Trial Outcomes & Findings for A Study of Selexipag Assessing Right Ventricular Remodeling in Pulmonary Arterial Hypertension by Cardiac Magnetic Resonance Imaging (NCT NCT04435782)

NCT ID: NCT04435782

Last Updated: 2025-03-30

Results Overview

Change from baseline to Week 26 in RVSV assessed by pulmonary artery flow MRI was reported.

Recruitment status

TERMINATED

Study phase

PHASE4

Target enrollment

9 participants

Primary outcome timeframe

Baseline, Week 26

Results posted on

2025-03-30

Participant Flow

Participant milestones

Participant milestones
Measure
Selexipag
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Overall Study
STARTED
9
Overall Study
COMPLETED
5
Overall Study
NOT COMPLETED
4

Reasons for withdrawal

Reasons for withdrawal
Measure
Selexipag
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Overall Study
Study terminated by sponsor
4

Baseline Characteristics

A Study of Selexipag Assessing Right Ventricular Remodeling in Pulmonary Arterial Hypertension by Cardiac Magnetic Resonance Imaging

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Selexipag
n=9 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Age, Continuous
42.2 years
STANDARD_DEVIATION 13.28 • n=93 Participants
Age, Customized
In utero
0 Participants
n=93 Participants
Age, Customized
Preterm newborn infants (gestational age < 37 wks)
0 Participants
n=93 Participants
Age, Customized
Newborns (0-27 days)
0 Participants
n=93 Participants
Age, Customized
Infants and toddlers (28 days-23 months)
0 Participants
n=93 Participants
Age, Customized
Children (2-11 years)
0 Participants
n=93 Participants
Age, Customized
Adolescents (12-17 years)
0 Participants
n=93 Participants
Age, Customized
Adults (18-64 years)
9 Participants
n=93 Participants
Age, Customized
From 65-84 years
0 Participants
n=93 Participants
Age, Customized
85 years and over
0 Participants
n=93 Participants
Sex: Female, Male
Female
6 Participants
n=93 Participants
Sex: Female, Male
Male
3 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
9 Participants
n=93 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=93 Participants
Race (NIH/OMB)
Asian
7 Participants
n=93 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=93 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=93 Participants
Race (NIH/OMB)
White
2 Participants
n=93 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=93 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants

PRIMARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure and "n" (Number Analyzed) signifies participants evaluable for specified rows. As pre-specified in the statistical analysis plan (SAP), participant wise data was collected and reported due to very limited number of participants enrolled.

Change from baseline to Week 26 in RVSV assessed by pulmonary artery flow MRI was reported.

Outcome measures

Outcome measures
Measure
Selexipag
n=6 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Change From Baseline to Week 26 in Right Ventricular Stroke Volume (RVSV) Assessed by Pulmonary Artery Flow Magnetic Resonance Imaging (MRI)
Participant 1
38.35 Milliliter (mL)
Change From Baseline to Week 26 in Right Ventricular Stroke Volume (RVSV) Assessed by Pulmonary Artery Flow Magnetic Resonance Imaging (MRI)
Participant 2
-1.53 Milliliter (mL)
Change From Baseline to Week 26 in Right Ventricular Stroke Volume (RVSV) Assessed by Pulmonary Artery Flow Magnetic Resonance Imaging (MRI)
Participant 3
16.53 Milliliter (mL)
Change From Baseline to Week 26 in Right Ventricular Stroke Volume (RVSV) Assessed by Pulmonary Artery Flow Magnetic Resonance Imaging (MRI)
Participant 4
11 Milliliter (mL)
Change From Baseline to Week 26 in Right Ventricular Stroke Volume (RVSV) Assessed by Pulmonary Artery Flow Magnetic Resonance Imaging (MRI)
Participant 5
27.2 Milliliter (mL)
Change From Baseline to Week 26 in Right Ventricular Stroke Volume (RVSV) Assessed by Pulmonary Artery Flow Magnetic Resonance Imaging (MRI)
Participant 6
14.07 Milliliter (mL)

SECONDARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure and "n" (Number Analyzed) signifies participants evaluable for specified rows. As pre-specified in the SAP, participant wise data was collected and reported due to very limited number of participants enrolled.

Change from baseline to Week 26 in RVEDV assessed by MRI was reported.

