Trial Outcomes & Findings for Study to Gather Information About the Actual Use of an Adhesive Patch Placed on the Skin to Deliver Oxytrol Through the Skin Into the Bloodstream. (NCT NCT04534491)

NCT ID: NCT04534491

Last Updated: 2020-10-20

Results Overview

For each participant who was defined as a primary endpoint misuser (i.e., subjects who did not stop using Oxytrol when they either developed a new symptom referred to anywhere in the labeling, with the addition of abdominal and/or pelvic pain, or when their OAB condition worsened) the full case report form was reviewed in order to determine if there were factors that would mitigate the incorrect decision to continue use. For example, if the subject had consulted a physician and was told to continue use, such continuation is acceptable. This process is termed "mitigation," because it involves determining if there are mitigating factors in the decision to continue use without posing any significant medical risk. Mitigation was conducted independently post-hoc by an external panel of advisors including two urologists and an urogynecologist and one physician employed by the sponsor.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

855 participants

Primary outcome timeframe

Approximately 15 weeks from subjects' initial purchase of Oxytrol

Results posted on

2020-10-20

Participant Flow

Study was conducted in US-sites and pharmacies from 25May2010 (first patient first visit) to 22Jun2011 (last patient last visit).

Twelve hundred thirty (1230) women arrived at the pharmacies for the enrollment phase and 855 qualified participants purchased Oxytrol and entered the actual use phase.

Participant milestones

Participant milestones
Measure
Oxybutynin (Oxytrol, BAY839380)
Subjects decided to purchase Oxytrol.
Overall Study
STARTED
855
Overall Study
Treated
727
Overall Study
COMPLETED
703
Overall Study
NOT COMPLETED
152

Reasons for withdrawal

Reasons for withdrawal
Measure
Oxybutynin (Oxytrol, BAY839380)
Subjects decided to purchase Oxytrol.
Overall Study
Not completed end-of-study interview
24
Overall Study
Non-users
70
Overall Study
Non-verifiable users
58

Baseline Characteristics

727 verified users.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Oxybutynin (Oxytrol, BAY839380)
n=855 Participants
Subjects decided to purchase Oxytrol.
Age, Continuous
58.4 Years
STANDARD_DEVIATION 15.0 • n=727 Participants • 727 verified users.
Sex: Female, Male
Female
727 Participants
n=727 Participants • 727 verified users.
Sex: Female, Male
Male
0 Participants
n=727 Participants • 727 verified users.
Race/Ethnicity, Customized
White
561 Participants
n=727 Participants • 727 verified users
Race/Ethnicity, Customized
Black or African American
66 Participants
n=727 Participants • 727 verified users
Race/Ethnicity, Customized
Hispanic or Latino
64 Participants
n=727 Participants • 727 verified users
Race/Ethnicity, Customized
Asian
12 Participants
n=727 Participants • 727 verified users
Race/Ethnicity, Customized
Other
24 Participants
n=727 Participants • 727 verified users

PRIMARY outcome

Timeframe: Approximately 15 weeks from subjects' initial purchase of Oxytrol

For each participant who was defined as a primary endpoint misuser (i.e., subjects who did not stop using Oxytrol when they either developed a new symptom referred to anywhere in the labeling, with the addition of abdominal and/or pelvic pain, or when their OAB condition worsened) the full case report form was reviewed in order to determine if there were factors that would mitigate the incorrect decision to continue use. For example, if the subject had consulted a physician and was told to continue use, such continuation is acceptable. This process is termed "mitigation," because it involves determining if there are mitigating factors in the decision to continue use without posing any significant medical risk. Mitigation was conducted independently post-hoc by an external panel of advisors including two urologists and an urogynecologist and one physician employed by the sponsor.

Outcome measures

Outcome measures
Measure
Oxybutynin (Oxytrol, BAY839380)
n=727 Participants
Subjects decided to purchase Oxytrol.
The Percentage of Participants Who Did Not Stop Use When They Either Developed a New Symptom Referred to Anywhere in the Labeling or When Their Condition Worsened Including Abdominal and/or Pelvic Pain.
Pre-mitigation
14.4 Percentage of participants
Interval 12.0 to 17.2
The Percentage of Participants Who Did Not Stop Use When They Either Developed a New Symptom Referred to Anywhere in the Labeling or When Their Condition Worsened Including Abdominal and/or Pelvic Pain.
Post-mitigation
3.4 Percentage of participants
Interval 2.2 to 5.0

SECONDARY outcome

Timeframe: Approximately 15 weeks from subjects' initial purchase of Oxytrol

This outcome measure did not include participants who developed abdominal and/or pelvic pain and was more reflective of how consumers stopped use according to the symptoms described on the Oxytrol labeling used in the study.

