A Study to Evaluate the Safety and Efficacy of Satralizumab in Participants With Neuromyelitis Optica Spectrum Disorder (NMOSD)

NCT ID: NCT04660539

Last Updated: 2024-12-27

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

119 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-03-02

Study Completion Date

2024-05-28

Brief Summary

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This multicenter, single-arm, open-label study will evaluate the long-term safety and efficacy of satralizumab in participants with neuromyelitis optica spectrum disorder (NMOSD) who completed open-label extension (OLE) period of studies BN40898 and BN40900. Participants will receive satralizumab as monotherapy or in combination with one of the following background immunosuppressive treatments: azathioprine (AZA), mycophenolate mofetil (MMF), or oral corticosteroids.

Detailed Description

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Conditions

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Neuromyelitis Optica Spectrum Disorder

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Satralizumab Treatment

Participants will receive satralizumab subcutaneously (SC) every 4 weeks (Q4W)

Group Type EXPERIMENTAL

satralizumab

Intervention Type DRUG

Satralizumab will be administered by SC injection in the abdominal or femoral region at a dose of 120 mg (fixed dose) Q4W for up to 3 years

azathioprine (AZA)

Intervention Type DRUG

Participants are permitted to use AZA during the study as background immunosuppressive treatment at a maximum dose of 3 milligram per kilogram per day (mg/kg/day)

mycophenolate mofetil (MMF)

Intervention Type DRUG

Participants are permitted to use MMF during the study as background immunosuppressive treatment at a maximum dose of 3000 mg/day

oral corticosteroids

Intervention Type DRUG

Participants are permitted to use oral corticosteroids (prednisolone equivalent) during the study as background immunosuppressive treatment at a maximum dose of 15 mg/day

Interventions

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satralizumab

Satralizumab will be administered by SC injection in the abdominal or femoral region at a dose of 120 mg (fixed dose) Q4W for up to 3 years

Intervention Type DRUG

azathioprine (AZA)

Participants are permitted to use AZA during the study as background immunosuppressive treatment at a maximum dose of 3 milligram per kilogram per day (mg/kg/day)

Intervention Type DRUG

mycophenolate mofetil (MMF)

Participants are permitted to use MMF during the study as background immunosuppressive treatment at a maximum dose of 3000 mg/day

Intervention Type DRUG

oral corticosteroids

Participants are permitted to use oral corticosteroids (prednisolone equivalent) during the study as background immunosuppressive treatment at a maximum dose of 15 mg/day

Intervention Type DRUG

Other Intervention Names

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Enspryng non-investigational medicinal product (NIMP) NIMP NIMP

Eligibility Criteria

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Inclusion Criteria

* Participants aged less than 18 years at the time of informed consent for Study BN40898 can continue treatment with a combination of oral corticosteroids and either AZA or MMF
* Participated in Study BN40898 or Study BN40900 with satralizumab in NMOSD, are on ongoing satralizumab treatment and were anti-aquaporin-4 IgG antibody (AQP4-IgG) seropositive at screening in these studies. Participants with NMOSD who were AQP4-IgG seronegative at screening in Study BN40898 or Study BN40900 can be enrolled if the investigator considers the continued treatment with satralizumab to be beneficial for the participant
* For women of childbearing potential: agreement to remain abstinent (refrain from heterosexual intercourse) or use adequate contraception during the treatment period and for 3 months after the final dose of satralizumab.

Exclusion Criteria

* Pregnant or breastfeeding, or intending to become pregnant during the study or within 3 months after the final dose of study drug. Women of childbearing potential must have a negative urine pregnancy test result on the baseline visit prior to initiation of study drug
* Evidence of any serious uncontrolled concomitant diseases that may preclude participation including nervous system disease, cardiovascular disease, hematologic/hematopoiesis disease, respiratory disease, muscular disease, endocrine disease, renal/urologic disease, digestive system disease, congenital or acquired severe immunodeficiency
* Known active infection that requires delaying the next satralizumab dose at the time of enrollment
* NMOSD relapse at the time of enrollment
* Laboratory abnormalities at the last assessment in Study BN40898 or Study BN40900 that preclude re-treatment with satralizumab
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Children's Hospital of Alabama

Birmingham, Alabama, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Columbus Research and Wellness

Columbus, Georgia, United States

Site Status

University of Chicago

Chicago, Illinois, United States

Site Status

Consultants in Neurology Ltd

Northbrook, Illinois, United States

Site Status

OSF Saint Francis Medical Center

Peoria, Illinois, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Wayne State University; UHC-4H

Detroit, Michigan, United States

Site Status

The Neurological Institute PA

Charlotte, North Carolina, United States

Site Status

OhioHealth Research Institute

Columbus, Ohio, United States

Site Status

Jefferson Hospital For Neuroscience; Jefferson Neurology Associates

Philadelphia, Pennsylvania, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Central Texas Neurology Consultants

