Trial Outcomes & Findings for Anti-neutrophil Cytoplasmic Antibody in Interstitial Lung Disease. (NCT NCT04413149)

NCT ID: NCT04413149

Last Updated: 2024-05-17

Results Overview

Death from all causes Retrieved from medical records.

Recruitment status

COMPLETED

Target enrollment

80 participants

Primary outcome timeframe

From baseline until the date of death from all cause, up to 5 years

Results posted on

2024-05-17

Participant Flow

Participant milestones

Participant milestones
Measure
MPA-ILD Group
Among all the patients with ANCA-positive ILD, patients who fulfilled the MPA criteria were defined as MPA-ILD group.
ANCA-IIP Group
Patients with isolated ANCA-positivity who did not fulfill the MPA criteria were classified as ANCA-IIP group.
Overall Study
STARTED
31
49
Overall Study
COMPLETED
20
44
Overall Study
NOT COMPLETED
11
5

Reasons for withdrawal

Reasons for withdrawal
Measure
MPA-ILD Group
Among all the patients with ANCA-positive ILD, patients who fulfilled the MPA criteria were defined as MPA-ILD group.
ANCA-IIP Group
Patients with isolated ANCA-positivity who did not fulfill the MPA criteria were classified as ANCA-IIP group.
Overall Study
Death
10
5
Overall Study
Lung transplantation
1
0

Baseline Characteristics

Anti-neutrophil Cytoplasmic Antibody in Interstitial Lung Disease.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
MPA-ILD Group
n=31 Participants
Among all the patients with ANCA-positive ILD, patients who fulfilled the MPA criteria were defined as MPA-ILD group.
ANCA-IIP Group
n=49 Participants
Patients with isolated ANCA-positivity who did not fulfill the MPA criteria were classified as ANCA-IIP group.
Total
n=80 Participants
Total of all reporting groups
Age, Continuous
62 years
n=5 Participants
59 years
n=7 Participants
60 years
n=5 Participants
Sex: Female, Male
Female
19 Participants
n=5 Participants
25 Participants
n=7 Participants
44 Participants
n=5 Participants
Sex: Female, Male
Male
12 Participants
n=5 Participants
24 Participants
n=7 Participants
36 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
31 Participants
n=5 Participants
49 Participants
n=7 Participants
80 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
White
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Region of Enrollment
China
31 participants
n=5 Participants
49 participants
n=7 Participants
80 participants
n=5 Participants
Follow-up time
36 months
n=5 Participants
41 months
n=7 Participants
40 months
n=5 Participants
Fever
16 Participants
n=5 Participants
10 Participants
n=7 Participants
26 Participants
n=5 Participants
Cough
28 Participants
n=5 Participants
42 Participants
n=7 Participants
70 Participants
n=5 Participants
Dyspnea
20 Participants
n=5 Participants
29 Participants
n=7 Participants
49 Participants
n=5 Participants
Fatigue
6 Participants
n=5 Participants
5 Participants
n=7 Participants
11 Participants
n=5 Participants
Arthralgia
8 Participants
n=5 Participants
15 Participants
n=7 Participants
23 Participants
n=5 Participants
Crackling sound
19 Participants
n=5 Participants
26 Participants
n=7 Participants
45 Participants
n=5 Participants
Rash
3 Participants
n=5 Participants
7 Participants
n=7 Participants
10 Participants
n=5 Participants
Clubbing fingers
5 Participants
n=5 Participants
2 Participants
n=7 Participants
7 Participants
n=5 Participants
Mechanics hand
0 Participants
n=5 Participants
2 Participants
n=7 Participants
2 Participants
n=5 Participants
Gottron's sign
1 Participants
n=5 Participants
2 Participants
n=7 Participants
3 Participants
n=5 Participants
Renal involvement
30 Participants
n=5 Participants
0 Participants
n=7 Participants
30 Participants
n=5 Participants
Nervous system involvement
3 Participants
n=5 Participants
0 Participants
n=7 Participants
3 Participants
n=5 Participants
Cardiovascular involvement
2 Participants
n=5 Participants
0 Participants
n=7 Participants
2 Participants
n=5 Participants
Retinal involvement
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
White blood cell
9.34 ×10^9 cells/L
n=5 Participants
7.44 ×10^9 cells/L
n=7 Participants
8.54 ×10^9 cells/L
n=5 Participants
Neutrophil
6.79 ×10^9 cells/L
n=5 Participants
4.68 ×10^9 cells/L
n=7 Participants
5.65 ×10^9 cells/L
n=5 Participants
Lymphocyte
1.47 ×10^9 cells/L
n=5 Participants
2 ×10^9 cells/L
n=7 Participants
1.90 ×10^9 cells/L
n=5 Participants
Hemoglobin
116 g/L
n=5 Participants
137 g/L
n=7 Participants
132 g/L
n=5 Participants
Platelet
251 ×10^9 cells/L
n=5 Participants
234 ×10^9 cells/L
n=7 Participants
246 ×10^9 cells/L
n=5 Participants
Erythrocyte sedimentation rate
86 mm/h
n=5 Participants
28 mm/h
n=7 Participants
53 mm/h
n=5 Participants
C reactive protein
35.77 mg/dL
n=5 Participants
13.87 mg/dL
n=7 Participants
15.92 mg/dL
n=5 Participants
PaO2
71.5 mmHg
n=5 Participants
77.4 mmHg
n=7 Participants
75.9 mmHg
n=5 Participants
Creatinine
73 μmol/L
n=5 Participants
67 μmol/L
n=7 Participants
68 μmol/L
n=5 Participants
MPO-ANCA positive
26 Participants
n=5 Participants
19 Participants
n=7 Participants
45 Participants
n=5 Participants
PR3-ANCA positive
0 Participants
n=5 Participants
2 Participants
n=7 Participants
2 Participants
n=5 Participants
Rheumatoid factor
113.1 IU/mL
n=5 Participants
26.7 IU/mL
n=7 Participants
55.9 IU/mL
n=5 Participants
ANA positive
15 Participants
n=5 Participants
30 Participants
n=7 Participants
45 Participants
n=5 Participants
Anti-CCP positive
0 Participants
n=5 Participants
8 Participants
n=7 Participants
8 Participants
n=5 Participants
SSA positive
3 Participants
n=5 Participants
6 Participants
n=7 Participants
9 Participants
n=5 Participants
SSB positive
2 Participants
n=5 Participants
2 Participants
n=7 Participants
4 Participants
n=5 Participants
Jo-1 positive
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Scl-70 positive
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
FEV1
79.36 percent predicted
STANDARD_DEVIATION 17.92 • n=5 Participants
84.03 percent predicted
STANDARD_DEVIATION 16.93 • n=7 Participants
82.35 percent predicted
STANDARD_DEVIATION 17.32 • n=5 Participants
FVC
78.30 percent predicted
STANDARD_DEVIATION 16.89 • n=5 Participants
83.84 percent predicted
STANDARD_DEVIATION 19.10 • n=7 Participants
81.85 percent predicted
STANDARD_DEVIATION 18.42 • n=5 Participants
TLC
74.16 percent predicted
STANDARD_DEVIATION 12.73 • n=5 Participants
79.53 percent predicted
STANDARD_DEVIATION 13.55 • n=7 Participants
77.59 percent predicted
STANDARD_DEVIATION 13.43 • n=5 Participants
DLCO
56.56 percent predicted
STANDARD_DEVIATION 17.52 • n=5 Participants
62.12 percent predicted
STANDARD_DEVIATION 14.09 • n=7 Participants
60.12 percent predicted
STANDARD_DEVIATION 15.53 • n=5 Participants
Ground-glass opacity
25 Participants
n=5 Participants
44 Participants
n=7 Participants
69 Participants
n=5 Participants
Consolidation
4 Participants
n=5 Participants
4 Participants
n=7 Participants
8 Participants
n=5 Participants
Traction bronchiectasis
16 Participants
n=5 Participants
20 Participants
n=7 Participants
36 Participants
n=5 Participants
Honeycombing
11 Participants
n=5 Participants
8 Participants
n=7 Participants
19 Participants
n=5 Participants
Pulmonary artery dilation
3 Participants
n=5 Participants
1 Participants
n=7 Participants
4 Participants
n=5 Participants
Reticular pattern
20 Participants
n=5 Participants
29 Participants
n=7 Participants
49 Participants
n=5 Participants
Curved linear opacity
5 Participants
n=5 Participants
12 Participants
n=7 Participants
17 Participants
n=5 Participants
Pleural thickening
4 Participants
n=5 Participants
9 Participants
n=7 Participants
13 Participants
n=5 Participants
Interlobular septal thickening
16 Participants
n=5 Participants
23 Participants
n=7 Participants
39 Participants
n=5 Participants
Micronodular pattern
5 Participants
n=5 Participants
6 Participants
n=7 Participants
11 Participants
n=5 Participants
Subpleural bulla
10 Participants
n=5 Participants
10 Participants
n=7 Participants
20 Participants
n=5 Participants
Enlarged mediastinal lymph node
2 Participants
n=5 Participants
3 Participants
n=7 Participants
5 Participants
n=5 Participants
Usual interstitial pneumonia
4 Participants
n=5 Participants
3 Participants
n=7 Participants
7 Participants
n=5 Participants
Nonspecific interstitial pneumonia
18 Participants
n=5 Participants
33 Participants
n=7 Participants
51 Participants
n=5 Participants
Unclassifiable HRCT pattern
9 Participants
n=5 Participants
13 Participants
n=7 Participants
22 Participants
n=5 Participants

