Trastuzumab Deruxtecan for Subjects With HER2-Positive Gastric Cancer or Gastro-Esophageal Junction Adenocarcinoma After Progression on or After a Trastuzumab-Containing Regimen (DESTINY-Gastric04)

NCT ID: NCT04704934

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

490 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-05-21

Study Completion Date

2026-08-31

Brief Summary

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This study will evaluate the efficacy and safety of trastuzumab deruxtecan (T-DXd) compared with ramucirumab and paclitaxel (Ram + PTX) in participants with HER2-positive gastric or gastro-esophageal junction (GEJ) adenocarcinoma who have progressed on or after a trastuzumab-containing regimen and have not received any additional systemic therapy.

Detailed Description

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This study will assess the efficacy and safety of T-DXd compared with Ram + PTX in participants with HER2-positive (defined as immunohistochemistry \[IHC\] 3+ or IHC 2+/in situ hybridization \[ISH\]+) gastric or GEJ adenocarcinoma (based on \[American Society of Clinical Oncology (ASCO) College of American Pathologists (CAP) guidelines who have progressed on or after a trastuzumab-containing regimen and have not received any additional systemic therapy. Participants will be randomized 1:1 to either T-DXd or Ram + PTX treatment. The primary objective will assess overall survival. Secondary objectives will further assess progression-free survival, objective response rate, duration of response, disease control rate, safety, pharmacokinetics, and immunogenicity of T-DXd.

Conditions

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Gastric Cancer, Adenocarcinoma Gastroesophageal Junction Adenocarcinoma

Keywords

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Gastric Cancer, Adenocarcinoma Gastroesophageal Junction Adenocarcinoma Trastuzumab deruxtecan T-DXd DS-8201a Ramucirumab Paclitaxel

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Trastuzumab deruxtecan

Participants who will be randomized to receive a 6.4 mg/kg intravenous (IV) dose of trastuzumab deruxtecan once every 3 weeks on Day 1 of each 21-day cycle.

Group Type EXPERIMENTAL

Trastuzumab deruxtecan

Intervention Type DRUG

6.4 mg/kg IV infusion every 3 weeks on Day 1 of each 21-day cycle

Ramucirumab + paclitaxel

Participants who will be randomized to receive a 8 mg/kg IV dose of ramucirumab on Days 1 and 15 in combination with 80 mg/m\^2 IV dose of paclitaxel on Days 1, 8, and 15 of a 28-day cycle.

Group Type ACTIVE_COMPARATOR

Ramucirumab

Intervention Type DRUG

8 mg/kg IV infusion on Days 1 and 15 of a 28-day cycle

Paclitaxel

Intervention Type DRUG

80 mg/m\^2 IV infusion on Days 1, 8, and 15 of a 28-day cycle

Interventions

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Trastuzumab deruxtecan

6.4 mg/kg IV infusion every 3 weeks on Day 1 of each 21-day cycle

Intervention Type DRUG

Ramucirumab

8 mg/kg IV infusion on Days 1 and 15 of a 28-day cycle

Intervention Type DRUG

Paclitaxel

80 mg/m\^2 IV infusion on Days 1, 8, and 15 of a 28-day cycle

Intervention Type DRUG

Other Intervention Names

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T-DXd DS-8201a ENHERTU® CYRAMZA®

Eligibility Criteria

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Inclusion Criteria

* Adults (according to local regulation) and able to provide informed consent for study participation.
* Pathologically documented gastric and GEJ adenocarcinoma that has been previously treated in the metastatic setting (unresectable, locally advanced, or metastatic disease).
* Progression on or after first-line therapy with a trastuzumab or approved trastuzumab biosimilar-containing regimen. Note: Prior neoadjuvant or adjuvant therapy with a trastuzumab-containing regimen can be counted as a line of therapy if the subject progressed on or within 6 months of completing neoadjuvant or adjuvant therapy. Prior neoadjuvant or adjuvant therapy that does not include trastuzumab will not be counted as a line of therapy regardless of the progression status of the subject.
* Locally or centrally confirmed HER2-positive (IHC 3+ or IHC 2+ and evidence of HER2 amplification by ISH) as classified by ASCO-CAP on a tumor biopsy obtained after progression on or after a first-line trastuzumab or approved trastuzumab biosimilar-containing regimen.
* Eastern Cooperative Oncology Group performance status of 0 or 1 at Screening.
* Adequate bone marrow, renal, hepatic function, and blood clotting function within 14 days of randomization.

