Trial Outcomes & Findings for A 18-month Study to Evaluate the Efficacy, Safety, Tolerability and Pharmacokinetics of Oral UCB0599 in Study Participants With Early-stage Parkinson's Disease (NCT NCT04658186)

NCT ID: NCT04658186

Last Updated: 2025-10-31

Results Overview

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

496 participants

Primary outcome timeframe

Day 0

Results posted on

2025-10-31

Participant Flow

The study started to enroll participants in December 2020 and concluded in September 2024.

The Participant Flow refers to the Randomized Set.

Participant milestones

Participant milestones
Measure
Placebo
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Overall Study
STARTED
165
166
165
Overall Study
COMPLETED
154
138
139
Overall Study
NOT COMPLETED
11
28
26

Reasons for withdrawal

Reasons for withdrawal
Measure
Placebo
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Overall Study
Adverse Event
4
18
15
Overall Study
Lack of Efficacy
1
1
0
Overall Study
Protocol Violation
0
0
1
Overall Study
Lost to Follow-up
0
0
2
Overall Study
Participant Not Eligible. Randomized In Error
1
0
1
Overall Study
Participant is Moving in Another Province
0
1
0
Overall Study
Non-Compliance
0
1
1
Overall Study
Site Closure; Participant declined transfer
0
1
0
Overall Study
Dropout on the Promotor's Decision
0
0
1
Overall Study
Worsening Symptoms; Participant Withdrew
0
0
1
Overall Study
PI Decision due to Participant Safety
0
0
1
Overall Study
Consent Withdrawn by Participant (not due to adverse event)
5
6
3

Baseline Characteristics

A 18-month Study to Evaluate the Efficacy, Safety, Tolerability and Pharmacokinetics of Oral UCB0599 in Study Participants With Early-stage Parkinson's Disease

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo
n=165 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=166 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=165 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Total
n=496 Participants
Total of all reporting groups
Age, Continuous
61.2 years
STANDARD_DEVIATION 8.3 • n=5 Participants
61.4 years
STANDARD_DEVIATION 7.8 • n=7 Participants
59.9 years
STANDARD_DEVIATION 8.4 • n=5 Participants
60.8 years
STANDARD_DEVIATION 8.2 • n=4 Participants
Age, Customized
18 years to less than (<) 65 years
98 Participants
n=5 Participants
105 Participants
n=7 Participants
110 Participants
n=5 Participants
313 Participants
n=4 Participants
Age, Customized
65 years to <85 years
67 Participants
n=5 Participants
61 Participants
n=7 Participants
55 Participants
n=5 Participants
183 Participants
n=4 Participants
Sex: Female, Male
Female
65 Participants
n=5 Participants
66 Participants
n=7 Participants
65 Participants
n=5 Participants
196 Participants
n=4 Participants
Sex: Female, Male
Male
100 Participants
n=5 Participants
100 Participants
n=7 Participants
100 Participants
n=5 Participants
300 Participants
n=4 Participants
Race/Ethnicity, Customized
Race · Asian
2 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
4 Participants
n=4 Participants
Race/Ethnicity, Customized
Race · White
134 Participants
n=5 Participants
143 Participants
n=7 Participants
143 Participants
n=5 Participants
420 Participants
n=4 Participants
Race/Ethnicity, Customized
Race · Other/Mixed
4 Participants
n=5 Participants
0 Participants
n=7 Participants
2 Participants
n=5 Participants
6 Participants
n=4 Participants
Race/Ethnicity, Customized
Race · Missing
25 Participants
n=5 Participants
22 Participants
n=7 Participants
19 Participants
n=5 Participants
66 Participants
n=4 Participants
Race/Ethnicity, Customized
Ethnicity · Hispanic or Latino
4 Participants
n=5 Participants
3 Participants
n=7 Participants
5 Participants
n=5 Participants
12 Participants
n=4 Participants
Race/Ethnicity, Customized
Ethnicity · Not Hispanic or Latino
136 Participants
n=5 Participants
141 Participants
n=7 Participants
141 Participants
n=5 Participants
418 Participants
n=4 Participants
Race/Ethnicity, Customized
Ethnicity · Missing
25 Participants
n=5 Participants
22 Participants
n=7 Participants
19 Participants
n=5 Participants
66 Participants
n=4 Participants

PRIMARY outcome

Timeframe: Day 0

Population: Full analysis set (FAS) included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=156 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=159 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=159 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I-III Sum Score at Day 0
34.0 score on a scale
Standard Deviation 13.2
33.9 score on a scale
Standard Deviation 16.4
30.6 score on a scale
Standard Deviation 13.4

PRIMARY outcome

Timeframe: Month 2

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=153 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=156 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=144 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I-III Sum Score at Month 2
34.7 score on a scale
Standard Deviation 13.9
34.8 score on a scale
Standard Deviation 18.0
30.3 score on a scale
Standard Deviation 14.6