Outcome measures

Outcome measures
Measure
Selexipag
n=6 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Change From Baseline to Week 26 in Right Ventricular End-Diastolic Volume (RVEDV) Assessed by MRI
Participant 1
40.57 Milliliter
Change From Baseline to Week 26 in Right Ventricular End-Diastolic Volume (RVEDV) Assessed by MRI
Participant 2
-8.89 Milliliter
Change From Baseline to Week 26 in Right Ventricular End-Diastolic Volume (RVEDV) Assessed by MRI
Participant 3
23.58 Milliliter
Change From Baseline to Week 26 in Right Ventricular End-Diastolic Volume (RVEDV) Assessed by MRI
Participant 4
6.79 Milliliter
Change From Baseline to Week 26 in Right Ventricular End-Diastolic Volume (RVEDV) Assessed by MRI
Participant 5
3.71 Milliliter
Change From Baseline to Week 26 in Right Ventricular End-Diastolic Volume (RVEDV) Assessed by MRI
Participant 6
7.82 Milliliter

SECONDARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure and "n" (Number Analyzed) signifies participants evaluable for specified rows. As pre-specified in the SAP, participant wise data was collected and reported due to very limited number of participants enrolled.

Change from baseline to Week 26 in RVESV assessed by MRI was reported.

Outcome measures

Outcome measures
Measure
Selexipag
n=6 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Change From Baseline to Week 26 in Right Ventricular End-Systolic Volume (RVESV) Assessed by MRI
Participant 1
2.23 Milliliter
Change From Baseline to Week 26 in Right Ventricular End-Systolic Volume (RVESV) Assessed by MRI
Participant 2
-7.36 Milliliter
Change From Baseline to Week 26 in Right Ventricular End-Systolic Volume (RVESV) Assessed by MRI
Participant 3
7.05 Milliliter
Change From Baseline to Week 26 in Right Ventricular End-Systolic Volume (RVESV) Assessed by MRI
Participant 4
-4.22 Milliliter
Change From Baseline to Week 26 in Right Ventricular End-Systolic Volume (RVESV) Assessed by MRI
Participant 5
-23.5 Milliliter
Change From Baseline to Week 26 in Right Ventricular End-Systolic Volume (RVESV) Assessed by MRI
Participant 6
-6.25 Milliliter

SECONDARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure and "n" (Number Analyzed) signifies participants evaluable for specified rows. As pre-specified in the SAP, participant wise data was collected and reported due to very limited number of participants enrolled.

Change from baseline to Week 26 in RVEF assessed by MRI was reported. RVEF was the fraction of the end-diastolic volume (EDV) that is ejected out of right ventricle with each contraction. EDV is the volume of blood within a ventricle immediately before a contraction.

Outcome measures

Outcome measures
Measure
Selexipag
n=6 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Change From Baseline to Week 26 in Right Ventricular Ejection Fraction (RVEF) Assessed by MRI
Participant 1
9.65 Percentage of EDV
Change From Baseline to Week 26 in Right Ventricular Ejection Fraction (RVEF) Assessed by MRI
Participant 2
0.42 Percentage of EDV
Change From Baseline to Week 26 in Right Ventricular Ejection Fraction (RVEF) Assessed by MRI
Participant 3
6.96 Percentage of EDV
Change From Baseline to Week 26 in Right Ventricular Ejection Fraction (RVEF) Assessed by MRI
Participant 4
5.01 Percentage of EDV
Change From Baseline to Week 26 in Right Ventricular Ejection Fraction (RVEF) Assessed by MRI
Participant 6
7.62 Percentage of EDV
Change From Baseline to Week 26 in Right Ventricular Ejection Fraction (RVEF) Assessed by MRI
Participant 5
19.12 Percentage of EDV

SECONDARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure and "n" (Number Analyzed) signifies participants evaluable for specified rows. As pre-specified in the SAP, participant wise data was collected and reported due to very limited number of participants enrolled.

Change from baseline to Week 26 in RV mass index assessed by MRI was reported.

