A Clinical Safety Study of AT-100 (rhSP-D) in Preterm Neonates at High Risk for Bronchopulmonary Dysplasia (BPD)

NCT ID: NCT04662151

Last Updated: 2024-07-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

37 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-09-01

Study Completion Date

2024-05-29

Brief Summary

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The purpose of this study is to determine if an investigational drug, AT-100, can reduce the occurrence of Bronchopulmonary Dysplasia (BPD) in babies born premature, as compared to babies born premature who receive an air-sham alone.

Detailed Description

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Conditions

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Bronchopulmonary Dysplasia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Phase 1b portion is a randomized, dual-armed, dose escalation study to establish the safest \& most tolerated AT-100 dose tested as compared to air-sham alone.
Primary Study Purpose

PREVENTION

Blinding Strategy

SINGLE

Participants

Study Groups

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Phase 1b open-label AT-100

Once daily AT-100 via intratracheal administration for up to 2 doses (initial Phase 1b dose-escalation portion) or 7 doses (latter Phase 1b highest tolerated \& safety dose level tested portion).

Group Type EXPERIMENTAL

AT-100

Intervention Type BIOLOGICAL

reconstituted AT-100 for intratracheal administration

Phase 1b open-label air-sham

Once daily air-sham via intratracheal administration for up to 2 doses (initial Phase 1b dose-escalation portion) or 7 doses (latter Phase 1b highest tolerated \& safety dose level tested portion).

Group Type SHAM_COMPARATOR

Air-sham

Intervention Type PROCEDURE

room air for intratracheal administration

Interventions

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AT-100

reconstituted AT-100 for intratracheal administration

Intervention Type BIOLOGICAL

Air-sham

room air for intratracheal administration

Intervention Type PROCEDURE

Other Intervention Names

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(rhSP-D)

Eligibility Criteria

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Inclusion Criteria

1. Preterm neonates born between Gestional Age (GA):

1. 25 0/7 weeks to 28 6/7 weeks in the initial dose escalation cohorts.
2. 23 0/7 weeks to 28 6/7 weeks in the latter cohort.
2. Intubated and on mechanical ventilation.
3. Receiving at least 1 dose of standard-of-care-indicated surfactant treatment (Curosurf®) after birth, and able to receive the first dose of AT-100 or air-sham within 96 hours of birth given at any time point after 15 minutes following any of the subject's Curosurf® dose(s).
4. Parent or legal guardian is able to provide informed consent.

Exclusion Criteria

1. Weight at time of birth \< 400 g or \> 1,800 g.
2. Major apparent congenital abnormalities impacting cardio and pulmonary function.
3. Active DNR (Do Not Resuscitate) order in place.
4. Known pulmonary air leaks (e.g. pneumothorax and pneumomediastinum) at the time of AT-100 or air-sham administration.
5. History of allergy or sensitivity to any surfactant or any component of the Investigational Product (AT-100).
6. AT-100 or air-sham dosing was set to occur before Data Safety Monitoring Committee recommendation to proceed to the next dose-escalation cohort.
7. Use of minimally invasive surfactant techniques (e.g., LISA, MIST) or INSURE or if, in the opinion of the care team, the infant is very likely too be extubated shortly after receiving Curosurf®.

a. Subjects extubated and re-intubated after their Curosurf® dose(s) are eligible, so long as the subject meets Inclusion #3.
8. Birth mother:

1. Has known active Hepatitis B, C, or E diagnosis.
2. Has a known illness or exposure that, in the judgement of the Investigator, is serious enough to induce an immune deficiency such as Human Immunodeficiency Virus (HIV) and/or is receiving chemotherapy.
3. Has known active Sexually Transmitted Infection (STI).
4. Has known Cytomegalovirus (CMV) active infection.
5. Has known history or evidence of alcohol or drug abuse, wit the exception of marijuana/marijuana-based products/THC, based on a positive maternal or infant drug screen as evidenced by the institution's standard-of-care practice.
9. Concurrent enrollment in an investigational drug, device, or treatment modulation trial that utilizes treatments outside of standard-of-care.
10. Any condition or situation which, in the Investigator's judgement, puts the mother or the neonate at significant risk, could confound the trial results, or may interfere significantly with the mother's or neonate's participation in the trial.
11. Symptomatic and confirmed COVID-19 infection of the mother around the time of birth.
Minimum Eligible Age

0 Minutes

Maximum Eligible Age

96 Hours

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Airway Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Marc O. Salzberg, MD

Role: STUDY_CHAIR

Airway Therapeutics, Inc.