PRIMARY outcome

Timeframe: Month 4

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=153 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=148 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=143 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I-III Sum Score at Month 4
34.7 score on a scale
Standard Deviation 14.9
34.3 score on a scale
Standard Deviation 18.6
31.4 score on a scale
Standard Deviation 15.0

PRIMARY outcome

Timeframe: Month 6

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=154 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=147 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=146 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I-III Sum Score at Month 6
37.9 score on a scale
Standard Deviation 16.0
36.6 score on a scale
Standard Deviation 20.0
32.9 score on a scale
Standard Deviation 15.7

PRIMARY outcome

Timeframe: Month 8

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=155 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=148 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=143 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I-III Sum Score at Month 8
35.6 score on a scale
Standard Deviation 14.3
34.6 score on a scale
Standard Deviation 19.7
32.9 score on a scale
Standard Deviation 15.5

PRIMARY outcome

Timeframe: Month 10

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=156 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=141 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=140 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I-III Sum Score at Month 10
35.6 score on a scale
Standard Deviation 13.6
33.7 score on a scale
Standard Deviation 18.4
33.2 score on a scale
Standard Deviation 15.6

PRIMARY outcome

Timeframe: Month 12

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=152 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=142 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=140 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I-III Sum Score at Month 12
37.3 score on a scale
Standard Deviation 15.3
36.5 score on a scale
Standard Deviation 19.2
34.5 score on a scale
Standard Deviation 15.4

PRIMARY outcome

Timeframe: Month 14

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=154 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=137 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=141 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I-III Sum Score at Month 14
37.1 score on a scale
Standard Deviation 14.6
34.8 score on a scale
Standard Deviation 18.8
33.9 score on a scale
Standard Deviation 16.9

PRIMARY outcome

Timeframe: Month 16

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=152 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=139 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=137 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I-III Sum Score at Month 16
37.2 score on a scale
Standard Deviation 15.6
35.9 score on a scale
Standard Deviation 19.8
33.6 score on a scale
Standard Deviation 15.4

PRIMARY outcome

Timeframe: Month 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

MDS-UPDRS is a multimodal scale. Part I assessed non-motor experiences of daily living and has 2 components (0-52 possible points). Part IA contains 6 questions and is assessed by the examiner (0-24 possible points). Part IB contains 7 questions on non-motor experiences of daily living completed by participant (0-28 possible points). Part II assessed motor experiences of daily living (0-52 possible points) and includes 13 questions completed by participant. Part III assessed motor signs of PD and was administered by rater (0-52 possible points). Part III contained 33 questions based on 18 items. For all questions of each part, numeric score response options linked to accepted clinical terms: 0 to 4, 0=Normal, 1=Slight, 2=Mild, 3=Moderate, 4=Severe. Total Score equals sum of Parts I, II, and III (Score: 0-236). Higher score = more severe PD symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=152 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=138 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=137 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Parts I-III Sum Score at Month 18
37.9 score on a scale
Standard Deviation 15.5
35.6 score on a scale
Standard Deviation 18.1
34.9 score on a scale
Standard Deviation 16.4

SECONDARY outcome

Timeframe: Day 0, Months 2, 4, 6, 8, 10, 12, 14, 16, 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment and number analyzed (n) signifies participants who were evaluable at specified timepoints.

