman TW, Markmann JF, Odorico J, Witkowski P, Fung JJ, Wijkstrom M, Kandeel F, de Koning EJP, Peters AL, Mathieu C, Kean LS, Bruinsma BG, Wang C, Mascia M, Sanna B, Marigowda G, Pagliuca F, Melton D, Ricordi C, Rickels MR; VX-880-101 FORWARD Study Group. Stem Cell-Derived, Fully Differentiated Islets for Type 1 Diabetes. N Engl J Med. 2025 Sep 4;393(9):858-868. doi: 10.1056/NEJMoa2506549. Epub 2025 Jun 20.

Reference Type DERIVED
PMID: 40544428 (View on PubMed)

Other Identifiers

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2024-513929-23-00

Identifier Type: OTHER

Identifier Source: secondary_id

VX20-880-101

Identifier Type: -

Identifier Source: org_study_id

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