A Study of TAR-200 in Combination With Cetrelimab, TAR-200 Alone, or Cetrelimab Alone in Participants With Non-Muscle Invasive Bladder Cancer (NMIBC) Unresponsive to Intravesical Bacillus Calmette-Guérin Who Are Ineligible for or Elected Not to Undergo Radical Cystectomy

NCT ID: NCT04640623

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

220 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-12-18

Study Completion Date

2027-07-02

Brief Summary

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The purpose of this study is to evaluate the overall complete response (CR) rate in participants treated with TAR-200 in combination with cetrelimab (Cohort 1), or TAR-200 alone (Cohort 2), or cetrelimab alone (Cohort 3) with Carcinoma in Situ (CIS), with or without concomitant high-grade Ta or T1 papillary disease; and disease-free survival (DFS) in participants treated with TAR-200 alone with papillary disease only (Cohort 4).

Detailed Description

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Conditions

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Urinary Bladder Neoplasms

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cohort 1: TAR-200 and Cetrelimab

TAR-200 is placed into the bladder through a urinary placement catheter in participants with carcinoma in situ (CIS), with or without papillary disease, on Day 0 and will be dosed every 3 weeks (Q3W) for up to the first 24 weeks (6 months), then every 12 weeks through Week 99 (Year 2). In addition, Cetrelimab will be dosed Q3W through Week 78 (18 months).

Group Type EXPERIMENTAL

TAR-200

Intervention Type DRUG

TAR-200 will be administered transuretherally.

Cetrelimab

Intervention Type BIOLOGICAL

Cetrelimab will be administered.

Cohort 2: TAR-200

TAR-200 is placed into the bladder through a urinary placement catheter in participants with CIS, with or without papillary disease, on Day 0 and will be dosed Q3W for up to the first 24 weeks (6 months), then every 12 weeks through Week 99 (Year 2).

Group Type EXPERIMENTAL

TAR-200

Intervention Type DRUG

TAR-200 will be administered transuretherally.

Cohort 3: Cetrelimab

Participants with CIS, with or without papillary disease, will receive Cetrelimab which will be dosed Q3W through Week 78 (18 months).

Group Type EXPERIMENTAL

Cetrelimab

Intervention Type BIOLOGICAL

Cetrelimab will be administered.

Cohort 4: TAR-200 (Participants with Papillary Disease only)

TAR-200 is placed into the bladder through a urinary placement catheter in participants with papillary disease only, on Day 0 and will be dosed Q3W for up to the first 24 weeks (6 months), then every 12 weeks through Week 99 (Year 2).

Group Type EXPERIMENTAL

TAR-200

Intervention Type DRUG

TAR-200 will be administered transuretherally.

Interventions

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TAR-200

TAR-200 will be administered transuretherally.

Intervention Type DRUG

Cetrelimab

Cetrelimab will be administered.

Intervention Type BIOLOGICAL

Other Intervention Names

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JNJ-17000139 Gemcitabine-Releasing Intravesical System JNJ-63723283

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed diagnosis of persistent or recurrent high-risk non-muscle invasive bladder cancer (HR-NMIBC), (carcinoma in situ \[CIS\] or tumor in situ \[Tis\]), with or without papillary disease (T1, high-grade Ta) or papillary disease only (high-grade Ta or any T1 and absence of CIS), within 12 months of completion of the last dose of Bacillus Calmette-Guerin (BCG) therapy, in participants who have received adequate BCG. Mixed histology tumors are allowed if urothelial differentiation (transitional cell histology) is predominant. However, the presence of neuroendocrine, micropapillary, signet ring cell, plasmacytoid, or sarcomatoid features will make a participant ineligible. For participants with lamina propria invasion (T1) on the screening biopsy/ transurethral resection of bladder tumor (TURBT), muscularis propria must be present in order to rule out Muscle Invasive Bladder Cancer (MIBC)
* All visible papillary disease must be fully resected (absent) prior to randomization (residual CIS is acceptable for participants eligible for Cohorts 1, 2, and 3 only) and documented in the electronic case report form (eCRF) at screening cystoscopy. For participants with papillary disease only (Cohort 4), local urine cytology at screening must be negative or atypical (for High-Grade Urothelial Carcinoma \[HGUC\])
* Participants must be ineligible for or have elected not to undergo radical cystectomy
* BCG-unresponsive high-risk NMIBC after treatment with adequate BCG therapy defined as a minimum of 5 of 6 full doses of an induction course (adequate induction) plus 2 of 3 doses of a maintenance course, or at least 2 of 6 doses of a second induction course
* Eastern Cooperative Oncology Group (ECOG) performance status Grade 0, 1, or 2

