OPT-302 With Aflibercept in Neovascular Age-related Macular Degeneration (nAMD)

NCT ID: NCT04757636

Last Updated: 2025-08-05

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

998 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-03-12

Study Completion Date

2025-03-31

Brief Summary

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A 2-year phase 3, multicentre, randomised, parallel-group, sham-controlled, double-masked study. Primary efficacy will be determined at Week 52.

Detailed Description

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Conditions

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Neovascular Age-related Macular Degeneration

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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2.0 mg aflibercept with Standard Dosing 2.0 mg OPT-302

2.0 mg aflibercept intravitreal injection administered at 4-weekly intervals for three treatments, and then at 8-weekly intervals.

2.0 mg OPT-302 intravitreal injection administered at 4-weekly intervals.

Group Type EXPERIMENTAL

2.0 mg OPT-302

Intervention Type BIOLOGICAL

intravitreal injection

2.0 aflibercept

Intervention Type BIOLOGICAL

intravitreal injection

2.0 mg aflibercept with Extended Dosing 2.0 mg OPT-302

2.0 mg aflibercept intravitreal injection administered at 4-weekly intervals for three treatments, and then at 8-weekly intervals.

2.0 mg OPT-302 intravitreal injection administered at 4-weekly intervals for three treatments, and then at 8-weekly intervals, with sham intravitreal injection administered at visits when OPT-302 is not.

Group Type EXPERIMENTAL

2.0 mg OPT-302

Intervention Type BIOLOGICAL

intravitreal injection

2.0 aflibercept

Intervention Type BIOLOGICAL

intravitreal injection

2.0 mg aflibercept with sham

2.0 mg aflibercept intravitreal injection administered at 4-weekly intervals for three treatments, and then at 8-weekly intervals.

Sham intravitreal injection administered at 4-weekly intervals.

Group Type SHAM_COMPARATOR

2.0 aflibercept

Intervention Type BIOLOGICAL

intravitreal injection

Sham

Intervention Type PROCEDURE

intravitreal injection

Interventions

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2.0 mg OPT-302

intravitreal injection

Intervention Type BIOLOGICAL

2.0 aflibercept

intravitreal injection

Intervention Type BIOLOGICAL

Sham

intravitreal injection

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

* Active subfoveal CNV lesion or juxtafoveal CNV lesion with foveal involvement that is secondary to AMD in the Study Eye.
* An ETDRS BCVA score between 60 and 25 (inclusive) letters in the Study Eye.

Exclusion Criteria

* Any previous treatment for neovascular AMD.
* Clinically significant ocular disorders (other than neovascular AMD), which may interfere with assessment of BCVA, assessment of safety, or fundus imaging.
* Any current (or history of a) social, psychological, or medical condition that precludes enrolment into the study.
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Opthea Limited

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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COAST Investigational Site

Phoenix, Arizona, United States

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Arcadia, California, United States

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Huntington Beach, California, United States

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Redlands, California, United States

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Sacramento, California, United States

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Danbury, Connecticut, United States

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Altamonte Springs, Florida, United States

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Boynton Beach, Florida, United States

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Coral Springs, Florida, United States

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Melbourne, Florida, United States

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Orlando, Florida, United States

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Plantation, Florida, United States

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Sarasota, Florida, United States

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St. Petersburg, Florida, United States

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Stuart, Florida, United States

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Winter Haven, Florida, United States

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Marietta, Georgia, United States

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‘Aiea, Hawaii, United States

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Chicago, Illinois, United States

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Springfield, Illinois, United States

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Urbana, Illinois, United States

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New Albany, Indiana, United States

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Lenexa, Kansas, United States

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Prairie Village, Kansas, United States

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West Monroe, Louisiana, United States

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Hagerstown, Maryland, United States

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Owings Mills, Maryland, United States

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Boston, Massachusetts, United States

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Worcester, Massachusetts, United States

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Jackson, Mississippi, United States

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Independence, Missouri, United States

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St Louis, Missouri, United States

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Edison, New Jersey, United States

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Albuquerque, New Mexico, United States

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Shirley, New York, United States

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Asheville, North Carolina, United States

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Wilmington, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Cincinnati, Ohio, United States

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Dayton, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Springfield, Oregon, United States

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Kingston, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Greenville, South Carolina, United States

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West Columbia, South Carolina, United States

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Rapid City, South Dakota, United States

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Germantown, Tennessee, United States

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Knoxville, Tennessee, United States

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Abilene, Texas, United States

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Austin, Texas, United States

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Burleson, Texas, United States

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Conroe, Texas, United States

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Dallas, Texas, United States

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Plano, Texas, United States

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Round Rock, Texas, United States

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Fairfax, Virginia, United States

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Bellevue, Washington, United States

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Spokane, Washington, United States

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Morgantown, West Virginia, United States

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Rosario, Santa Fe Province, Argentina