MDS-UPDRS part III includes motor items assessing speech, facial expression, rigidity, finger tapping, hand movements, pronation supination movements of hands, toe tapping, leg agility, arising from chair, gait, freezing of gait, postural stability, posture, global spontaneity of movement (body bradykinesia), postural tremor of the hands, kinetic tremor of the hands, rest tremor amplitude, and constancy of rest tremor. It included 33 scores based on 18-items, each anchored with 5 responses: 0 = normal, 1 = slight, 2 = mild, 3 = moderate, and 4 = severe. The scale range was from 0 to 132, with a lower score indicating better motor function and a higher score indicating more severe motor symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=159 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=162 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
MDS-UPDRS Part III Subscale
Month 8
23.3 score on a scale
Standard Deviation 10.0
22.2 score on a scale
Standard Deviation 12.6
21.0 score on a scale
Standard Deviation 10.7
MDS-UPDRS Part III Subscale
Month 14
24.1 score on a scale
Standard Deviation 10.1
22.2 score on a scale
Standard Deviation 11.9
21.8 score on a scale
Standard Deviation 11.4
MDS-UPDRS Part III Subscale
Month 16
24.3 score on a scale
Standard Deviation 10.1
22.8 score on a scale
Standard Deviation 12.3
21.7 score on a scale
Standard Deviation 10.7
MDS-UPDRS Part III Subscale
Day 0
22.6 score on a scale
Standard Deviation 9.8
21.9 score on a scale
Standard Deviation 11.3
20.4 score on a scale
Standard Deviation 9.5
MDS-UPDRS Part III Subscale
Month 2
22.9 score on a scale
Standard Deviation 10.2
22.7 score on a scale
Standard Deviation 12.4
20.0 score on a scale
Standard Deviation 10.3
MDS-UPDRS Part III Subscale
Month 4
23.1 score on a scale
Standard Deviation 10.5
22.5 score on a scale
Standard Deviation 12.7
20.7 score on a scale
Standard Deviation 10.6
MDS-UPDRS Part III Subscale
Month 6
24.3 score on a scale
Standard Deviation 10.9
23.2 score on a scale
Standard Deviation 12.4
21.3 score on a scale
Standard Deviation 10.8
MDS-UPDRS Part III Subscale
Month 10
23.3 score on a scale
Standard Deviation 9.2
21.6 score on a scale
Standard Deviation 12.1
21.0 score on a scale
Standard Deviation 11.0
MDS-UPDRS Part III Subscale
Month 12
24.1 score on a scale
Standard Deviation 10.0
22.8 score on a scale
Standard Deviation 12.0
21.8 score on a scale
Standard Deviation 10.5
MDS-UPDRS Part III Subscale
Month 18
24.2 score on a scale
Standard Deviation 10.1
23.0 score on a scale
Standard Deviation 11.7
22.2 score on a scale
Standard Deviation 10.9

SECONDARY outcome

Timeframe: Day 0, Months 2, 4, 6, 8, 10, 12, 14, 16, 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment and 'n' signifies participants who were evaluable at specified timepoints.

The early-stage Parkinson's disease (ePD) subscore is derived from a 15-item subset of the MDS-UPDRS Part III (Motor Examination). It includes all rigidity assessments (neck, upper limbs \[right/left\], and lower limbs \[right/left\]) and bradykinesia-related tasks: finger tapping (right/left), hand movements (right/left), pronation-supination of hands (right/left), toe tapping (right/left), and leg agility (right/left). Each item is scored on a 5-point likert scale (0 = no problem to 4 = severe), resulting in a total ePD subscore range of 0 to 60. Higher scores indicate greater motor impairment, while lower scores reflect better motor function.

Outcome measures

Outcome measures
Measure
Placebo
n=159 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=162 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
MDS-UPDRS Part III Early-stage Parkinson's Disease (ePD) Subscore on Selected Items
Day 0
13.3 score on a scale
Standard Deviation 7.11
12.6 score on a scale
Standard Deviation 7.96
11.8 score on a scale
Standard Deviation 6.85
MDS-UPDRS Part III Early-stage Parkinson's Disease (ePD) Subscore on Selected Items
Month 6
13.9 score on a scale
Standard Deviation 7.39
13.4 score on a scale
Standard Deviation 8.42
12.4 score on a scale
Standard Deviation 7.58
MDS-UPDRS Part III Early-stage Parkinson's Disease (ePD) Subscore on Selected Items
Month 10
13.4 score on a scale
Standard Deviation 6.46
12.1 score on a scale
Standard Deviation 8.14
11.9 score on a scale
Standard Deviation 7.98
MDS-UPDRS Part III Early-stage Parkinson's Disease (ePD) Subscore on Selected Items
Month 12
13.7 score on a scale
Standard Deviation 6.98
12.7 score on a scale
Standard Deviation 8.20
12.9 score on a scale
Standard Deviation 7.61
MDS-UPDRS Part III Early-stage Parkinson's Disease (ePD) Subscore on Selected Items
Month 8
13.4 score on a scale
Standard Deviation 6.82
12.7 score on a scale
Standard Deviation 8.60
11.8 score on a scale
Standard Deviation 7.49
MDS-UPDRS Part III Early-stage Parkinson's Disease (ePD) Subscore on Selected Items
Month 14
13.8 score on a scale
Standard Deviation 7.14
12.7 score on a scale
Standard Deviation 8.35
12.5 score on a scale
Standard Deviation 7.88
MDS-UPDRS Part III Early-stage Parkinson's Disease (ePD) Subscore on Selected Items
Month 16
13.8 score on a scale
Standard Deviation 7.24
12.9 score on a scale
Standard Deviation 8.26
12.4 score on a scale
Standard Deviation 7.83
MDS-UPDRS Part III Early-stage Parkinson's Disease (ePD) Subscore on Selected Items
Month 18
13.8 score on a scale
Standard Deviation 7.34
12.9 score on a scale
Standard Deviation 7.90
12.6 score on a scale
Standard Deviation 7.61
MDS-UPDRS Part III Early-stage Parkinson's Disease (ePD) Subscore on Selected Items
Month 4
13.4 score on a scale
Standard Deviation 7.50
13.1 score on a scale
Standard Deviation 8.76
11.8 score on a scale
Standard Deviation 7.64
MDS-UPDRS Part III Early-stage Parkinson's Disease (ePD) Subscore on Selected Items
Month 2
13.2 score on a scale
Standard Deviation 7.33
13.2 score on a scale
Standard Deviation 8.48
11.6 score on a scale
Standard Deviation 7.57

SECONDARY outcome

Timeframe: Day 0, Months 2, 4, 6, 8, 10, 12, 14, 16, 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment and 'n' signifies participants who were evaluable at specified timepoints.