Exclusion Criteria

* Use of anticancer therapy after trastuzumab-containing treatment
* Medical history of myocardial infarction (MI) within 6 months before randomization/enrollment, symptomatic congestive heart failure (New York Heart Association Class II to IV).
* Has a QT interval corrected by Fridericia's formula (QTcF) prolongation to \>470 msec (female subjects) or \>450 msec (male subjects) based on average of the Screening triplicate12-lead ECG.
* Has a history of (non-infectious) interstitial lung disease (ILD/pneumonitis) that required steroids, has current ILD/pneumonitis, or where suspected ILD/pneumonitis cannot be ruled out by imaging at Screening.
* Any autoimmune, connective tissue or inflammatory disorders (eg, rheumatoid arthritis, Sjögren syndrome, sarcoidosis, etc.) where there is documented (or a suspicion of) pulmonary involvement at the time of Screening.
* Prior complete pneumonectomy.
* Spinal cord compression or clinically active central nervous system metastases, defined as untreated and symptomatic or requiring therapy with corticosteroids or anticonvulsants to control associated symptoms.
* Has multiple primary malignancies within 3 years, except adequately resected non-melanoma skin cancer, curatively treated in-situ disease, other solid tumors curatively treated.
* History of severe hypersensitivity reactions to either the T-DXd or inactive ingredients in T-DXd.
* History of severe hypersensitivity reactions to other monoclonal antibodies, including ramucirumab or to any of its excipients.
* Known allergy or hypersensitivity to paclitaxel or any components used in the paclitaxel preparation or other contraindication for taxane therapy.
* Current uncontrolled infection requiring antibiotics, antivirals, or antifungals or an unexplained fever \>38.0°C during Screening visits or on the first scheduled day of dosing (at the discretion of the Investigator, participants with tumor fever may be enrolled), which in the Investigator's opinion might compromise the participant's participation in the study or affect the study outcome
* Clinically significant gastrointestinal disorder (eg, including hepatic disorders, bleeding, inflammation, occlusion, ileus, diarrhea Grade \>1, jaundice, intestinal paralysis, malabsorption syndrome, ulcerative colitis, inflammatory bowel disease, or partial bowel obstruction) in the opinion of Investigator
* Has history of receiving live, attenuated vaccine (mRNA and replication deficient adenoviral vaccines are not considered attenuated live vaccines) within 30 days prior to the first exposure to study intervention
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role collaborator

Daiichi Sankyo

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Global Clinical Leader

Role: STUDY_DIRECTOR

Daiichi Sankyo

Locations

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Instituto Medico Especializado Alexander Fleming

Colegiales, Buenos Aires F.D., Argentina

Site Status

IONC Instituto Oncologico de Cordoba - Fundacion Richardet Longo

Nueva Cordoba, Córdoba Province, Argentina

Site Status

Exelsus

San Miguel de Tucumán, Tucumán Province, Argentina

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Fundacion Cenit

Buenos Aires, , Argentina

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UCL St. Luc

Brussels, , Belgium

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Antwerp University Hospital

Edegem, , Belgium

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Pôle Hospitalier Jolimont

Haine-Saint-Paul, , Belgium

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UZ Leuven

Leuven, , Belgium

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PERSONAL - Oncologia de Precisao e Personalizada

Belo Horizonte, , Brazil

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Hospital Sirio Libanes

Brasília, , Brazil

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ONCOSITE - Centro de Pesquisa Clinica em Oncologia LTDA

Ijuí, , Brazil

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Hospital Ernesto Dornelles

Porto Alegre, , Brazil

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SIM Centro de Investigacion Clinica