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Rosario, Sante Fe, Argentina

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Ciudad Autonoma de Buenos Aire, , Argentina

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Ciudad Autonoma de Buenos Aire, , Argentina

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Ciudad Autonoma de Buenos Aire, , Argentina

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Mendoza, , Argentina

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Liverpool, New South Wales, Australia

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Parramatta, New South Wales, Australia

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Strathfield, New South Wales, Australia

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Adelaide, South Australia, Australia

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East Melbourne, Victoria, Australia

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Rowville, Victoria, Australia

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Graz, , Austria

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Belo Horizonte, Minas Gerais, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Sofia, , Bulgaria

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Stara Zagora, , Bulgaria

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Brampton, Ontario, Canada

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North York, Ontario, Canada

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Ottawa, Ontario, Canada

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Ottawa, Ontario, Canada

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Medellín, Antioquia, Colombia

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Bogotá, Cundinamarca, Colombia

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Cali, Valle del Cauca Department, Colombia

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Barranquilla, , Colombia

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Bogotá, , Colombia

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Cali, , Colombia

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Medellín, , Colombia

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Osijek, , Croatia

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Osijek, , Croatia

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Split, , Croatia

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Zagreb, , Croatia

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Hradec Králové, Cech Republic, Czechia

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Brno, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Praha 4-Krc, , Czechia

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Roskilde, , Denmark

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Tallinn, , Estonia

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Tallinn, , Estonia

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Tallinn, , Estonia

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Lyon, Rhone, France

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Poitiers, Vienne, France

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Dijon, , France

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Paris, , France

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Tübingen, Baden Wu, Germany

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Cologne, North Rhine-Westphalia, Germany

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Mainz, Rhineland-Palatinate, Germany

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Berlin, , Germany

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Athens, , Greece

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Heraklion, , Greece

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Larissa, , Greece

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Thessaloniki, , Greece

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Nyíregyháza, , Hungary

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Pécs, , Hungary

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Pécs, , Hungary

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Zalaegerszeg, , Hungary

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Hyderabad, Andhra Pradesh, India

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Ranchi, Jharkhand, India

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Mysore, Karnataka, India

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Nashik, Maharashtra, India

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Bhubaneswar, Odisha, India

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Madurai, Tamil Nadu, India

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Afula, , Israel

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Haifa, , Israel

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Haifa, , Israel

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Jerusalem, , Israel

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Jerusalem, , Israel

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Rehovot, , Israel

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Tel Aviv, , Israel

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Ancona, Perugia, Italy

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Florence, , Italy

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Milan, , Italy

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Milan, , Italy

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Milan, , Italy

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Pisa, , Italy

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Roma, , Italy

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Rome, , Italy

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Rozzano, , Italy

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Riga, , Latvia

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Riga, , Latvia

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Kaunas, , Lithuania

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Klaipėda, , Lithuania

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Vilnius, , Lithuania

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Nijmegen, , Netherlands

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Rotterdam, , Netherlands

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Tilburg, , Netherlands

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Santo Tomas, Batangas, Philippines

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Makati, , Philippines

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Makati City, , Philippines

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Pasig, , Philippines

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Quezon City, , Philippines

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Bielsko-Biala, , Poland

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Bydgoszcz, , Poland

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Bydgoszcz, , Poland

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Bytom, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Olsztyn, , Poland

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Poznan, , Poland

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Arecibo, , Puerto Rico

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Bratislava, , Slovakia

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Trebišov, , Slovakia

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Trenčín, , Slovakia

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Žilina, , Slovakia

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Seongnam-si, Gyeonggi-do, South Korea

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Suwon, Gyeonggi-do, South Korea

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Busan, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Soeul, , South Korea

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Badalona, Barcelona, Spain

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Majadahonda, Madrid, Spain

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Oviedo, Principality of Asturias, Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Madrid, , Spain

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Valencia, , Spain

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Zaragoza, , Spain

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Zaragoza, , Spain

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Kaohsiung City, , Taiwan

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Kaohsiung City, , Taiwan

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Taichung, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taoyuan, , Taiwan

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Plymouth, Devon, United Kingdom

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Westcliff-on-Sea, Essex, United Kingdom

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Manchester, Greater Manchester, United Kingdom

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Liverpool, Merseyside, United Kingdom

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Gorleston-on-Sea, Norfolk, United Kingdom

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Frimley, Surrey, United Kingdom

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Sunderland, Tyne and Wear, United Kingdom

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Leeds, West Yorkshire, United Kingdom

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London, , United Kingdom

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Countries

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United States Argentina Australia Austria Brazil Bulgaria Canada Colombia Croatia Czechia Denmark Estonia France Germany Greece Hungary India Israel Italy Latvia Lithuania Netherlands Philippines Poland Puerto Rico Slovakia South Korea Spain Taiwan United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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OPT-302-1005

Identifier Type: -

Identifier Source: org_study_id

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