Apremilast Pediatric Study in Children With Active Oral Ulcers Associated With Behçet's Disease

NCT ID: NCT04528082

Last Updated: 2025-12-01

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-09-09

Study Completion Date

2030-12-17

Brief Summary

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The aim of this study is to estimate the efficacy of apremilast compared to placebo in the treatment of oral ulcers in pediatric participants from 2 to \< 18 years of age with oral ulcers associated with Behçet's disease (BD) through week 12.

Detailed Description

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Conditions

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Behçet Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

The participants will be randomized to receive apremilast or placebo in the double-blind 12 week treatment phase. Then, the participants will all receive apremilast for a further 40 weeks in the active treatment phase. The participants will then complete the 30 days safety follow-up period after the last dose of apremilast in the active treatment phase.

Participants who complete the 52 weeks of treatment may have the opportunity to continue receiving apremilast through an open-label extension study (NCT05767047) . The participants who choose not to participate in the optional open-label, long-term study will complete the 30 days safety follow-up period after the last dose of apremilast in the active treatment phase.
Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Apremilast

Participants will receive apremilast orally in the double-blind 12 week treatment phase. Then the participants will continue to receive apremilast in the active 40 weeks treatment phase.

Group Type EXPERIMENTAL

Apremilast

Intervention Type DRUG

Participants will receive apremilast orally.

Placebo to Apremilast

Participants will receive the matching placebo orally in the double-blind 12 week treatment phase. Then the participants will receive apremilast in the active 40 weeks treatment phase.

Group Type PLACEBO_COMPARATOR

Apremilast

Intervention Type DRUG

Participants will receive apremilast orally.

Placebo

Intervention Type DRUG

Participants will receive the matching placebo orally.

Interventions

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Apremilast

Participants will receive apremilast orally.

Intervention Type DRUG

Placebo

Participants will receive the matching placebo orally.

Intervention Type DRUG

Other Intervention Names

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Otezla®

Eligibility Criteria

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Inclusion Criteria

* Male or Female participants 2 to \< 18 years of age at randomization.
* Diagnosed with BD meeting the ISGBD criteria at any time prior to the screening visit.
* Oral ulcers that occurred ≥ 3 times within the 12-month period prior to the screening visit.
* Participant must have ≥ 2 oral ulcers at both the screening visit and on day 1.
* Participant has had prior treatment with ≥ 1 non-biologic BD therapy, such as, but not limited to, topical corticosteroids or systemic treatment.

Exclusion Criteria

* Behçet's disease-related active major organ involvement - pulmonary (eg, pulmonary artery aneurysm), vascular (eg, thrombophlebitis), gastrointestinal (eg, ulcers along the gastrointestinal tract), or CNS (eg, meningoencephalitis) manifestations, or ocular lesions (eg, uveitis) requiring immunosuppressive therapy; however:

* Previous major organ involvement is allowed if it occurred ≥1 year prior to the screening visit and is not active at time of enrollment
* Participants with mild BD-related ocular lesions not requiring systemic immunosuppressive therapy are allowed
* Participants with BD-related arthritis and BD-skin manifestations are also allowed.
* Previous exposure to biologic therapies for the treatment of BD oral ulcers, previous biologic exposure is allowed for other indications (including other manifestations of BD).
Minimum Eligible Age

2 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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Hospices Civils de Lyon Hopital Femme Mere Enfant

Bron, , France

Site Status RECRUITING

Hopital Necker Enfants Malades

Paris, , France

Site Status TERMINATED

Hopital Robert Debre

Paris, , France

Site Status RECRUITING

Agia Sofia Children Hospital

Athens, , Greece

Site Status RECRUITING

Attikon University General Hospital

Athens, , Greece

Site Status RECRUITING

General Hospital of Thessaloniki Ippokrateio

Thessaloniki, , Greece

Site Status RECRUITING

Meir Medical Center

Kfar Saba, , Israel

Site Status RECRUITING

Ospedale Santissima Annunziata

Chieti, , Italy

Site Status RECRUITING

IRCCS Istituto Giannina Gaslini

Genova, , Italy

Site Status RECRUITING

Azienda Socio Sanitaria Territoriale Centro Specialistico Ortopedico Traumatologico Gaetano Pini

Milan, , Italy

Site Status RECRUITING

IRCCS Ospedale Pediatrico Bambino Gesu

Roma, , Italy

Site Status RECRUITING

Hospital Universitario Virgen del Rocio

Seville, Andalusia, Spain

Site Status RECRUITING

Hospital Universitari Vall d Hebron

Barcelona, Catalonia, Spain

Site Status RECRUITING

Hospital Sant Joan de Deu

Esplugues de Llobregat, Catalonia, Spain

Site Status RECRUITING

Hospital Universitari i Politecnic La Fe

Valencia, Valencia, Spain

Site Status RECRUITING

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status TERMINATED

Centre Hospitalier Universitaire Vaudois

Lausanne, , Switzerland

Site Status TERMINATED

Hacettepe Universitesi Tip Fakultesi Hastanesi

Ankara, , Turkey (Türkiye)

Site Status RECRUITING

Istanbul Universitesi Istanbul Tip Fakultesi Hastanesi

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Istanbul Universitesi Cerrahpasa Tip Fakultesi

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Umraniye Egitim ve Arastirma Hastanesi

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Dokuz Eylul Universitesi Tip Fakultesi Hastanesi

Izmir, , Turkey (Türkiye)

Site Status TERMINATED

Erciyes Universitesi Tip Fakultesi Hastanesi

Kayseri, , Turkey (Türkiye)

Site Status RECRUITING

Birmingham Childrens Hospital

Birmingham, , United Kingdom

Site Status TERMINATED

Alder Hey Childrens Hospital

Liverpool, , United Kingdom

Site Status RECRUITING

John Radcliffe Hospital

Oxford, , United Kingdom

Site Status RECRUITING

Countries

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France Greece Israel Italy Spain Switzerland Turkey (Türkiye) United Kingdom

Central Contacts

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Amgen Call Center

Role: CONTACT

866-572-6436

Related Links

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http://www.amgentrials.com

AmgenTrials clinical trials website

Other Identifiers

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2023-503436-40-00

Identifier Type: CTIS

Identifier Source: secondary_id

20190530

Identifier Type: -

Identifier Source: org_study_id

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