Vascular Endothelial Growth Factor-B (VEGF-B) Blockade With the Monoclonal Antibody CSL346 in Subjects With Diabetic Kidney Disease

NCT ID: NCT04419467

Last Updated: 2023-12-06

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

114 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-09-14

Study Completion Date

2022-10-24

Brief Summary

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This phase 2a, double-blind, randomized, placebo-controlled study will assess the efficacy, safety, tolerability, and pharmacokinetics (PK), of repeat doses of CSL346 in subjects with diabetic kidney disease (DKD) and albuminuria receiving standard of care treatment.

Detailed Description

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Conditions

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Diabetic Kidney Disease (DKD)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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CSL346 (low dose)

Administered as a single intravenous (IV) loading dose followed by subcutaneous (SC) infusions

Group Type EXPERIMENTAL

CSL346

Intervention Type BIOLOGICAL

VEGF-B antagonist monoclonal antibody

CSL346 (high dose)

Administered as a single intravenous (IV) loading dose followed by subcutaneous (SC) infusions

Group Type EXPERIMENTAL

CSL346

Intervention Type BIOLOGICAL

VEGF-B antagonist monoclonal antibody

Placebo

Administered as a single IV loading dose followed by SC infusions

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Normal saline

Interventions

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CSL346

VEGF-B antagonist monoclonal antibody

Intervention Type BIOLOGICAL

Placebo

Normal saline

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male and female subjects ≥ 25 years of age with a diagnosis of type 2 diabetes mellitus (T2DM)
* Urinary ACR ≥ 150 mg/g
* eGFR \> 20 mL/min/1.73m2
* Glycosylated HbA1c \< 12%

Exclusion Criteria

* Current diagnosis of type 1 diabetes mellitus
* History of acute kidney injury or chronic dialysis/renal transplant
* Uncontrolled hypertension or class III / IV heart failure
* Left ventricular ejection fraction \< 50% by echocardiogram
* Troponin-I \> the upper reference limit
* b-type natriuretic peptide \> 200 pg/mL
* ALT \> 2x the upper limit of normal
Minimum Eligible Age

25 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CSL Behring

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

CSL Behring

Locations

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California Kidney Specialists (CKS) - Citrus Office

Covina, California, United States

Site Status

Valley Research - Fresno

Fresno, California, United States

Site Status

Torrance Clinical Research (TCR) - Lomita

Lomita, California, United States

Site Status

Renal Medical Associate/NARI

Lynwood, California, United States

Site Status

Amicis Research Center

Northridge, California, United States

Site Status

California Medical Research Associates, Inc

Northridge, California, United States

Site Status

Riverside Nephrology Group

Riverside, California, United States

Site Status

West Orange Endocrinology

Ocoee, Florida, United States

Site Status

East-West Medical Research Institute

Honolulu, Hawaii, United States

Site Status

Omega Clinical Research

Metairie, Louisiana, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Renal and Transplant Associates

Springfield, Massachusetts, United States

Site Status

University of Missouri Health System

Columbia, Missouri, United States

Site Status

Palm Medical Group, LLC - Las Vegas

Las Vegas, Nevada, United States

Site Status

Center for Thyroid & Parathyroid Disorders

Staten Island, New York, United States

Site Status

Physicians East, P.A. - Endocrinology

Greenville, North Carolina, United States

Site Status

Vanderbilt University School of Medicine

Nashville, Tennessee, United States

Site Status

Juno Research, L.L.C.

Houston, Texas, United States

Site Status

The Endocrine Center

Houston, Texas, United States

Site Status

Renal Associates, P.A. - San Antonio

San Antonio, Texas, United States

Site Status

Primary Care Providers of Texas

San Antonio, Texas, United States

Site Status

Diabetes and Metabolism Specialists (DMS) - San Antonio

San Antonio, Texas, United States

Site Status

Hunter Diabetes Centre - The AIM Centre

Merewether, New South Wales, Australia

Site Status

St Vincent's Hospital

Fitzroy, Victoria, Australia

Site Status

The Austin Hospital

Heidelberg, Victoria, Australia

Site Status

The Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status

Sunshine Hospital

St Albans, Victoria, Australia

Site Status

Lyell McEwin Hospital

Elizabeth Vale, , Australia

Site Status

1240130 - University Health Network

Toronto, Ontario, Canada

Site Status

3760045 - Kaplan Medical Center

Rehovot, , Israel

Site Status

3760044 - Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

Middlemore Hospital

Auckland, , New Zealand

Site Status

Christchurch Hospital

Christchurch, , New Zealand

Site Status

Lipid and Diabetes Research Group

Christchurch, , New Zealand

Site Status

Endocrine Associates - Wellington

Wellington, , New Zealand

Site Status

Fundación de Investigación

San Juan, , Puerto Rico

Site Status

University of Puerto Rico - Puerto Rico Clinical and TRC

San Juan, , Puerto Rico

Site Status

Countries

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United States Australia Canada Israel New Zealand Puerto Rico

References

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Cooper M, Cherney DZI, Greene TH, Heerspink HJL, Jardine M, Lewis JB, Wong MG, Baquero E, Heise M, Jochems J, Lanchoney D, Liss C, Reiser D, Scotney P, Velkoska E, Dwyer JP. Vascular Endothelial Growth Factor-B Blockade with CSL346 in Diabetic Kidney Disease: A Phase 2A Randomized Controlled Trial. J Am Soc Nephrol. 2024 Nov 1;35(11):1546-1557. doi: 10.1681/ASN.0000000000000438. Epub 2024 Aug 16.

Reference Type DERIVED
PMID: 39150859 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CSL346_2001

Identifier Type: -

Identifier Source: org_study_id