Temuco, Cautin, Chile

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Fundacion Arturo Lopez Perez

Santiago, Santiago Metropolitan, Chile

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Clinica San Carlos de Apoquindo

Santiago, Santiago Metropolitan, Chile

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Anhui Provincial Hospital

Heifi, Anhui, China

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Fujian Medical University - Fujian Provincial Cancer Hospital

Fuzhou, Fuijan, China

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Xiamen University - The First Affiliated Hospital

Xiamen, Fujian, China

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The Sixth Affiliated Hospital of Sun Yat-Sen University

Guangzhou, Guangdong, China

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1Affiliated H of Sun Yat Sen U

Guangzhou, Guangdong, China

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Hebei Medical Univ 4th Hosp

Shijiazhuang, Hebei, China

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Harbin Medical University Cancer Hospital

Harbin, Heilongjiang, China

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The First Affiliated Hospital of Zhengzhou University

Zhengzhou, Henan, China

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Zhongnan univ Xiangya hosp

Changshan, Hunan, China

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Jiangsu Province Hosp

Nanjing, Jiangsu, China

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Liaoning Cancer Hospital

Shenyang, Liaoning, China

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1st Hosp of China Medical Univ

Shenyang, Liaoning, China

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Shandong Cancer Hospital & Institute

Jinan, Shandong, China

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Zhongshan Hosp Fudan Univ

Shanghai, Shanghai Municipality, China

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Shanghai First People's Hosp

Shanghai, Shanghai Municipality, China

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Xinjiang Medical University - Cancer Hospital

Ürümqi, Xinjiang, China

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Zhejiang Medical University - Zhejiang Cancer Hospital

Hangzhou, Zhejiang, China

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Beijing Cancer Hospital

Beijing, , China

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Peking Univ 3rd Hosp

Beijing, , China

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The 1st Hospital of Jilin Univ

Changchun, , China

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Sir Run Run Shaw Hospital

Hangzhou, , China

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Linyi Cancer Hospital

Linyi, , China

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1 Affiliated H of Nanchang U

Nanchang, , China

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Fudan University - Shanghai Cancer Center

Shanghai, , China

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CHU Besançon

Besançon, , France

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CHRU

Brest, , France

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Centre Oscar Lambret

Lille, , France

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Centre Leon Berard

Lyon, , France

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Hopital de la Timone

Marseille, , France

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Institut de Recherche en Cancerologie de Montpellier IRCM

Montpellier, , France

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Hopital Saint Antoine

Paris, , France

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L Institut Mutualiste Montsouris

Paris, , France

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Hopital Europeen G. Pompidou

Paris, , France

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Pharmacie ICLN

Saint-Priest-en-Jarez, , France

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Gustave Roussy, étage -1.

Villejuif, , France

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Charité-Unimedizin Berlin

Berlin, , Germany

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Uniklinikum Carl-Gustav-Carus

Dresden Sachsen, , Germany

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Evang. Klin. Essen-Mitte gGmbH

Essen, , Germany

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Ins. für klinische onk. Forschung

Frankfurt Am Main Hessen, , Germany

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Häm-Onk. Praxis Eppendorf

Hamburg, , Germany

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Asklepios Tumorzentrum Altona

Hamburg, , Germany

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Uni zu Koln-Unikl. Koln

Kln Nordrhein-westfalen, , Germany

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Universitares Krebszentrum

Leipzig, , Germany

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Pamela Youde Nethersole Eastern Hospital

Chai Wan, , Hong Kong

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Princess Margaret Hospital

Hong Kong, , Hong Kong

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Queen Mary Hospital

Hong Kong, , Hong Kong

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The Chinese University of Hong Kong (CUHK) - Prince of Wales Hospital (PWH) - Vascular and Interventional Radiology Foundation (VIRF) Clinical Science Centre

Hong Kong, , Hong Kong

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Magyar Honvedseg Egeszs. K

Budapest, , Hungary

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Debreceni Egyetem Klinikai

Debrecen, , Hungary

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Tolna M. Balassa Janos Korhaz