Outcome measures

Outcome measures
Measure
Oxybutynin (Oxytrol, BAY839380)
n=727 Participants
Subjects decided to purchase Oxytrol.
The Percentage of Verified Users Who Did Not Stop Use When Their Condition Worsened or They Developed a New Symptom Referred to in the Labeling.
Pre-Mitigation
13.1 Percentage of participants
Interval 10.7 to 15.7
The Percentage of Verified Users Who Did Not Stop Use When Their Condition Worsened or They Developed a New Symptom Referred to in the Labeling.
Post-Mitigation
3.2 Percentage of participants
Interval 2.0 to 4.7

SECONDARY outcome

Timeframe: Approximately 15 weeks from subjects' initial purchase of Oxytrol

This outcome measure evaluated the number of days it took for a subject to discontinue use of Oxytrol after their symptoms worsened or had stayed the same after 2 weeks of treatment. This was calculated using diary card data.

Outcome measures

Outcome measures
Measure
Oxybutynin (Oxytrol, BAY839380)
n=187 Participants
Subjects decided to purchase Oxytrol.
The Median Time Taken to Discontinue Oxytrol Use by Verified Users Who Did Not Experience Improvement in Their Symptoms After Two Weeks of Treatment.
35 Days
Interval 26.0 to 46.0

SECONDARY outcome

Timeframe: Approximately 15 weeks from subjects' initial purchase of Oxytrol

Factors considered in this mitigation included providing: a response to one or more open ended questions that indicated a thoughtful, informed reason for continuing use; the subject talked to a physician, and the physician advised the subject that it was acceptable to continue using product; the subject had improved by Week 7 and indicated a thoughtful, informed reason for continuing use; as well as other reasons explained in the guidelines. This outcome measure was analyzed based on pre- and post-mitigation assessments but the post-mitigation analysis includes all subject data and is a better reflection of the subject's overall behavior. This was calculated by dividing the total number of subjects by the number of subjects who used the Oxytrol patch at least once.

Outcome measures

Outcome measures
Measure
Oxybutynin (Oxytrol, BAY839380)
n=643 Participants
Subjects decided to purchase Oxytrol.
The Percentage of Verified Users Who Did Not Stop Oxytrol Use Within Two Weeks After Experiencing no Improvement in Their Symptoms.
All Subjects Pre-Mitigation
22.6 Percentage of participants
Interval 19.4 to 26.0
The Percentage of Verified Users Who Did Not Stop Oxytrol Use Within Two Weeks After Experiencing no Improvement in Their Symptoms.
All Subjects Post-Mitigation
11.0 Percentage of participants
Interval 8.7 to 13.7

SECONDARY outcome

Timeframe: Approximately 15 weeks from subjects' initial purchase of Oxytrol

Population: 324 participants continued Oxytrol therapy and experienced new symptoms of interest or whose OAB symptoms did not improve.

The medical risk of the newly developed symptom(s) or no sign of symptom improvement was categorized according to prospectively defined medical risk categories of 'medical risk', 'possible medical risk', and minimal/insignificant medical risk'. Mitigated data was not included in this endpoint.

Outcome measures

Outcome measures
Measure
Oxybutynin (Oxytrol, BAY839380)
n=324 Participants
Subjects decided to purchase Oxytrol.
Number of Participants With Medical Risk Associated With the Development of New Symptoms or When Symptoms Did Not Improve for Patients That Continued Oxytrol Treatment.
Medical risk (subjects)
16 Participants
Number of Participants With Medical Risk Associated With the Development of New Symptoms or When Symptoms Did Not Improve for Patients That Continued Oxytrol Treatment.
Possible medical risk (subjects)
24 Participants
Number of Participants With Medical Risk Associated With the Development of New Symptoms or When Symptoms Did Not Improve for Patients That Continued Oxytrol Treatment.
Minimal/insignificant medical risk (subjects)
284 Participants

SECONDARY outcome

Timeframe: Approximately 15 weeks from subjects' initial purchase of Oxytrol

Factors considered in this mitigation for incorrect duration included most of the duration of patch use being correct, subject indicated understanding of the label but perhaps forgetting for a patch or two, etc. Factors considered in mitigation for simultaneous use include obvious diary errors, a subject stating that she did not do this, or a subject's doctor telling her to wear two patches at a time.