Locations

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Airway Therapeutics Investigational Site

Tucson, Arizona, United States

Site Status

Airway Therapeutics Investigational Site

Little Rock, Arkansas, United States

Site Status

Airway Therapeutics Investigational Site

Los Angeles, California, United States

Site Status

Airway Therapeutics Investigational Site

Miami, Florida, United States

Site Status

Airway Therapeutics Investigational Site

Atlanta, Georgia, United States

Site Status

Airway Therapeutics Investigational Site

Indianapolis, Indiana, United States

Site Status

Airway Therapeutics Investigational Site

Boston, Massachusetts, United States

Site Status

Airway Therapeutics Investigational Site

Durham, North Carolina, United States

Site Status

Airway Therapeutics Investigational Site

Norfolk, Virginia, United States

Site Status

Airway Therapeutics Investigational Site

Cadiz, Andalusia, Spain

Site Status

Airway Therapeutics Investigational Site

Barcelona, Catalonia, Spain

Site Status

Airway Therapeutics Investigational Site

Santiago de Compostela, Galicia, Spain

Site Status

Airway Therapeutics Investigational Site

Madrid, Madrid, Spain

Site Status

Airway Therapeutics Investigational Site

Madrid, Madrid, Spain

Site Status

Airway Therapeutics Investigational Site

Alicante, Valencia, Spain

Site Status

Airway Therapeutics Investigational Site

Valencia, Valencia, Spain

Site Status

Airway Therapeutics Investigational Site

A Coruña, , Spain

Site Status

Airway Therapeutics Investigational Site

Lleida, , Spain

Site Status

Airway Therapeutics Investigational Site

Málaga, , Spain

Site Status

Countries

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United States Spain

References

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Thebaud B, Goss KN, Laughon M, Whitsett JA, Abman SH, Steinhorn RH, Aschner JL, Davis PG, McGrath-Morrow SA, Soll RF, Jobe AH. Bronchopulmonary dysplasia. Nat Rev Dis Primers. 2019 Nov 14;5(1):78. doi: 10.1038/s41572-019-0127-7.

Reference Type BACKGROUND
PMID: 31727986 (View on PubMed)

Jensen EA, Dysart K, Gantz MG, McDonald S, Bamat NA, Keszler M, Kirpalani H, Laughon MM, Poindexter BB, Duncan AF, Yoder BA, Eichenwald EC, DeMauro SB. The Diagnosis of Bronchopulmonary Dysplasia in Very Preterm Infants. An Evidence-based Approach. Am J Respir Crit Care Med. 2019 Sep 15;200(6):751-759. doi: 10.1164/rccm.201812-2348OC.

Reference Type BACKGROUND
PMID: 30995069 (View on PubMed)

Sorensen GL. Surfactant Protein D in Respiratory and Non-Respiratory Diseases. Front Med (Lausanne). 2018 Feb 8;5:18. doi: 10.3389/fmed.2018.00018. eCollection 2018.

Reference Type BACKGROUND
PMID: 29473039 (View on PubMed)

Sato A, Whitsett JA, Scheule RK, Ikegami M. Surfactant protein-d inhibits lung inflammation caused by ventilation in premature newborn lambs. Am J Respir Crit Care Med. 2010 May 15;181(10):1098-105. doi: 10.1164/rccm.200912-1818OC. Epub 2010 Feb 4.

Reference Type BACKGROUND
PMID: 20133924 (View on PubMed)

Ikegami M, Carter K, Bishop K, Yadav A, Masterjohn E, Brondyk W, Scheule RK, Whitsett JA. Intratracheal recombinant surfactant protein d prevents endotoxin shock in the newborn preterm lamb. Am J Respir Crit Care Med. 2006 Jun 15;173(12):1342-7. doi: 10.1164/rccm.200509-1485OC. Epub 2006 Mar 23.

Reference Type BACKGROUND
PMID: 16556693 (View on PubMed)

Alonso-Ojembarrena A, Poindexter B, Aleem S, Healy H, Aguar-Carrascosa M, Moliner-Calderon E, Serrano-Martin MDM, Arroyo R, Vento M. A phase 1b randomized, multicenter, dose determination trial of zelpultide alfa (recombinant human surfactant protein D) in preterm neonates at high risk of developing bronchopulmonary dysplasia. Front Pediatr. 2025 Sep 12;13:1639573. doi: 10.3389/fped.2025.1639573. eCollection 2025.

Reference Type DERIVED
PMID: 41018057 (View on PubMed)

Related Links

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http://www.airwaytherapeutics.com

Airway Therapeutics' corporate website

Other Identifiers

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AT-100/001

Identifier Type: -

Identifier Source: org_study_id

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