Szekszárd, , Hungary

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Cork University Hospital

Cork, , Ireland

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Tallaght University Hospital

Dublin, , Ireland

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Beaumont Hospital

Dublin, , Ireland

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St James's Hospital

Dublin, , Ireland

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Soroka Univ Medical CTR

Be'er-Sheva Southern, , Israel

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Davidoff Center

Petah Tikva, , Israel

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The Chaim Sheba Medical Center

Ramat Gan, , Israel

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AOU Pisana

Barone, , Italy

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IRCC-FPO Candiolo

Candiolo, , Italy

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AOU Mater Domini

Catanzaro, , Italy

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Istituto Europeo di Oncologia S.r.L Divisione di Oncologia Medica Gastrointestinale e Tumori Neuroendocrini

Milan, , Italy

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Ospedale Niguarda

Milan, , Italy

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San Raffaele Hospital

Milan, , Italy

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Istituto Nazionale dei Tumori

Milan, , Italy

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Azienda Ospedaliero-Universitaria di Modena

Modena, , Italy

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Aou Vanvitelli

Napoli, , Italy

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Istituto Oncologico Veneto

Padua, , Italy

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Azienda Ospedaliero-Universitaria Pisana

Pisa, , Italy

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Aichi Cancer Center Hospital

Nagoya, Aichia, Japan

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National Cancer Center Hospital

Chūōku, , Japan

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Osaka International Cancer Institute

Chūōku, , Japan

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Gifu University Hospital

Gifu, , Japan

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National Cancer Center Hospital East

Kashiwa, , Japan

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Kobe City Medical Center General Hospital

Kobe, , Japan

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Kochi Health Sciences Center

Kochi, , Japan

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The Cancer Institute Hospital of JFCR

Kōtoku, , Japan

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National Hospital Organization Shikoku Cancer Center

Matsuyama, , Japan

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Niigata Cancer Center Hospital

Niigata, , Japan

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Kindai University Hospital

Ōsaka-sayama, , Japan

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Osaka University Hospital

Suita, , Japan

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Sklodowska-Curie Inst Oncology

Warsaw, , Poland

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Uniwersytecki Szpital Kliniczny im.Mikulicza-Radeckiego

Wroclaw, , Poland

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Hospital Sra da Oliveira

Creixomil E Mariz, , Portugal

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Instituto Portugues De Oncologia Do Porto Francisco Gentil, E.P.E.

Porto, , Portugal

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C Hosp Tras Montes Alto Douro

Vila Real, , Portugal

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S.C. Oncopremium-Team SRL

Baia Mare, , Romania

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Institutul Oncologic Prof. Dr. Alexandru Trestiorean Bucuresti IOB

Bucharest, , Romania

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S.C. Medisprof SRL

Cluj-Napoca, , Romania

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Centrul de Oncologie Sf. Nectarie

Craiova, , Romania

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SBIH Chelyabinsk Regional Clinical Centre of Oncology and Nuclear Medicine

Chelyabinsk, , Russia

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Private Medical Institution "Euromedservice"

Saint Petersburg, , Russia

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City Clinical Oncology Dispensary

Saint Petersburg, , Russia

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Republican Clinical Oncology Dispensary

Ufa, , Russia

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National Univ Cancer Inst SGP

Singapore, , Singapore

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National Cancer Centre Singapore

Singapore, , Singapore

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Kyungpook Nat Uni Chilgok Hos

Daegu, , South Korea

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Chonnam National University Hwasun Hospital

Hwasun, , South Korea

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Seoul Nati Univ Bundang Hosp

Seongnam, , South Korea

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Korea Univ Anam Hosp

Seoul, , South Korea

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Seoul National University Hospital

Seoul, , South Korea

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Severance Hospital

Seoul, , South Korea

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Asan Medical Center

Seoul, , South Korea

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Samsung Medical Center

Seoul, , South Korea

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Seoul St. Marys Hospital

Seoul, , South Korea

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Chonbuk National University Hospital - Jeonbuk Regional Cancer Center