Exclusion Criteria

* Presence or history of histologically confirmed, muscle-invasive, locally advanced, nonresectable, or metastatic urothelial carcinoma (that is, T2, T3, T4, and/or Stage IV)
* Must not have had urothelial carcinoma or histological variant at any site outside of the urinary bladder. Ta/T1/CIS of the upper urinary tract (including renal pelvis and ureter) is allowable if treated with complete nephroureterectomy more than 24 months prior to randomization
* Received a live virus vaccine within 30 days prior to the initiation of study treatment. Inactivated (non-live or non-replicating) vaccines approved or authorized for emergency use (for example, COVID-19) by local health authorities are allowed
* Active hepatitis B or C infection (for example, participants with history of hepatitis C infection but undetectable hepatitis C virus polymerase chain reaction (PCR) test and participants with history of hepatitis B infection with positive hepatitis B surface antigen (HBsAg) antibody and undetectable PCR are allowed)
* Prior therapy with an anti-programmed-cell death 1 (PD-1), anti-PD-ligand 2 (L2) agent, or with an agent directed to another co-inhibitory T-cell receptor
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Janssen Research & Development, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Janssen Research & Development, LLC Clinical Trial

Role: STUDY_DIRECTOR

Janssen Research & Development, LLC

Locations

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Urological Associates of Southern Arizona, P.C.

Tucson, Arizona, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

Genesis Healthcare Partners - Genesis Research Greater Los Angeles

Sherman Oaks, California, United States

Site Status

The Urology Center of Colorado

Denver, Colorado, United States

Site Status

Foothills Urology - Golden Off

Golden, Colorado, United States

Site Status

DuPage Medical Group

Lisle, Illinois, United States

Site Status

Urology of Indiana

Greenwood, Indiana, United States

Site Status

Wichita Urology Group

Wichita, Kansas, United States

Site Status

Michigan Institute of Urology

Troy, Michigan, United States

Site Status

NYU Langone Health

New York, New York, United States

Site Status

SUNY Upstate Medical University

Syracuse, New York, United States

Site Status

Associated Medical Professionals

Syracuse, New York, United States

Site Status

Levine Cancer Institute

Charlotte, North Carolina, United States

Site Status

The Urology Group

Cincinnati, Ohio, United States

Site Status

Urologic Consultants of Southeastern Pennsylvania

Bala-Cynwyd, Pennsylvania, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

Urology Associates, PC

Nashville, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Urology Austin

Austin, Texas, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

Urology San Antonio Research

San Antonio, Texas, United States

Site Status

Spokane Urology

Spokane, Washington, United States

Site Status

Flinders Medical Centre

Bedford Park, , Australia

Site Status

Eastern Health Research

Box Hill, , Australia

Site Status

Macquarie University Hospital

Sydney, , Australia

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Algemeen Ziekenhuis Sint-Jan

Assebroek, , Belgium

Site Status

AZ St.-Jan Brugge-Oostende AV

Bruges, , Belgium

Site Status

Hopital Erasme

Brussels, , Belgium

Site Status

Algemeen ziekenhuis Maria Middelares

Ghent, , Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status

Algemeen Ziekenhuis Delta

Roeselare, , Belgium

Site Status

AZ Nikolaas

Sint-Niklaas, , Belgium

Site Status

Exdeo Clinical Research Inc

Abbotsford, British Columbia, Canada

Site Status

William Osler Health System

Brampton, Ontario, Canada

Site Status

Princess Margaret Hospital- UHN

Toronto, Ontario, Canada

Site Status

McGill University Health Centre

Montreal, Quebec, Canada

Site Status

Universite de Sherbrooke

Sherbrooke, Quebec, Canada

Site Status

Hopital Pellegrin CHU Bordeaux

Bordeaux, , France

Site Status

Polyclinique Bordeaux Nord Acquitaine

Bordeaux, , France

Site Status

CHU Grenoble

Grenoble, , France

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Clinique Sainte Marguerite

Hyères, , France

Site Status

Polyclinique de Limoges - Francois Chenieux

Limoges, , France

Site Status

Hôpital Edouard Herriot

Lyon, , France

Site Status

Institut Paoli-Calmettes

Marseille, , France

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Centre de Cancerologie du Grand Montpellier

