Basket Study of Tucatinib and Trastuzumab in Solid Tumors With HER2 Alterations

NCT ID: NCT04579380

Last Updated: 2025-12-19

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

217 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-01-11

Study Completion Date

2026-04-30

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This trial studies how well tucatinib works for solid tumors that make either more HER2 or a different type of HER2 than usual (HER2 alterations) The solid tumors studied in this trial have either spread to other parts of the body (metastatic) or cannot be removed completely with surgery (unresectable).

All participants will get both tucatinib and trastuzumab. People with hormone-receptor positive breast cancer will also get a drug called fulvestrant.

The trial will also look at what side effects happen. A side effect is anything a drug does besides treating cancer.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

There are multiple cohorts in this trial:

* 5 tumor specific cohorts with HER2 overexpression/amplification (cervical cancer, uterine cancer, biliary tract cancer, urothelial cancer, and non-squamous non-small cell lung cancer \[NSCLC\])
* 2 tumor specific cohorts with HER2 mutations (non-squamous NSCLC and breast cancer)
* 2 cohorts which will enroll all other HER2 amplified/overexpressed solid tumor types (except breast cancer, gastric or gastroesophageal junction adenocarcinoma \[GEC\], and colorectal cancer \[CRC\]) or HER2-mutated solid tumor types.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Uterine Neoplasms Uterine Cervical Neoplasms Biliary Tract Neoplasms Urologic Neoplasms Carcinoma, Non-Small-Cell Lung HER2 Mutations Breast Neoplasms

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

Cervical cancer Uterine cancer Biliary tract cancer Urothelial cancer Non-squamous non-small cell lung cancer Non-squamous NSCLC Breast cancer Colorectal cancer Ampullary cancer Solid tumors Solid tumors harboring somatic HER2 mutations Seattle Genetics

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Tucatinib + Trastuzumab (+ Fulvestrant)

Tucatinib + trastuzumab (+ fulvestrant in hormone-receptor positive HER2-mutant breast cancer only)

Group Type EXPERIMENTAL

tucatinib

Intervention Type DRUG

300 mg orally twice daily

trastuzumab

Intervention Type DRUG

Given into the vein (intravenously; IV). 8mg/kg IV on Cycle 1 Day 1, and 6mg/kg every 21 days starting on Cycle 2 Day 1

fulvestrant

Intervention Type DRUG

Given into the muscle (intramuscular; IM) once every 4 weeks starting from Cycle 1 Day 1, plus one dose on Cycle 1 Day 15. Only administered to participants with hormone-receptor positive breast cancer.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

tucatinib

300 mg orally twice daily

Intervention Type DRUG

trastuzumab

Given into the vein (intravenously; IV). 8mg/kg IV on Cycle 1 Day 1, and 6mg/kg every 21 days starting on Cycle 2 Day 1

Intervention Type DRUG

fulvestrant

Given into the muscle (intramuscular; IM) once every 4 weeks starting from Cycle 1 Day 1, plus one dose on Cycle 1 Day 15. Only administered to participants with hormone-receptor positive breast cancer.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

TUKYSA, ARRY-380, ONT-380 Herceptin Faslodex

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Histologically or cytologically confirmed diagnosis of locally-advanced unresectable or metastatic solid tumor, including primary brain tumors
* Participants with non-squamous NSCLC must have progressed during or after standard treatment or for which no standard treatment is available
* Participants with other disease types must have progressed during or after ≥1 prior line of systemic therapy for locally-advanced unresectable or metastatic disease
* Disease progression during or after, or intolerance of, the most recent line of systemic therapy
* Disease demonstrating HER2 alterations (overexpression/amplification or HER2 activating mutations), as determined by local or central testing processed in a Clinical Laboratory Improvement Amendments (CLIA)- or International Organization for Standardization (ISO) accredited laboratory, according to one of the following:

* HER2 overexpression/amplification from fresh or archival tumor tissue or blood
* Known activating HER2 mutations detected in fresh or archival tumor tissue or blood
* Have measurable disease per RECIST v1.1 criteria according to investigator assessment
* Have Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1

