A Phase II Clinical Trial Comparing the Efficacy of RO7198457 Versus Watchful Waiting in Patients With ctDNA-positive, Resected Stage II (High Risk) and Stage III Colorectal Cancer

NCT ID: NCT04486378

Last Updated: 2026-01-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

327 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-03-08

Study Completion Date

2030-08-31

Brief Summary

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This is a multi-site, open-label, Phase II, randomized, trial to compare the efficacy of RO7198457 versus watchful waiting in patients with circulating tumor DNA (ctDNA) positive, surgically resected Stage II/III rectal cancer, or Stage II (high risk)/Stage III colon cancer.

Detailed Description

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Patients will receive up to 15 doses of RO7198457 over the course of trial treatment.

Conditions

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Colorectal Cancer Stage II Colorectal Cancer Stage III

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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RO7198457

Participants will receive a recommended dose of RO7198457.

Group Type EXPERIMENTAL

RO7198457 intravenous (IV)

Intervention Type DRUG

RO7198457 administered as an IV injection at protocol-specified intervals over 12 months.

Observational Group

Observational group will undergo watchful waiting, which is the standard of care in this setting.

Group Type OTHER

Observational group (no intervention)

Intervention Type OTHER

watchful waiting

Biomarker Cohort

Group Type EXPERIMENTAL

RO7198457 intravenous (IV)

Intervention Type DRUG

RO7198457 administered as an IV injection at protocol-specified intervals over 12 months.

Exploratory Cohort

Group Type EXPERIMENTAL

RO7198457 intravenous (IV)

Intervention Type DRUG

RO7198457 administered as an IV injection at protocol-specified intervals over 12 months.

Colorectal Liver Metastasis (CLM) Cohort

Group Type EXPERIMENTAL

RO7198457 intravenous (IV)

Intervention Type DRUG

RO7198457 administered as an IV injection at protocol-specified intervals over 12 months.

Interventions

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RO7198457 intravenous (IV)

RO7198457 administered as an IV injection at protocol-specified intervals over 12 months.

Intervention Type DRUG

Observational group (no intervention)

watchful waiting

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Patients must be a man or woman of at least 18 years of age.
* Patients must have Stage II/Stage III rectal cancer or Stage II (high risk)/Stage III colon cancer per American Joint Committee on Cancer (AJCC) 2017 that has been surgically totally resected (R0 confirmed by pathology report). Stage II (high risk) colon cancer is defined as Stage II disease with any of the following risk factors for recurrence:

* T4
* Grade ≥ 3.
* Clinical presentation with bowel obstruction or perforation.
* Histological signs of vascular, lymphatic or perineural invasion.
* \< 12 nodes evaluated after surgery.

* For the CLM Cohort: patients must have metastatic colorectal cancer (mCRC) (Stage IV) with resected CLM (synchronous and metachronous CLM within 6 months of initial diagnosis) per AJCC 2017, after standard of care (SoC) primary resection and curative-intent hepatectomy (R0 confirmed by pathology report) with or without (neo-)adjuvant chemotherapy (prior to hepatectomy), and planned adjuvant chemotherapy.
* For the Biomarker Cohort: patients with tumors of the colon, including but not limited to, colon adenocarcinoma, carcinoid tumors (including goblet cell carcinoid/adenocarcinoma), and tumors of the appendix, whose tumors were surgically resected and are planned for adjuvant chemotherapy (per institutional standards), can be included.
* Patients must have detectable ctDNA prior to start of adjuvant chemotherapy (AdCTx) (except for the Biomarker Cohort).

