A Study to Evaluate the Efficacy, Safety, and Tolerability of Brivaracetam as Monotherapy in Patients 2 to 25 Years of Age With Childhood Absence Epilepsy or Juvenile Absence Epilepsy

NCT ID: NCT04666610

Last Updated: 2026-01-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

160 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-07-29

Study Completion Date

2026-08-24

Brief Summary

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The purpose of the study is to test the efficacy, safety and tolerability of brivaracetam monotherapy in study participants 2 to 25 years of age inclusive with childhood absence epilepsy (CAE) or juvenile absence epilepsy (JAE).

Detailed Description

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Conditions

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Childhood Absence Epilepsy Juvenile Absence Epilepsy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo received during RDW

Randomized Withdrawal (RDW) Period:

Only study participants who are absence seizure-free based on the outcome of the 24h EEG of Visit 5 will enter the RDW Period. Study participants who are randomized to the placebo arm in the RDW Period will be tapered down to 0 mg and receive 0 mg for 2 weeks.

Group Type EXPERIMENTAL

Brivaracetam

Intervention Type DRUG

* Pharmaceutical form: Oral solution
* Route of administration: Oral use

Brivaracetam (oral solution \[10 mg/ml, 5 mg/ml or 2.5 mg/ml\] will be administered.

Placebo

Intervention Type OTHER

Subjects will receive placebo at pre-specified time-points to maintain the blinding.

Brivaracetam 200 mg

Placebo-Controlled (PC) and Active Treatment (AT) Period:

Stage 1: Study participants randomized to brivaracetam (BRV) 200mg/day (or equivalent dose) will receive these doses during the 2-week PC period and subsequent 11-week AT period.

Group Type EXPERIMENTAL

Brivaracetam

Intervention Type DRUG

* Pharmaceutical form: Oral solution
* Route of administration: Oral use

Brivaracetam (oral solution \[10 mg/ml, 5 mg/ml or 2.5 mg/ml\] will be administered.

Placebo to 200 mg brivaracetam

Placebo-Controlled (PC) and Active Treatment (AT) Period:

Stage 1: Study participants randomized to 'placebo to BRV 200mg/day' (or equivalent dose) will receive placebo during the PC period followed by BRV 200mg/day (or equivalent dose) during the AT period.

Group Type EXPERIMENTAL

Brivaracetam

Intervention Type DRUG

* Pharmaceutical form: Oral solution
* Route of administration: Oral use

Brivaracetam (oral solution \[10 mg/ml, 5 mg/ml or 2.5 mg/ml\] will be administered.

Placebo

Intervention Type OTHER

Subjects will receive placebo at pre-specified time-points to maintain the blinding.

Brivaracetam 100 mg

Placebo-Controlled (PC) and Active Treatment (AT) Period:

Stage 1: Study participants randomized to BRV 100mg/day (or equivalent dose) will receive these doses during the 2-week PC period and subsequent 11-week AT period.

Group Type EXPERIMENTAL

Brivaracetam

Intervention Type DRUG

* Pharmaceutical form: Oral solution
* Route of administration: Oral use

Brivaracetam (oral solution \[10 mg/ml, 5 mg/ml or 2.5 mg/ml\] will be administered.

Placebo to 100 mg brivaracetam

Placebo-Controlled (PC) and Active Treatment (AT) Period:

Stage 1: Study participants randomized to 'placebo to BRV 100mg/day' (or equivalent dose) will receive placebo during the PC period followed by BRV 100mg/day (or equivalent dose) during the AT period.

Group Type EXPERIMENTAL

Brivaracetam

Intervention Type DRUG

* Pharmaceutical form: Oral solution
* Route of administration: Oral use

Brivaracetam (oral solution \[10 mg/ml, 5 mg/ml or 2.5 mg/ml\] will be administered.

Placebo

Intervention Type OTHER

Subjects will receive placebo at pre-specified time-points to maintain the blinding.