Outcome measures

Outcome measures
Measure
Selexipag
n=6 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Change From Baseline to Week 26 in Right Ventricular (RV) Mass Index Assessed by MRI
Participant 2
2.72 Grams per meter square (g/m^2)
Change From Baseline to Week 26 in Right Ventricular (RV) Mass Index Assessed by MRI
Participant 3
-12.69 Grams per meter square (g/m^2)
Change From Baseline to Week 26 in Right Ventricular (RV) Mass Index Assessed by MRI
Participant 4
0.09 Grams per meter square (g/m^2)
Change From Baseline to Week 26 in Right Ventricular (RV) Mass Index Assessed by MRI
Participant 5
-16.56 Grams per meter square (g/m^2)
Change From Baseline to Week 26 in Right Ventricular (RV) Mass Index Assessed by MRI
Participant 6
-2.41 Grams per meter square (g/m^2)
Change From Baseline to Week 26 in Right Ventricular (RV) Mass Index Assessed by MRI
Participant 1
-11.03 Grams per meter square (g/m^2)

SECONDARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure and "n" (Number Analyzed) signifies participants evaluable for specified rows. As pre-specified in the SAP, participant wise data was collected and reported due to very limited number of participants enrolled.

Change in RVGLS was a measure of longitudinal percent change in length of endocardium at Week 26 from baseline length assessed by MRI.

Outcome measures

Outcome measures
Measure
Selexipag
n=6 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Change From Baseline to Week 26 in Right Ventricular Global Longitudinal Strain (RVGLS) Assessed by MRI
Participant 1: RVGLS Endocardium
-4.26 Percent change in length of endocardium
Change From Baseline to Week 26 in Right Ventricular Global Longitudinal Strain (RVGLS) Assessed by MRI
Participant 2: RVGLS Endocardium
-5.31 Percent change in length of endocardium
Change From Baseline to Week 26 in Right Ventricular Global Longitudinal Strain (RVGLS) Assessed by MRI
Participant 3: RVGLS Endocardium
-12.8 Percent change in length of endocardium
Change From Baseline to Week 26 in Right Ventricular Global Longitudinal Strain (RVGLS) Assessed by MRI
Participant 4: RVGLS Endocardium
-5.61 Percent change in length of endocardium
Change From Baseline to Week 26 in Right Ventricular Global Longitudinal Strain (RVGLS) Assessed by MRI
Participant 5: RVGLS Endocardium
-14.45 Percent change in length of endocardium
Change From Baseline to Week 26 in Right Ventricular Global Longitudinal Strain (RVGLS) Assessed by MRI
Participant 6: RVGLS Endocardium
-1.74 Percent change in length of endocardium

SECONDARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure.

WHO functional classification for PAH ranged from Class I (no limitation in physical activity, ordinary physical activity does not cause undue dyspnea or fatigue, chest pain or near syncope), Class II (slight limitation of physical activity, ordinary physical activity cause undue dyspnea or fatigue, chest pain or near syncope), Class III (marked limitation of physical activity, less than ordinary activity cause undue dyspnea or fatigue, chest pain or near syncope) and Class IV (cannot perform a physical activity without any symptoms, dyspnea and/or fatigue may even be present at rest). Change from baseline in WHO functional class was classified into "Improved", "No change" and "Worsened". Improvement =reduction in functional class; worsened =increase in functional class; and no change = no change in functional class.

Outcome measures

Outcome measures
Measure
Selexipag
n=8 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Number of Participants With Change From Baseline to Week 26 in World Health Organization (WHO) Functional Class
Baseline: Class I
0 Participants
Number of Participants With Change From Baseline to Week 26 in World Health Organization (WHO) Functional Class
Baseline: Class II
4 Participants
Number of Participants With Change From Baseline to Week 26 in World Health Organization (WHO) Functional Class
Baseline: Class III
4 Participants
Number of Participants With Change From Baseline to Week 26 in World Health Organization (WHO) Functional Class
Baseline: Class IV
0 Participants
Number of Participants With Change From Baseline to Week 26 in World Health Organization (WHO) Functional Class
Week 26: Improved
3 Participants
Number of Participants With Change From Baseline to Week 26 in World Health Organization (WHO) Functional Class
Week 26: Unchanged
5 Participants
Number of Participants With Change From Baseline to Week 26 in World Health Organization (WHO) Functional Class
Week 26: Worsened
0 Participants

SECONDARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure and "n" (Number Analyzed) signifies participants evaluable for specified rows. As pre-specified in the SAP, participant wise data was collected and reported due to very limited number of participants enrolled.