* ctDNA assay must be performed through this trial or study BNT000-001 ctDNA screening protocol.
* Patients must have an Eastern Cooperative Oncology Group Performance Status of 0-1.
* Patients must have adequate hematologic, bone marrow and organ function as defined by the protocol.
* Adequate tumor material in formalin-fixed paraffin embedded blocks or as sectioned tissue (only upon approval by sponsor) must be available (as described in the laboratory manual). For the CLM Cohort: tumor material must come from primary resection for patients who undergo staged approach, or from available archival material from the previously untreated tumor biopsy from the primary.
* At least 5 tumor neoantigens identified in the provided tumor sample.
* The patient has started a standard of care AdCTx preferably within 8 weeks but no later than 10 weeks post-surgery and has completed at least 3 months of treatment of a 3- or a 6-month course of chemotherapy (including rest days). For the CLM Cohort: patient must have completed AdCTx with or without (neo-)adjuvant chemotherapy for up to 6 months in total or total intended amount determined by care providers per SoC. AdCTx must have started preferably within 8 weeks, but no later than 10 weeks, after hepatectomy. For the Biomarker Cohort: patient must have received at least one cycle of adjuvant chemotherapy per institutional standards.

Exclusion Criteria

* Patients with uncontrolled intercurrent illness as defined by the protocol.
* Diagnosed microsatellite instability high tumors.
* Prior therapy with any of the following:

* Neo-adjuvant (radio)chemotherapy prior to surgery.
* Treatment with systemic immunosuppressive medication within 2 weeks prior to initiation of trial treatment or anticipation of need for systemic immunosuppressive medication during trial treatment, with the exception of low dose steroids defined as 10 mg oral prednisone (or equivalent).
* Current or recent (within the 28 days prior to randomization) treatment with another investigational drug.

* Exception for the CLM Cohort: primary tumor must be resected and (neo-)adjuvant chemotherapy prior to curative-intent hepatectomy is accepted.
* Toxicities from previous anti-cancer therapies that have not resolved to baseline levels or to Grade 1 or less except for alopecia and peripheral neuropathy.
* Patients who developed metastatic disease during screening/receiving standard of care treatment (not applicable for the Exploratory Cohort or the Biomarker Cohort).
* Patients with known past or current malignancy other than inclusion diagnosis, except for:

* Cervical carcinoma of Stage 1B or less.
* Non-invasive basal cell or squamous cell skin carcinoma.
* Non-invasive, superficial bladder cancer.
* Prostate cancer with a current prostate-specific antigen level \< 0.1 ng/mL.
* Any curable cancer with a complete response of \> 2 years duration.
* Patients with known allergies, hypersensitivity, or intolerance to RO7198457 or its excipients.
* Patients who had major surgery (e.g., surgery requiring general anesthesia) within 4 weeks before screening, or will not have fully recovered from surgery, or have surgery planned during the time the patient are expected to participate in the trial.
* Patients with positive serology for hepatitis B indicative of active hepatitis B infection:

* Positive test for hepatitis B surface antigen (HBsAg) OR
* Negative test for HBsAg AND positive test for antibodies to hepatitis B core antigens (anti-HBc) AND positive test for hepatitis B virus (HBV) DNA.

* Serological markers indicative of vaccination (isolated antibodies to hepatitis B surface antigens \[anti-HBs\]) or resolved natural infection without viral load (anti-HBc with negative HBsAg and negative HBV DNA) are not exclusionary.
* Active Hepatitis C virus (HCV) infection; patients who have completed curative antiviral treatment with HCV viral load below the limit of quantification are allowed.
* Patients who have a history of human immunodeficiency virus (HIV) antibody positivity, or tests positive for HIV at screening.
* Patients who have had prior splenectomy.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Genentech, Inc.

INDUSTRY

Sponsor Role collaborator

BioNTech SE

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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BioNTech Responsible Person