Exclusion Criteria

* Participants with breast cancer, gastric or gastroesophageal junction adenocarcinoma, or CRC whose disease shows HER2 amplification/overexpression.
* Previous treatment with HER2-directed therapy; participants with uterine serous carcinoma or HER2-mutated gastric or gastroesophageal junction adenocarcinoma without HER2-overexpression/amplification may have received prior trastuzumab
* Known hypersensitivity to any component of the drug formulation of tucatinib or trastuzumab (drug substance, excipients, murine proteins), or any component of the drug formulation of fulvestrant in participants with HR+ HER2-mutated breast cancer
* History of exposure to a 360 mg/m² doxorubicin-equivalent or \>720 mg/m\^2 epirubicin-equivalent cumulative dose of anthracyclines
* Treatment with any systemic anti-cancer therapy, radiation therapy, major surgery, or experimental agent within ≤3 weeks of first dose of study treatment or are currently participating in another interventional clinical trial.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Seagen, a wholly owned subsidiary of Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

HonorHealth

Phoenix, Arizona, United States

Site Status

HonorHealth

Tempe, Arizona, United States

Site Status

The University of Arizona Cancer Center-North Campus

Tucson, Arizona, United States

Site Status

City of Hope at Huntington Beach

Huntington Beach, California, United States

Site Status

City of Hope at Irvine Sand Canyon

Irvine, California, United States

Site Status

Koman Family Outpatient Pavilion

La Jolla, California, United States

Site Status

UC San Diego Medical Center - La Jolla (Jacobs Medical Center / Thornton Pavilion)

La Jolla, California, United States

Site Status

UC San Diego Moores Cancer Center- Investigational Drug Services

La Jolla, California, United States

Site Status

UC San Diego Moores Cancer Center

La Jolla, California, United States

Site Status

City of Hope at Long Beach Worsham

Long Beach, California, United States

Site Status

City of Hope at Long Beach Elm

Long Beach, California, United States

Site Status

City of Hope at Newport Beach Lido

Newport Beach, California, United States

Site Status

City of Hope Torrance

Torrance, California, United States

Site Status

Rocky Mountain Cancer Centers

Aurora, Colorado, United States

Site Status

Rocky Mountain Cancer Centers

Boulder, Colorado, United States

Site Status

Rocky Mountain Cancer Centers

Thornton, Colorado, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Minnesota Oncology Hematology, PA

Coon Rapids, Minnesota, United States

Site Status

Metro Minnesota Community Oncology Research Consortium (MMCORC)

Saint Louis Park, Minnesota, United States

Site Status

Washington University School of Medicine - Obstetrics & Gynecology [Academic Offices)

St Louis, Missouri, United States

Site Status

Barnes-Jewish Hospital Investigational Drug Pharmacy (IDS)

St Louis, Missouri, United States

Site Status

Washington University School of Medicine - Obstetrics & Gynecology

St Louis, Missouri, United States

Site Status

Washington University School of Medicine [Patient Clinics]

St Louis, Missouri, United States

Site Status

Oncology Hematology West P.C. dba Nebraska Cancer Specialists

Omaha, Nebraska, United States

Site Status

Oncology Hematology West P.C. dba Nebraska Cancer Specialists

Omaha, Nebraska, United States

Site Status

NYU Langone Health - Long Island (Winthrop Hospital)

Mineola, New York, United States

Site Status

Perlmutter Cancer Center at NYU Langone GYN Oncology Associates

Mineola, New York, United States

Site Status

Perlmutter Cancer Center at NYU Langone Hospital - Long Island

Mineola, New York, United States

Site Status

Laura and Isaac Perlmutter Cancer Center at NYU Langone

New York, New York, United States

Site Status

NYU Langone Medical Center

New York, New York, United States

Site Status

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status

Duke University Medical Center/Duke Cancer Center

Durham, North Carolina, United States

Site Status

University Hospitals Cleveland Medical Center

Cleveland, Ohio, United States

Site Status

OSU Wexner Medical Center, CarePoint East

Columbus, Ohio, United States

Site Status

OSU Wexner Medical Center, Ohio State University Hospital East

Columbus, Ohio, United States

Site Status

OSU Wexner Medical Center, Arther G. James Cancer Hospital, and Solove Research Institute