Optimal dose of BRV (defined following Stage 1)

Placebo-Controlled (PC) and Active Treatment Period (AT):

Stage 2: Study participants will be randomized in Stage 2 to receive a fixed dose of the optimal dose of brivaracetam (defined following Stage 1). Study participants randomized to the BRV optimal dose will receive this dose during the 2-week PC period and subsequent 11-week AT period.

Group Type EXPERIMENTAL

Brivaracetam

Intervention Type DRUG

* Pharmaceutical form: Oral solution
* Route of administration: Oral use

Brivaracetam (oral solution \[10 mg/ml, 5 mg/ml or 2.5 mg/ml\] will be administered.

Placebo to BRV optimal dose (defined following Stage 1)

Placebo-Controlled (PC) and Active Treatment (AT) Period:

Stage 2: Study participants will be randomized in Stage 2 of the study to 'placebo to BRV optimal dose'. Study participants randomized to placebo to brivaracetam (BRV) optimal dose will receive placebo during the PC period followed by BRV optimal dose during the AT period.

Group Type EXPERIMENTAL

Brivaracetam

Intervention Type DRUG

* Pharmaceutical form: Oral solution
* Route of administration: Oral use

Brivaracetam (oral solution \[10 mg/ml, 5 mg/ml or 2.5 mg/ml\] will be administered.

Placebo

Intervention Type OTHER

Subjects will receive placebo at pre-specified time-points to maintain the blinding.

Brivaracetam received during RDW

Randomized Withdrawal (RDW) Period:

Only study participants who are absence seizure-free based on the outcome of the 24h EEG of Visit 5 will enter the RDW Period. Participants who are randomized to this arm will continue on the Brivaracetam dose they were receiving in the AT period.

Group Type EXPERIMENTAL

Brivaracetam

Intervention Type DRUG

* Pharmaceutical form: Oral solution
* Route of administration: Oral use

Brivaracetam (oral solution \[10 mg/ml, 5 mg/ml or 2.5 mg/ml\] will be administered.

Interventions

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Brivaracetam

* Pharmaceutical form: Oral solution
* Route of administration: Oral use

Brivaracetam (oral solution \[10 mg/ml, 5 mg/ml or 2.5 mg/ml\] will be administered.

Intervention Type DRUG

Placebo

Subjects will receive placebo at pre-specified time-points to maintain the blinding.

Intervention Type OTHER

Other Intervention Names

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BRV PBO

Eligibility Criteria

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Inclusion Criteria

* Study participant is 2 to 25 years of age inclusive, at the time of signing the informed consent. No study participants from 2 to \<4 years of age will be included in Stage 1
* Study participant is diagnosed with either childhood absence epilepsy (CAE) or juvenile absence epilepsy (JAE) as defined by the International League Against Epilepsy (ILAE) criteria
* Study participants 2 to \<4 years of age and participants who had onset of absence seizures at an age younger than 4 years must have a negative glucose transporter type 1 deficiency syndrome (GLUT1DS) genetic test
* Study participant is untreated with antiepileptic drugs (AEDs) or pretreated for absence seizures with a maximum of 2 historical AEDs, but without AED treatment for a period of at least 5 half-lives of the AED before randomization into this study. The UCB study physician should be consulted if in doubt
* Study participant has electroencephalogram (EEG) evidence of bilateral synchronous, symmetric generalized paroxysmal spike waves (2.5-6 hertz) with normal background activity and with at least 1 electrographically recorded seizure lasting 3 seconds or more on a 1-hour EEG with hyperventilation (HV) while awake at Visit 1 (V1), or on a historical EEG up to 12 weeks before enrollment
* Study participant has a history of clinically evident absence seizures occurring on at least 3 days per week in the 2 weeks prior to enrollment
* Study participant is without treatment with psychoactive drugs or on a stable dose for at least 2 weeks prior to randomization
* Study participant has normal neurological examination, head size, development and cognition
* Body weight is ≥9 kg
* Male and female