Role: STUDY_DIRECTOR

BioNTech SE

Locations

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Mayo Clinic - Scottsdale

Scottsdale, Arizona, United States

Site Status WITHDRAWN

John Muir Clinical Research Center

Concord, California, United States

Site Status ACTIVE_NOT_RECRUITING

The Oncology Institute of Hope and Innovation

Glendale, California, United States

Site Status WITHDRAWN

Marin Cancer Care

Greenbrae, California, United States

Site Status ACTIVE_NOT_RECRUITING

St Joseph Hospital of Orange

Orange, California, United States

Site Status WITHDRAWN

Sansum Clinic

Santa Barbara, California, United States

Site Status ACTIVE_NOT_RECRUITING

Rocky Mountain Cancer Centers - Denver Midtwon

Denver, Colorado, United States

Site Status ACTIVE_NOT_RECRUITING

Boca Raton Regional Hospital

Boca Raton, Florida, United States

Site Status WITHDRAWN

Florida Cancer Specialist South

Fort Myers, Florida, United States

Site Status WITHDRAWN

Mayo Clinic Florida

Jacksonville, Florida, United States

Site Status WITHDRAWN

Florida Cancer Specialists

West Palm Beach, Florida, United States

Site Status WITHDRAWN

Cancer Care Center of Decatur, Cancer Care Specialists of IL

Decatur, Illinois, United States

Site Status ACTIVE_NOT_RECRUITING

Indiana University Melvin and Bren Simon Comprehensive Cancer

Indianapolis, Indiana, United States

Site Status ACTIVE_NOT_RECRUITING

University of Kansas Cancer Center

Westwood, Kansas, United States

Site Status WITHDRAWN

University of Louisville - James Graham Brown Cancer Center

Louisville, Kentucky, United States

Site Status WITHDRAWN

Josephine Ford Cancer Center-Henry Ford Cancer Center

Detroit, Michigan, United States

Site Status WITHDRAWN

Allina Health

Minneapolis, Minnesota, United States

Site Status ACTIVE_NOT_RECRUITING

Mayo Clinic Rochester

Rochester, Minnesota, United States

Site Status WITHDRAWN

New York Oncology Hematology, P.C.

Albany, New York, United States

Site Status WITHDRAWN

Weill Cornell Medical College

New York, New York, United States

Site Status WITHDRAWN

New York - Presbyterian Hospital - Columbia University Medical center

New York, New York, United States

Site Status WITHDRAWN

Oncology Hematology Care Clinical Trials

Cincinnati, Ohio, United States

Site Status ACTIVE_NOT_RECRUITING

Willamette Valley Cancer Institute and Research Center

Eugene, Oregon, United States

Site Status WITHDRAWN

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status ACTIVE_NOT_RECRUITING

Hollings Cancer Center Medical University Of South Carolina

Charleston, South Carolina, United States

Site Status WITHDRAWN

Sarah Cannon (Tennessee Oncology - Nashville)

Nashville, Tennessee, United States

Site Status WITHDRAWN

Sarah Cannon Research Institute (SCRI) Oncology Partners

Nashville, Tennessee, United States

Site Status ACTIVE_NOT_RECRUITING

Texas Oncology, P.A. - Austin

Austin, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

Texas Oncology-Baylor Charles A. Sammons Cancer Center

Dallas, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

The University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status RECRUITING

Texas Oncology-San Antonio Medical Center

San Antonio, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

Texas Oncology - Northeast Texas

Tyler, Texas, United States

Site Status ACTIVE_NOT_RECRUITING

Virginia Cancer Specialists

Fairfax, Virginia, United States

Site Status ACTIVE_NOT_RECRUITING

Benaroya Research Institute at Virginia Mason

Seattle, Washington, United States

Site Status ACTIVE_NOT_RECRUITING

University of Washington

Seattle, Washington, United States

Site Status ACTIVE_NOT_RECRUITING

MultiCare Institute for Research & Innovation

Spokane, Washington, United States

Site Status WITHDRAWN

Northwest Cancer Specialists P.C.

Vancouver, Washington, United States

Site Status ACTIVE_NOT_RECRUITING

University of Wisconsin Carbone Cancer Center

Madison, Wisconsin, United States

Site Status ACTIVE_NOT_RECRUITING

Froedtert Hospital and Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status WITHDRAWN

Imeldaziekenhuis General Hospital

Bonheiden, , Belgium

Site Status ACTIVE_NOT_RECRUITING

VZW Algemeen Ziekenhuis AZ Klina

Brasschaat, , Belgium

Site Status ACTIVE_NOT_RECRUITING

Institut Jules Bordet

Brussels, , Belgium

Site Status WITHDRAWN

GHDC (Grand Hopital de Charleroi)

