Trial Outcomes & Findings for Safety and Efficacy of Autologous Platelet-Rich Plasma for Erectile Dysfunction. (NCT NCT04396795)

NCT ID: NCT04396795

Last Updated: 2024-01-09

Results Overview

Minimal clinically important difference (MCID) is measured by the number of participants who have achieved an increase in International Index of Erectile Function - Erectile Function Subdomain Score (IIEF-EF) based on their Erectile Dysfunction (ED) severity at baseline (an increase of 2 points from baseline for participants with mild ED and an increase of 5 points for participants with moderate ED). MCID in IIEF-EF scores are used to determine treatment efficacy of PRP compared to placebo. IIEF-EF is a 5-item subdomain self- evaluation questionnaire of erectile function with a total score ranging from 0-25 with the higher score indicating better erectile function. This outcome is reported as the number of participants who achieve MCID in each treatment group.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

61 participants

Primary outcome timeframe

1 month, 3 month, 6 month

Results posted on

2024-01-09

Participant Flow

Participant milestones

Participant milestones
Measure
PRP Group
Participants in this group will receive 2 sessions of autologous PRP penile injection, each administered 1 month apart ± 7 days Autologous Platelet Rich Plasma: Each injection session will consist of a total of 5 mL PRP infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum.
Placebo Group
Participants in this group will receive 2 sessions of placebo injection, each administered 1 month apart ± 7 days. Saline solution: Each injection session will consist of a total of 5 mL saline solution infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum
Baseline
STARTED
28
33
Baseline
COMPLETED
28
33
Baseline
NOT COMPLETED
0
0
Month 1
STARTED
28
33
Month 1
COMPLETED
26
30
Month 1
NOT COMPLETED
2
3
Month 3
STARTED
26
30
Month 3
COMPLETED
25
27
Month 3
NOT COMPLETED
1
3
Month 6
STARTED
25
27
Month 6
COMPLETED
22
24
Month 6
NOT COMPLETED
3
3

Reasons for withdrawal

Reasons for withdrawal
Measure
PRP Group
Participants in this group will receive 2 sessions of autologous PRP penile injection, each administered 1 month apart ± 7 days Autologous Platelet Rich Plasma: Each injection session will consist of a total of 5 mL PRP infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum.
Placebo Group
Participants in this group will receive 2 sessions of placebo injection, each administered 1 month apart ± 7 days. Saline solution: Each injection session will consist of a total of 5 mL saline solution infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum
Month 1
Lost to Follow-up
2
3
Month 3
Lost to Follow-up
1
3
Month 6
Lost to Follow-up
3
3

Baseline Characteristics

Safety and Efficacy of Autologous Platelet-Rich Plasma for Erectile Dysfunction.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
PRP Group
n=28 Participants
Participants in this group will receive 2 sessions of autologous PRP penile injection, each administered 1 month apart ± 7 days Autologous Platelet Rich Plasma: Each injection session will consist of a total of 5 mL PRP infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum.
Placebo Group
n=33 Participants
Participants in this group will receive 2 sessions of placebo injection, each administered 1 month apart ± 7 days. Saline solution: Each injection session will consist of a total of 5 mL saline solution infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum
Total
n=61 Participants
Total of all reporting groups
Age, Continuous
49 years
n=5 Participants
46 years
n=7 Participants
47 years
n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Sex: Female, Male
Male
28 Participants
n=5 Participants
33 Participants
n=7 Participants
61 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
15 Participants
n=5 Participants
21 Participants
n=7 Participants
36 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
13 Participants
n=5 Participants
12 Participants
n=7 Participants
25 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
4 Participants
n=5 Participants
6 Participants
n=7 Participants
10 Participants
n=5 Participants
Race (NIH/OMB)
White
23 Participants
n=5 Participants
26 Participants
n=7 Participants
49 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 1 month, 3 month, 6 month

Population: Not all subjects completed all visits due to lost to follow up or did not complete the IIEF questionnaire.

Minimal clinically important difference (MCID) is measured by the number of participants who have achieved an increase in International Index of Erectile Function - Erectile Function Subdomain Score (IIEF-EF) based on their Erectile Dysfunction (ED) severity at baseline (an increase of 2 points from baseline for participants with mild ED and an increase of 5 points for participants with moderate ED). MCID in IIEF-EF scores are used to determine treatment efficacy of PRP compared to placebo. IIEF-EF is a 5-item subdomain self- evaluation questionnaire of erectile function with a total score ranging from 0-25 with the higher score indicating better erectile function. This outcome is reported as the number of participants who achieve MCID in each treatment group.

Outcome measures

Outcome measures
Measure
PRP Group
n=24 Participants
Participants in this group will receive 2 sessions of autologous PRP penile injection, each administered 1 month apart ± 7 days Autologous Platelet Rich Plasma: Each injection session will consist of a total of 5 mL PRP infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum.
Placebo Group
n=28 Participants
Participants in this group will receive 2 sessions of placebo injection, each administered 1 month apart ± 7 days. Saline solution: Each injection session will consist of a total of 5 mL saline solution infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum
Number of Participants Achieving MCID in IIEF-EF.
Month 1
14 Participants
15 Participants
Number of Participants Achieving MCID in IIEF-EF.
Month 3
10 Participants
13 Participants
Number of Participants Achieving MCID in IIEF-EF.
Month 6
12 Participants
10 Participants

SECONDARY outcome

Timeframe: Baseline up to Month 1, Month 3, and Month 6

Population: Not all subjects completed all visits due to lost to follow up or did not complete the IIEF questionnaire.