a) A sexually active male study participant must agree to use contraception during the treatment period and for at least 2 days, corresponding to the time needed to eliminate study treatment, after the last dose of study treatment and refrain from donating sperm during this period b) A female study participant is eligible to participate if she is not pregnant, not breastfeeding, and at least 1 of the following conditions applies: The study participant is premenarchial OR A woman of childbearing potential (WOCBP) who agrees to follow the contraceptive guidance during the treatment period and for at least 2 days after the last dose of study treatment, corresponding to the time needed to eliminate study treatment
* Study participant provides consent/assent, and the study participant's parent/legal representative/caregiver provides signed informed consent for minor study participants, which includes compliance with the requirements and restrictions listed in the informed consent form (ICF) and in this protocol

Exclusion Criteria

* Study participant has a history of nonfebrile seizures other than absence seizures (eg, generalized tonic-clonic seizures or myoclonic seizures)
* Study participant has a history of absence status epilepticus
* Study participant has a history or presence of paroxysmal nonepileptic seizures
* Study participant has a clinically relevant electrocardiogram (ECG) abnormality in the opinion of the Principal Investigator
* Study participant has hepatic impairment (Child Pugh Score A, B, or C) based on the Investigator's assessment
* Study participant has a history of major psychiatric disease or any clinically significant medical condition that would preclude appropriate study participation
* Study participant has active suicidal ideation prior to study entry as indicated by a positive response ("Yes") to either Question 4 or Question 5 of the Columbia-Suicide Severity Rating Scale (C-SSRS; for study participants 6 years or older) or clinical judgement (for study participants younger than 6 years). The study participant should be referred immediately to a Mental Healthcare Professional
* Study participant has a lifetime history of suicide attempt (including an active attempt, interrupted attempt, or aborted attempt). The study participant should be immediately evaluated by a Mental Healthcare Professional to address safety concerns
* Study participant with known fructose intolerance or hypersensitivity of any of the ingredients in brivaracetam oral solution
* Study participant has end-stage kidney disease requiring dialysis
* Concomitant use of rifampicin/rifampin; prior use must have been stopped at least 2 months before randomization
* Concomitant use of strong CYP2C19 inhibitors like fluconazole, fluoxetine and fluvoxamine, prior use must have been stopped at least 1 week before randomization
* Study participant has participated in another study of an investigational medicinal product (IMP; and/or an investigational device) within the previous 30 days prior to informed consent
* Study participant has clinical or EEG findings not consistent with a diagnosis of childhood absence epilepsy (CAE) or juvenile absence epilepsy (JAE)
Minimum Eligible Age

2 Years

Maximum Eligible Age

25 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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UCB Biopharma SRL

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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UCB Cares

Role: STUDY_DIRECTOR

001 844 599 2273 (UCB)