Charleroi, , Belgium

Site Status ACTIVE_NOT_RECRUITING

AZ Groeninge

Kortrijk, , Belgium

Site Status ACTIVE_NOT_RECRUITING

Centres Hospitaliers Jolimont

La Louvière, , Belgium

Site Status ACTIVE_NOT_RECRUITING

Universitaire Ziekenhuizen Leuven

Leuven, , Belgium

Site Status ACTIVE_NOT_RECRUITING

AZ Delta Roeselare

Roeselare, , Belgium

Site Status ACTIVE_NOT_RECRUITING

GasthuisZusters Antwerpen - Sint-Augustinus

Wilrijk, , Belgium

Site Status ACTIVE_NOT_RECRUITING

Universite Catholique de Louvain (UCL) - Cliniques Universitaires Saint-Luc

Woluwe-Saint-Lambert, , Belgium

Site Status ACTIVE_NOT_RECRUITING

The Ottawa Hospital Cancer Centre

Ottawa, , Canada

Site Status ACTIVE_NOT_RECRUITING

Princess Margaret Cancer Centre

Toronto, , Canada

Site Status ACTIVE_NOT_RECRUITING

Charité - Universitätsmedizin Berlin

Berlin, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitaetsklinikum St. Josef-Hospital Bochum

Bochum, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitätsklinikum Bonn, Med. Klinik u. Poliklinik I

Bonn, , Germany

Site Status ACTIVE_NOT_RECRUITING

Klinikum Esslingen GmbH

Esslingen am Neckar, , Germany

Site Status ACTIVE_NOT_RECRUITING

Krankenhaus Nordwest GmbH - Institut Fuer Klinisch-Onkologische Forschung (IKF)

Frankfurt am Main, , Germany

Site Status ACTIVE_NOT_RECRUITING

Klinikum der Johann Wolfgang Goethe-Universitaet Frankfurt

Frankfurt am Main, , Germany

Site Status ACTIVE_NOT_RECRUITING

Studiengesellschaft BSF

Halle, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitätsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status ACTIVE_NOT_RECRUITING

Hämatologisch-Onkologische Praxis Eppendorf

Hamburg, , Germany

Site Status ACTIVE_NOT_RECRUITING

Asklepios Klinik Altona

Hamburg, , Germany

Site Status ACTIVE_NOT_RECRUITING

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status ACTIVE_NOT_RECRUITING

National Center for Tumor Diseases (NCT) Heidelberg

Heidelberg, , Germany

Site Status ACTIVE_NOT_RECRUITING

SLK-Kliniken Heilbronn GmbH

Heilbronn, , Germany

Site Status ACTIVE_NOT_RECRUITING

Staedtisches Krankenhaus Kiel gGmbH

Kiel, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitaetsklinikum Leipzig AoeR

Leipzig, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitaetsmedizin der Johannes Gutenberg Universitaet Mainz KoeR

Mainz, , Germany

Site Status ACTIVE_NOT_RECRUITING

Klinikum der Philipps-Universität Marburg

Marburg, , Germany

Site Status ACTIVE_NOT_RECRUITING

LMU Klinikum (Campus Großhadern) Medizinische Klinik Universität München

München, , Germany

Site Status ACTIVE_NOT_RECRUITING

Städtisches Klinikum München GmbH, Klinikum Neuperlach

München, , Germany

Site Status ACTIVE_NOT_RECRUITING

OhO Ostholstein Onkologie

Oldenburg in Holstein, , Germany

Site Status ACTIVE_NOT_RECRUITING

Prosper Hospital

Recklinghausen, , Germany

Site Status ACTIVE_NOT_RECRUITING

Robert-Bosch-Krankenhaus - Centrum fuer Tumorerkrankungen

Stuttgart, , Germany

Site Status WITHDRAWN

Universitätsklinikum Ulm

Ulm, , Germany

Site Status ACTIVE_NOT_RECRUITING

Universitätsklinikum Würzburg

Würzburg, , Germany

Site Status ACTIVE_NOT_RECRUITING

Complejo Hospitalario Universitario A Coruna

A Coruña, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Nuestra Senora de Sonsoles

Ávila, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitari Germans Trias - ICO Badalona

Badalona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Institut Clinic Hematolo/Oncologia- ICMHO, Hospital Clinic i Provincial de Barcelona

Barcelona, , Spain

Site Status RECRUITING

Hospital de la Santa Creu i Sant Pau

Barcelona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Clinica Universidad Navarra