NT pro-BNP is a cardiac biomarker that is released in the blood in response to changes in the pressure inside of the heart. Levels go up when heart failure develops or gets worse, and levels go down when heart failure is stable or improves. This biomarker helps to measure the changes in the severity of heart failure over time in response to therapy.

Outcome measures

Outcome measures
Measure
Selexipag
n=6 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Change From Baseline to Week 26 in N-terminal-Pro-Hormone Brain Natriuretic Peptide (NT-proBNP)
Participant 1
-202.376 nanograms/liter (ng/L)
Change From Baseline to Week 26 in N-terminal-Pro-Hormone Brain Natriuretic Peptide (NT-proBNP)
Participant 2
142.9233 nanograms/liter (ng/L)
Change From Baseline to Week 26 in N-terminal-Pro-Hormone Brain Natriuretic Peptide (NT-proBNP)
Participant 3
-261.4904 nanograms/liter (ng/L)
Change From Baseline to Week 26 in N-terminal-Pro-Hormone Brain Natriuretic Peptide (NT-proBNP)
Participant 4
78.6501 nanograms/liter (ng/L)
Change From Baseline to Week 26 in N-terminal-Pro-Hormone Brain Natriuretic Peptide (NT-proBNP)
Participant 5
-215.8226 nanograms/liter (ng/L)
Change From Baseline to Week 26 in N-terminal-Pro-Hormone Brain Natriuretic Peptide (NT-proBNP)
Participant 6
-762.5677 nanograms/liter (ng/L)

SECONDARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure and "n" (Number Analyzed) signifies participants evaluable for specified rows. As pre-specified in the SAP, participant wise data was collected and reported due to very limited number of participants enrolled.

6MWD was the distance that a participant could walk in 6 minutes. Participants were asked to perform the test at a pace that was comfortable to them, with as many breaks as they needed.

Outcome measures

Outcome measures
Measure
Selexipag
n=6 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Change From Baseline to Week 26 in 6-Minute Walk Distance (6MWD)
Participant 1
-72 Meter
Change From Baseline to Week 26 in 6-Minute Walk Distance (6MWD)
Participant 2
0 Meter
Change From Baseline to Week 26 in 6-Minute Walk Distance (6MWD)
Participant 3
275 Meter
Change From Baseline to Week 26 in 6-Minute Walk Distance (6MWD)
Participant 4
14 Meter
Change From Baseline to Week 26 in 6-Minute Walk Distance (6MWD)
Participant 5
17 Meter
Change From Baseline to Week 26 in 6-Minute Walk Distance (6MWD)
Participant 6
16 Meter

SECONDARY outcome

Timeframe: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)

Population: Safety analysis set included all participants who received at least 1 dose of study intervention.

An AE was any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship. Serious adverse event (SAE) was any untoward medical occurrence that at any dose resulted in death, was life-threatening, requires inpatient hospitalization or prolongation of existing hospitalization, resulted in persistent or significant disability/incapacity, was a congenital anomaly/birth defect, was a suspected transmission of any infectious agent via a medicinal product. Any AE occurring at or after the initial administration of study intervention up to 3 days after last dose of study intervention was considered as treatment-emergent.

Outcome measures

Outcome measures
Measure
Selexipag
n=9 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Number of Participants With Treatment-Emergent Adverse Events (AEs) and Serious Adverse Events (SAEs)
AEs
9 Participants
Number of Participants With Treatment-Emergent Adverse Events (AEs) and Serious Adverse Events (SAEs)
SAEs
1 Participants

SECONDARY outcome

Timeframe: Day 1 up to last dose of study drug (up to Week 52)

Population: Safety analysis set included all participants who received at least 1 dose of study intervention.

Number of participants with AEs leading to premature discontinuation of study drug were reported. An AE was any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship.

Outcome measures

Outcome measures
Measure
Selexipag
n=9 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Number of Participants With Adverse Events (AEs) Leading to Premature Discontinuation of Study Drug
0 Participants

SECONDARY outcome

Timeframe: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)

Population: Safety analysis set included all participants who received at least 1 dose of study intervention.

