Carboplatin-paclitaxel With Retifanlimab or Placebo in Participants With Locally Advanced or Metastatic Squamous Cell Anal Carcinoma (POD1UM-303/InterAACT 2).

NCT ID: NCT04472429

Last Updated: 2025-11-03

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

308 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-01-12

Study Completion Date

2025-09-26

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study is a Phase 3 global, multicenter, placebo-controlled double-blind randomized study that will enroll participants with inoperable locally recurrent or metastatic SCAC not previously treated with systemic chemotherapy.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Squamous Cell Carcinoma of the Anal Canal

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors
Double Blind

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Group A : carboplatin+paclitaxel+placebo

Participants will receive carboplatin on Day 1,paclitaxel on Day1,8, 15, and placebo on Day 1 of each 28 day cycle

Group Type PLACEBO_COMPARATOR

carboplatin

Intervention Type DRUG

carboplatin will be administered intravenous on Day 1 of each 28 day cycle

paclitaxel

Intervention Type DRUG

paclitaxel will be administered intravenous on Days 1,8, and 15 of each 28 day cycle

Group B : carboplatin+paclitaxel+retifanlimab

Participants will receive carboplatin on Day 1,paclitaxel on Day1,8, 15, and retifanlimab on Day 1 of each 28 day cycle

Group Type EXPERIMENTAL

carboplatin

Intervention Type DRUG

carboplatin will be administered intravenous on Day 1 of each 28 day cycle

paclitaxel

Intervention Type DRUG

paclitaxel will be administered intravenous on Days 1,8, and 15 of each 28 day cycle

retifanlimab

Intervention Type DRUG

retifanlimab will be administered intravenous on Day 1 of each 28 day cycle

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

carboplatin

carboplatin will be administered intravenous on Day 1 of each 28 day cycle

Intervention Type DRUG

paclitaxel

paclitaxel will be administered intravenous on Days 1,8, and 15 of each 28 day cycle

Intervention Type DRUG

retifanlimab

retifanlimab will be administered intravenous on Day 1 of each 28 day cycle

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

INCMGA00012

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Able to comprehend and willing to sign a written ICF for the study.

* Are 18 years of age or older (or as applicable per local country requirements).
* Histologically or cytologically verified, inoperable locally recurrent or metastatic SCAC.
* No prior systemic therapy other than the following: a. Chemotherapy administered concomitantly with radiotherapy as a radiosensitizing agent is permitted.

b. Prior neoadjuvant or adjuvant therapy if completed ≥ 6 months before study entry.
* Has measurable disease per RECIST v1.1 as determined by local site investigator/radiology assessment. Tumor lesions situated in a previously irradiated area, or in an area subjected to other loco-regional therapy, are usually not considered measurable unless there has been demonstrated progression in the lesion.
* Able and willing to provide adequate tissue sample and whole blood sample with central testing result prior to randomization. Biopsy for archival samples should have occurred within 9 months prior to randomization.
* ECOG performance status 0 to 1.
* If HIV-positive, then must be stable as defined by: a. CD4+ count ≥ 200/μL, b. Undetectable viral load per standard of care assay, c. Receiving antiretroviral therapy (ART/HAART) for at least 4 weeks prior to study enrollment, and have not experienced any HIV-related opportunistic infection for at least 4 weeks prior to study enrollment.
* Willingness to avoid pregnancy or fathering children

Exclusion Criteria

* Has received prior PD-(L)1 directed therapy
* Has received prior radiotherapy with or without radiosensitizing chemotherapy within 28 days of Cycle 1 Day 1 except for palliative radiation (30 Gy or less) which is restricted for 14 days of Cycle 1 Day 1 (note: all toxicities associated should have resolved to Grade ≤ 1).
* Participants with laboratory outside of the protocol defined ranges.
* History of second malignancy within 3 years (with exceptions).
* Clinically significant pulmonary, cardiac, gastrointestinal or autoimmune disorders.
* Active bacterial, fungal, or viral infections, including hepatitis A, B, and C and IV antibiotic use within 7 days of Cycle 1 Day 1.
* Receipt of a live vaccine within 28 days of planned start of study therapy.
* History of organ transplant, including allogeneic stem cell transplantation.
* Known active CNS metastases and/or carcinomatous meningitis.
* Known hypersensitivity to platinum, paclitaxel, another monoclonal antibody, or any of the excipients that cannot be controlled with standard measures (eg, antihistamines, corticosteroids).
* Participant is pregnant or breastfeeding.
* Current use of protocol defined prohibited medication.
* Has pre-existing peripheral neuropathy that is ≥ Grade 2 by CTCAE v5.
* Inability or unlikely, in the opinion of the investigator, to comply with the Protocol requirements
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