MDS-UPDRS part II includes motor items assessing speech, saliva and drooling, chewing and swallowing, eating tasks (cutting food and handling utensils), dressing, hygiene, handwriting, doing hobbies and other activities, turning in bed, tremor, getting out of bed, a car or a deep chair, walking and balance, and freezing. Each of the items in the UPDRS is measured on a scale. It included 13-items, each anchored with 5 responses: 0 = normal, 1 = slight, 2 = mild, 3 = moderate, and 4 = severe. The scale range for Part II was 0-52, with higher scores reflecting greater severity.

Outcome measures

Outcome measures
Measure
Placebo
n=163 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=163 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=161 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
MDS-UPDRS Part II Subscale
Day 0
6.0 score on a scale
Standard Deviation 4.0
6.3 score on a scale
Standard Deviation 4.6
5.7 score on a scale
Standard Deviation 4.3
MDS-UPDRS Part II Subscale
Month 6
7.7 score on a scale
Standard Deviation 5.1
7.7 score on a scale
Standard Deviation 6.2
6.7 score on a scale
Standard Deviation 5.0
MDS-UPDRS Part II Subscale
Month 14
7.1 score on a scale
Standard Deviation 4.8
7.2 score on a scale
Standard Deviation 5.8
7.0 score on a scale
Standard Deviation 5.1
MDS-UPDRS Part II Subscale
Month 2
6.5 score on a scale
Standard Deviation 4.3
6.9 score on a scale
Standard Deviation 5.2
6.1 score on a scale
Standard Deviation 4.1
MDS-UPDRS Part II Subscale
Month 4
6.8 score on a scale
Standard Deviation 4.6
7.1 score on a scale
Standard Deviation 5.4
6.4 score on a scale
Standard Deviation 4.5
MDS-UPDRS Part II Subscale
Month 8
7.0 score on a scale
Standard Deviation 4.6
7.1 score on a scale
Standard Deviation 5.7
6.9 score on a scale
Standard Deviation 4.7
MDS-UPDRS Part II Subscale
Month 10
6.9 score on a scale
Standard Deviation 4.5
6.7 score on a scale
Standard Deviation 5.4
7.1 score on a scale
Standard Deviation 4.7
MDS-UPDRS Part II Subscale
Month 12
6.9 score on a scale
Standard Deviation 4.9
7.3 score on a scale
Standard Deviation 5.5
7.3 score on a scale
Standard Deviation 5.1
MDS-UPDRS Part II Subscale
Month 16
7.1 score on a scale
Standard Deviation 5.1
7.2 score on a scale
Standard Deviation 5.7
6.7 score on a scale
Standard Deviation 4.5
MDS-UPDRS Part II Subscale
Month 18
7.3 score on a scale
Standard Deviation 5.0
6.8 score on a scale
Standard Deviation 5.2
7.3 score on a scale
Standard Deviation 5.3

SECONDARY outcome

Timeframe: Day 0, Months 2, 4, 6, 8, 10, 12, 14, 16, 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment and 'n' signifies participants who were evaluable at specified timepoints.