Seoul, , South Korea

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Hospital Vall d'Hebron

Barcelona, , Spain

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Hospital Clinic de Barcelona

Barcelona, , Spain

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Hospital Germans Trias i Pujol

Barcelona, , Spain

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H. Gregorio Maranon

Madrid, , Spain

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Hosp Univ Ramón y Cajal

Madrid, , Spain

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Hospital Universitario La Paz

Madrid, , Spain

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Hospital de Navarra

Pamplona, , Spain

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Hospital Clinico Universitario de Santiago de Compostela

Santiago de Compostela, , Spain

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H. Clinico U. de Valencia

Valencia, , Spain

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KMUH

Kaohsiung City, , Taiwan

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CGMF-Kaohsiung Branch

Kaohsiung City, , Taiwan

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China Medical Univ Hosp

Taichung, , Taiwan

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National Cheng Kung Univ Hosp

Tainan, , Taiwan

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National Taiwan University Hospital NTUH

Taipei, , Taiwan

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MacKay Memorial Hospital

Taipei, , Taiwan

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Taipei Veterans General Hosp

Taipei, , Taiwan

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CGMF-Linkou Branch

Taoyuan District, , Taiwan

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SBU Adana Sehir Hastanesi

Adana, , Turkey (Türkiye)

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Trakya Universitesi Balkan

Edirne, , Turkey (Türkiye)

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Suleyman Yalcin Seh. Hast.

Istanbul, , Turkey (Türkiye)

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Inonu Uni. Turgut Ozal Tip

Malatya, , Turkey (Türkiye)

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National Cancer Institute

Kyiv, , Ukraine

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MedicalCenter ASKLEPION LLC

Kyiv, , Ukraine

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LLC "Oncolife"

Zaporizhzhia, , Ukraine

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University Hospitals Birmingham UHB NHS Foundation Trust - Queen Elizabeth Hospital Birmingham QEHB

Birmingham, , United Kingdom

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Addenbrooke's Hospital

Cambridge, , United Kingdom

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Velindre NHS Trust - Velindre Cancer Centre VCC

Cardiff, , United Kingdom

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Ninewells Hospital

Dundee, , United Kingdom

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Beatson West of Scotland Cancer Centre

Glasgow, , United Kingdom

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The Clatterbridge Cancer Centre NHS Foundation Trust

Liverpool, , United Kingdom

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UCLH Trust

London, , United Kingdom

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Royal Marsden NHS

London, , United Kingdom

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Christie Hospital

Manchester, , United Kingdom

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University of Oxford, The Churchill Hospital

Oxford, , United Kingdom

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Royal Marsden Sutton

Sutton, , United Kingdom

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Leeds Teaching Hospitals NHS Trust

West Yorkshire, , United Kingdom

Site Status

Countries

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Argentina Belgium Brazil Chile China France Germany Hong Kong Hungary Ireland Israel Italy Japan Poland Portugal Romania Russia Singapore South Korea Spain Taiwan Turkey (Türkiye) Ukraine United Kingdom

References

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Shitara K, Van Cutsem E, Gumus M, Lonardi S, de la Fouchardiere C, Coutzac C, Dekervel J, Hochhauser D, Shen L, Mansoor W, Liu B, Fornaro L, Ryu MH, Lee J, Faustino C, Metges JP, Tabernero J, Franke F, Janjigian YY, Souza F, Jukofsky L, Zhao Y, Kamio T, Zaanan A, Pietrantonio F; DESTINY-Gastric04 Trial Investigators. Trastuzumab Deruxtecan or Ramucirumab plus Paclitaxel in Gastric Cancer. N Engl J Med. 2025 Jul 24;393(4):336-348. doi: 10.1056/NEJMoa2503119. Epub 2025 May 31.

Reference Type DERIVED
PMID: 40454632 (View on PubMed)

Other Identifiers

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2020-004559-34

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

DS8201-A-U306

Identifier Type: -

Identifier Source: org_study_id