Columbus, Ohio, United States

Site Status

OSU Wexner Medical Center, Investigational Drug Services(IP Ship to)

Columbus, Ohio, United States

Site Status

Osu Wexner Medical Center, The Ohio State University Hospital

Columbus, Ohio, United States

Site Status

OSU Wexner Medical Center, Stephanie Spielman Comprehensive Breast Center

Columbus, Ohio, United States

Site Status

OSU Wexner Medical Center, Martha Morehouse Medical Plaza

Columbus, Ohio, United States

Site Status

OSU Wexner Medical Center, OutPatient Care Upper Arlington

Columbus, Ohio, United States

Site Status

OSU Wexner Medical Center, CarePoint Gahanna

Gahanna, Ohio, United States

Site Status

OSU Wexner Medical Center, Gynecologic Oncology at Mill Run

Hilliard, Ohio, United States

Site Status

OSU Wexner Medical Center, Outpatient Care Lewis Center

Lewis Center, Ohio, United States

Site Status

UH Minoff Health Center at Chagrin Highlands

Orange, Ohio, United States

Site Status

OSU Wexner Medical Center, Outpatient Care New Albany

Westerville, Ohio, United States

Site Status

Northwest Cancer Specialists, P.C.

Portland, Oregon, United States

Site Status

Northwest Cancer Specialists, P.C.

Portland, Oregon, United States

Site Status

Northwest Cancer Specialists, P.C.

Tigard, Oregon, United States

Site Status

UPMC Hillman Cancer Center - Washington

Washington, Pennsylvania, United States

Site Status

Prisma Health Cancer Institute

Boiling Springs, South Carolina, United States

Site Status

Prisma Health Cancer Institute

Easley, South Carolina, United States

Site Status

Prisma Health Cancer Institute

Greenville, South Carolina, United States

Site Status

Prisma Health Cancer Institute

Greenville, South Carolina, United States

Site Status

Prisma Health Cancer Institute

Greer, South Carolina, United States

Site Status

Prisma Health Cancer Institute

Seneca, South Carolina, United States

Site Status

Tennessee Oncology, PLLC

Gallatin, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Hendersonville, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Shelbyville, Tennessee, United States

Site Status

Texas oncology-West Texas

Abilene, Texas, United States

Site Status

US Oncology Investigational Product Center (IPC)

Irving, Texas, United States

Site Status

US Oncology Investigational Products Center (IPC)

Irving, Texas, United States

Site Status

US Oncology lnvestigational Products Center (IPC)

Irving, Texas, United States

Site Status

Texas Oncology - Central South

Waco, Texas, United States

Site Status

Huntsman Cancer Institute, University of Utah

Salt Lake City, Utah, United States

Site Status

Virginia Cancer Specialists, PC

Alexandria, Virginia, United States

Site Status

Virginia Cancer Specialists, PC

Arlington, Virginia, United States

Site Status

Virginia Cancer Specialists, PC

Fairfax, Virginia, United States

Site Status

Virginia Cancer Specialists, PC

Gainesville, Virginia, United States

Site Status

Fred Hutchinson Cancer Center

Seattle, Washington, United States

Site Status

University of Washington Medical Center

Seattle, Washington, United States

Site Status

Northwest Cancer Specialists, P.C.