Montpellier, , France

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CHU Nimes

Nîmes, , France

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Hopital Saint Louis

Paris, , France

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Hôpital Universitaire Pitié-Salpêtrière

Paris, , France

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Hopital Europeen Georges-Pompidou

Paris, , France

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Groupe Hospitalier Diaconesses Croix Saint Simon

Paris, , France

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Hopital Bichat Claude Bernard

Paris, , France

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Clinical La Croix Du Sud - Ramsay Santé

Quint-Fonsegrives, , France

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Hopital Pontchaillou

Rennes, , France

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CHP Saint Gregoire

Saint-Grégoire, , France

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Institut de Cancerologie Strasbourg Europe ICANS

Strasbourg, , France

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Hopital Foch

Suresnes, , France

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Hopital Rangueil

Toulouse, , France

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Urologische Partnerschaft Koln UPK

Cologne, , Germany

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Urologicum Duisburg

Duisburg, , Germany

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Klinikum Herne - Urologie

Herne, , Germany

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Matthias Schulze - Germany

Markkleeberg, , Germany

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Urologie Neandertal Praxis Mettmann

Mettmann, , Germany

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Universitatsklinikum Munster

Münster, , Germany

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Schön Klinik Nürnberg Fürth

Nuremberg, , Germany

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Studienpraxis Urologie Nürtingen - Germany

Nürtingen, , Germany

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Urologische Praxis am Wasserturm - Germany

Würselen, , Germany

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Metropolitan General A E

Cholargós, , Greece

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Athens Medical Center

Marousi, , Greece

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Bioclinic - Thessaloniki

Thessaloniki, , Greece

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General Hospital of Thessaloniki G. Gennimatas

Thessaloniki, , Greece

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Euromedica General Clinic

Thessaloniki, , Greece

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Papageorgiou General Hospital Of Thessaloniki

Thessaloniki, , Greece

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Azienda Ospedaliero Universitaria Consorziale Policlinico di Bari

Bari, , Italy

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Azienda Ospedaliero Universitaria Consorziale Policlinico di Bari

Bari, , Italy

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Azienda Ospedaliera Universitaria Careggi

Florence, , Italy

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Ospedale San Martino

Genova, , Italy

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Ospedale San Raffaele

Milan, , Italy

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Azienda Ospedaliero Universitaria Pisana

Pisa, , Italy

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Azienda Ospedaliera Sant Andrea

Roma, , Italy

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Istituto Nazionale Tumori Regina Elena

Rome, , Italy

Site Status

Azienda Ospedaliera Universitaria Citta della Salute e della Scienza di Torino

Torino, , Italy

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Ospedale di Circolo e Fondazione Macchi

Varese, , Italy

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Ospedale San Bortolo

Vicenza, , Italy

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Aso Co.,Ltd Iizuka Hospital

Iizuka, , Japan

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St Marianna University Hospital

Kanagawa, , Japan

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Nara Medical University Hospital

Kashihara-shi, , Japan

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Kimitsu Chuo Hospital

Kisarazu-shi, , Japan

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Nagasaki University Hospital

Nagasaki, , Japan

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JOHAS Osaka Rosai Hospital

Osaka, , Japan

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Toranomon Hospital

Tokyo, , Japan

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Toyama University Hospital

Toyama, , Japan

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Fujita Health University Hospital

Toyoake, , Japan

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University of Tsukuba Hospital

Tsukuba, , Japan

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Yokohama City University Medical Center

Yokohama, , Japan

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Antoni van Leeuwenhoek

Amsterdam, , Netherlands

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Catharina Ziekenhuis

Eindhoven, , Netherlands

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Canisius-Wilhelmina Ziekenhuis

Nijmegen, , Netherlands

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The Julius Center - Utrecht Science Park - Stratenum

Utrecht, , Netherlands

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Hospital Garcia de Orta

Almada, , Portugal

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Uls Regiao Aveiro - Hosp. Infante D. Pedro

Aveiro, , Portugal

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Uls Alto Ave - Hosp. Sra. Da Oliveira Guimaraes

Guimarães, , Portugal

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Centro Hospitalar de Lisboa Central

Lisbon, , Portugal

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Fund. Champalimaud

Lisbon, , Portugal

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Uls Loures Odivelas - Hosp. Loures