Round Rock, Texas, United States

Site Status

UMHAT 'Dr. Georgi Stranski', EAD

Pleven, , Bulgaria

Site Status

Multiprofile Hospital for Active Treatment of Neurology and Psychiatry Sv. Naum EAD

Sofia, , Bulgaria

Site Status

University Multiprofile Hospital for Active Treatment Aleksandrovska EAD

Sofia, , Bulgaria

Site Status

MS Clinical Trials Group

Vancouver, British Columbia, Canada

Site Status

Centre hospitalier de l'Universite de Montreal (CHUM)

Montreal, Quebec, Canada

Site Status

Clinical Hospital Centre Osijek

Osijek, , Croatia

Site Status

Ruhr Universitat Bochum

Bochum, , Germany

Site Status

Jahn Ferenc Del-Pesti Korhaz es Rendelointezet

Budapest, , Hungary

Site Status

Azienda Ospedaliera Sant'Andrea

Rome, Lazio, Italy

Site Status

Azienda Ospedaliero Universitaria Policlinico Vittorio Emanuele

Catania, Sicily, Italy

Site Status

Kyushu University Hospital

Fukuoka, , Japan

Site Status

Tohoku University Hospital

Miyagi, , Japan

Site Status

Niigata University Medical & Dental Hospital

Niigata, , Japan

Site Status

Osaka University Hospital

Osaka, , Japan

Site Status

Kindai University Hospital

Osaka, , Japan

Site Status

Tokyo Women's Medical University Hospital

Tokyo, , Japan

Site Status

National Center of Neurology and Psychiatry

Tokyo, , Japan

Site Status

Hospital Kuala Lumpur

Kuala Lumpur, FED. Territory of Kuala Lumpur, Malaysia

Site Status

NZOZ Wielospecjalistyczna Poradnia Lekarska SYNAPSIS

Katowice, , Poland

Site Status

M.A. - LEK A. M. Maciejowscy SC. Centrum Terapii SM

Katowice, , Poland

Site Status

Samodzielny Publiczny Szpital Kliniczny Nr 4 w Lublinie; Klinika Neurologii

Lublin, , Poland

Site Status

Uniwersyteckie Centrum Kliniczne WUM, Centralny Szpital Kliniczny; Klinika Neurologii

Warsaw, , Poland

Site Status

Instytut Psychiatrii i Neurologii

Warsaw, , Poland

Site Status

Miedzyleski Szpital Specjalistyczny w Warszawie

Warsaw, , Poland

Site Status

San Juan MS Center

Guaynabo, , Puerto Rico

Site Status

SC Clubul Sanatatii SRL

Campulung Muscel, , Romania

Site Status

Korea University Anam Hospital

Seoul, , South Korea

Site Status

Asan Medical Center - PPDS

Seoul, , South Korea

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hosp. Clinico San Carlos

Madrid, , Spain

Site Status

China Medical University Hospital

North Dist., , Taiwan

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Bilim University Medical Faculty Florence Nightingale Hospital

Istanbul, , Turkey (Türkiye)

Site Status

Municipal Non-Profit Enterprise City Clinical Hospital #16 of Dnipro City Council

Dnipro, Katerynoslav Governorate, Ukraine

Site Status

Municipal Non-Commercial Enterprise Odesa RMC for Mental Health of Odessa Regional Council

Odesa, Kherson Governorate, Ukraine

Site Status

Communal NPE Vinnytsia Reg. Clin. Psychoneurolog. Hosp. n.a. O.I. Yushchenko of Vinnytsia RC

Vinnytsia, Podolia Governorate, Ukraine

Site Status

Communal Nonprofit enterprise Ternopil Regional Clinical Psychoneurological Hospital of TRC

Ternopil, Volhynian Governorate, Ukraine

Site Status

National Hospital For Neurology and Neurosurgery

London, , United Kingdom

Site Status

Countries

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United States Bulgaria Canada Croatia Germany Hungary Italy Japan Malaysia Poland Puerto Rico Romania South Korea Spain Taiwan Turkey (Türkiye) Ukraine United Kingdom

References

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Bennett JL, Fujihara K, Saiz A, Traboulsee AL, Greenberg BM, Weinshenker BG, Patti F, Kleiter I, Palace J, De Seze J, Evans R, Blondeau K, Klingelschmitt G, Vodopivec I, Rahim M, Yamamura T. Long-Term Efficacy and Safety of Satralizumab in Patients With Neuromyelitis Optica Spectrum Disorder From the SAkuraMoon Open-Label Extension Study. Neurol Neuroimmunol Neuroinflamm. 2025 Sep;12(5):e200450. doi: 10.1212/NXI.0000000000200450. Epub 2025 Jul 31.

Reference Type DERIVED
PMID: 40743487 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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2020-003413-35

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

WN42349

Identifier Type: -

Identifier Source: org_study_id