Trial Outcomes & Findings for A Phase 1/ Phase 2 Study of TTHX1114(NM141) (NCT NCT04520321)

NCT ID: NCT04520321

Last Updated: 2023-10-30

Results Overview

Suspected Adverse Reactions Reported Following Study Drug Adminsitration

Recruitment status

COMPLETED

Study phase

PHASE1/PHASE2

Target enrollment

22 participants

Primary outcome timeframe

Day 90

Results posted on

2023-10-30

Participant Flow

Participant milestones

Participant milestones
Measure
Vehicle (Placebo)
Placebo weekly x 4 Vehicle (placebo): Placebo
Low Dose
TTHX1114(NM141) low-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
Mid-dose
TTHX1114(NM141) mid-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
High-dose
TTHX1114(NM141) high-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
Overall Study
STARTED
5
7
3
7
Overall Study
COMPLETED
5
7
3
7
Overall Study
NOT COMPLETED
0
0
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

A Phase 1/ Phase 2 Study of TTHX1114(NM141)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Vehicle (Placebo)
n=5 Participants
Placebo weekly x 4 Vehicle (placebo): Placebo
Low Dose
n=7 Participants
TTHX1114(NM141) low-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
Mid-dose
n=3 Participants
TTHX1114(NM141) mid-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
High-dose
n=7 Participants
TTHX1114(NM141) high-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
Total
n=22 Participants
Total of all reporting groups
Sex: Female, Male
Female
5 Participants
n=5 Participants
5 Participants
n=7 Participants
2 Participants
n=5 Participants
7 Participants
n=4 Participants
19 Participants
n=21 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
2 Participants
n=7 Participants
1 Participants
n=5 Participants
0 Participants
n=4 Participants
3 Participants
n=21 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
5 Participants
n=5 Participants
7 Participants
n=7 Participants
3 Participants
n=5 Participants
7 Participants
n=4 Participants
22 Participants
n=21 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
Race (NIH/OMB)
American Indian or Alaska Native
5 Participants
n=5 Participants
7 Participants
n=7 Participants
3 Participants
n=5 Participants
7 Participants
n=4 Participants
22 Participants
n=21 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
Race (NIH/OMB)
White
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
0 Participants
n=21 Participants
Age, Continuous
76.6 years
STANDARD_DEVIATION 11.8 • n=5 Participants
75.7 years
STANDARD_DEVIATION 7.8 • n=7 Participants
81.3 years
STANDARD_DEVIATION 11.0 • n=5 Participants
68.9 years
STANDARD_DEVIATION 11.1 • n=4 Participants
74.5 years
STANDARD_DEVIATION 10.5 • n=21 Participants

PRIMARY outcome

Timeframe: Day 90

Population: Safety

Suspected Adverse Reactions Reported Following Study Drug Adminsitration

Outcome measures

Outcome measures
Measure
Vehicle (Placebo)
n=5 Participants
Placebo weekly x 4 Vehicle (placebo): Placebo
Low Dose
n=7 Participants
TTHX1114(NM141) low-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
Mid-dose
n=3 Participants
TTHX1114(NM141) mid-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
High-dose
n=7 Participants
TTHX1114(NM141) high-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
DLTs/ Adverse Reactions
0 Participants
0 Participants
0 Participants
0 Participants

Adverse Events

Vehicle (Placebo)

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

Low Dose

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Mid-dose

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

High-dose

Serious events: 0 serious events
Other events: 3 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Vehicle (Placebo)
n=5 participants at risk
Placebo weekly x 4 Vehicle (placebo): Placebo
Low Dose
n=7 participants at risk
TTHX1114(NM141) low-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
Mid-dose
n=3 participants at risk
TTHX1114(NM141) mid-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
High-dose
n=7 participants at risk
TTHX1114(NM141) high-dose weekly x 4 TTHX1114(NM141): engineered FGF-1 delivered intracamerally
Eye disorders
Conjunctival haemorrhage
20.0%
1/5 • Number of events 1 • 90 days
0.00%
0/7 • 90 days
0.00%
0/3 • 90 days
0.00%
0/7 • 90 days
Eye disorders
Eye irritation
0.00%
0/5 • 90 days
0.00%
0/7 • 90 days
0.00%
0/3 • 90 days
14.3%
1/7 • 90 days
Eye disorders
Eye pain
0.00%
0/5 • 90 days
0.00%
0/7 • 90 days
33.3%
1/3 • 90 days
14.3%
1/7 • 90 days
Eye disorders
Foreign body sensation in eyes
20.0%
1/5 • Number of events 1 • 90 days
0.00%
0/7 • 90 days
0.00%
0/3 • 90 days
0.00%
0/7 • 90 days
Eye disorders
Iritis
0.00%
0/5 • 90 days
0.00%
0/7 • 90 days
0.00%
0/3 • 90 days
14.3%
1/7 • Number of events 1 • 90 days
Eye disorders
Photophobia
0.00%
0/5 • 90 days
14.3%
1/7 • 90 days
0.00%
0/3 • 90 days
14.3%
1/7 • 90 days
Eye disorders
Punctate keratitis
0.00%
0/5 • 90 days
0.00%
0/7 • 90 days
0.00%
0/3 • 90 days
14.3%
1/7 • 90 days
General disorders
Malaise
20.0%
1/5 • Number of events 1 • 90 days
0.00%
0/7 • 90 days
0.00%
0/3 • 90 days
0.00%
0/7 • 90 days
Injury, poisoning and procedural complications
Hand fracture
0.00%
0/5 • 90 days
14.3%
1/7 • 90 days
0.00%
0/3 • 90 days
0.00%
0/7 • 90 days
Injury, poisoning and procedural complications
Ligament sprain
0.00%
0/5 • 90 days
14.3%
1/7 • 90 days
0.00%
0/3 • 90 days
0.00%
0/7 • 90 days
Respiratory, thoracic and mediastinal disorders
Dyspnoea
20.0%
1/5 • Number of events 1 • 90 days
0.00%
0/7 • 90 days
0.00%
0/3 • 90 days
0.00%
0/7 • 90 days
Respiratory, thoracic and mediastinal disorders
Sinus congestion
0.00%
0/5 • 90 days
0.00%
0/7 • 90 days
33.3%
1/3 • 90 days
0.00%
0/7 • 90 days
Vascular disorders
Lymphoedema
20.0%
1/5 • Number of events 1 • 90 days
0.00%
0/7 • 90 days
0.00%
0/3 • 90 days
0.00%
0/7 • 90 days

Additional Information

Thomas M Tremblay, RN, BSN

Trefoil Therapeutics.com

Phone: 4153053491

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place