Outcome measures

Outcome measures
Measure
Oxybutynin (Oxytrol, BAY839380)
n=727 Participants
Subjects decided to purchase Oxytrol.
The Percentage of Verified Users Who Misused the Patch (Incorrect Duration of Use or Simultaneous Use).
Total Subjects Pre-Mitigation
51.7 Percentage of participants
Interval 47.9 to 55.4
The Percentage of Verified Users Who Misused the Patch (Incorrect Duration of Use or Simultaneous Use).
Total Subjects Post-Mitigation
21.2 Percentage of participants
Interval 18.3 to 24.4

Adverse Events

Oxybutynin (Oxytrol, BAY839380)

Serious events: 35 serious events
Other events: 509 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Oxybutynin (Oxytrol, BAY839380)
n=785 participants at risk
Subjects decided to purchase Oxytrol.
Cardiac disorders
Arrhythmia
0.13%
1/785 • 15 weeks
Cardiac disorders
Cardiac disorder
0.13%
1/785 • 15 weeks
Gastrointestinal disorders
Diarrhoea haemorrhagic
0.13%
1/785 • 15 weeks
General disorders
Chest pain
0.25%
2/785 • 15 weeks
Hepatobiliary disorders
Cholecystitis
0.25%
2/785 • 15 weeks
Hepatobiliary disorders
Hepatic failure
0.13%
1/785 • 15 weeks
Immune system disorders
Hypersensitivity
0.13%
1/785 • 15 weeks
Infections and infestations
Bronchitis
0.13%
1/785 • 15 weeks
Infections and infestations
Cellulitis
0.13%
1/785 • 15 weeks
Infections and infestations
Pelvic inflammatory disease
0.13%
1/785 • 15 weeks
Infections and infestations
Pneumonia viral
0.13%
1/785 • 15 weeks
Infections and infestations
Urinary tract infection
0.38%
3/785 • 15 weeks
Injury, poisoning and procedural complications
Anaesthetic complication
0.13%
1/785 • 15 weeks
Injury, poisoning and procedural complications
Cardiac pacemaker malfunction
0.13%
1/785 • 15 weeks
Injury, poisoning and procedural complications
Concussion
0.13%
1/785 • 15 weeks
Injury, poisoning and procedural complications
Foot fracture
0.13%
1/785 • 15 weeks
Injury, poisoning and procedural complications
Multiple fractures
0.13%
1/785 • 15 weeks
Injury, poisoning and procedural complications
Skin laceration
0.13%
1/785 • 15 weeks
Injury, poisoning and procedural complications
Upper limb fracture
0.13%
1/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Back pain
0.13%
1/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Arthralgia
0.13%
1/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Spinal osteoarthritis
0.13%
1/785 • 15 weeks
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Breast cancer
0.13%
1/785 • 15 weeks
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Gammopathy
0.13%
1/785 • 15 weeks
Nervous system disorders
Cerebrovascular accident
0.13%
1/785 • 15 weeks
Nervous system disorders
Convulsion
0.13%
1/785 • 15 weeks
Nervous system disorders
Syncope
0.13%
1/785 • 15 weeks
Nervous system disorders
Transient ischaemic attack
0.13%
1/785 • 15 weeks
Psychiatric disorders
Anxiety
0.13%
1/785 • 15 weeks
Psychiatric disorders
Depression
0.13%
1/785 • 15 weeks
Psychiatric disorders
Schizoaffective disorder
0.13%
1/785 • 15 weeks
Reproductive system and breast disorders
Pelvic prolapse
0.13%
1/785 • 15 weeks
Reproductive system and breast disorders
Uterine prolapse
0.13%
1/785 • 15 weeks
Respiratory, thoracic and mediastinal disorders
Chronic obstructive pulmonary disease
0.13%
1/785 • 15 weeks
Skin and subcutaneous tissue disorders
Blister
0.13%
1/785 • 15 weeks
Vascular disorders
Thrombosis
0.13%
1/785 • 15 weeks