Loures, , Portugal

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Instituto Portugues de Oncologia do Porto Francisco Gentil

Porto, , Portugal

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Centro Hospitalar de Vila Nova de Gaia Espinho E P E

Vila Nova de Gaia, , Portugal

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Centro Hospitalar de Trás os Montes e Alto-Douro

Vila Real, , Portugal

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Hertzen Oncology Research Institute

Moscow, , Russia

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Privolzhsky District Medical Centre

Nizhny Novgorod, , Russia

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Avicenna Medical Center

Novosibirsk, , Russia

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A. Tsyb Medical Radiological Research Center

Obninsk, , Russia

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BHI of Omsk region Clinical Oncology Dispensary

Omsk, , Russia

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Ultrasound Clinic 4D

Pyatigorsk, , Russia

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Saratov State Medical University

Saratov, , Russia

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Multifunctional clinical medical center 'Medical city'

Tyumen, , Russia

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Bashkir State Medical University

Ufa, , Russia

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Inje University Haeundae Paik Hospital

Busan, , South Korea

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Kyungpook National University Chilgok Hospital

Daegu, , South Korea

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Keimyung University Dongsan Hospital

Daegu, , South Korea

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National Cancer Center

Goyang-si, , South Korea

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Chonnam National University Hospital

Gwangju, , South Korea

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Seoul National University Hospital

Seoul, , South Korea

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Severance Hospital

Seoul, , South Korea

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Gangnam Severance Hospital

Seoul, , South Korea

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The Catholic University of Korea Seoul St Mary s Hospital

Seoul, , South Korea

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Pusan National University Yangsan Hospital

Yangsan, , South Korea

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Hosp Univ A Coruna

A Coruña, , Spain

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Hosp. Univ. Germans Trias I Pujol

Badalona, , Spain

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Fund. Puigvert

Barcelona, , Spain

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Hosp. Puerta Del Mar

Cadiz, , Spain

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Hosp. Univ. Virgen de Las Nieves

Granada, , Spain

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Hosp. de Jerez de La Frontera

Jerez de la Frontera, , Spain

Site Status

Hosp. Univ. Ramon Y Cajal

Madrid, , Spain

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Hosp. Univ. 12 de Octubre

Madrid, , Spain

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Hosp. Univ. La Paz

Madrid, , Spain

Site Status

Hosp. Univ. Hm Monteprincipe

Madrid, , Spain

Site Status

Hosp Virgen de La Victoria

Málaga, , Spain

Site Status

Corporacio Sanitari Parc Tauli

Sabadell, , Spain

Site Status

Instituto Valenciano de Oncologia

Valencia, , Spain

Site Status

Chernihivskyi oblasnyi onkolohichnyi dyspanser

Chernihiv, , Ukraine

Site Status

Asklepion LLC

Kiev, , Ukraine

Site Status

Sumy Regional Clinical Oncology Centre

Sumy, , Ukraine

Site Status

NHS Greater Glasgow and Clyde

Glasgow, , United Kingdom

Site Status

Leeds Teaching Hospitals NHS Trust

Leeds, , United Kingdom

Site Status

Countries

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Turkey (Türkiye) United States Australia Belgium Canada France Germany Greece Italy Japan Netherlands Portugal Russia South Korea Spain Ukraine United Kingdom

References

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Daneshmand S, Van der Heijden MS, Jacob JM, Guerrero-Ramos F, Bogemann M, Simone G, Pieczonka CM, Casco NC, Zainfeld D, Spiegelhalder P, Xylinas E, Cahn D, Lotan Y, Murray KS, Kawahara T, Stromberg K, Martin J, Shukla A, Cutie CJ, Bertzos K, Hampras S, Sweiti H, Necchi A; SunRISe-1 Study. TAR-200 for Bacillus Calmette-Guerin-Unresponsive High-Risk Non-Muscle-Invasive Bladder Cancer: Results From the Phase IIb SunRISe-1 Study. J Clin Oncol. 2025 Jul 30:JCO2501651. doi: 10.1200/JCO-25-01651. Online ahead of print.

Reference Type DERIVED
PMID: 40737582 (View on PubMed)

Other Identifiers

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17000139BLC2001

Identifier Type: OTHER

Identifier Source: secondary_id

2020-002646-16

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

2023-506146-23-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

CR108921

Identifier Type: -

Identifier Source: org_study_id