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Ramón y Cajal

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Clinico San Carlos

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Fundacion Jimenez Diaz

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario La Paz

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario HMN Sanchinarro, Centro Integral Oncologico Clara Campal (CIOCC)

Madrid, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Puerta de Hierro de Majadahonda

Majadahonda, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Regional Universitario Carlos Haya Malaga - Instituto de Investigacion Biomedica de Malaga

Málaga, , Spain

Site Status ACTIVE_NOT_RECRUITING

Complejo Hospitalario de Orense

Ourense, , Spain

Site Status ACTIVE_NOT_RECRUITING

Clinica Universitaria de Navarra

Pamplona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Complejo Hospitalario de Navarra (CHN)

Pamplona, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Marques De Valdecilla

Santander, , Spain

Site Status ACTIVE_NOT_RECRUITING

Complejo Hospitalario Universitario De Santiago De Compostela

Santiago de Compostela, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Virgen del Rocio - Hospital de la Mujer

Seville, , Spain

Site Status ACTIVE_NOT_RECRUITING

Consorcio Hospital General Valencia

Valencia, , Spain

Site Status ACTIVE_NOT_RECRUITING

Complexo Hospitalario Universitario de Vigo (CHUVI)

Vigo, , Spain

Site Status ACTIVE_NOT_RECRUITING

Hospital Universitario Miguel Servet

Zaragoza, , Spain

Site Status ACTIVE_NOT_RECRUITING

Lunds Universitet - Medicinska Fakulteten (Lund University Faculty of Medicine)

Lund, , Sweden

Site Status ACTIVE_NOT_RECRUITING

Sodersjukhuset, Onkologiska Kliniken

Stockholm, , Sweden

Site Status ACTIVE_NOT_RECRUITING

Karolinska Universitetssjukhuset Solna

Stockholm, , Sweden

Site Status WITHDRAWN

The Clatterbridge Cancer Centre NHS Foundation Trust

Bebington, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Queen Elizabeth Hospital Birmingham-University Hospitals Birmingham NHS Foundation Trust

Birmingham, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Velindre NHS Trust, Velindre Cancer Centre

Cardiff, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Hull and East Yorkshire Hospitals NHS Trust - Castle Hill Hospital

Cottingham, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Dorset County Hospital NHS Foundation Trust - Dorset County Hospital

Dorchester, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Beatson West of Scotland Cancer Centre - Gartnavel Royal Hospital - NHS Greater Glasgow and Clyde

Glasgow, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

St Bartholomew's Hospital-Barts Health NHS Trust

London, , United Kingdom

Site Status RECRUITING

University College London Hospitals NHS Foundation Trust

London, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Royal Free London NHS Foundation Trust

London, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Guy's and St Thomas' Hospital NHS Foundation Trust

London, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

The Royal Marsden NHS Foundation Trust- Chelsea

London, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

The Christie NHS Foundation Trust

Manchester, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

The Newcastle upon Tyne Hospitals NHS Foundation Trust - Freeman Hospital

Newcastle upon Tyne, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Churchill Hospital - Oxford University Hospitals NHS Foundation Trust

Oxford, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Royal Preston Hospital - Lancashire Teaching Hospitals NHS Foundation Trust

Preston, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

University Hospital Southampton NHS Foundation Trust - Southampton General Hospital

Southampton, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

The Royal Marsden NHS Foundation Trust

Sutton, , United Kingdom

Site Status RECRUITING

Torbay Hospital - South Devon Healthcare Nhs Foundation Trust, Lowes Bridge

Torquay, , United Kingdom

Site Status ACTIVE_NOT_RECRUITING

Countries

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United States Belgium Canada Germany Spain Sweden United Kingdom

Central Contacts

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BioNTech clinical trials patient information

Role: CONTACT

+49 6131 9084 ext. 0

Other Identifiers

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2020-000451-12

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

U1111-1250-5294

Identifier Type: OTHER

Identifier Source: secondary_id

2023-509516-28-00

Identifier Type: CTIS

Identifier Source: secondary_id

BNT122-01

Identifier Type: -

Identifier Source: org_study_id

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