The University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status

City of Hope National Medical Center

Duarte, California, United States

Site Status

UC Davis Comprehensive Cancer Center

Sacramento, California, United States

Site Status

Sansum Clinic

Santa Barbara, California, United States

Site Status

Rocky Mountain Cancer Center

Denver, Colorado, United States

Site Status

Ochsner Clinic

New Orleans, Louisiana, United States

Site Status

Maryland Oncology Hematology, P.A.

Columbia, Maryland, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Texas Oncology

Austin, Texas, United States

Site Status

Baylor Scott and White Research Institute

Dallas, Texas, United States

Site Status

Renovatio Clinical Consultants Llc

The Woodlands, Texas, United States

Site Status

Texas Oncology-Wichita Falls Texoma Cancer Center

Wichita Falls, Texas, United States

Site Status

Virginia Cancer Specialists, Pc

Arlington, Virginia, United States

Site Status

Blue Ridge Cancer Care

Roanoke, Virginia, United States

Site Status

Princess Alexandra Hospital Australia

Woolloongabba, Queensland, Australia

Site Status

Flinders Medical Centre

Bedford Park, South Australia, Australia

Site Status

Monash Medical Centre Clayton

Clayton, Victoria, Australia

Site Status

Zna Middelheim

Antwerp, , Belgium

Site Status

Ulb Hospital Erasme

Brussels, , Belgium

Site Status

Herlev Og Gentofte Hospital

Herlev, , Denmark

Site Status

Vejle Hospital

Vejle, , Denmark

Site Status

Institut de Cancerologie de L Ouest - Site Paul Papin

Angers, , France

Site Status

Chu Besancon Hospital Jean Minjoz

Besançon, , France

Site Status

Centre Hospitalier Universitaire de Bordeaux

Bordeaux, , France

Site Status

Centre Leon Berard

Lyon, , France

Site Status

Chu Hopital de La Timone

Marseille, , France

Site Status

Institut Du Cancer de Montpellier

Montpellier, , France

Site Status

Centre Antoine Laccassagne

Nice, , France

Site Status

Hospital Universitaire Pitie-Salpetriere

Paris, , France

Site Status

Hospital de La Miletrie

Poitiers, , France

Site Status

Chu de Rennes - Hospital Pontchaillou

Rennes, , France

Site Status

Hopital Charles Nicolle Chu Rouen Hospital de Bois-Guillaume

Rouen, , France

Site Status

Centre de Lutte Contre Le Cancer - Institut de Cancerologie de L'Ouest - Rene Gauducheau

Saint-Herblain, , France

Site Status

Institut de Cancerologie de Strasbourg

Strasbourg, , France

Site Status

Chu Toulouse Hopital Rangueil

Toulouse, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

Universitatsklinikum Bonn Aoer

Bonn, , Germany

Site Status

University Clinic Carl Gustav Carus Technical University Dresden

Dresden, , Germany

Site Status

Asklepios Klinik Altona

Hamburg, , Germany

Site Status

Fondazione Irccs Ca Granda Ospedale Maggiore

Milan, , Italy

Site Status

Azienda Socio Sanitaria Territoriale Grande Ospedale Metropolitano Niguarda

Milan, , Italy

Site Status

Comitato Etico Fondazione Irccs Istituto Nazionale Dei Tumori Milano

Milan, , Italy

Site Status

European Institute of Oncology

Milan, , Italy

Site Status

Azienda Socio Sanitaria Territoriale Grande Ospedale Metropolitano Niguarda

Milan, , Italy

Site Status

University Di Cagliari-Presidio Policlinico Monserrato

Monserrato, , Italy

Site Status

Azienda Ospedaliera Universitaria University Degli Studi Della Campania Luigi Vanvitelli