Other adverse events

Other adverse events
Measure
Oxybutynin (Oxytrol, BAY839380)
n=785 participants at risk
Subjects decided to purchase Oxytrol.
Ear and labyrinth disorders
Vertigo
0.25%
2/785 • 15 weeks
Eye disorders
Cataract
0.64%
5/785 • 15 weeks
Eye disorders
Dry eye
1.3%
10/785 • 15 weeks
Eye disorders
Vision blurred
0.64%
5/785 • 15 weeks
Eye disorders
Visual acuity reduced
0.38%
3/785 • 15 weeks
Eye disorders
Visual impairment
0.25%
2/785 • 15 weeks
Gastrointestinal disorders
Abdominal discomfort
0.25%
2/785 • 15 weeks
Gastrointestinal disorders
Abdominal pain
0.64%
5/785 • 15 weeks
Gastrointestinal disorders
Abdominal pain lower
0.64%
5/785 • 15 weeks
Gastrointestinal disorders
Constipation
2.5%
20/785 • 15 weeks
Gastrointestinal disorders
Diarrhoea
2.0%
16/785 • 15 weeks
Gastrointestinal disorders
Dry mouth
4.1%
32/785 • 15 weeks
Gastrointestinal disorders
Faecal incontinence
0.25%
2/785 • 15 weeks
Gastrointestinal disorders
Gastrooesophageal reflux disease
0.38%
3/785 • 15 weeks
Gastrointestinal disorders
Nausea
2.0%
16/785 • 15 weeks
Gastrointestinal disorders
Toothache
0.38%
3/785 • 15 weeks
Gastrointestinal disorders
Vomiting
0.25%
2/785 • 15 weeks
General disorders
Application site erythema
1.1%
9/785 • 15 weeks
General disorders
Application site irritation
18.1%
142/785 • 15 weeks
General disorders
Application site pruritus
1.0%
8/785 • 15 weeks
General disorders
Application site rash
0.51%
4/785 • 15 weeks
General disorders
Application site reaction
1.7%
13/785 • 15 weeks
General disorders
Fatigue
1.4%
11/785 • 15 weeks
General disorders
Irritability
0.38%
3/785 • 15 weeks
General disorders
Oedema peripheral
0.51%
4/785 • 15 weeks
Immune system disorders
Hypersensitivity
0.89%
7/785 • 15 weeks
Immune system disorders
Seasonal allergy
0.38%
3/785 • 15 weeks
Infections and infestations
Bronchitis
1.3%
10/785 • 15 weeks
Infections and infestations
Cystitis
2.0%
16/785 • 15 weeks
Infections and infestations
Diverticulitis
0.38%
3/785 • 15 weeks
Infections and infestations
Fungal infection
0.76%
6/785 • 15 weeks
Infections and infestations
Gastroenteritis viral
1.0%
8/785 • 15 weeks
Infections and infestations
Herpes zoster
0.25%
2/785 • 15 weeks
Infections and infestations
Infection
0.25%
2/785 • 15 weeks
Infections and infestations
Influenza
2.3%
18/785 • 15 weeks
Infections and infestations
Nasopharyngitis
5.9%
46/785 • 15 weeks
Infections and infestations
Pharyngitis streptococcal
0.25%
2/785 • 15 weeks
Infections and infestations
Pneumonia
0.25%
2/785 • 15 weeks
Infections and infestations
Respiratory tract infection
0.25%
2/785 • 15 weeks
Infections and infestations
Sinusitis
2.7%
21/785 • 15 weeks
Infections and infestations
Tooth infection
0.25%
2/785 • 15 weeks
Infections and infestations
Upper respiratory tract infection
0.25%
2/785 • 15 weeks
Infections and infestations
Urinary tract infection
6.0%
47/785 • 15 weeks
Infections and infestations
Vulvovaginal mycotic infection
0.25%
2/785 • 15 weeks
Injury, poisoning and procedural complications
Arthropod bite
0.25%
2/785 • 15 weeks
Injury, poisoning and procedural complications
Contusion
0.25%
2/785 • 15 weeks
Injury, poisoning and procedural complications
Excoriation
0.38%
3/785 • 15 weeks
Injury, poisoning and procedural complications
Fall
0.38%
3/785 • 15 weeks
Injury, poisoning and procedural complications
Joint sprain
0.38%
3/785 • 15 weeks
Injury, poisoning and procedural complications
Skin laceration
0.38%
3/785 • 15 weeks
Injury, poisoning and procedural complications
Wrist fracture
0.38%
3/785 • 15 weeks
Investigations
Blood cholesterol increased
0.51%
4/785 • 15 weeks
Investigations
Blood glucose increased
0.25%