Vancouver, Washington, United States

Site Status

1 S Park St Medical Center

Madison, Wisconsin, United States

Site Status

University of Wisconsin Clinical Science Center

Madison, Wisconsin, United States

Site Status

Grand Hopital de Charleroi

Charleroi, Hainaut, Belgium

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Antwerpen

Edegem, , Belgium

Site Status

AZ Groeninge

Kortrijk, , Belgium

Site Status

CHU de Liege

Liège, , Belgium

Site Status

AZ Sint-Maarten

Mechelen, , Belgium

Site Status

Charite Universitatsmedizin Berlin

Berlin, , Germany

Site Status

Divisione di Sviluppo di Nuovi Farmaci per Terapie Innovative lstituto Europeo di Oncologia

Milan, Milan, Italy

Site Status

Aichi Cancer Center Hospital

Nagoya, Aichi-ken, Japan

Site Status

National Cancer Center Hospital East

Kashiwa-shi, Chiba, Japan

Site Status

St. Marianna University School of Medicine Hospital

Kawasaki, Kanagawa, Japan

Site Status

Kindai University Hospital

Osakasayama-shi, Osaka, Japan

Site Status

National Cancer Center Hospital

Cho-ku, Tokyo, Japan

Site Status

The Cancer Institute Hospital of JFCR

Tokyo, , Japan

Site Status

Seoul National University Bundang Hospital

Seongnam-si, Gyeonggi-do, South Korea

Site Status

Severance Hospital Yonsei University Health System

Seoul, Other, South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Institut Catala d'Oncologia Hospitalet

L'Hospitalet de Llobregat, Other, Spain

Site Status

Cetir Centre Medic

Barcelona, , Spain

Site Status

Hospital Clínico Universitario de Valencia. Fundación Investigación Clínico de Valencia.

Valencia, , Spain

Site Status

Ascires Eresa Campanar

Valencia, , Spain

Site Status

Hospital Vithas Valencia 9 de Octubre

Valencia, , Spain

Site Status

Sarah Cannon Research Institute UK

London, Budapest, United Kingdom

Site Status

Diagnostic Centre

London, Others, United Kingdom

Site Status

The Royal Marsden NHS Foundation Trust

Sutton, Surrey, United Kingdom

Site Status

Guy's Hospital

London, , United Kingdom

Site Status

Jonathan Poon

London, , United Kingdom

Site Status

The Royal Marsden NHS Foundation Trust

London, , United Kingdom

Site Status

The Harley Street Clinic

London, , United Kingdom

Site Status

Radiology

London, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

Netherlands Poland United States Belgium Germany Italy Japan South Korea Spain United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Okines AFC, Curigliano G, Mizuno N, Oh DY, Rorive A, Soliman H, Takahashi S, Bekaii-Saab T, Burkard ME, Chung KY, Debruyne PR, Fox JR, Gambardella V, Gil-Martin M, Hamilton EP, Monk BJ, Nakamura Y, Nguyen D, O'Malley DM, Olawaiye AB, Pothuri B, Reck M, Sudo K, Sunakawa Y, Van Marcke C, Yu EY, Ramos J, Tan S, Bieda M, Stinchcombe TE, Pohlmann PR. Tucatinib and trastuzumab in HER2-mutated metastatic breast cancer: a phase 2 basket trial. Nat Med. 2025 Mar;31(3):909-916. doi: 10.1038/s41591-024-03462-0. Epub 2025 Jan 17.

Reference Type DERIVED
PMID: 39825152 (View on PubMed)

Nakamura Y, Mizuno N, Sunakawa Y, Canon JL, Galsky MD, Hamilton E, Hayashi H, Jerusalem G, Kim ST, Lee KW, Kankeu Fonkoua LA, Monk BJ, Nguyen D, Oh DY, Okines A, O'Malley DM, Pohlmann P, Reck M, Shin SJ, Sudo K, Takahashi S, Van Marcke C, Yu EY, Groisberg R, Ramos J, Tan S, Stinchcombe TE, Bekaii-Saab T. Tucatinib and Trastuzumab for Previously Treated Human Epidermal Growth Factor Receptor 2-Positive Metastatic Biliary Tract Cancer (SGNTUC-019): A Phase II Basket Study. J Clin Oncol. 2023 Dec 20;41(36):5569-5578. doi: 10.1200/JCO.23.00606. Epub 2023 Sep 26.

Reference Type DERIVED
PMID: 37751561 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

SGNTUC-019

Identifier Type: -

Identifier Source: org_study_id