PRIMARY outcome

Timeframe: From baseline until the date of death from all cause, up to 5 years

Death from all causes Retrieved from medical records.

Outcome measures

Outcome measures
Measure
MPA-ILD Group
n=31 Participants
Among all the patients with ANCA-positive ILD, patients who fulfilled the MPA criteria were defined as MPA-ILD group.
ANCA-IIP Group
n=49 Participants
Patients with isolated ANCA-positivity who did not fulfill the MPA criteria were classified as ANCA-IIP group.
Death From All Causes
10 Participants
5 Participants

PRIMARY outcome

Timeframe: From baseline until the date of transplantation, up to 5 years

Number of patients who underwent lung transplantation Retrieved from medical records.

Outcome measures

Outcome measures
Measure
MPA-ILD Group
n=31 Participants
Among all the patients with ANCA-positive ILD, patients who fulfilled the MPA criteria were defined as MPA-ILD group.
ANCA-IIP Group
n=49 Participants
Patients with isolated ANCA-positivity who did not fulfill the MPA criteria were classified as ANCA-IIP group.
Number of Patients Who Underwent Lung Transplantation
1 Participants
0 Participants

Adverse Events

MPA-ILD Group

Serious events: 0 serious events
Other events: 0 other events
Deaths: 10 deaths

ANCA-IIP Group

Serious events: 0 serious events
Other events: 0 other events
Deaths: 5 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Dr. Shi Juhong

Peking Union Medical College Hospital

Phone: +86-13701178492

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place