A Study of Bempegaldesleukin (BEMPEG: NKTR-214) in Combination With Nivolumab in Children, Adolescents and Young Adults With Recurrent or Treatment-resistant Cancer

NCT ID: NCT04730349

Last Updated: 2023-03-24

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE1/PHASE2

Total Enrollment

15 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-06-03

Study Completion Date

2022-06-22

Brief Summary

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The purpose of this study is to first, in Part A, assess the safety, tolerability and drug levels of Bempegaldesleukin (BEMPEG) in combination with nivolumab and then, in Part B, to estimate the preliminary efficacy in children, adolescents and young adults with recurrent or treatment-resistant cancer.

Detailed Description

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Conditions

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Ependymoma Ewing Sarcoma High-grade Glioma Leukemia and Lymphoma Medulloblastoma Miscellaneous Brain Tumors Miscellaneous Solid Tumors Neuroblastoma Relapsed, Refractory Malignant Neoplasms Rhabdomyosarcoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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A1W Dosing schema

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

A1F Dosing schema

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

A2W Dosing schema

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

A2F Dosing schema

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

Part B: Cohort B1 Neuroblastoma

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

Part B: Cohort B2 Ewing sarcoma

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

Part B: Cohort B3 Rhabdomyosarcoma

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

Part B: Cohort B4 Miscellaneous solid tumors

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

Part B: Cohort B5 NHL/leukemia

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

Part B: Cohort B6 High-grade glioma

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

Part B: Cohort B7 Medulloblastoma and Embryonal Tumors

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

Part B: Cohort B8 Ependymoma

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

Part B: Cohort B9 Miscellaneous brain tumors

Group Type EXPERIMENTAL

Nivolumab

Intervention Type BIOLOGICAL

Specified dose on specified days

NKTR-214

Intervention Type BIOLOGICAL

Specified dose on specified days

Interventions

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Nivolumab

Specified dose on specified days

Intervention Type BIOLOGICAL

NKTR-214

Specified dose on specified days

Intervention Type BIOLOGICAL

Other Intervention Names

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BMS-936558-01 Bempegaldesleukin (BEMPEG)

Eligibility Criteria

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Inclusion Criteria

* Age \< 18 years for Part A and Part B
* Age up to 30 years for Part B Cohorts B2, B3 and B4
* Must have received standard of care therapy and there must be no potentially curative treatment available
* Histologically confirmed with malignant neoplasms that are refractory, relapsed, or curative treatments are lacking
* Must have measurable or evaluable disease based on Response Evaluation Criteria in Solid Tumors (RECIST) v1.1 for solid tumors, Response Assessment in Neuro-Oncology (RANO) or Response Assessment in Pediatric Neuro-Oncology (RAPNO) for central nervous system tumors, International Pediatric Non-Hodgkin Lymphoma Response Criteria for non-Hodgkin lymphoma (NHL), revised International Neuroblastoma Response Criteria (INRC) for neuroblastoma, modified National Comprehensive Cancer Network (NCCN) Criteria for acute lymphoblastic leukemia, and modified Cheson et al International Working Group criteria for acute myeloid leukemia
* Lansky play score for age ≤ 16 years or Karnofsky performance score for age \> 16 years assessed within 2 weeks of enrollment must be ≥ 60

Exclusion Criteria

* Osteosarcoma, T-cell/Natural Killer (NK) cell leukemia/lymphoma, and Hodgkin's lymphoma
* Need for \> 2 antihypertensive medications for management of hypertension (including diuretics)
* Known cardiovascular history, including unstable or deteriorating cardiac disease, within the previous 12 months prior to screening
* Inadequately treated adrenal insufficiency
* Active, known, or suspected autoimmune disease
* Active infection requiring systemic therapy within 14 days prior to first dose
* Condition requiring systemic treatment with either corticosteroids or other immunosuppressive medications within 14 days of start of study treatment
* Prior allogeneic stem cell transplant
* Previous severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2) infection either suspected or confirmed within 4 weeks prior to screening
Maximum Eligible Age

30 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Nektar Therapeutics

INDUSTRY

Sponsor Role collaborator

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Local Institution - 0029

Little Rock, Arkansas, United States

Site Status

Local Institution - 0011

St Louis, Missouri, United States

Site Status

Local Institution - 0001

Randwick, New South Wales, Australia

Site Status

Local Institution

South Brisbane, Queensland, Australia

Site Status

Local Institution - 0002

Parkville, Victoria, Australia

Site Status

Local Institution - 0003

Perth, Western Australia, Australia

Site Status

Local Institution - 0013

Villejuif, Val-de-Marne, France

Site Status

Local Institution - 0014

Lyon, , France

Site Status

Local Institution - 0016

Marseille, , France

Site Status

Local Institution - 0015

Paris, , France

Site Status

Local Institution - 0038

Hamburg, , Germany

Site Status

Local Institution - 0039

Tübingen, , Germany

Site Status

Local Institution - 0037

Würzburg, , Germany

Site Status

Local Institution - 0027

Milan, , Italy

Site Status

Local Institution - 0009

Madrid, Madrid, Comunidad de, Spain

Site Status

Local Institution - 0008

Barcelona, , Spain

Site Status

Local Institution - 0059

Seville, , Spain

Site Status

Local Institution - 0028

Valencia, , Spain

Site Status

Countries

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United States Australia France Germany Italy Spain

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2020-000854-85

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CA045-020

Identifier Type: -

Identifier Source: org_study_id

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