Napoli, , Italy

Site Status

Iov - Istituto Oncologico Veneto Irccs

Padua, , Italy

Site Status

Azienda Ospedaliero Universitaria Pisana

Pisa, , Italy

Site Status

Ospedale Degli Infermi

Rimini, , Italy

Site Status

I.R.C.C.S. Casa Sollievo Della Sofferenza

San Giovanni Rotondo, , Italy

Site Status

Azienda Ospedaliero Universitaria Ospedali Riuniti

Torrette, , Italy

Site Status

National Cancer Center Hospital

Chūōku, , Japan

Site Status

Kyushu University Hospital

Fukuoka, , Japan

Site Status

Saitama Medical University International Medical Center

Hidaka-shi, , Japan

Site Status

Aichi Cancer Center Hospital

Nagoya, , Japan

Site Status

Osaka International Cancer Institute

Osaka, , Japan

Site Status

Tohoku University Hospital

Sendai, , Japan

Site Status

Center Hospital of the National Center For Global Health and Medicine

Shinjuku-ku, , Japan

Site Status

Haukeland University Hospital

Bergen, , Norway

Site Status

Oslo Universitetssykehus

Oslo, , Norway

Site Status

Panoncology Trials Pan American Center For Oncology Trials, Llc

San Juan, , Puerto Rico

Site Status

Complejo Hospitalario Universitario A Coruna

A Coruña, , Spain

Site Status

Hospital General Universitario Vall D Hebron

Barcelona, , Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario de La Paz

Madrid, , Spain

Site Status

Son Espases University Hospital

Palma de Mallorca, , Spain

Site Status

Hospital Universitario Virgen Del Rocio

Seville, , Spain

Site Status

Hospital Universitario Miguel Servet

Zaragoza, , Spain

Site Status

Sahlgrenska University Hospital

Gothenburg, , Sweden

Site Status

Skaenes Universitetssjukhus Lund

Lund, , Sweden

Site Status

Stockholm South General Hospital Sodersjukhuset

Stockholm, , Sweden

Site Status

Royal Sussex County Hospital

Brighton, , United Kingdom

Site Status

Addenbrooke'S Hospital

Cambridge, , United Kingdom

Site Status

Royal Surrey County Hospital

Guildford, , United Kingdom

Site Status

Castle Hill Hospital

Hull, , United Kingdom

Site Status

Leeds Teaching Hospital

Leeds, , United Kingdom

Site Status

Royal Free London Nhs Foundation Trust

London, , United Kingdom

Site Status

The Royal Marsden Nhs Foundation Trust - Chelsea

London, , United Kingdom

Site Status

The Christie Nhs Foundation Trust Uk

Manchester, , United Kingdom

Site Status

Churchill Hospital

Oxford, , United Kingdom

Site Status

Royal Preston Hospital

Preston, , United Kingdom

Site Status

The Royal Marsden Nhs Foundation Trust - Sutton

Sutton, , United Kingdom

Site Status

Royal Cornwall Hospital Truro Sunrise Centre

Truro, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Belgium Denmark France Germany Italy Japan Norway Puerto Rico Spain Sweden United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Rao S, Samalin-Scalzi E, Evesque L, Ben Abdelghani M, Morano F, Roy A, Dahan L, Tamberi S, Dhadda AS, Saunders MP, Casanova N, Guimbaud R, Lievre A, Maurel J, Fakih M, Tian C, Harrison J, Jones MM, Cornfeld M, Spano JP, Rochefort P; POD1UM-303/InterAACT-2 study investigators. Retifanlimab with carboplatin and paclitaxel for locally recurrent or metastatic squamous cell carcinoma of the anal canal (POD1UM-303/InterAACT-2): a global, phase 3 randomised controlled trial. Lancet. 2025 Jun 14;405(10495):2144-2152. doi: 10.1016/S0140-6736(25)00631-2.

Reference Type DERIVED
PMID: 40517007 (View on PubMed)

Rao S, Jones M, Bowman J, Tian C, Spano JP. POD1UM-303/InterAACT 2: A phase III, global, randomized, double-blind study of retifanlimab or placebo plus carboplatin-paclitaxel in patients with locally advanced or metastatic squamous cell anal carcinoma. Front Oncol. 2022 Aug 24;12:935383. doi: 10.3389/fonc.2022.935383. eCollection 2022.

Reference Type DERIVED
PMID: 36091159 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2024-512331-72-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

2020-000826-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCMGA 0012-303

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Vectibix for the Treatment of Anal Cancer
NCT01285778 COMPLETED PHASE2