PN-943 in Adults With Moderate to Severe Active Ulcerative Colitis (UC)

NCT ID: NCT04504383

Last Updated: 2023-04-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

169 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-08-05

Study Completion Date

2023-02-16

Brief Summary

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The purpose of the study is to evaluate the safety, tolerability, and clinical efficacy of PN-943 450 mg twice daily \[BID\] and PN-943 150 mg BID, compared with placebo BID, in subjects with moderate to severe active Ulcerative Colitis (UC).

Detailed Description

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The study consists of a 12-week double-blind, placebo-controlled treatment period. Participants will be randomized in a 1:1:1 ratio to PN-943 450 mg BID, PN-943 150 mg BID, or matching placebo BID.

Participants who successfully complete the double-blind period may be eligible for an extended treatment period of 40 weeks duration.

Conditions

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Ulcerative Colitis Chronic Moderate Ulcerative Colitis Chronic Severe

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

12-week randomized, double-blind, placebo-controlled, parallel design study in patients with moderate to severe active UC. It will be followed by 40 weeks of Extended Active Treatment.
Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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PN-943 450 mg BID

Oral administration of PN-943 450 mg BID

Group Type EXPERIMENTAL

PN-943

Intervention Type DRUG

Administered by the oral route BID for the duration of the study.

PN-943 150 mg BID

Oral administration of PN-943 150 mg BID

Group Type EXPERIMENTAL

PN-943

Intervention Type DRUG

Administered by the oral route BID for the duration of the study.

Placebo BID

Oral administration of matching placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Administered by the oral route BID for 12 weeks.

Interventions

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PN-943

Administered by the oral route BID for the duration of the study.

Intervention Type DRUG

Placebo

Administered by the oral route BID for 12 weeks.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Male and female subjects age 18 (or the minimum country specific age of consent if \>18) to 75 years.
2. Subject understands the study procedures and agrees to participate in the study by giving written informed consent.
3. Diagnosis of UC supported by appropriate documentation of biopsy results consistent with UC.
4. Moderate to severe active UC.
5. Demonstrated inadequate response, loss of response, or intolerance of at least 1 of oral aminosalicylates (5-ASAs), corticosteroids, immunomodulators, or a biologic (excluding vedolizumab).

Exclusion Criteria

1. Subject with a current diagnosis of Crohn's disease (CD), indeterminate colitis (IC), microscopic colitis, ischemic colitis, radiation colitis.
2. History of colonic dysplasia other than completely removed low-grade dysplastic lesion.
3. History of active bacterial, viral, fungal or mycobacterial infection requiring hospitalization or IV antibiotic/anti-infective treatment within 4 weeks of screening or oral antibiotics/anti-infectives within 2 weeks of screening.
4. Prior treatment with vedolizumab, natalizumab, or any agent targeting the α4β7 or β1 integrin or planned during the study.
5. Positive stool test for C. difficile.
6. Chronic recurrent or serious infection.
7. Known primary or secondary immunodeficiency.
8. Pregnant or lactating female or considering becoming pregnant during the study or within 30 days after the last dose of study medication.
9. History of any major neurological disorders.
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Protagonist Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Protagonist Investigational Site

Tucson, Arizona, United States

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Garden Grove, California, United States

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Los Angeles, California, United States

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Murrieta, California, United States

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San Francisco, California, United States

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Colorado Springs, Colorado, United States

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Kissimmee, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Saint Augustine, Florida, United States

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Wesley Chapel, Florida, United States

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Metairie, Louisiana, United States

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Glen Burnie, Maryland, United States

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Chesterfield, Michigan, United States

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Troy, Michigan, United States

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Jackson, Mississippi, United States

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St Louis, Missouri, United States

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Englewood, New Jersey, United States

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North Massapequa, New York, United States

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Charlotte, North Carolina, United States

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Norman, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Orangeburg, South Carolina, United States

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Nashville, Tennessee, United States

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Austin, Texas, United States

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Garland, Texas, United States

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Pasadena, Texas, United States

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Spring, Texas, United States

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Lynchburg, Virginia, United States

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Innsbruck, , Austria

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Salzburg, , Austria

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Vienna, , Austria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Kelowna, British Columbia, Canada

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Vancouver, British Columbia, Canada

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West Vancouver, British Columbia, Canada

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North Bay, Ontario, Canada

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Toronto, Ontario, Canada

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Vaughan, Ontario, Canada

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Berlin, , Germany

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Berlin, , Germany

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Kiel, , Germany

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Tübingen, , Germany

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Budapest, , Hungary

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Debrecen, , Hungary

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Székesfehérvár, , Hungary

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Castellana Grotte, , Italy

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Modena, , Italy

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Negrar, , Italy

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Padua, , Italy

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Roma, , Italy

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Roma, , Italy

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San Giovanni Rotondo, , Italy

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Poznan, Greater Poland Voivodeship, Poland

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Bydgoszcz, , Poland

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Bydgoszcz, , Poland

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Częstochowa, , Poland

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Częstochowa, , Poland

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Katowice, , Poland

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Krakow, , Poland

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Ksawerów, , Poland

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Lodz, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Nowy Targ, , Poland

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Piotrkow Trybunalski, , Poland

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Poznan, , Poland

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Poznan, , Poland

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Rzeszów, , Poland

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Sopot, , Poland

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Swidnica, , Poland

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Torun, , Poland

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Tychy, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Wroclaw, , Poland

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Wroclaw, , Poland

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Wroclaw, , Poland

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Włocławek, , Poland

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Chelyabinsk, , Russia

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Moscow, , Russia

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Novosibirsk, , Russia

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Novosibirsk, , Russia

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Perm, , Russia

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Pyatigorsk, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Samara, , Russia

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Saratov, , Russia

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Stavropol, , Russia

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Tomsk, , Russia

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Tyumen, , Russia

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Zrenjanin, , Serbia

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Busan, , South Korea

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Busan, , South Korea

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Daegu, , South Korea

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Daegu, , South Korea

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Daejeon, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Ivano-Frankivsk, , Ukraine

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Kherson, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Lviv, , Ukraine

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Vinnytsia, , Ukraine

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Vinnytsia, , Ukraine

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Zhytomyr, , Ukraine

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Countries

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United States Austria Bulgaria Canada Georgia Germany Hungary Italy Poland Russia Serbia South Korea Ukraine

Other Identifiers

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PN-943-03

Identifier Type: -

Identifier Source: org_study_id

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