IIEF-EF is a 5-item subdomain self-evaluation questionnaire of erectile function. Each item is scored from 0-5 with the total score ranging from 0-25 with the higher score indicating better erectile function.

Outcome measures

Outcome measures
Measure
PRP Group
n=24 Participants
Participants in this group will receive 2 sessions of autologous PRP penile injection, each administered 1 month apart ± 7 days Autologous Platelet Rich Plasma: Each injection session will consist of a total of 5 mL PRP infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum.
Placebo Group
n=28 Participants
Participants in this group will receive 2 sessions of placebo injection, each administered 1 month apart ± 7 days. Saline solution: Each injection session will consist of a total of 5 mL saline solution infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum
Change in IIEF-EF Scores
Baseline to Month 1
4.5 score on a scale
Interval 0.0 to 8.5
2 score on a scale
Interval -0.5 to 8.0
Change in IIEF-EF Scores
Baseline to Month 3
1 score on a scale
Interval -3.0 to 7.5
2 score on a scale
Interval -1.0 to 6.0
Change in IIEF-EF Scores
Baseline to Month 6
3.5 score on a scale
Interval 0.0 to 9.5
2 score on a scale
Interval -2.5 to 7.0

SECONDARY outcome

Timeframe: Baseline to Month 6

Population: Not all subjects completed all visits due to lost to follow up.

Change in Peak Systolic Velocity (PSV) assessed in cm/sec via ultrasound.

Outcome measures

Outcome measures
Measure
PRP Group
n=22 Participants
Participants in this group will receive 2 sessions of autologous PRP penile injection, each administered 1 month apart ± 7 days Autologous Platelet Rich Plasma: Each injection session will consist of a total of 5 mL PRP infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum.
Placebo Group
n=24 Participants
Participants in this group will receive 2 sessions of placebo injection, each administered 1 month apart ± 7 days. Saline solution: Each injection session will consist of a total of 5 mL saline solution infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum
Change in Doppler Ultrasound Parameters - Peak Systolic Velocity (PSV)
0.4 cm/sec
Interval -9.6 to 15.3
1.5 cm/sec
Interval -3.4 to 14.8

SECONDARY outcome

Timeframe: 24 weeks

Incidence of adverse events were reported as all urological and/or reproductive system AEs and all AEs with severity grade 3 or higher. Adverse Events severity was determined using CTCAE v5 criteria.

Outcome measures

Outcome measures
Measure
PRP Group
n=28 Participants
Participants in this group will receive 2 sessions of autologous PRP penile injection, each administered 1 month apart ± 7 days Autologous Platelet Rich Plasma: Each injection session will consist of a total of 5 mL PRP infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum.
Placebo Group
n=33 Participants
Participants in this group will receive 2 sessions of placebo injection, each administered 1 month apart ± 7 days. Saline solution: Each injection session will consist of a total of 5 mL saline solution infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum
Number of Adverse Events
1 events
1 events

SECONDARY outcome

Timeframe: Baseline and Month 6

Population: The number of participants analyzed are different in certain rows due to attrition and lost to follow up.

Number of participants who had an End Diastolic Velocity (EDV) value of greater than 0, as assessed by penile doppler ultrasound.

Outcome measures

Outcome measures
Measure
PRP Group
n=28 Participants
Participants in this group will receive 2 sessions of autologous PRP penile injection, each administered 1 month apart ± 7 days Autologous Platelet Rich Plasma: Each injection session will consist of a total of 5 mL PRP infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum.
Placebo Group
n=33 Participants
Participants in this group will receive 2 sessions of placebo injection, each administered 1 month apart ± 7 days. Saline solution: Each injection session will consist of a total of 5 mL saline solution infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum
Number of Participants With an End Diastolic Velocity (EDV) Value Greater Than 0, as Assessed by Penile Doppler Ultrasound at Baseline and Month 6.
Baseline
6 Participants
11 Participants
Number of Participants With an End Diastolic Velocity (EDV) Value Greater Than 0, as Assessed by Penile Doppler Ultrasound at Baseline and Month 6.
Month 6
9 Participants
8 Participants

Adverse Events

PRP Group

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Placebo Group

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
PRP Group
n=28 participants at risk
Participants in this group will receive 2 sessions of autologous PRP penile injection, each administered 1 month apart ± 7 days Autologous Platelet Rich Plasma: Each injection session will consist of a total of 5 mL PRP infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum.
Placebo Group
n=33 participants at risk
Participants in this group will receive 2 sessions of placebo injection, each administered 1 month apart ± 7 days. Saline solution: Each injection session will consist of a total of 5 mL saline solution infused slowly over a 2-minute period; 2.5 mL each injected to the right and left corpus cavernosum
Vascular disorders
Hematoma
0.00%
0/28 • 6 months
3.0%
1/33 • Number of events 1 • 6 months
Reproductive system and breast disorders
Reproductive system and breast disorders - Other, specify
3.6%
1/28 • Number of events 1 • 6 months
0.00%
0/33 • 6 months

Additional Information

Dr Ranjith Ramasamy

University of Miami, Miller School of Medicine - Desai Sethi Urology Institute

Phone: 305-243-4562

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place