2/785 • 15 weeks
Metabolism and nutrition disorders
Decreased appetite
0.25%
2/785 • 15 weeks
Metabolism and nutrition disorders
Diabetes mellitus
0.25%
2/785 • 15 weeks
Metabolism and nutrition disorders
Hyperlipidaemia
0.38%
3/785 • 15 weeks
Metabolism and nutrition disorders
Hypoglycaemia
0.25%
2/785 • 15 weeks
Metabolism and nutrition disorders
Vitamin D deficiency
0.25%
2/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Arthralgia
1.1%
9/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Arthritis
0.51%
4/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Back pain
2.2%
17/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Flank pain
0.51%
4/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Joint swelling
0.38%
3/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Muscle spasms
0.76%
6/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Musculoskeletal pain
0.38%
3/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Neck pain
0.38%
3/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Osteopenia
0.25%
2/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Pain in extremity
0.89%
7/785 • 15 weeks
Musculoskeletal and connective tissue disorders
Plantar fasciitis
0.25%
2/785 • 15 weeks
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Melanocytic naevus
0.25%
2/785 • 15 weeks
Nervous system disorders
Balance disorder
0.25%
2/785 • 15 weeks
Nervous system disorders
Dizziness
1.9%
15/785 • 15 weeks
Nervous system disorders
Dysgeusia
0.25%
2/785 • 15 weeks
Nervous system disorders
Headache
2.5%
20/785 • 15 weeks
Nervous system disorders
Migraine
0.25%
2/785 • 15 weeks
Nervous system disorders
Paraesthesia
0.25%
2/785 • 15 weeks
Nervous system disorders
Sciatica
0.25%
2/785 • 15 weeks
Nervous system disorders
Somnolence
1.8%
14/785 • 15 weeks
Psychiatric disorders
Anxiety
0.38%
3/785 • 15 weeks
Psychiatric disorders
Depression
0.51%
4/785 • 15 weeks
Psychiatric disorders
Insomnia
0.38%
3/785 • 15 weeks
Renal and urinary disorders
Dysuria
1.5%
12/785 • 15 weeks
Renal and urinary disorders
Haematuria
0.38%
3/785 • 15 weeks
Renal and urinary disorders
Hypertonic bladder
0.64%
5/785 • 15 weeks
Renal and urinary disorders
Micturition urgency
0.51%
4/785 • 15 weeks
Renal and urinary disorders
Urge incontinence
3.1%
24/785 • 15 weeks
Renal and urinary disorders
Urinary incontinence
0.38%
3/785 • 15 weeks
Renal and urinary disorders
Urinary retention
0.89%
7/785 • 15 weeks
Renal and urinary disorders
Urine odour abnormal
0.64%
5/785 • 15 weeks
Reproductive system and breast disorders
Breast tenderness
0.25%
2/785 • 15 weeks
Reproductive system and breast disorders
Menorrhagia
0.25%
2/785 • 15 weeks
Reproductive system and breast disorders
Vaginal haemorrhage
0.25%
2/785 • 15 weeks
Respiratory, thoracic and mediastinal disorders
Cough
1.9%
15/785 • 15 weeks
Respiratory, thoracic and mediastinal disorders
Dry throat
0.25%
2/785 • 15 weeks
Respiratory, thoracic and mediastinal disorders
Nasal congestion
0.25%
2/785 • 15 weeks
Respiratory, thoracic and mediastinal disorders
Oropharyngeal pain
0.51%
4/785 • 15 weeks
Skin and subcutaneous tissue disorders
Blister
0.25%
2/785 • 15 weeks
Skin and subcutaneous tissue disorders
Erythema
0.25%
2/785 • 15 weeks
Skin and subcutaneous tissue disorders
Hyperhidrosis
0.25%
2/785 • 15 weeks
Skin and subcutaneous tissue disorders
Pruritus
0.64%
5/785 • 15 weeks
Skin and subcutaneous tissue disorders
Rash
0.64%
5/785 • 15 weeks
Vascular disorders
Hot flush
0.25%
2/785 • 15 weeks
Vascular disorders
Hypertension
1.0%
8/785 • 15 weeks

Additional Information

Therapeutic Area Head

Bayer

Phone: (+)1-888-84 22937

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: GT60