Locations

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N01269 115

Birmingham, Alabama, United States

Site Status RECRUITING

N01269 118

Long Beach, California, United States

Site Status WITHDRAWN

N01269 105

Orange, California, United States

Site Status RECRUITING

N01269 116

Denver, Colorado, United States

Site Status COMPLETED

N01269 103

Loxahatchee Groves, Florida, United States

Site Status WITHDRAWN

N01269 111

Miami, Florida, United States

Site Status RECRUITING

N01269 101

Tampa, Florida, United States

Site Status COMPLETED

N01269 104

Winter Park, Florida, United States

Site Status COMPLETED

N01269 110

Augusta, Georgia, United States

Site Status COMPLETED

N01269 100

New Brunswick, New Jersey, United States

Site Status RECRUITING

N01269 109

Winston-Salem, North Carolina, United States

Site Status RECRUITING

N01269 106

Philadelphia, Pennsylvania, United States

Site Status COMPLETED

N01269 203

Heidelberg, , Australia

Site Status WITHDRAWN

N01269 202

Melbourne, , Australia

Site Status WITHDRAWN

N01269 200

Randwick, , Australia

Site Status WITHDRAWN

N01269 201

South Brisbane, , Australia

Site Status WITHDRAWN

N01269 301

Brussels, , Belgium

Site Status WITHDRAWN

N01269 300

Edegem, , Belgium

Site Status WITHDRAWN

N01269 400

Tbilisi, , Georgia

Site Status RECRUITING

N01269 401

Tbilisi, , Georgia

Site Status RECRUITING

N01269 402

Tbilisi, , Georgia

Site Status COMPLETED

N01269 403

Tbilisi, , Georgia

Site Status RECRUITING

N01269 405

Tbilisi, , Georgia

Site Status RECRUITING

N01269 323

Messina, , Italy

Site Status RECRUITING

N01269 321

Milan, , Italy

Site Status RECRUITING

N01269 324

Milan, , Italy

Site Status RECRUITING

N01269 320

Pavia, , Italy

Site Status RECRUITING

N01269 322

Roma, , Italy

Site Status RECRUITING

N01269 325

Roma, , Italy

Site Status RECRUITING

N01269 326

Verona, , Italy

Site Status RECRUITING

N01269 533

Gdansk, , Poland

Site Status WITHDRAWN

N01269 530

Krakow, , Poland

Site Status WITHDRAWN

N01269 534

Lodz, , Poland

Site Status WITHDRAWN

N01269 531

Lublin, , Poland

Site Status WITHDRAWN

N01269 532

Warsaw, , Poland

Site Status WITHDRAWN

N01269 562

Bucharest, , Romania

Site Status RECRUITING

N01269 563

Bucharest, , Romania

Site Status RECRUITING

N01269 560

Iași, , Romania

Site Status RECRUITING

N01269 561

Timişoara, Judeţ Timiş, , Romania

Site Status RECRUITING

N01269 632

Bardejov, , Slovakia

Site Status RECRUITING

N01269 630

Dubnica nad Váhom, , Slovakia

Site Status RECRUITING

N01269 631

Nové Zámky, , Slovakia

Site Status COMPLETED

N01269 351

Madrid, , Spain

Site Status WITHDRAWN

N01269 353

Seville, , Spain

Site Status WITHDRAWN

N01269 354

Terrassa, , Spain

Site Status COMPLETED

N01269 600

Dnipro, , Ukraine

Site Status COMPLETED

N01269 601

Dnipro, , Ukraine

Site Status COMPLETED

N01269 604

Kharkiv, , Ukraine

Site Status COMPLETED

N01269 608

Kharkiv, , Ukraine

Site Status WITHDRAWN

N01269 603

Kyiv, , Ukraine

Site Status WITHDRAWN

N01269 606

Kyiv, , Ukraine

Site Status WITHDRAWN

N01269 607

Uzhhorod, , Ukraine

Site Status ACTIVE_NOT_RECRUITING

N01269 602

Vinnytsia, , Ukraine

Site Status COMPLETED

Countries

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United States Australia Belgium Georgia Italy Poland Romania Slovakia Spain Ukraine

Central Contacts

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UCB Cares

Role: CONTACT

+1844599 ext. 2273

References

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Bast T, Schulz AL, Floricel F, Morita D, Cleveland JM, Elshoff JP. Efficacy and tolerability of brivaracetam monotherapy in childhood and juvenile absence epilepsy: An innovative adaptive trial design. Epilepsia Open. 2022 Dec;7(4):588-597. doi: 10.1002/epi4.12628. Epub 2022 Aug 4.

Reference Type RESULT
PMID: 35844134 (View on PubMed)

Other Identifiers

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2020-002750-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-510428-55-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

U1111-1303-2521

Identifier Type: OTHER

Identifier Source: secondary_id

N01269

Identifier Type: -

Identifier Source: org_study_id

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