MDS-UPDRS part I include several non-motor aspects of experiences of daily living including cognitive impairment, hallucinations and psychosis, depressed mood, anxious mood, apathy, features of dopamine dysregulation syndrome during part 1A and sleep problems, daytime sleepiness, pain and other sensation, urinary problems, constipation problems, lightheadedness on standing, and fatigue during Part 1B. Part I assessed non-motor experiences of daily living and has 2 components (Range 0-52). Part IA contained 6 questions and were assessed by examiner (Range 0-24). Part IB contained 7 questions on non-motor experiences of daily living which were completed by participant (Range 0-28). Each of items in UPDRS is measured on a scale of 0 to 4, where 0 is normal and 4 (higher score) represents severe abnormalities/worse outcome. Total Score Range 0 to 52. Total score is sum of Part IA (0-24) and Part IB (0-28) subscale scores. Higher scores indicated greater severity of non-motor symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=158 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=161 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=158 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
MDS-UPDRS Part I Subscale
Month 4
5.1 score on a scale
Standard Deviation 4.4
5.0 score on a scale
Standard Deviation 4.0
4.5 score on a scale
Standard Deviation 3.8
MDS-UPDRS Part I Subscale
Day 0
5.4 score on a scale
Standard Deviation 3.9
5.5 score on a scale
Standard Deviation 4.4
4.7 score on a scale
Standard Deviation 3.7
MDS-UPDRS Part I Subscale
Month 2
5.2 score on a scale
Standard Deviation 4.2
5.2 score on a scale
Standard Deviation 3.8
4.3 score on a scale
Standard Deviation 3.5
MDS-UPDRS Part I Subscale
Month 6
5.9 score on a scale
Standard Deviation 4.8
5.7 score on a scale
Standard Deviation 4.5
5.1 score on a scale
Standard Deviation 3.9
MDS-UPDRS Part I Subscale
Month 8
5.5 score on a scale
Standard Deviation 4.4
5.3 score on a scale
Standard Deviation 4.2
5.0 score on a scale
Standard Deviation 3.9
MDS-UPDRS Part I Subscale
Month 10
5.4 score on a scale
Standard Deviation 4.2
5.4 score on a scale
Standard Deviation 4.1
4.9 score on a scale
Standard Deviation 4.1
MDS-UPDRS Part I Subscale
Month 12
6.2 score on a scale
Standard Deviation 5.1
6.2 score on a scale
Standard Deviation 4.8
5.3 score on a scale
Standard Deviation 4.4
MDS-UPDRS Part I Subscale
Month 14
5.9 score on a scale
Standard Deviation 4.6
5.8 score on a scale
Standard Deviation 5.0
5.0 score on a scale
Standard Deviation 4.2
MDS-UPDRS Part I Subscale
Month 16
5.9 score on a scale
Standard Deviation 4.8
5.9 score on a scale
Standard Deviation 5.1
5.1 score on a scale
Standard Deviation 4.1
MDS-UPDRS Part I Subscale
Month 18
6.4 score on a scale
Standard Deviation 5.1
5.9 score on a scale
Standard Deviation 4.6
5.3 score on a scale
Standard Deviation 4.5

SECONDARY outcome

Timeframe: Baseline to Month 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment.

The participant was considered to have an emerging symptom for the item, if the change from Baseline for the item is greater than 0 for 2 consecutive visits. The magnitude of change from Baseline was not considered to determine the emerging symptom. Movement Disorder Society Unified Parkinson's Disease Rating Scale (MDS-UPDRS) part II includes motor items assessing speech, saliva and drooling, chewing and swallowing, eating tasks (cutting food and handling utensils), dressing, hygiene, handwriting, doing hobbies and other activities, turning in bed, tremor, getting out of bed, a car or a deep chair, walking and balance, and freezing. This included 13-items, each anchored with 5 responses: 0 = normal, 1 = slight, 2 = mild, 3 = moderate, and 4 = severe. The scale range for Part II was 0-52, with higher scores reflecting greater severity.

Outcome measures

Outcome measures
Measure
Placebo
n=163 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=164 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 3
37 Participants
15 Participants
26 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 0
28 Participants
36 Participants
38 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 1
18 Participants
41 Participants
31 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 2
35 Participants
33 Participants
23 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 4
15 Participants
13 Participants
15 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 5
15 Participants
13 Participants
14 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 6
4 Participants
7 Participants
10 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 7
4 Participants
4 Participants
4 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 8
4 Participants
1 Participants
3 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 9
2 Participants
1 Participants
0 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 10
1 Participants
0 Participants
0 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 11
0 Participants
0 Participants
0 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 12
0 Participants
0 Participants
0 Participants
Emerging Symptoms in Participants as Measured by MDS-UPDRS Part II
Number of Emerging symptoms: 13
0 Participants
0 Participants
0 Participants

SECONDARY outcome

Timeframe: Baseline to Month 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment.

Time to worsening of the disease on the MDS-UPDRS III scale as defined by a 5-point increase in MDS-UPDRS III, within the 18-month period. MDS-UPDRS part III includes motor items assessing speech, facial expression, rigidity, finger tapping, hand movements, pronation supination movements of hands, toe tapping, leg agility, arising from chair, gait, freezing of gait, postural stability, posture, global spontaneity of movement (body bradykinesia), postural tremor of the hands, kinetic tremor of the hands, rest tremor amplitude, and constancy of rest tremor. It included 33 scores based on 18-items, each anchored with 5 responses: 0 = normal, 1 = slight, 2 = mild, 3 = moderate, and 4 = severe. The scale range was from 0 to 132, with a lower score indicating better motor function and a higher score indicating more severe motor symptoms.