Number of participants with AESI were reported. An AE was any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship. AESI were anaemia, bleeding events, gastrointestinal disturbances denoting intestinal intussusception (manifested as ileus or obstruction), hyperthyroidism, hypotension, light-dependent non-melanoma skin malignancies, major adverse cardiovascular events (MACE), medication errors, ophthalmological effects associated to retinal vascular system, pregnancy, pulmonary venoocclusive disease associated with pulmonary oedema, renal function impairment / acute renal failure.

Outcome measures

Outcome measures
Measure
Selexipag
n=9 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Number of Participants With Adverse Events of Special Interest (AESI)
3 Participants

SECONDARY outcome

Timeframe: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)

Population: Safety analysis set included all participants who received at least 1 dose of study intervention.

Number of participants with treatment-emergent marked laboratory abnormalities in alanine aminotransferase, aspartate aminotransferase, alkaline phosphatase, total bilirubin, creatinine, sodium, potassium, hemoglobin, hematocrit; EVF; PCV (male), hematocrit; EVF; PCV (female), platelets (assuming no platelet cluster), leukocytes; white blood cells, Neutrophils (Abs), Eosinophils (Abs), lymphocytes (Abs) were reported. Abnormalities that occurred after study treatment start and up to 3 days after study treatment discontinuation, that were not present at baseline, were treatment-emergent. Treatment-emergent marked laboratory abnormalities were determined at the investigator's discretion.

Outcome measures

Outcome measures
Measure
Selexipag
n=9 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Number of Participants With Treatment-Emergent Marked Laboratory Abnormalities
3 Participants

SECONDARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure and "n" (Number Analyzed) signifies participants evaluable for specified rows. As pre-specified in the SAP, participant wise data was collected and reported due to very limited number of participants enrolled.

The risk score is derived for each participant considering the following non-invasive low-risk criteria among the 8 variables: absence of clinical signs of right heart failure, absence of symptoms progression, absence of syncope, WHO FC I-II, 6MWD greater than (\>) 440 meter, NT-proBNP less than (\<) 300 ng/L, Right atrial (RA) area \<18 centimeter square (cm\^2) as determined by echocardiography (Echo), absence of pericardial effusion, as determined by Echo. Number of low-risk criteria at baseline and Week 26 constitutes risk score and were derived for each participant by adding '1' for each of above criteria met. Number of low-risk criteria among the 8 variables for each participant can vary from 0 (worse participants) to 8 (healthier participants). Higher score indicated healthier participants.

Outcome measures

Outcome measures
Measure
Selexipag
n=6 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 8 Variables
Participant 1
1 Score on a scale
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 8 Variables
Participant 2
1 Score on a scale
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 8 Variables
Participant 3
3 Score on a scale
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 8 Variables
Participant 4
1 Score on a scale
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 8 Variables
Participant 5
1 Score on a scale
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 8 Variables
Participant 6
1 Score on a scale

SECONDARY outcome

Timeframe: Baseline, Week 26

Population: Safety analysis set included all participants who received at least 1 dose of study intervention. Here, "N" (Overall number of participants analyzed) signifies participants evaluable for this outcome measure and "n" (Number Analyzed) signifies participants evaluable for specified rows. As pre-specified in the SAP, participant wise data was collected and reported due to very limited number of participants enrolled.

The risk score is derived for each participant considering the following non-invasive low-risk criteria among the 3 variables: WHO FC I-II, 6MWD \>440 m, NT-proBNP \< 300 ng/L. Number of low-risk criteria at baseline and Week 26 constitutes risk score and were derived for each participant by adding '1' for each of above criteria met. Number of low-risk criteria among the 3 variables for each participant can vary from 0 (worse participants) to 3 (healthier participants). Higher score indicated healthier participants.

Outcome measures

Outcome measures
Measure
Selexipag
n=6 Participants
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 3 Variables
Participant 1
1 Score on a scale
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 3 Variables
Participant 2
0 Score on a scale
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 3 Variables
Participant 3
2 Score on a scale
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 3 Variables
Participant 4
1 Score on a scale
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 3 Variables
Participant 5
1 Score on a scale
Change From Baseline to Week 26 in Number of Non-invasive Low-risk Criteria Among the 3 Variables
Participant 6
1 Score on a scale

Adverse Events

Selexipag

Serious events: 1 serious events
Other events: 9 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Selexipag
n=9 participants at risk
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Cardiac disorders
Cardiac Failure
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Reproductive system and breast disorders
Vaginal Haemorrhage
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.