Outcome measures

Outcome measures
Measure
Placebo
n=163 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=164 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Time to Worsening of the Disease as Measured by MDS-UPDRS Part III
8.64 months
Interval 7.7236 to 9.5635
8.95 months
Interval 7.8974 to 10.0012
9.45 months
Interval 8.4743 to 10.434

SECONDARY outcome

Timeframe: Screening, Month 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, 'n' signifies participants who were evaluable at each specified timepoints.

The Montreal Cognitive Assessment (MoCA) is a standardized screening tool used to evaluate mild cognitive impairment across multiple cognitive functions i.e. visuospatial/executive function, naming, memory, attention, language, abstraction, delayed recall, and orientation. The total possible score is calculated by summing the scores across all functions ranges from: 0 to 30. A score of 26 or above is considered normal, a lower score indicates cognitive impairment.

Outcome measures

Outcome measures
Measure
Placebo
n=163 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=164 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Montreal Cognitive Assessment (MoCA)
Screening
27.8 score on a scale
Standard Deviation 1.8
27.6 score on a scale
Standard Deviation 2.0
27.8 score on a scale
Standard Deviation 1.7
Montreal Cognitive Assessment (MoCA)
Month 18
27.4 score on a scale
Standard Deviation 2.2
27.3 score on a scale
Standard Deviation 2.4
27.3 score on a scale
Standard Deviation 2.4

SECONDARY outcome

Timeframe: Screening, Months 12 and 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment and 'n' signifies participants who were evaluable at each specified timepoints.

The change from screening in mean striatum specific binding ratios (SBR) was assessed by DaT-SPECT using 123I-Ioflupane as radiopharmaceutical. The whole striatum was calculated as the average of the SBR data values for the four following "small" regions: left caudate small, left putamen small, right caudate small and right putamen small. The SBR was calculated for each region with the occipital cortex as a reference region, where a lower SBR indicates worse disease. The following formula was used to calculate this: (Average \[Small region\] - Average \[Occipital region\])/ (Average \[Occipital region\]).

Outcome measures

Outcome measures
Measure
Placebo
n=140 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=133 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=130 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Ipsilateral putamen small: Month 18
-0.208 specific binding ratio
Standard Deviation 0.252
-0.150 specific binding ratio
Standard Deviation 0.260
-0.179 specific binding ratio
Standard Deviation 0.270
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Whole striatum: Month 12
-0.202 specific binding ratio
Standard Deviation 0.215
-0.141 specific binding ratio
Standard Deviation 0.194
-0.102 specific binding ratio
Standard Deviation 0.254
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Whole striatum: Month 18
-0.233 specific binding ratio
Standard Deviation 0.226
-0.182 specific binding ratio
Standard Deviation 0.232
-0.193 specific binding ratio
Standard Deviation 0.254
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Ipsilateral striatum: Month 12
-0.237 specific binding ratio
Standard Deviation 0.262
-0.161 specific binding ratio
Standard Deviation 0.246
-0.093 specific binding ratio
Standard Deviation 0.294
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Ipsilateral striatum: Month 18
-0.260 specific binding ratio
Standard Deviation 0.263
-0.211 specific binding ratio
Standard Deviation 0.282
-0.194 specific binding ratio
Standard Deviation 0.318
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Contralateral striatum: Month 12
-0.161 specific binding ratio
Standard Deviation 0.210
-0.138 specific binding ratio
Standard Deviation 0.209
-0.099 specific binding ratio
Standard Deviation 0.278
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Contralateral striatum: Month 18
-0.203 specific binding ratio
Standard Deviation 0.214
-0.169 specific binding ratio
Standard Deviation 0.237
-0.188 specific binding ratio
Standard Deviation 0.259
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Ipsilateral caudate small: Month 12
-0.296 specific binding ratio
Standard Deviation 0.380
-0.196 specific binding ratio
Standard Deviation 0.352
-0.080 specific binding ratio
Standard Deviation 0.485
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Ipsilateral caudate small: Month 18
-0.312 specific binding ratio
Standard Deviation 0.383
-0.273 specific binding ratio
Standard Deviation 0.390
-0.210 specific binding ratio
Standard Deviation 0.439
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Ipsilateral putamen small: Month 12
-0.178 specific binding ratio
Standard Deviation 0.260
-0.125 specific binding ratio
Standard Deviation 0.255
-0.106 specific binding ratio
Standard Deviation 0.219
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Contralateral caudate small: Month 12
-0.256 specific binding ratio
Standard Deviation 0.328
-0.183 specific binding ratio
Standard Deviation 0.332
-0.145 specific binding ratio
Standard Deviation 0.363
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Contralateral caudate small: Month 18
-0.291 specific binding ratio
Standard Deviation 0.330
-0.263 specific binding ratio
Standard Deviation 0.370
-0.248 specific binding ratio
Standard Deviation 0.398
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Contralateral putamen small: Month 12
-0.066 specific binding ratio
Standard Deviation 0.190
-0.094 specific binding ratio
Standard Deviation 0.223
-0.053 specific binding ratio
Standard Deviation 0.304
Change From Screening in Dopamine Transporter Imaging With Single Photon Emission Computed Tomography (DaT-SPECT) Mean Striatum Specific Binding Ratios (SBR)
Contralateral putamen small: Month 18
-0.115 specific binding ratio
Standard Deviation 0.190
-0.076 specific binding ratio
Standard Deviation 0.197
-0.128 specific binding ratio
Standard Deviation 0.209

SECONDARY outcome

Timeframe: Baseline to Month 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment.

Time to start of symptomatic treatment (ST) within the 18-month period.

Outcome measures

Outcome measures
Measure
Placebo
n=163 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=164 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Time to Start of Symptomatic Treatment (ST)
10.58 months
Interval 9.6242 to 11.5456
11.59 months
Interval 10.6084 to 12.5623
11.80 months
Interval 10.8312 to 12.7735

SECONDARY outcome

Timeframe: Month 18

Population: FAS included all randomized study participants who received at least a partial dose of study medication, have at least 1 post-Baseline assessment. Here, number of participants analyzed included all participants who were evaluable for this assessment.

Cumulative number of participants on symptomatic treatment (ST) at 18 months are reported.

Outcome measures

Outcome measures
Measure
Placebo
n=153 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=139 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=140 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Symptomatic Treatment (ST) Intake
111 Participants
89 Participants
88 Participants

SECONDARY outcome

Timeframe: From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)

Population: Safety set included all randomized study participants who receive at least a partial dose of study medication.

An AE is any untoward medical occurrence in a patient or clinical study participant, temporally associated with the use of study medication, whether or not considered related to the study medication. A TEAE is defined as any AE with a start date on or after the first dose of treatment or any unresolved event already present before administration of treatment that worsens in intensity following exposure to the treatment.

Outcome measures

Outcome measures
Measure
Placebo
n=164 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=165 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Percentage of Participants With Treatment-emergent Adverse Events (TEAEs)
87.8 percentage of participants
86.7 percentage of participants
87.2 percentage of participants

SECONDARY outcome

Timeframe: From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)

Population: Safety set included all randomized study participants who receive at least a partial dose of study medication.

Serious adverse event: Death, a life-threatening adverse event, inpatient hospitalization or prolongation of existing hospitalization, a persistent or significant incapacity or substantial disruption of the ability to conduct normal life functions, or a congenital anomaly/birth defect. Important medical events that may not result in death, be life-threatening, or require hospitalization may be considered serious when, based upon appropriate medical judgment, they may jeopardize the patient or subject and may require medical or surgical intervention to prevent one of the outcomes listed in this definition.

Outcome measures

Outcome measures
Measure
Placebo
n=164 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=165 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Percentage of Participants With Serious TEAEs
5.5 percentage of participants
7.9 percentage of participants
8.5 percentage of participants

SECONDARY outcome

Timeframe: From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)

Population: Safety set included all randomized study participants who receive at least a partial dose of study medication.

An AE is any untoward medical occurrence in a patient or clinical study participant, temporally associated with the use of study medication, whether or not considered related to the study medication. A TEAE is defined as any AE with a start date on or after the first dose of treatment or any unresolved event already present before administration of treatment that worsens in intensity following exposure to the treatment.

Outcome measures

Outcome measures
Measure
Placebo
n=164 Participants
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=165 Participants
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 Participants
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Percentage of Participants With TEAEs Leading to Participant Withdrawal
2.4 percentage of participants
10.9 percentage of participants
9.8 percentage of participants