Other adverse events

Other adverse events
Measure
Selexipag
n=9 participants at risk
Participants with pulmonary arterial hypertension (PAH) received a 200 microgram (mcg) selexipag tablet orally on the evening of Day 1, followed by twice-daily dosing starting from Day 2. The dose of selexipag was increased by 200 mcg each week to allow each participant to reach their individual maximum dose (iMD), up to 1600 mcg twice daily, by the end of Week 12. From Week 13 onwards, participants received their iMD of 1600 mcg selexipag tablets orally twice daily until Week 52. Participants were then followed for safety up to 30 days after the last dose of selexipag.
Blood and lymphatic system disorders
Anaemia
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Ear and labyrinth disorders
Vertigo
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Eye disorders
Xerophthalmia
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Gastrointestinal disorders
Abdominal Discomfort
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Gastrointestinal disorders
Dental Caries
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Gastrointestinal disorders
Diarrhoea
55.6%
5/9 • Number of events 8 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Gastrointestinal disorders
Dyspepsia
11.1%
1/9 • Number of events 2 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Gastrointestinal disorders
Nausea
77.8%
7/9 • Number of events 8 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Gastrointestinal disorders
Vomiting
22.2%
2/9 • Number of events 3 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
General disorders
Chest Pain
22.2%
2/9 • Number of events 2 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
General disorders
Face Oedema
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
General disorders
Fatigue
22.2%
2/9 • Number of events 2 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
General disorders
Oedema Peripheral
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
General disorders
Pyrexia
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Infections and infestations
Covid-19
33.3%
3/9 • Number of events 3 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Infections and infestations
Fungal Skin Infection
11.1%
1/9 • Number of events 2 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Infections and infestations
Nasopharyngitis
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Infections and infestations
Urinary Tract Infection
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Investigations
Alanine Aminotransferase Increased
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Investigations
Aspartate Aminotransferase Increased
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Investigations
Body Temperature Increased
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Investigations
Vitamin D Decreased
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Investigations
Weight Decreased
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Metabolism and nutrition disorders
Decreased Appetite
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Metabolism and nutrition disorders
Iron Deficiency
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Musculoskeletal and connective tissue disorders
Back Pain
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Musculoskeletal and connective tissue disorders
Joint Swelling
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Musculoskeletal and connective tissue disorders
Myalgia
55.6%
5/9 • Number of events 6 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Musculoskeletal and connective tissue disorders
Pain in Jaw
44.4%
4/9 • Number of events 4 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Nervous system disorders
Dizziness Exertional
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Nervous system disorders
Headache
66.7%
6/9 • Number of events 7 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Nervous system disorders
Hypoaesthesia
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Nervous system disorders
Paraesthesia
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Renal and urinary disorders
Haematuria
11.1%
1/9 • Number of events 2 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Renal and urinary disorders
Renal Pain
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Reproductive system and breast disorders
Uterine Polyp
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Respiratory, thoracic and mediastinal disorders
Dyspnoea
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Respiratory, thoracic and mediastinal disorders
Dyspnoea Exertional
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Respiratory, thoracic and mediastinal disorders
Oropharyngeal Pain
22.2%
2/9 • Number of events 2 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Skin and subcutaneous tissue disorders
Rash
11.1%
1/9 • Number of events 2 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Vascular disorders
Flushing
22.2%
2/9 • Number of events 2 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Vascular disorders
Hot Flush
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.
Vascular disorders
Hypotension
11.1%
1/9 • Number of events 1 • All Cause Mortality: Day 1 up to 30 days after last dose of drug (up to Week 56), SAEs and non-SAEs: Day 1 up to 3 days after last dose of study drug (up to 52 weeks and 3 days that is 367 days)
Safety analysis set included all participants who received at least 1 dose of study intervention.

Additional Information

Study Responsible Scientist

Actelion Pharmaceuticals Ltd

Phone: 844-434-4210

Results disclosure agreements

  • Principal investigator is a sponsor employee If an investigator wishes to publish information from the study, a copy of the manuscript must be provided to the sponsor for review at least 60 days before submission for publication or presentation. If requested by the sponsor in writing, the investigator will withhold such publication for up to an additional 60 days to allow for filing of a patent application.
  • Publication restrictions are in place

Restriction type: OTHER