Adverse Events

Placebo

Serious events: 9 serious events
Other events: 102 other events
Deaths: 0 deaths

UCB0599 180 mg/Day

Serious events: 13 serious events
Other events: 97 other events
Deaths: 1 deaths

UCB0599 360 mg/Day

Serious events: 14 serious events
Other events: 89 other events
Deaths: 1 deaths

Serious adverse events

Serious adverse events
Measure
Placebo
n=164 participants at risk
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=165 participants at risk
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 participants at risk
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Cardiac disorders
Palpitations
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Cardiac disorders
Acute coronary syndrome
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Cardiac disorders
Angina pectoris
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Cardiac disorders
Mitral valve prolapse
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Cardiac disorders
Atrial fibrillation
1.2%
2/164 • Number of events 2 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Cardiac disorders
Cardiac arrest
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Gastrointestinal disorders
Pancreatitis acute
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Gastrointestinal disorders
Intestinal polyp
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 2 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Gastrointestinal disorders
Diarrhoea
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Gastrointestinal disorders
Inguinal hernia
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Gastrointestinal disorders
Rectal haemorrhage
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Gastrointestinal disorders
Gastrointestinal haemorrhage
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
General disorders
Chest pain
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Hepatobiliary disorders
Hepatic cytolysis
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Immune system disorders
Drug hypersensitivity
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
Diverticulitis
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
Coronavirus infection
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
Pneumonia
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
Pneumonia aspiration
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
Infectious pleural effusion
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
Urosepsis
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
Urinary tract infection
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Injury, poisoning and procedural complications
Postoperative ileus
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Injury, poisoning and procedural complications
Hip fracture
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Injury, poisoning and procedural complications
Fall
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Injury, poisoning and procedural complications
Jaw fracture
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Gastric cancer
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Metastatic gastric cancer
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Prostate cancer
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Lung neoplasm malignant
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Malignant melanoma
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Nervous system disorders
Transient ischaemic attack
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Nervous system disorders
Vocal cord paralysis
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Renal and urinary disorders
Urinary bladder polyp
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Renal and urinary disorders
Acute kidney injury
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Renal and urinary disorders
Nephrolithiasis
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Renal and urinary disorders
Renal colic
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Respiratory, thoracic and mediastinal disorders
Dyspnoea
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Skin and subcutaneous tissue disorders
Angioedema
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Skin and subcutaneous tissue disorders
Erythema
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/165 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/164 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Skin and subcutaneous tissue disorders
Rash
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.61%
1/165 • Number of events 1 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
0.00%
0/164 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.

Other adverse events

Other adverse events
Measure
Placebo
n=164 participants at risk
Participants received UCB0599 matching-placebo capsules, orally, from Day 1 up to 18 months during treatment period.
UCB0599 180 mg/Day
n=165 participants at risk
Participants received UCB0599 90 milligram (mg) capsules twice daily (BID), for a total daily dose of 180 mg, along with matching placebo capsules BID, administered orally from Day 1 up to 18 months during treatment period.
UCB0599 360 mg/Day
n=164 participants at risk
Participants received UCB0599 180 mg capsules twice daily (BID), for a total daily dose of 360 mg, administered orally from Day 1 up to 18 months during treatment period.
Gastrointestinal disorders
Nausea
4.9%
8/164 • Number of events 15 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
7.3%
12/165 • Number of events 14 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
4.9%
8/164 • Number of events 8 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Gastrointestinal disorders
Diarrhoea
4.9%
8/164 • Number of events 10 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
6.1%
10/165 • Number of events 18 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
5.5%
9/164 • Number of events 10 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Gastrointestinal disorders
Constipation
8.5%
14/164 • Number of events 14 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
4.2%
7/165 • Number of events 7 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
4.9%
8/164 • Number of events 9 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
General disorders
Fatigue
7.3%
12/164 • Number of events 14 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
7.9%
13/165 • Number of events 15 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
4.3%
7/164 • Number of events 7 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
COVID-19
21.3%
35/164 • Number of events 38 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
13.3%
22/165 • Number of events 23 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
19.5%
32/164 • Number of events 33 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
Urinary tract infection
9.1%
15/164 • Number of events 20 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
10.9%
18/165 • Number of events 26 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
7.3%
12/164 • Number of events 14 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
Nasopharyngitis
11.6%
19/164 • Number of events 20 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
8.5%
14/165 • Number of events 16 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
8.5%
14/164 • Number of events 15 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Infections and infestations
Influenza
6.1%
10/164 • Number of events 10 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
3.6%
6/165 • Number of events 7 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
8.5%
14/164 • Number of events 15 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Injury, poisoning and procedural complications
Fall
5.5%
9/164 • Number of events 9 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
10.3%
17/165 • Number of events 22 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
7.3%
12/164 • Number of events 14 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Musculoskeletal and connective tissue disorders
Back pain
10.4%
17/164 • Number of events 17 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
9.1%
15/165 • Number of events 19 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
7.3%
12/164 • Number of events 14 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Musculoskeletal and connective tissue disorders
Arthralgia
11.6%
19/164 • Number of events 22 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
8.5%
14/165 • Number of events 14 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
2.4%
4/164 • Number of events 4 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Nervous system disorders
Headache
9.8%
16/164 • Number of events 17 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
6.7%
11/165 • Number of events 25 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
9.8%
16/164 • Number of events 24 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
Skin and subcutaneous tissue disorders
Rash
5.5%
9/164 • Number of events 10 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
3.0%
5/165 • Number of events 5 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.
6.7%
11/164 • Number of events 11 • From Baseline up to 30 days of safety follow-up after the last dose of the study drug (up to 19 months)
Safety analysis set included all randomized study participants who received at least a partial dose of study medication.

Additional Information

UCB

Cares

Phone: +1-844-599-2273

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: GT60